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  • Saturday, Jun 24th
    13:00 – 14:15 ET
    OC 04.6 - Hemophilia Basic Science - FVIII and FIX
    Room: 520
    Moderator: Steven W. Pipe, MD – University of Michigan, Ann Arbor, MI, USA
    Moderator: Orla Rawley, PhD (she/her/hers) – Queen's University, Pathology and Molecular Medicine
    Hemophilia and Rare Bleeding Disorders
  • Saturday, Jun 24th
    13:00 – 14:15 ET
    OC 06.6 - Management of Acquired Bleeding
    Room: 510
    Moderator: Pratima Chowdary, MD – Katharine Dormandy Haemophilia and Thrombosis Centre, Royal Free London NHS Foundation Trust, London, United Kingdom
    Moderator: Rungrote Natesirinilkul, MD – Department of Pediatrics, Faculty of Medicine, Chiang Mai University, Chiang Mai, Thailand
    Hemophilia and Rare Bleeding Disorders
  • Saturday, Jun 24th
    13:00 – 14:15 ET
    OC 07.6 - Rare Bleeding Disorders I
    Room: 524
    Moderator: Roseline d'Oiron, MD – Centre for Haemophilia and Rare Congenital Bleeding Disorders, Bicêtre Hospital AP-HP, University of Paris-Saclay and UMR_S1176 INSERM, Le Kremlin-Bicêtre, France
    Moderator: Joel Livingston, MSc, MD, FRCPC – Stollery Children's Hospital / The University of Alberta
    Hemophilia and Rare Bleeding Disorders
  • Saturday, Jun 24th
    13:00 – 13:15 ET
    OC 04.1 - Exploring the hemostatic properties of extravascular factor IX in a hemophilia B mouse model
    Room: 520
    Presenting Author: Bonnie Chu (she/her/hers) – McMaster University
    Co-Author: Wajeeha Zaheer (she/her/hers) – McMaster University
    Co-Author: Paul Tieu – Thrombosis & Atherosclerosis Research Institute, McMaster University, Hamilton, Canada
    Co-Author: Hasam Madarati – McMaster University
    Co-Author: Colin Kretz, PhD – McMaster University
    Co-Author: Peter L. Gross, MD MSc FRCP(c) (he/him/his) – Department of Medicine, McMaster University
    Co-Author: Anthony KC. Chan, MBBS – McMaster University, McMaster Children’s Hospital, Hamilton, Canada
    Co-Author: Davide Matino, MD (he/him/his) – Department of Medicine, Division of Hematology, McMaster University, Hamilton, ON
    Hemophilia and Rare Bleeding Disorders
  • Saturday, Jun 24th
    13:00 – 13:15 ET
    OC 06.1 - Trauma Induces Mechanistic and Morphological Changes in Microfluidic Hemostasis
    Room: 510
    Co-Author: Rassam M.G. Rassam – Trauma and Transfusion Medicine Research Center, Department of Surgery, University of Pittsburgh
    Presenting Author: Devin M. Dishong – Trauma and Transfusion Medicine Research Center, Department of Surgery, University of Pittsburgh
    Co-Author: Katelin C. Rahn – Trauma and Transfusion Medicine Research Center, Department of Surgery, University of Pittsburgh
    Co-Author: Ronit Kar – University of Pittsburgh - School of Medicine
    Co-Author: Ricardo Fonseca – Department of Surgery, Washington University in St. Louis
    Co-Author: Melissa Canas – Department of Surgery, Washington University in St. Louis
    Co-Author: Jose Aldana – Department of Surgery, Washington University in St. Louis
    Co-Author: Hussain Afzal – Department of Surgery, Washington University in St. Louis,
    Co-Author: Kelly Bochicchio – Department of Surgery, Washington University in St. Louis
    Co-Author: Kimberly A. Thomas – Vitalant Research Institute
    Co-Author: Matthew D. Neal, MD FACS (he/him/his) – University of Pittsburgh
    Co-Author: Grant Bochicchio – Department of Surgery, Washington University in St. Louis
    Co-Author: Philip C. Spinella, MD – University of Pittsburgh School of Medicine
    Co-Author: Susan M. Shea, MSME, PhD (she/her/hers) – Trauma and Transfusion Medicine Research Center, Department of Surgery and Department of Bioengineering, University of Pittsburgh
    Hemophilia and Rare Bleeding Disorders
  • Saturday, Jun 24th
    13:00 – 13:15 ET
    OC 07.1 - Autologous CRISPR/Cas9 correction of a missense variant from a patient with severe, inherited FVII deficiency
    Room: 524
    Presenting Author: Giacomo Roman, MSc – Department of Hematology, Oslo University Hospital, Oslo, Norway
    Co-Author: Knut H. Lauritzen – Department of Hematology, Oslo University Hospital, Oslo, Norway
    Co-Author: Sean Harrison – Oslo University Hospital
    Co-Author: Gareth J Sullivan – Department of Pediatric Research, Oslo University Hospital, Oslo, Norway
    Co-Author: Nina Iversen – Department of Medical Genetics, Oslo University Hospital, Oslo, Norway
    Co-Author: Carola Elisabeth Henriksson – Institute of Clinical Medicine, University of Oslo, Oslo
    Co-Author: Heidi Glosli – Division of Paediatric and Adolescent Medicine Centre for Rare Disorders Oslo University Hospital Oslo Norway.
    Co-Author: Per Morten Sandset – Oslo University Hospital
    Co-Author: Benedicte Stavik – Department of Hematology, Oslo University Hospital, Oslo, Norway
    Co-Author: Maria Eugenia Chollet Dugarte, MD, PhD (she/her/hers) – Department of Hematology, Research Institute of Internal Medicine, Oslo University Hospital
    Hemophilia and Rare Bleeding Disorders
  • Saturday, Jun 24th
    13:15 – 13:30 ET
    OC 04.2 - B-Domain deleted Factor VIII shows clear differences in intracellular processing and cellular responses when compared to full length Factor VIII
    Room: 520
    Presenting Author: Rawya Al Rifai – Institute of Experimental Haematology and Transfusion Medicine and Center for Rare Diseases, University Hospital Bonn, Bonn, Germany
    Co-Author: Muhammad Ahmer Jamil – Institute of Experimental Haematology and Transfusion Medicine and Center for Rare Diseases, University Hospital Bonn, Bonn, Germany
    Co-Author: Salime El Hazzouri – University Clinic Bonn, Institute of experimental Haematology and Transfusion medicine
    Co-Author: Mira Ibrahim, MS – Institute of Experimental Haematology and Transfusion Medicine and Center for Rare Diseases, University Hospital Bonn, Bonn, Germany
    Co-Author: Nicole Nüsgen – Institute of Experimental Haematology and Transfusion Medicine and Center for Rare Diseases, University Hospital Bonn, Bonn, Germany
    Co-Author: Johannes Oldenburg, MD (he/him/his) – University Clinic Bonn AöR, Institute of Experimental Haematology and Transfusion Medicine, Bonn, Germany
    Co-Author: Osman EL-Maarri, Priv Doz, PhD (he/him/his) – Institute of Experimental Haematology and Transfusion Medicine and Center for Rare Diseases, University Hospital Bonn, Bonn, Germany
    Hemophilia and Rare Bleeding Disorders
  • Saturday, Jun 24th
    13:15 – 13:30 ET
    OC 06.2 - Emicizumab for Acquired Hemophilia A - A Case Series
    Room: 510
    Presenting Author: Matthias M Engelen, MD – University Hospitals Leuven, Belgium
    Co-Author: Johan Vandesande – University Hospitals Leuven, Belgium
    Co-Author: Johan De Bent – University Hospitals Leuven, Belgium
    Co-Author: Christine Van Laer, Clin Biol – University Hospitals Leuven, Belgium
    Co-Author: Veerle Labarque, MD, PhD – University Hospitals Leuven, Belgium
    Co-Author: Marc Jacquemin – University Hospitals Leuven, Belgium
    Co-Author: Kathelijne Peerlinck – University Hospitals Leuven, Belgium
    Co-Author: Peter Verhamme, MD, PhD – University Hospitals Leuven, Belgium
    Co-Author: Thomas Vanassche, MD PhD – University Hospitals Leuven, Belgium
    Hemophilia and Rare Bleeding Disorders
  • Saturday, Jun 24th
    13:15 – 13:30 ET
    OC 07.2 - Investigating the dominant negative effect of heterozygous F13B gene mutations detected from mild FXIII deficiency patients
    Room: 524
    Presenting Author: Haroon Javed, MSc – Institute of Experimental Haematology and Transfusion Medicine, University Hospital Bonn
    Co-Author: Sneha Singh, PhD (she/her/hers) – Institute of Experimental Hematology and Transfusion Medicine, University Clinic Bonn
    Co-Author: Samhitha Urs Ramaraje Urs, MSc – Institute of Experimental Haematology and Transfusion Medicine, University Clinic Bonn
    Co-Author: Hamideh Yadegari, PhD – University Clinic Bonn Institute of Experimental Hematology and Transfusion Medicine Venusberg-Campus 1
    Co-Author: Johannes Oldenburg, MD (he/him/his) – University Clinic Bonn AöR, Institute of Experimental Haematology and Transfusion Medicine, Bonn, Germany
    Co-Author: Arijit Biswas, PD Dr (Biol) – Institute of Experimental Haematology and Transfusion Medicine, University Clinic Bonn
    Hemophilia and Rare Bleeding Disorders
  • Saturday, Jun 24th
    13:30 – 13:45 ET
    OC 04.3 - Prospective FVIII intracellular trafficking routes involving GABARAP
    Room: 520
    Presenting Author: Salime El Hazzouri – University Clinic Bonn, Institute of experimental Haematology and Transfusion medicine
    Co-Author: Nicole Nüsgen – Institute of Experimental Haematology and Transfusion Medicine and Center for Rare Diseases, University Hospital Bonn, Bonn, Germany
    Co-Author: Rawya Al Rifai – Institute of Experimental Haematology and Transfusion Medicine and Center for Rare Diseases, University Hospital Bonn, Bonn, Germany
    Co-Author: Heike Singer – University Clinic Bonn, Institue of experimental Haematology and Transfusion medicine
    Co-Author: Nasim Shahidi Hamedani, PharmD PhD (she/her/hers) – University Hospital Bonn; Institute of Experimental Haematologie and Transfusion Medicine
    Co-Author: Johannes Oldenburg, MD (he/him/his) – University Clinic Bonn AöR, Institute of Experimental Haematology and Transfusion Medicine, Bonn, Germany
    Co-Author: Osman EL-Maarri, Priv Doz, PhD (he/him/his) – Institute of Experimental Haematology and Transfusion Medicine and Center for Rare Diseases, University Hospital Bonn, Bonn, Germany
    Hemophilia and Rare Bleeding Disorders
  • Saturday, Jun 24th
    13:30 – 13:45 ET
    OC 06.3 - Final Analysis Results from a Phase III Study of Emicizumab Prophylaxis for Acquired Hemophilia A (AGEHA)
    Room: 510
    Presenting Author: Midori Shima, MD, PhD – Thrombosis and Hemostasis Research Center, Nara Medical University, Kashihara, Japan
    Co-Author: Nobuaki Suzuki – Department of Transfusion Medicine, Nagoya University Hospital, Nagoya, Japan
    Co-Author: Hidekazu Nishikii – Department of Hematology, Faculty of Medicine, University of Tsukuba, Tsukuba, Japan
    Co-Author: Kagehiro Amano – Department of Laboratory Medicine, Tokyo Medical University
    Co-Author: Yoshiyuki Ogawa, MD, PhD – Department of Hematology, Gunma University Graduate School of Medicine, Maebashi, Japan
    Co-Author: Ryota Kobayashi – Chugai Pharmaceutical Co., Ltd., Tokyo, Japan
    Co-Author: Ryoto Ozaki – Chugai Pharmaceutical Co., Ltd., Tokyo, Japan
    Co-Author: Koichiro Yoneyama, MSc – Chugai Pharmaceutical Co., Ltd., Tokyo, Japan
    Co-Author: Narumi Mizuno – Chugai Pharmaceutical Co., Ltd., Tokyo, Japan
    Co-Author: Emiko Sakaida – Department of Hematology, Chiba University Hospital, Chiba, Japan
    Co-Author: Makoto Saito – Blood Disorders Center, Aiiku Hospital, Sapporo, Japan
    Co-Author: Takashi Okamura – Department of Hematology, St. Mary’s Hospital, Kurume, Japan
    Co-Author: Toshihiro Ito – Department of Infectious Diseases, National Hospital Organization Sendai Medical Center, Sendai, Japan
    Co-Author: Norimichi Hattori – Division of Hematology, Department of Medicine, Showa University School of Medicine, Tokyo, Japan
    Co-Author: Satoshi Higasa – Department of Hematology, Hyogo College of Medicine Hospital, Nishinomiya, Japan
    Co-Author: Yoshinobu Seki, MD, PhD – Department of Hematology, Uonuma Institute of Community Medicine, Niigata University Medical and Dental Hospital, Minami-uonuma, Japan
    Co-Author: Keiji Nogami – Nara Medical University, Nara, Japan
    Hemophilia and Rare Bleeding Disorders
  • Saturday, Jun 24th
    13:30 – 13:45 ET
    OC 07.3 - In vitro and ex vivo rescue of a nonsense mutation (F5 p.Arg1161Ter) responsible for severe coagulation factor V deficiency
    Room: 524
    Presenting Author: Alice M. Todaro, MSc – Department of Biochemistry, CARIM, Maastricht University, Maastricht (The Netherlands)
    Co-Author: Claudia M. Radu – Department of Medicine, Thrombotic and Haemorrhagic Diseases Unit, University of Padua Medical School, Padua (Italy)
    Co-Author: Maria Ciccone – Department of Medical Sciences, Section of Haematology, Sant’Anna Hospital, Ferrara University, Ferrara (Italy)
    Co-Author: Serena Toffanin – Department of Medicine, Thrombotic and Haemorrhagic Diseases Unit, University of Padua Medical School, Padua (Italy)
    Co-Author: Maria Luisa Serino – Department of Medical Sciences, Section of Haematology, Sant’Anna Hospital, Ferrara University, Ferrara (Italy)
    Co-Author: Elena Campello, MD, PhD (she/her/hers) – Department of Medicine, University of Padova, Italy
    Co-Author: Cristiana Bulato – Department of Medicine, Thrombotic and Haemorrhagic Diseases Unit, University of Padua Medical School, Padua (Italy)
    Co-Author: Barbara Lunghi – Department of Life Sciences and Biotechnology, Section of Biochemistry and Molecular Biology, Ferrara University, Ferrara (Italy)
    Co-Author: Donato Gemmati – Department of Medical Sciences, Section of Haematology, Sant’Anna Hospital, Ferrara University, Ferrara (Italy)
    Co-Author: Antonio Cuneo – Department of Medical Sciences, Section of Haematology, Sant’Anna Hospital, Ferrara University
    Co-Author: Tilman M. Hackeng, PhD – Coagulation Profile, Maastricht, The Netherlands
    Co-Author: Paolo Simioni, MD, PhD (he/him/his) – Department of Medicine, Thrombotic and Haemorrhagic Diseases Unit, University of Padua Medical School, Padua (Italy)
    Co-Author: Francesco Bernardi – Department of Life Sciences and Biotechnology, Section of Biochemistry and Molecular Biology, Ferrara University, Ferrara (Italy)
    Co-Author: Elisabetta Castoldi, PhD – Department of Biochemistry, CARIM, Maastricht University, Maastricht (The Netherlands)
    Hemophilia and Rare Bleeding Disorders
  • Saturday, Jun 24th
    13:45 – 14:00 ET
    OC 04.4 - A novel tailored correction approach for recurrent hemophilia-causing nonsense mutations through AntiCodon-Engineered suppressor tRNAs
    Room: 520
    Presenting Author: Maria Francesca Testa, PhD – Department of Life Sciences and Biotechnology and LTTA Center, University of Ferrara, Ferrara 44121, Italy
    Co-Author: Jhon D. Lueck – Department of Physiology and Pharmacology, University of Rochester School of Medicine and Dentistry, Rochester, NY 14642, USA
    Co-Author: Francesco Bernardi – Department of Life Sciences and Biotechnology, Section of Biochemistry and Molecular Biology, Ferrara University, Ferrara (Italy)
    Co-Author: Mirko Pinotti – Department of Life Sciences and Biotechnology and LTTA Center, University of Ferrara, Ferrara 44121, Italy
    Co-Author: Alessio Branchini – Department of Life Sciences and Biotechnology and LTTA Center, University of Ferrara, Ferrara 44121, Italy
    Hemophilia and Rare Bleeding Disorders
  • Saturday, Jun 24th
    13:45 – 14:00 ET
    OC 06.4 - Therapeutic efficacy of a novel humanized anti-ADAMTS13 antibody to treat left ventricular assist device-induced acquired von Willebrand syndrome
    Room: 510
    Presenting Author: Shannen J. Deconinck, PhD – Laboratory for Thrombosis Research, KU Leuven Kulak Kortrijk, Kortrijk, Belgium
    Co-Author: Christoph Nix – Abiomed Europe GmbH, Aachen, Germany
    Co-Author: Eveline Bennek-Schöpping – Abiomed Europe GmbH, Aachen, Germany
    Co-Author: An-Sofie Schelpe – Laboratory for Thrombosis Research, KU Leuven Campus Kulak Kortrijk, Kortrijk, Belgium
    Co-Author: Inge Pareyn – Laboratory for Thrombosis Research, KU Leuven Campus Kulak Kortrijk, Kortrijk, Belgium
    Co-Author: Joshua Muia, PhD – Department of Biochemistry and Microbiology, Oklahoma State University Center for Health Sciences, Tulsa, Oklahoma
    Co-Author: Bart Meyns – Department of Cardiovascular Sciences, University Hospitals Leuven, Leuven, Belgium
    Co-Author: Claudia Tersteeg – Laboratory for Thrombosis Research, KU Leuven Campus Kulak Kortrijk, Kortrijk, Belgium
    Co-Author: Simon F. De Meyer – Laboratory for Thrombosis Research, KU Leuven Campus Kulak Kortrijk, Kortrijk, Belgium
    Co-Author: Steven Jacobs – Department of Cardiovascular Sciences, University Hospitals Leuven, Leuven, Belgium
    Co-Author: Karen Vanhoorelbeke, PhD – KU Leuven
    Hemophilia and Rare Bleeding Disorders
  • Saturday, Jun 24th
    13:45 – 14:00 ET
    OC 07.4 - HMB-001, a bispecific anti-FVIIa/anti-TLT-1 antibody, demonstrates effect in models of FVII deficiency
    Room: 524
    Presenting Author: Henrik Ostergaard, PhD – Hemab Therapeutics
    Co-Author: Paolo Ferraresi – University of Ferrara, Department of Life Sciences and Biotechnology
    Co-Author: Marcello Baroni – University of Ferrara, Department of Life Sciences and Biotechnology
    Co-Author: Elena Tonetto – University of Ferrara, Department of Life Sciences and Biotechnology
    Co-Author: Amalie Carnbring Bonde – Hemab Therapeutics
    Co-Author: Catherine J. Rea, MA, PhD – Hemab Therapeutics
    Co-Author: Minka Zivkovic, MSc – Center for Benign Haematology, Thrombosis and Haemostasis, Van Creveldkliniek, University Medical Center Utrecht, Utrecht University, Utrecht, the Netherlands
    Co-Author: Rolf T. Urbanus, PhD – Center for Benign Haematology, Thrombosis and Haemostasis, Van Creveldkliniek, University Medical Center Utrecht, Utrecht University, Utrecht, the Netherlands
    Co-Author: Johan H. Faber – Hemab Therapeutics
    Co-Author: Benny Sorensen – Hemab Therapeutics
    Co-Author: Mirko Pinotti – University of Ferrara, Department of Life Sciences and Biotechnology
    Co-Author: Francesco Bernardi – University of Ferrara, Department of Life Sciences and Biotechnology
    Co-Author: Prafull S. Gandhi – Hemab Therapeutics
    Hemophilia and Rare Bleeding Disorders
  • Saturday, Jun 24th
    14:00 – 14:15 ET
    OC 04.5 - Structural, functional, and immunogenicity implications of F9 gene recoding
    Room: 520
    Presenting Author: Upendra K. Katneni, PhD – US Food and Drug Administration
    Co-Author: Aikaterini Alexaki – US Food and Drug Admininstration
    Co-Author: Ryan Hunt – US Food and Drug Administration
    Co-Author: Nobuko Hamasaki-Katagiri – US Food and Drug Administration
    Co-Author: Gaya Hettiarachchi – US Food and Drug Administration
    Co-Author: Brian Lin, PhD – US Food and Drug Administration
    Co-Author: Leonid Parunov, PhD (he/him/his) – US Food and Drug Administration
    Co-Author: Mikhail V. Ovanesov – US Food and Drug Administration
    Co-Author: Darón I. Freedberg – US Food and Drug Administration
    Co-Author: Haim Bar – University of Connecticut
    Co-Author: Anton A. Komar – Cleveland State University
    Co-Author: Zuben E. Sauna – U.S. Food and Drug Administration
    Co-Author: Chava Kimchi-Sarfaty – US Food and Drug Administration
    Hemophilia and Rare Bleeding Disorders
  • Saturday, Jun 24th
    14:00 – 14:15 ET
    OC 06.5 - Use of Emicizumab for the treatment of Acquired Hemophilia A: A Systematic Review
    Room: 510
    Presenting Author: Zainab S. Al Housni, Bhcs, MD, FRCPath – McMaster University
    Co-Author: Andres Valenzuela Suárez – McMaster University
    Co-Author: Essam AlTowyan – McMaster University
    Co-Author: Alfonso Iorio – Department of Health Research Methods, Evidence, and Impact, McMaster University, Hamilton, ON
    Co-Author: Davide Matino, MD (he/him/his) – Department of Medicine, Division of Hematology, McMaster University, Hamilton, ON
    Hemophilia and Rare Bleeding Disorders
  • Saturday, Jun 24th
    14:00 – 14:15 ET
    OC 07.5 - Modeling and correcting FVII deficiency using human stem cell-derived hepatic organoids
    Room: 524
    Presenting Author: Maria Eugenia Chollet Dugarte, MD, PhD (she/her/hers) – Department of Hematology, Research Institute of Internal Medicine, Oslo University Hospital
    Co-Author: Elisabeth Andersen – Oslo University Hospital
    Co-Author: Sean Harrison – Oslo University Hospital
    Co-Author: Maria Eugenia de la Morena-Barrio, PhD – Servicio de Hematología y Oncología Médica, Hospital Universitario Morales Meseguer, Centro Regional de Hemodonación, Universidad de Murcia, IMIB-Arrixaca, CIBERER, Murcia, Spain
    Co-Author: Saphira Baumgarten – University of Oslo
    Co-Author: Anindita Bhattacharya – University of Oslo
    Co-Author: Giacomo Roman, MSc – Department of Hematology, Oslo University Hospital, Oslo, Norway
    Co-Author: Mariane Andresen – Oslo University Hospital
    Co-Author: Carlos Bravo – Department of Hematology and Oncology, University Hospital Morales Meseguer, Centro Regional de Hemodonación, University of Murcia, IMIB, CIBERER, Murcia, Spain
    Co-Author: Marie-Christine Mowinckel – Oslo University Hospital
    Co-Author: Javier Corral, PhD – Servicio de Hematología y Oncología Médica, Hospital Universitario Morales Meseguer, Centro Regional de Hemodonación, Universidad de Murcia, IMIB-Pascual Parrilla, CIBERER, Murcia, Spain
    Co-Author: Per Morten Sandset – University of Oslo
    Co-Author: Gareth J Sullivan – Department of Pediatric Research, Oslo University Hospital, Oslo, Norway
    Co-Author: Benedicte Stavik – Department of Hematology, Oslo University Hospital, Oslo, Norway
    Hemophilia and Rare Bleeding Disorders
  • Sunday, Jun 25th
    07:00 – 07:45 ET
    MC 07.1 - Managing Surgeries and Deliveries in Carriers of Hemophilia
    Room: Bernhardt Room at the InterContinental Montreal
    Hemophilia and Rare Bleeding Disorders
  • Sunday, Jun 25th
    10:45 – 11:00 ET
    LB 01.1 - Efanesoctocog Alfa Prophylaxis for Previously Treated Patients <12 Years of Age With Severe Hemophilia A
    Room: 517
    Presenting Author: Lynn Malec, MD, MSc – Versiti Blood Research Institute, Milwaukee, WI, USA; Division of Hematology & Oncology, Departments of Medicine and Pediatrics, Medical College of Wisconsin, Milwaukee, WI, USA
    Co-Author: Flora Peyvandi, MD, PhD (she/her/hers) – IRCCS Ca' Granda Maggiore Hospital Foundation, Angelo Bianchi Bonomi Hemophilia and Thrombosis Center, Milano, Italy; Università degli Studi di Milano, Department of Pathophysiology and Transplantation, Milano, Italy
    Co-Author: Anthony KC. Chan, MBBS – McMaster University, McMaster Children’s Hospital, Hamilton, Canada
    Co-Author: Christoph Koenigs, Dr. Dr. – University Hospital Frankfurt, Department of Paediatrics and Adolescent Medicine, Frankfurt, Germany
    Co-Author: Bulent Bulent Zulfikar, MD – Department of Pediatric Hematology, Istanbul University Oncology Institute, Inherited Bleeding Disorders Center, Istanbul, Turkey
    Co-Author: Huixing Yuan – Sanofi, Cambridge, MA, USA
    Co-Author: Mindy L. Simpson – Rush University Medical Center, Rush Hemophilia and Thrombophilia Center, Chicago, IL, USA
    Co-Author: Maria Teresa Alvarez-Román, MD, PhD – Department of Hematology, University Hospital La Paz, Autonoma University of Madrid, Madrid, Spain
    Co-Author: Manuel Carcao, MD, FRCPC – Division of Haematology/Oncology, Department of Paediatrics, Hospital for Sick Children, University of Toronto, Toronto, Canada
    Co-Author: Janice M. Staber – Divison of Hematology/Oncology, Department of Pediatrics, Carver College of Medicine, University of Iowa Stead Family Children’s Hospital, Iowa City, IA, USA
    Co-Author: Amy L. Dunn – Oncology and Bone Marrow Transplant, Nationwide Children's Hospital and The Ohio State University College of Medicine, OH, USA
    Co-Author: Sheng-Chieh Chou – Department of Internal Medicine, National Taiwan University Hospital, Taipei, Taiwan
    Co-Author: Roseline d'Oiron, MD – Centre for Haemophilia and Rare Congenital Bleeding Disorders, Bicêtre Hospital AP-HP, University of Paris-Saclay and UMR_S1176 INSERM, Le Kremlin-Bicêtre, France
    Co-Author: Manuela Albisetti – University Children’s Hospital Zurich, Zurich, Switzerland
    Co-Author: Marek Demissie – Sanofi, Cambridge, Massachusetts, United States
    Co-Author: Elena Santagostino – Sobi, Basel, Switzerland
    Co-Author: Abhimanyu Yarramaneni – Sanofi, Bridgewater, NJ, USA
    Co-Author: Lydia Abad-Franch – Sobi, Basel, Switzerland
    Co-Author: Sriya Gunawardena – Sanofi, Bridgewater, NJ, USA
    Co-Author: Karin Fijnvandraat – Amsterdam UMC, University of Amsterdam, Emma Children’s Hospital, Pediatric Hematology Amsterdam, Netherlands
    Hemophilia and Rare Bleeding Disorders
  • Sunday, Jun 25th
    10:45 – 12:00 ET
    OC 12.6 - Hemophilia Clinical – MSK and Outcomes
    Room: 710A
    Moderator: Cedric Hermans, MD, PhD (he/him/his) – St-Luc University Hospital
    Moderator: Linda Sun, MD MHSc (she/her/hers) – University of Alberta
    Hemophilia and Rare Bleeding Disorders
  • Sunday, Jun 25th
    10:45 – 11:00 ET
    OC 12.1 - First evidence of improvement of long-term joint outcomes through ultrasound for hemophilia; from 3-years prospective J-DaUPHIN study
    Room: 710A
    Presenting Author: Azusa Nagao, MD, MSc – Department of Blood Coagulation, Ogikubo Hospital, Tokyo, Japan
    Co-Author: Satoko Orita – Ogikubo Hospital
    Co-Author: Katsuyuki Fukutake – Department of Blood Coagulation, Ogikubo Hospital
    Co-Author: Hideyuki Takedani – IMSUT Hospital of the Institute of Medical Science, the University of Tokyo
    Hemophilia and Rare Bleeding Disorders
  • Sunday, Jun 25th
    11:00 – 11:15 ET
    LB 01.2 - Emicizumab prophylaxis instead of immunosuppressive therapy in patients with acquired hemophilia A (AHA)
    Room: 517
    Presenting Author: Andreas Tiede, MD PhD (he/him/his) – Department of Hematology, Hemostasis, Oncology and Stem Cell Transplantation, Hannover Medical School, Hannover, Germany
    Co-Author: Christina Hart – Department of Hematology and Oncology, University Hospital Regensburg
    Co-Author: Paul Knoebl, MD – Department of Medicine 1, Division of Hematology and Hemostasis, Medical University of Vienna, Vienna, Austria
    Co-Author: Richard Greil – IIIrd Medical Department, Paracelsus Medical University Salzburg
    Co-Author: Johannes Oldenburg, MD (he/him/his) – University Clinic Bonn AöR, Institute of Experimental Haematology and Transfusion Medicine, Bonn, Germany
    Co-Author: Ulrich J. J. Sachs, MD – Department of Thrombosis and Haemostasis, Giessen University Hospital
    Co-Author: Wolfgang Miesbach, MD – University Hospital Frankfurt, Frankfurt, Germany
    Co-Author: Christian Pfrepper, MD – Division of Hemostaseology, University Hospital Leipzig, Germany
    Co-Author: Karolin Trautmann-Grill – Medical Clinic I, University Hospital Carl Gustav Carus
    Co-Author: Katharina Holstein, MD (she/her/hers) – University Hospital Hamburg Eppendorf
    Co-Author: Jan Pilch, MD – Institute of Clinical Hemostaseology and Transfusion Medicine, Saarland University School of Medicine and Saarland University Medical Center
    Co-Author: Patrick Möhnle – Department of Transfusion Medicine, Cellular Therapeutics and Hemostaseology, Department of Anesthesiology, Hospital of Ludwig Maximilian University
    Co-Author: Christoph Schindler – Center for Clinical Trials (ZKS), Hannover Medical School
    Co-Author: Carmen Weigt – GWT-TUD
    Co-Author: Dorothea Schipp – GWT-TUD
    Co-Author: Marcus May – Hematology, Hemostasis, Oncology, and Stem Cell Transplantation, Hannover Medical School
    Co-Author: Christiane Dobbelstein – Hematology, Hemostasis, Oncology, and Stem Cell Transplantation, Hannover Medical School
    Co-Author: Sonja Werwitzke – Department of Hematology, Hemostasis, Oncology and Stem Cell Transplantation, Hannover Medical School, Hannover, Germany
    Co-Author: Robert Klamroth, MD, PhD (he/him/his) – Vivantes Klinikum im Friedrichshain, Clinic for Internal Medicine Angiology and Haemostaseology
    Hemophilia and Rare Bleeding Disorders
  • Sunday, Jun 25th
    11:00 – 11:15 ET
    OC 12.2 - Decreased quality of life in non-severe hemophilia patients with an increased bleeding phenotype
    Room: 710A
    Presenting Author: Marieke Verhagen, MD – Department of Hematology, Radboud University Medical Center, Nijmegen, the Netherlands. Hemophilia Treatment Center Nijmegen-Eindhoven-Maastricht, Nijmegen, the Netherlands. Laboratory of hematology, Radboud university medical center, Nijmegen, the Netherlands
    Co-Author: Erna van Balen – Department of Clinical Epidemiology, Leiden University Medical Center, Leiden, the Netherlands
    Co-Author: Nicole M.A. Blijlevens – Department of Hematology, Radboud university medical center, Nijmegen, the Netherlands
    Co-Author: Waander L. van Heerde – Department of Hematology, Radboud university medical center, Nijmegen, The Netherlands. Hemophilia Treatment Center Nijmegen – Eindhoven – Maastricht, The Netherlands. Enzyre BV, Novio Tech Campus, Nijmegen, The Netherlands.
    Co-Author: Samantha Gouw, MD, PhD (she/her/hers) – The University of Amsterdam
    Co-Author: Saskia E.M. Schols – Department of Hematology, Radboud university medical center, Nijmegen, The Netherlands. Hemophilia Treatment Center Nijmegen – Eindhoven – Maastricht, The Netherlands
    Hemophilia and Rare Bleeding Disorders
  • Sunday, Jun 25th
    11:15 – 11:30 ET
    OC 12.3 - Rates of Venous Thromboembolism and use of thromboprophylaxis after major orthopedic surgery in patients with congenital Hemophilia A or B: a systematic review
    Room: 710A
    Presenting Author: Davide Santagata, MD (he/him/his) – Department of Medicine and Surgery, University of Insubria, Varese, Italy
    Co-Author: Alessia Abenante – Department of Medicine and Surgery, University of Insubria, Varese, Italy
    Co-Author: Alessandro Squizzato – Department of Medicine and Surgery, University of Insubria, Varese, Italy
    Co-Author: Marco Paolo Donadini, MD, PhD – Department of Medicine and Surgery, University of Insubria, Varese, Italy
    Co-Author: Francesco Dentali – Department of Medicine and Surgery, University of Insubria, Varese, Italy
    Co-Author: Walter Ageno, MD (he/him/his) – Department of Medicine and Surgery, University of Insubria, Varese, Italy
    Co-Author: Ingrid Pabinger, MD – Clinical Division of Hematology and Hemostaseology, Department of Medicine I, Medical University of Vienna, Vienna, Austria
    Co-Author: Andreas Tiede, MD PhD (he/him/his) – Department of Hematology, Hemostasis, Oncology and Stem Cell Transplantation, Hannover Medical School, Hannover, Germany
    Co-Author: Cihan Ay, MD (he/him/his) – Clinical Division of Haematology and Haemostaseology, Department of Medicine I, Medical University of Vienna, Vienna, Austria
    Hemophilia and Rare Bleeding Disorders
  • Sunday, Jun 25th
    11:45 – 12:00 ET
    OC 12.5 - Correlation of Biomarkers, Conventional X ray score, Hemophilia Joint Healthy Score and Joint Sonography for Assessment of Hemophilic Arthropathy Severity
    Room: 710A
    Presenting Author: Yeu-Chin Chen, MD – Hemophilia care & research center, Division of Hematology/Oncology, Tri-Service General Hospital, National Defense Medical Centerr, Taipei, Taiwan
    Co-Author: Chia-Yau Chang, assistant professor – 1. Department of Pediatrics, School of Medicine, College of Medicine, Taipei Medical University; 2. Division of Pediatric Hematology and Oncology, Department of Pediatrics, Taipei Medical University Hospital, Taipei, Taiwan.
    Co-Author: Shin-Nan Cheng, Medical Doctor – Hemophilia center, Department of Pediatrics, Tungs’ Taichung MetroHarbor Hospital, Taichung
    Co-Author: Shiue-Wei Lai, PhD – Division of Hematology/Oncology, Department of Internal Medicine, Tri-service General Hospital, National Defense Medical Center, Taipei, Taiwan.
    Co-Author: Tsung-Ying Li – Department of Physical Medicine and Rehabilitation, Tri-Service General Hospital, National Defense Medical Center
    Co-Author: Shu-Hsia Hu – Hemophilia Care and Research Center, Tri-Service General Hospital, Taipei, Taiwan.
    Hemophilia and Rare Bleeding Disorders
  • Sunday, Jun 25th
    14:45 – 16:00 ET
    OC 20.6 - Hemophilia Gene Therapy for Hemophilia A
    Room: 517
    Moderator: Margareth C. Ozelo, MD, PhD (she/her/hers) – Hemocentro UNICAMP, Department of Internal Medicine, School of Medical Sciences, University of Campinas, Campinas, São Paulo, Brazil
    Moderator: Paul Batty, MBBS, PhD (he/him/his) – University College London
    Hemophilia and Rare Bleeding Disorders
  • Sunday, Jun 25th
    14:45 – 16:00 ET
    OC 24.6 - Hemophilia Clinical – Factor Levels and Pharmacokinetics
    Room: 520
    Moderator: Courtney Thornburg, MD, MS (she/her/hers) – Rady Children's Hospital-San Diego
    Moderator: Guy Young, MD – Children's Hospital Los Angeles
    Hemophilia and Rare Bleeding Disorders
  • Sunday, Jun 25th
    14:45 – 15:00 ET
    OC 20.1 - Bleeding, FVIII activity, and safety 3 years after gene transfer with valoctocogene roxaparvovec: Results from GENEr8-1
    Room: 517
    Presenting Author: Johnny Mahlangu, MD (he/him/his) – Haemophilia Comprehensive Care Centre, Charlotte Maxeke Johannesburg Academic Hospital, University of the Witwatersrand and National Health Laboratory Service, Johannesburg, South Africa
    Co-Author: Annette von Drygalski, MD – University of California San Diego
    Co-Author: Susan Shapiro, MD, PhD (she/her/hers) – Oxford University Hospitals National Health Service Foundation Trust, Oxford, UK
    Co-Author: Sheng-Chieh Chou, MD. (he/him/his) – Division of Hematology, Department of Internal Medicine, National Taiwan University Hospital
    Co-Author: Margareth C. Ozelo, MD, PhD (she/her/hers) – Hemocentro UNICAMP, Department of Internal Medicine, School of Medical Sciences, University of Campinas, Campinas, São Paulo, Brazil
    Co-Author: Gili Kenet, MD – The National Hemophilia Center, and Amalia Biron Research Institute of Thrombosis and Hemostasis, Sheba Medical Center, Tel Hashomer, Tel Aviv University, Tel Aviv, Israel
    Co-Author: Flora Peyvandi, MD, PhD (she/her/hers) – IRCCS Ca' Granda Maggiore Hospital Foundation, Angelo Bianchi Bonomi Hemophilia and Thrombosis Center, Milano, Italy; Università degli Studi di Milano, Department of Pathophysiology and Transplantation, Milano, Italy
    Co-Author: Bella Madan, MD FRCP FRCPath – Guy's & St. Thomas’ NHS Foundation Trust, London, UK
    Co-Author: Michael A. Laffan, MD – Centre for Haematology, Imperial College London, London, UK
    Co-Author: Amy L. Dunn – Oncology and Bone Marrow Transplant, Nationwide Children's Hospital and The Ohio State University College of Medicine, OH, USA
    Co-Author: Jane Mason – Queensland Haemophilia Centre, Cancer Care Services, Royal Brisbane and Women's Hospital, Brisbane, QLD, Australia
    Co-Author: Doris V. Quon, MD, PhD (she/her/hers) – Luskin Orthopaedic Institute for Children
    Co-Author: Andrew D. Leavitt – Adult Hemophilia Treatment Center, University of California San Francisco, San Francisco, CA, USA
    Co-Author: Johannes Oldenburg, MD (he/him/his) – University Clinic Bonn AöR, Institute of Experimental Haematology and Transfusion Medicine, Bonn, Germany
    Co-Author: Hervé Chambost – AP-HM, Department of Pediatric Hematology Oncology, Children Hospital La Timone & Aix Marseille University, INSERM, INRA, C2VN, Marseille, France
    Co-Author: Mark T. Reding – Center for Bleeding and Clotting Disorders, University of Minnesota, Minneapolis, MN, USA
    Co-Author: Kala Jayaram – BioMarin Pharmaceutical Inc., Novato, CA, USA
    Co-Author: Hua Yu – BioMarin Pharmaceutical Inc., Novato, CA, USA
    Co-Author: Tara M. Robinson – BioMarin Pharmaceutical Inc., Novato, CA, USA
    Co-Author: Steven W. Pipe, MD – University of Michigan, Ann Arbor, MI, USA
    Hemophilia and Rare Bleeding Disorders
  • Sunday, Jun 25th
    14:45 – 15:00 ET
    OC 24.1 - Effect of the type of F9 mutation on the pharmacokinetic profile of patients with hemophilia B treated with extended half-life FIX concentrates.
    Room: 520
    Presenting Author: Davide Matino, MD (he/him/his) – Department of Medicine, Division of Hematology, McMaster University, Hamilton, ON
    Co-Author: Pierre Chelle, PhD – University of Waterloo
    Co-Author: Shannon Jackson, MD (she/her/hers) – Providence Hematology, St. Paul’s Hospital, Vancouver, BC, Canada
    Co-Author: Jerome Teitel, MD – St Michael's Hospital Haemophilia Treatment Centre, University of Toronto
    Co-Author: Giancarlo Castaman, MD – Center for Bleeding Disorders and Coagulation, Careggi University Hospital, Florence, Italy
    Co-Author: Arun Keepanasseril – Department of Health Research Methods, Evidence, and Impact (HEI), McMaster University, Hamilton, Canada
    Co-Author: Emma Iserman – Department of Health Research Methods, Evidence, and Impact, McMaster University, Hamilton, ON
    Co-Author: David Lillicrap, MD – Department of Pathology and Molecular Medicine, Queen's University
    Co-Author: Anthony KC. Chan, MBBS – McMaster University, McMaster Children’s Hospital, Hamilton, Canada
    Co-Author: Alfonso Iorio – Department of Health Research Methods, Evidence, and Impact, McMaster University, Hamilton, ON
    Hemophilia and Rare Bleeding Disorders
  • Sunday, Jun 25th
    15:00 – 15:15 ET
    OC 20.2 - Gene Therapy in Hemophilia A: the Impact of Valoctocogene Roxaparvovec on Patient Outcomes – Initial Results from Patient Reported Outcomes, Burdens and Experiences (PROBE) from the GENEr8-1 Trial
    Room: 517
    Presenting Author: Mark W. Skinner, JD (he/him/his) – Institute for Policy Advancement Ltd.
    Co-Author: Er Chen – BioMarin Pharmaceuticals Inc.
    Co-Author: Quazi Ibrahim – Department of Health Research Methods, Evidence, and Impact, McMaster University, Hamilton, ON
    Co-Author: Alexandra Kucher – Patient Outcomes Research Group Ltd
    Co-Author: Federico Germini, MD, MSc, PhD – Department of Medicine, McMaster University, Hamilton, ON
    Co-Author: Milad Karimi – BioMarin Pharmaceuticals Inc.
    Co-Author: Elizabeth Clearfield – Institute for Policy Advancement Ltd.
    Co-Author: Brian O'Mahony – Irish Hemophilia Society
    Co-Author: Mohit Jain – BioMarin Pharmaceuticals Inc.
    Hemophilia and Rare Bleeding Disorders
  • Sunday, Jun 25th
    15:00 – 15:15 ET
    OC 24.2 - Estimated Factor VIII Activity Levels at the Time of Bleeding Events in Individuals with Hemophilia A without Inhibitors
    Room: 520
    Presenting Author: Pierre Chelle, PhD – University of Waterloo
    Co-Author: Dagmar Hajducek – University of Waterloo
    Co-Author: Nabil Daoud – American Thrombosis and Hemostasis Network
    Co-Author: Emma Iserman – Department of Health Research Methods, Evidence, and Impact, McMaster University, Hamilton, ON
    Co-Author: Christine Gerber – American Thrombosis and Hemostasis Network
    Co-Author: Federico Germini, MD, MSc, PhD – Department of Medicine, McMaster University, Hamilton, ON
    Co-Author: Alfonso Iorio – Department of Health Research Methods, Evidence, and Impact, McMaster University, Hamilton, ON
    Co-Author: Andrea Edginton – University of Waterloo
    Co-Author: Michael Recht, MD, PhD, MBA (he/him/his) – National Hemophilia Foundation
    Hemophilia and Rare Bleeding Disorders
  • Sunday, Jun 25th
    15:15 – 15:30 ET
    OC 20.3 - Improved Joint Health After Gene Therapy with Dirloctocogene Samoparvovec (SPK-8011) in People with Hemophilia A
    Room: 517
    Presenting Author: Benjamin J. Samelson-Jones, PhD, MD – Division of Hematology and the Raymond G. Perelman Center for Cellular and Molecular Therapeutics, Children’s Hospital of Philadelphia
    Co-Author: Margaret V. Ragni, MD, MPH (she/her/hers) – Department of Medicine, University of Pittsburgh, Pittsburgh, PA, USA
    Co-Author: John E.J. Rasko – Department of Cell and Molecular Therapies, Royal Prince Alfred Hospital, and the Gene and Stem Cell Therapy Program, Centenary Institute, Faculty of Medicine and Health, University of Sydney
    Co-Author: Kristina M. Haley – Department of Pediatrics, Oregon Health & Science University
    Co-Author: Stacy E. Croteau – Department of Pediatrics, Harvard Medical School, and the Division of Hematology and Oncology, Boston Children’s Hospital
    Co-Author: Jerome Teitel, MD – St Michael's Hospital Haemophilia Treatment Centre, University of Toronto
    Co-Author: Huyen Tran – Australian Centre for Blood Diseases, Monash University
    Co-Author: Peter H. Cygan – Department of Medicine, Division of Blood and Vascular Disorders, Penn State Health Milton S. Hershey Medical Center
    Co-Author: Spencer Sullivan – Mississippi Center for Advanced Medicine
    Co-Author: Jill Moormeier – Department of Medicine, UMKC School of Medicine
    Co-Author: Savina Jaeger – Spark Therapeutics, Inc.
    Co-Author: Alex Long – Spark Therapeutics, Inc.
    Co-Author: Gallia Levy – Spark Therapeutics, Inc.
    Co-Author: Amy MacDougall – Spark Therapeutics, Inc.
    Co-Author: Kristen Jaworski – Spark Therapeutics, Inc.
    Co-Author: Tiffany Chang – Spark Therapeutics, Inc.
    Hemophilia and Rare Bleeding Disorders
  • Sunday, Jun 25th
    15:15 – 15:30 ET
    OC 24.3 - Minimum Baseline FVIII Levels Required to Prevent Joint Bleeding Episodes: a Study in Mild Hemophilia A
    Room: 520
    Presenting Author: Pasquale Agosti, MD, PhD – Università degli Studi di Milano, Department of Pathophysiology and Transplantation and Fondazione Luigi Villa, Milan, Italy
    Co-Author: Simona Maria Siboni – Fondazione IRCCS Ca' Granda, Ospedale Maggiore Policlinico, Angelo Bianchi Bonomi Hemophilia and Thrombosis Center
    Co-Author: Sara Scardo – Fondazione IRCCS Ca’ Granda Ospedale Maggiore Policlinico, Angelo Bianchi Bonomi Hemophilia and Thrombosis Center, Milan, Italy
    Co-Author: Roberta Gualtierotti, MD, PhD – Fondazione IRCCS Ca' Granda - Ospedale Maggiore Policlinico, Centro Emofilia e Trombosi Angelo Bianchi Bonomi
    Co-Author: Flora Peyvandi, MD, PhD (she/her/hers) – IRCCS Ca' Granda Maggiore Hospital Foundation, Angelo Bianchi Bonomi Hemophilia and Thrombosis Center, Milano, Italy; Università degli Studi di Milano, Department of Pathophysiology and Transplantation, Milano, Italy
    Hemophilia and Rare Bleeding Disorders
  • Sunday, Jun 25th
    15:30 – 15:45 ET
    OC 20.4 - The impact of gene therapy on the musculoskeletal health of patients with severe hemophilia A
    Room: 517
    Presenting Author: Gabriela G. Yamaguti-Hayakawa, MD, PhD (she/her/hers) – Hemocentro UNICAMP, University of Campinas, Campinas, SP, Brazil
    Co-Author: Janaina B. S. Ricciardi – Hemocentro UNICAMP, University of Campinas, Campinas, SP, Brazil
    Co-Author: Jessica O. Frade-Guanaes, MsC – Hemocentro UNICAMP, University of Campinas, Campinas, SP, Brazil
    Co-Author: Vanessa B. Faiotto – Hemocentro UNICAMP, University of Campinas, Campinas, SP, Brazil
    Co-Author: Luiz G. R. R. De Lima – Hemocentro UNICAMP, University of Campinas, Campinas, SP, Brazil
    Co-Author: Glenda Feldberg – Hemocentro UNICAMP, University of Campinas, Campinas, SP, Brazil
    Co-Author: Emerson T. I. Sakuma – Department of Anesthesiology, Oncology and Radiology, School of Medical Sciences, University of Campinas, UNICAMP, Campinas, SP, Brazil
    Co-Author: Daniela M. De Paulo – Hemocentro UNICAMP, University of Campinas, Campinas, SP, Brazil
    Co-Author: Andrea L. A. Sambo – Hemocentro UNICAMP, University of Campinas, Campinas, SP, Brazil
    Co-Author: Mariana M. T. Hosokawa – Hemocentro UNICAMP, University of Campinas, Campinas, SP, Brazil
    Co-Author: Valdirene C. F. Stahl – Hemocentro UNICAMP, University of Campinas, Campinas, SP, Brazil
    Co-Author: Samuel S. Medina – Hemocentro UNICAMP, University of Campinas, Campinas, SP, Brazil
    Co-Author: Marina P. P. Colella – Hemocentro UNICAMP, University of Campinas, Campinas, SP, Brazil
    Co-Author: Nivia M. Foschi – Hemocentro UNICAMP, University of Campinas, Campinas, SP, Brazil
    Co-Author: Carolina Costa-Lima, Master's degree and PHD student (she/her/hers) – Hemocentro UNICAMP, University of Campinas, Campinas, SP, Brazil
    Co-Author: Margareth C. Ozelo, MD, PhD (she/her/hers) – Hemocentro UNICAMP, Department of Internal Medicine, School of Medical Sciences, University of Campinas, Campinas, São Paulo, Brazil
    Hemophilia and Rare Bleeding Disorders
  • Sunday, Jun 25th
    15:30 – 15:45 ET
    OC 24.4 - Effect of F8 mutations and Von Willebrand factor on pharmacokinetics of FVIII concentrates in severe hemophilia A
    Room: 520
    Presenting Author: Federico Germini, MD, MSc, PhD – Department of Medicine, McMaster University, Hamilton, ON
    Co-Author: Zainab S. Al Housni, Bhcs, MD, FRCPath – McMaster University
    Co-Author: Anthony KC. Chan, MBBS – McMaster University, McMaster Children’s Hospital, Hamilton, Canada
    Co-Author: Kay Decker – Hamilton Health Scienes
    Co-Author: Alfonso Iorio – Department of Health Research Methods, Evidence, and Impact, McMaster University, Hamilton, ON
    Co-Author: Davide Matino, MD (he/him/his) – Department of Medicine, Division of Hematology, McMaster University, Hamilton, ON
    Hemophilia and Rare Bleeding Disorders
  • Sunday, Jun 25th
    15:45 – 16:00 ET
    OC 20.5 - The WFH Gene Therapy Registry: A Collaborative Approach Towards a Global Resource for the Long-term Follow-up of People with Hemophilia Treated with Gene Therapy
    Room: 517
    Presenting Author: Barbara A. Konkle, MD (she/her/hers) – University of Washington
    Co-Author: Donna Coffin, MSc Epid (she/her/hers) – World Federation of Hemophilia
    Co-Author: Mayss Naccache, MSc – World Federation of Hemophilia
    Co-Author: Toong Youttananukorn, PhD – World Federation of Hemophilia
    Co-Author: Cary Clark – International Society on Thrombosis and Haemostasis
    Co-Author: Lindsey A. George, MD – University of Pennsylvania
    Co-Author: Alfonso Iorio – Department of Health Research Methods, Evidence, and Impact, McMaster University, Hamilton, ON
    Co-Author: Wolfgang Miesbach, MD – University Hospital Frankfurt, Frankfurt, Germany
    Co-Author: Declan Noone – European Haemophilia Consortium
    Co-Author: Flora Peyvandi, MD, PhD (she/her/hers) – IRCCS Ca' Granda Maggiore Hospital Foundation, Angelo Bianchi Bonomi Hemophilia and Thrombosis Center, Milano, Italy; Università degli Studi di Milano, Department of Pathophysiology and Transplantation, Milano, Italy
    Co-Author: Steven W. Pipe, MD – University of Michigan, Ann Arbor, MI, USA
    Co-Author: Michael Recht, MD, PhD, MBA (he/him/his) – National Hemophilia Foundation
    Co-Author: Mark W. Skinner, JD (he/him/his) – Institute for Policy Advancement Ltd.
    Co-Author: Leonard A. Valentino – Rush Hemophilia and Thrombophilia Center, Rush University Medical Center, Chicago, Illinois, USA
    Co-Author: Johnny Mahlangu, MD (he/him/his) – Haemophilia Comprehensive Care Centre, Charlotte Maxeke Johannesburg Academic Hospital, University of the Witwatersrand and National Health Laboratory Service, Johannesburg, South Africa
    Co-Author: Glenn F. Pierce, MD PhD – World Federation of Hemophilia
    Hemophilia and Rare Bleeding Disorders
  • Sunday, Jun 25th
    15:45 – 16:00 ET
    OC 24.5 - A Phase 1 Study to Evaluate the Pharmacokinetics and Safety of a PEGylated-Recombinant Human Coagulation Factor VIII-Fc Fusion Protein in Patients With Severe Hemophilia A
    Room: 520
    Co-Author: Feng Xue, MD – Institute of haematology and Blood Diseaes Hospital, Chinese Academy of Medical Sciences and Pkeing Union Medical College
    Co-Author: Yun Chen – Jinan central hospital, Shandong, P.R. China
    Co-Author: Jing Sun – Nanfang Hospital of Southern Medical University, Guangzhou, P.R. China
    Co-Author: Shuxia Guo – Zhengzhou People's Hospital
    Co-Author: Qing Wen – Jinan central hospital, Shandong, P.R. China
    Co-Author: Chongyuan Xu – Nanfang Hospital of Southern Medical University, Guangzhou, P.R. China
    Co-Author: Ping Liu – Zhengzhou People's Hospital
    Presenting Author: Renchi Yang, MD (he/him/his) – Institute of Hematology and Blood Diseases Hospital, Chinese Academy of Medical Sciences and Peking Union Medical College, Tianjin, China
    Hemophilia and Rare Bleeding Disorders
  • Sunday, Jun 25th
    18:30 – 19:30 ET
    PB0142 - FVIII-containing immune complexes interrupt platelet aggregation in an ex-vivo model of primary hemostasis
    Room: Exhibition
    Presenting Author: Olga Oleshko, MD (she/her/hers) – Department of Hematology, Hemostasis, Oncology and Stem Cell Transplantation, Hannover Medical School, Hannover, Germany
    Co-Author: Annika Klingberg – Department of Hematology, Hemostasis, Oncology and Stem Cell Transplantation, Hannover Medical School, Hannover, Germany
    Co-Author: Ute Curth – Institute for Biophysical Chemistry, Hannover Medical School, Hannover, Germany
    Co-Author: Sonja Werwitzke – Department of Hematology, Hemostasis, Oncology and Stem Cell Transplantation, Hannover Medical School, Hannover, Germany
    Co-Author: Amrita Sarkar – Division of Hematology, Children's Hospital of Philadelphia, Philadelphia, PA
    Co-Author: Lubica Rauova, MD, PhD – Division of Hematology, Children's Hospital of Philadelphia, Philadelphia, PA
    Co-Author: Mortimer Poncz – Division of Hematology, Children's Hospital of Philadelphia, Philadelphia, PA
    Co-Author: Andreas Tiede, MD PhD (he/him/his) – Department of Hematology, Hemostasis, Oncology and Stem Cell Transplantation, Hannover Medical School, Hannover, Germany
    Hemophilia and Rare Bleeding Disorders
  • Sunday, Jun 25th
    18:30 – 19:30 ET
    PB0143 - Induced B cell tolerance in Hemophilia A mice is destroyed by infections
    Room: Exhibition
    Co-Author: Blanca Jurado-Mestre – Institute of Molecular Medicine and Experimental Immunology (IMMEI), University Clinic Bonn
    Co-Author: Amina Abdelmageed – Institute of Molecular Medicine and Experimental Immunology (IMMEI), University Clinic Bonn
    Co-Author: Vadim Kotov – Institute of Molecular Medicine and Experimental Immunology (IMMEI), University Clinic Bonn
    Co-Author: Thilo Albert – Institute of Experimental Haematology and Transfusion Medicine, University Clinic Bonn
    Co-Author: Johannes Oldenburg, MD (he/him/his) – University Clinic Bonn AöR, Institute of Experimental Haematology and Transfusion Medicine, Bonn, Germany
    Co-Author: Christian Kurts – Institute of Molecular Medicine and Experimental Immunology (IMMEI), University Clinic Bonn
    Presenting Author: Janine Becker-Gotot, Dr rer nat (she/her/hers) – Institute of Molecular Medicine and Experimental Immunology (IMMEI), University Clinic Bonn
    Hemophilia and Rare Bleeding Disorders
  • Sunday, Jun 25th
    18:30 – 19:30 ET
    PB0145 - Extra-hemostatic roles of FVIII in musculoskeletal system in a FVIII knockout mice model
    Room: Exhibition
    Presenting Author: Babuty Antoine, MD (he/him/his) – Nantes University Hospital, Nantes, France, Nantes Université, CNRS UMR6286, US2B, Nantes, France.
    Co-Author: Javier Munoz garcia – Nantes Université, CNRS UMR6286, US2B, Nantes, France,Institut de Cancérologie de ‘Ouest, Saint-Herblain, France.
    Co-Author: laurie Fradet – Institut de Cancérologie de ‘Ouest, Saint-Herblain, France.
    Co-Author: Denis Cochonneau – Institut de Cancérologie de ‘Ouest, Saint-Herblain, France.
    Co-Author: Marie-Françoise Heymann – Nantes Université, CNRS UMR6286, US2B, Nantes, France,Institut de Cancérologie de ‘Ouest, Saint-Herblain, France.
    Co-Author: Frank Driessler – Bayer Consumer Care AG, Peter Merian Straße 84, CH-4052 BASEL
    Co-Author: Dominique heymann – Nantes Université, CNRS UMR6286, US2B, Nantes, France, Institut de Cancérologie de ‘Ouest, Saint-Herblain, France. Institut de Cancérologie de ‘Ouest, Saint-Herblain, France.
    Hemophilia and Rare Bleeding Disorders
  • Sunday, Jun 25th
    18:30 – 19:30 ET
    PB0146 - Functional Characterization of a Human F9 Gene-inserted Product in Hemophilia B Mice
    Room: Exhibition
    Presenting Author: Dan Chalothorn, PhD – Regeneron Pharmaceuticals, Inc.
    Co-Author: Leah Sabin – Regeneron Pharmaceuticals, Inc.
    Co-Author: KehDih Lai – Regeneron Pharmaceuticals, Inc.
    Co-Author: Yong Kim – Regeneron Pharmaceuticals, Inc.
    Co-Author: Rachel Sattler – Regeneron Pharmaceuticals, Inc.
    Co-Author: Catherine Moroski-Erkul – Intellia Therapeutics, Inc.
    Co-Author: Kathryn Walsh – Intellia Therapeutics, Inc.
    Co-Author: Cindy Shaw – Intellia Therapeutics, Inc.
    Co-Author: Jonathan Phillips – Intellia Therapeutics, Inc.
    Co-Author: David Gutstein – Regeneron Pharmaceuticals, Inc.
    Co-Author: Christos Kyratsous – Regeneron Pharmaceuticals, Inc.
    Co-Author: Lori Morton – Regeneron Pharmaceuticals, Inc.
    Hemophilia and Rare Bleeding Disorders
  • Sunday, Jun 25th
    18:30 – 19:30 ET
    PB0147 - FVIII/anti-FVIII immune complexes prevent FVIII-specific activation of B cells in a hemophilia A mouse model
    Room: Exhibition
    Presenting Author: Ghazaleh Dadashi Zadeh, Msc – McMaster University
    Co-Author: Arthi Velusamy – Mcmaster university
    Co-Author: Wajeeha Zaheer (she/her/hers) – McMaster University
    Co-Author: Hasam Madarati – McMaster University
    Co-Author: Anthony KC. Chan, MBBS – McMaster University, McMaster Children’s Hospital, Hamilton, Canada
    Co-Author: Davide Matino, MD (he/him/his) – Department of Medicine, Division of Hematology, McMaster University, Hamilton, ON
    Hemophilia and Rare Bleeding Disorders
  • Sunday, Jun 25th
    18:30 – 19:30 ET
    PB0150 - Fibrin clot formation is a reliable biological marker to evaluate FVIII replacement therapy in hemophilia A patients.
    Room: Exhibition
    Presenting Author: Debora Bertaggia Calderara, PhD – Division and Central Laboratory of Hematology, Lausanne University Hospital (CHUV) and University of Lausanne, Lausanne, Switzerland
    Co-Author: Ana Patricia P. Batista Mesquita Sauvage – Division and Central Laboratory of Hematology, Lausanne University Hospital (CHUV) and University of Lausanne, Lausanne, Switzerland
    Co-Author: Francisco Javier J. Gomez – Division and Central Laboratory of Hematology, Lausanne University Hospital (CHUV) and University of Lausanne, Lausanne, Switzerland
    Co-Author: Maxime Grégoire G. Zermatten – Division and Central Laboratory of Hematology, Lausanne University Hospital (CHUV) and University of Lausanne, Lausanne, Switzerland
    Co-Author: Lucas Veuthey, BSc, MSc (he/him/his) – Division and Central Laboratory of Hematology, Lausanne University Hospital (CHUV) and University of Lausanne, Lausanne, Switzerland
    Co-Author: Durre Shehwar, MSc MPhil – Department of Biochemistry, Quaid-i-Azam University, Islamabad, Pakistan
    Co-Author: Cindy Pereira Portela, MD Student – Division and Central Laboratory of Hematology, Lausanne University Hospital (CHUV) and University of Lausanne, Lausanne, Switzerland
    Co-Author: Alessandro Aliotta, PhD – Division and Central Laboratory of Hematology, Lausanne University Hospital (CHUV) and University of Lausanne, Lausanne, Switzerland
    Co-Author: Lorenzo Alberio, MD (he/him/his) – Division and Central Laboratory of Hematology, Lausanne University Hospital (CHUV) and University of Lausanne, Lausanne, Switzerland
    Hemophilia and Rare Bleeding Disorders
  • Sunday, Jun 25th
    18:30 – 19:30 ET
    PB0151 - The Effect of Single and Combined Knockouts of GABARAPs proteins family on FVIII Intracellular Localization and Secretion
    Room: Exhibition
    Co-Author: Mira Ibrahim, MS – Institute of Experimental Haematology and Transfusion Medicine and Center for Rare Diseases, University Hospital Bonn, Bonn, Germany
    Co-Author: Rawya Al Rifai – Institute of Experimental Haematology and Transfusion Medicine and Center for Rare Diseases, University Hospital Bonn, Bonn, Germany
    Co-Author: Salime El Hazzouri – University Clinic Bonn, Institute of experimental Haematology and Transfusion medicine
    Co-Author: Nicole Nüsgen – Institute of Experimental Haematology and Transfusion Medicine and Center for Rare Diseases, University Hospital Bonn, Bonn, Germany
    Co-Author: Johannes Oldenburg, MD (he/him/his) – University Clinic Bonn AöR, Institute of Experimental Haematology and Transfusion Medicine, Bonn, Germany
    Presenting Author: Osman EL-Maarri, Priv Doz, PhD (he/him/his) – Institute of Experimental Haematology and Transfusion Medicine and Center for Rare Diseases, University Hospital Bonn, Bonn, Germany
    Hemophilia and Rare Bleeding Disorders
  • Sunday, Jun 25th
    18:30 – 19:30 ET
    PB0152 - The spectrum of FVIII-specific antibodies in persons with hemophilia A: a cross-sectional nationwide population study
    Room: Exhibition
    Presenting Author: Ilja Oomen, MD (she/her/hers) – Amsterdam UMC location University of Amsterdam, Department of Pediatric Hematology, Meibergdreef 9, Amsterdam, The Netherlands
    Co-Author: Marieke Verhagen, MD – Department of Hematology, Radboud University Medical Center, Nijmegen, the Netherlands. Hemophilia Treatment Center Nijmegen-Eindhoven-Maastricht, Nijmegen, the Netherlands. Laboratory of hematology, Radboud university medical center, Nijmegen, the Netherlands
    Co-Author: Mariarosaria Miranda, MA – Department of Molecular Hematology, Sanquin Research and Landsteiner Laboratory, Amsterdam, The Netherlands
    Co-Author: Peter Allacher – Institute Krems Bioanalytics, IMC University of Applied Sciences Krems, Krems, Austria
    Co-Author: Paul Kaijen – Department of Molecular Hematology, Sanquin Research and Landsteiner Laboratory, Amsterdam, The Netherlands
    Co-Author: Shermarke Hassan – Centre for Tropical Medicine and Global Health
    Co-Author: Daniëlle Meijer – Department of Laboratory Medicine, Laboratory of Hematology, Radboud university medical center, Nijmegen, the Netherlands
    Co-Author: Sanna R. Rijpma, PhD – Department of Laboratory Medicine, Laboratory of Hematology, Radboud university medical center, Nijmegen, the Netherlands
    Co-Author: Helmut Schweiger – Institute Krems Bioanalytics, IMC University of Applied Sciences Krems, Krems, Austria
    Co-Author: Karin Fijnvandraat – Amsterdam UMC, University of Amsterdam, Emma Children’s Hospital, Pediatric Hematology Amsterdam, Netherlands
    Co-Author: Jan Voorberg – Department of Molecular Hematology, Sanquin Research and Landsteiner Laboratory
    Co-Author: Saskia E.M. Schols – Department of Hematology, Radboud university medical center, Nijmegen, The Netherlands. Hemophilia Treatment Center Nijmegen – Eindhoven – Maastricht, The Netherlands
    Co-Author: Samantha Gouw, MD, PhD (she/her/hers) – The University of Amsterdam
    Hemophilia and Rare Bleeding Disorders
  • Sunday, Jun 25th
    18:30 – 19:30 ET
    PB0153 - Evaluation of cell type-specificity of native enhancer elements from the F8 locus
    Room: Exhibition
    Presenting Author: Fateme Babaha, MSC (she/her/hers) – Queen's University, Departement of Pathology and Molecular Medicine
    Co-Author: Nathalie Tijet – Queen's University, Kingston, Ontario, Canada
    Co-Author: David Lillicrap, MD – Department of Pathology and Molecular Medicine, Queen's University
    Hemophilia and Rare Bleeding Disorders
  • Sunday, Jun 25th
    18:30 – 19:30 ET
    PB0154 - Blood-induced Inflammation in Hemophilia is Associated with Impaired Macrophage Function
    Room: Exhibition
    Co-Author: Lynn M. Knowles – Institute of Clinical Hemostaseology and Transfusion Medicine, Saarland University School of Medicine and Saarland University Medical Center
    Co-Author: Carolin Wolter, MSc – Institute of Clinical Hemostaseology and Transfusion Medicine, Saarland University School of Medicine and Saarland University Medical Center
    Co-Author: Michael D. Menger – Institute for Clinical and Experimental Surgery, Saarland University School of Medicine and Saarland University Medical Center
    Co-Author: Matthias W. Laschke – Institute for Clinical and Experimental Surgery, Saarland University School of Medicine and Saarland University Medical Center
    Co-Author: Felix Haegele – Institute of Clinical Hemostaseology and Transfusion Medicine, Saarland University School of Medicine and Saarland University Medical Center
    Co-Author: Hermann Eichler, MD (he/him/his) – Institute of Clinical Haemostaseology and Transfusion Medicine, University and University Hospital of the Saarland, Homburg, Germany
    Presenting Author: Jan Pilch, MD – Institute of Clinical Hemostaseology and Transfusion Medicine, Saarland University School of Medicine and Saarland University Medical Center
    Hemophilia and Rare Bleeding Disorders
  • Sunday, Jun 25th
    18:30 – 19:30 ET
    PB0155 - Characterization of zebrafish f8 mutant and modeling Hemophilia A
    Room: Exhibition
    Co-Author: Ayah Al Qaryoute – University of North Texas
    Co-Author: Anthony De Maria – University of North Texas
    Co-Author: Pudur Jagadeeswaran, PhD – University of North Texas
    Hemophilia and Rare Bleeding Disorders
  • Sunday, Jun 25th
    18:30 – 19:30 ET
    PB0156 - Higher Thrombin Generation Is Predicted When Switching Directly From Emicizumab to MIM8 in Patients With Hemophilia A
    Room: Exhibition
    Co-Author: Mads Kreilgaard – Novo Nordisk A/S
    Presenting Author: Jacob Lund, PhD (he/him/his) – Novo Nordisk
    Co-Author: Irina Matytsina, MD, MSc Pharm Med – Novo Nordisk A/S
    Hemophilia and Rare Bleeding Disorders
  • Sunday, Jun 25th
    18:30 – 19:30 ET
    PB0157 - In vitro thrombin generation in the presence of emicizumab sequence identical analogue (emi-SIA) and concizumab
    Room: Exhibition
    Presenting Author: Marianne Kjalke, PhD (she/her/hers) – Department of Rare Blood Disorders, Novo Nordisk A/S, Måløv, Denmark
    Co-Author: Trine Høyer Rose – Novo Nordisk A/S, Måløv, Denmark
    Co-Author: Thomas Porstmann – Novo Nordisk Health Care AG, Zurich, Switzerland
    Hemophilia and Rare Bleeding Disorders
  • Sunday, Jun 25th
    18:30 – 19:30 ET
    PB0158 - Preanalytical Quenching of FVIII Using FVIII-Inhibitors Improves the Specificity of Functional Emicizumab Testing
    Room: Exhibition
    Presenting Author: Nasim Shahidi Hamedani, PharmD PhD (she/her/hers) – University Hospital Bonn; Institute of Experimental Haematologie and Transfusion Medicine
    Co-Author: Claudia Klein – University Hospital Bonn; Institute of Experimental Haematologie and Transfusion Medicine
    Co-Author: Georg Goldmann – University Hospital Bonn; Institute of Experimental Haematologie and Transfusion Medicine
    Co-Author: Natascha Marquardt, MD – Institute for Experimental Hematology and Transfusion Medicine, University Clinic Bonn
    Co-Author: Heiko Rühl – Institute of Experimental Haematology and Transfusion Medicine, University Hospital Bonn
    Co-Author: Bernd Pötzsch – University Hospital Bonn; Institute of Experimental Haematologie and Transfusion Medicine
    Co-Author: Johannes Oldenburg, MD (he/him/his) – University Clinic Bonn AöR, Institute of Experimental Haematology and Transfusion Medicine, Bonn, Germany
    Co-Author: Jens Mueller – University Hospital Bonn; Institute of Experimental Haematologie and Transfusion Medicine
    Hemophilia and Rare Bleeding Disorders
  • Sunday, Jun 25th
    18:30 – 19:30 ET
    PB0159 - Relative Role of Auxiliary Plasma Protease Inhibitors in Thrombin Inhibition at Reduced Antithrombin Levels
    Room: Exhibition
    Presenting Author: Dougald M. Monroe, PhD – UNC Blood Research Center, Chapel Hill, NC
    Co-Author: Allen Ma – UNC Blood Research Center
    Co-Author: Maureane Hoffman – Duke University Medical Center
    Hemophilia and Rare Bleeding Disorders
  • Sunday, Jun 25th
    18:30 – 19:30 ET
    PB0160 - The impact of past inhibitor on health status in patients with haemophilia a in The Netherlands
    Room: Exhibition
    Presenting Author: Letícia Lemos Jardim, PhD (she/her/hers) – Instituto René Rachou (Fiocruz Minas), Belo Horizonte, Minas Gerais, Brazil
    Co-Author: Johanna G. Bom, van der – Department Clinical Epidemiology, Leiden University Medical Center, Leiden, the Netherlands
    Co-Author: Suely Rezende, MD, PhD (she/her/hers) – Universidade Federal de Minas Gerais
    Co-Author: Lize F.D. van Vulpen – Center for Benign Haematology, Thrombosis and Haemostasis, Van Creveldkliniek, University Medical Center Utrecht, Utrecht University, The Netherlands
    Co-Author: Jeroen C.J Eikenboom, MD. PhD – Leiden University Medical Center
    Co-Author: Erik A.M. Beckers – Department of Hematology, Maastricht University Medical Center + and Maastricht University, Maastricht, The Netherlands
    Co-Author: Louise Hooijmeijer – Division of Hematology/Oncology, Department of Pediatrics, University Medical Center Groningen, University of Groningen, Groningen, The Netherlands
    Co-Author: Michiel Coppens, MD, PhD (he/him/his) – Amsterdam University Medical Centers, Amsterdam, The Netherlands
    Co-Author: Saskia E.M. Schols – Department of Hematology, Radboud university medical center, Nijmegen, The Netherlands. Hemophilia Treatment Center Nijmegen – Eindhoven – Maastricht, The Netherlands
    Co-Author: Frank W.G. Leebeek, MD, PhD – Erasmus MC, University Medical Center Rotterdam, The Netherlands
    Co-Author: Mariëtte Driessens – Dutch Association of Hemophilia Patients
    Co-Author: Frits R. R. Rosendaal – Department of Clinical Epidemiology, Leiden University Medical Center, Leiden, The Netherlands
    Co-Author: Samantha Gouw, MD, PhD (she/her/hers) – The University of Amsterdam
    Hemophilia and Rare Bleeding Disorders
  • Sunday, Jun 25th
    18:30 – 19:30 ET
    PB0161 - The potential role of Matrix Metalloproteinases in the onset of Haemophilic Arthropathy
    Room: Exhibition
    Co-Author: Wayne Hauw, MBBs, FRCPA, FRACP – Central Clinical School, Faculty of Medicine, Nursing and Health Sciences, Monash University, Victoria, Australia
    Presenting Author: Harshal Nandurkar, MD, PhD, FRACP, FRCPA (he/him/his) – Alfred Health and Monash University
    Co-Author: Maithili Sashindranath – Australian Centre for Blood Diseases, Monash University
    Co-Author: Joanna Chia – Australian Centre for Blood Diseases
    Co-Author: Carly Selan – Australian Centre for Blood Diseases, Monash University
    Co-Author: Ilaria Calvello – Australian Centre for Blood Diseases, Monash University
    Co-Author: Amy Vuong – Australian Centre for Blood Diseases
    Co-Author: Ioanna Savvidou – Alfred Health, Monash University
    Hemophilia and Rare Bleeding Disorders
  • Sunday, Jun 25th
    18:30 – 19:30 ET
    PB0163 - Differential binding of recombinant FVIII products to platelets, and impact of FVIII on VWF expression and platelet contractility in vitro
    Room: Exhibition
    Co-Author: Anja Strebel – Laboratory of Applied Mechanobiology, Department of Health Sciences and Technology, ETH Zurich
    Presenting Author: Fabrizio A. Pennacchio, PhD (he/him/his) – Laboratory of Applied Mechanobiology, Department of Health Sciences and Technology, ETH Zurich
    Co-Author: Sebastian Lickert – Laboratory of Applied Mechanobiology, Department of Health Sciences and Technology, ETH Zurich
    Co-Author: Kateryna Selçuk – Laboratory of Applied Mechanobiology, Department of Health Sciences and Technology, ETH Zurich
    Co-Author: Konstantin Wolf – Laboratory of Applied Mechanobiology, Department of Health Sciences and Technology, ETH Zurich
    Co-Author: Viola Vogel, Prof. Dr. Dr. hc. (she/her/hers) – Laboratory of Applied Mechanobiology, Department of Health Sciences and Technology, ETH Zurich
    Hemophilia and Rare Bleeding Disorders
  • Sunday, Jun 25th
    18:30 – 19:30 ET
    PB0164 - Full characterization of three F8 deletions causing severe hemophilia A with high responding FVIII inhibitors may be associated with the mechanism of microhomology-mediated break-induced replication.
    Room: Exhibition
    Presenting Author: Miguel M. Abelleyro, PhD – Instituto de Medicina Experimental (IMEX), CONICET-Academia Nacional de Medicina
    Co-Author: Betiana M. Ziegler – Instituto de Medicina Experimental (IMEX), CONICET-Academia Nacional de Medicina
    Co-Author: Daniela Neme – Fundación de la Hemofilia Alfredo Pavlovsky
    Co-Author: Liliana C. Rossetti, PhD – Instituto de Medicina Experimental (IMEX), CONICET-Academia Nacional de Medicina
    Co-Author: Claudia P. Radic – Instituto de Medicina Experimental (IMEX), CONICET-Academia Nacional de Medicina
    Co-Author: Carlos D. De Brasi – Instituto de Medicina Experimental (IMEX), CONICET-Academia Nacional de Medicina
    Hemophilia and Rare Bleeding Disorders
  • Sunday, Jun 25th
    18:30 – 19:30 ET
    PB0165 - Gene correction of human hemophilia B mutation by PAM-flexible Cas9-mediated base-editing approach
    Room: Exhibition
    Co-Author: Takafumi Hiramoto – Department of Biochemistry, Jichi Medical University School of Medicine
    Co-Author: Yuji Kashiwakura, PhD (he/him/his) – Department of Biochemistry, Jichi Medical University School of Medicine
    Co-Author: Morisada Hayakawa – Department of Biochemistry, Jichi Medical University School of Medicine
    Co-Author: Nemekhbayar Baatartsogt – Department of Biochemistry, Jichi Medical University School of Medicine
    Co-Author: Nobuhiko Kamoshita – Department of Biochemistry, Jichi Medical University School of Medicine
    Co-Author: Tomoyuki Abe – Division of Regenerative Medicine, Center for Molecular Medicine, Jichi Medical University
    Co-Author: Hiroshi Inaba, PhD – Department of Laboratory Medicine, Tokyo Medical University
    Co-Author: Hiroshi Nishimasu – Structural Biology Division, Research Center for Advanced Science and Technology, The University of Tokyo
    Co-Author: Hideki Uosaki – Division of Regenerative Medicine, Center for Molecular Medicine, Jichi Medical University
    Co-Author: Yutaka Hanazono – Division of Regenerative Medicine, Center for Molecular Medicine, Jichi Medical University
    Co-Author: Osamu Nureki – Department of Biological Sciences, Graduate School of Science, The University of Tokyo
    Presenting Author: Tsukasa Ohmori, MD, PhD (he/him/his) – Department of Biochemistry, Jichi Medical University School of Medicine
    Hemophilia and Rare Bleeding Disorders
  • Sunday, Jun 25th
    18:30 – 19:30 ET
    PB0166 - Liver directed gene therapy in hemophilia A mice is dependent on Notch pathway driven endothelial development
    Room: Exhibition
    Co-Author: Omika Katoch – University of Pittsburgh
    Co-Author: Ziming Li – University of Pittsburgh
    Co-Author: Ramakrishna UV – University of Pittsburgh
    Co-Author: Tirthadipa Pradhan-Sundd, PhD – University of Pittsburgh
    Presenting Author: Tomasz W. Kaminski, PharmD – University of Pittsburgh
    Hemophilia and Rare Bleeding Disorders
  • Sunday, Jun 25th
    18:30 – 19:30 ET
    PB0167 - DE NOVO INTRON 22 INVERSION CARRIER DETECTION – THE EMERGING VALUE OF GENETIC ANALYSIS IN A DEVLOPING COUNTRY
    Room: Exhibition
    Presenting Author: Jean F. Kloppers, MMedSc – University of the Free State and National Health Laboratory Services
    Co-Author: Jan Du Plessis – University of the Free State and Free State Department of Health
    Co-Author: Walter Janse van Rensburg – University of the Free State
    Hemophilia and Rare Bleeding Disorders
  • Sunday, Jun 25th
    18:30 – 19:30 ET
    PB0168 - In vitro assessment of clinical coagulation assays in the presence of concizumab
    Room: Exhibition
    Presenting Author: Cecilia Augustsson, PhD – Department of Clinical Chemistry and Pharmacology, Coagulation Laboratory Malmö, Division of Laboratory Medicine, Region Skåne, Sweden
    Co-Author: Karin Strandberg – Department of Clinical Chemistry and Pharmacology, Coagulation Laboratory Malmö, Division of Laboratory Medicine, Region Skåne, Sweden
    Co-Author: Marianne Kjalke, PhD (she/her/hers) – Department of Rare Blood Disorders, Novo Nordisk A/S, Måløv, Denmark
    Hemophilia and Rare Bleeding Disorders
  • Sunday, Jun 25th
    18:30 – 19:30 ET
    PB0169 - Unearthing the genotype-inhibitor phenotype association in severe hemophilia A: a north Indian cohort study
    Room: Exhibition
    Presenting Author: Debadrita Ray, DM (she/her/hers) – PGIMER, Chandigarh
    Co-Author: Chander Hans – Dept . of Hematology ,PGIMER, Chandigarh
    Co-Author: Anita Kler – Dept. of Hematology ,PGIMER, Chandigarh
    Co-Author: Ritika Sharma, 82.6% – PGIMER, Chandigarh
    Co-Author: Manu Jamwal – PGIMER, Chandigarh
    Co-Author: Hari Kishan Sene – PGIMER, Chandigarh
    Co-Author: Rozy Thakur – PGIMER, Chandigarh
    Co-Author: Meenu Singh – PGIMER, Chandigarh
    Co-Author: Prateek Bhatia – PGIMER, Chandigarh
    Co-Author: Deepak Bansal – PGIMER, Chandigarh
    Co-Author: Arihant Jain – Department of Clinical Hematology and Medical Oncology, Postgraduate Institute of Medical Education and Research, Chandigarh, India
    Co-Author: Pankaj Malhotra, MD – Department of Clinical Hematology and Medical Oncology, Postgraduate Institute of Medical Education and Research, Chandigarh, India
    Co-Author: Jasmina Ahluwalia, MD (she/her/hers) – Department of Hematology, Postgraduate Institute of Medical Education and Research, Chandigarh, India
    Co-Author: Reena Das – PGIMER, Chandigarh
    Hemophilia and Rare Bleeding Disorders
  • Sunday, Jun 25th
    18:30 – 19:30 ET
    PB0170 - Evaluation of the Extended-Half Life FVIII products' measurement accuracy and precision with five different types of laboratory assays.
    Room: Exhibition
    Co-Author: Monica Sacco – Catholic University, Translational Medicine and Surgery Department Rome, Italy
    Co-Author: Stefano Lancellotti, PhD – Fondazione Policlinico Universitario A. Gemelli, IRCCS, Center for Hemorrhagic and Thrombotic Diseases and Haemophilia Center, Rome, Italy
    Co-Author: Maira Tardugno, Dr – Catholic University, Translational Medicine and Surgery Department Rome, Italy
    Co-Author: Maria Elisa Mancuso – Center for Thrombosis and Hemorrhagic Diseases, IRCCS Humanitas Research Hospital, Rozzano, Milan, Italy.
    Presenting Author: Raimondo De Cristofaro, MD, PhD – 1.Fondazione Policlinico Universitario A. Gemelli, IRCCS, Center for Hemorrhagic and Thrombotic Diseases and Haemophilia Center, Rome, Italy; 2. Catholic University, Translational Medicine and Surgery Department Rome, Italy
    Hemophilia and Rare Bleeding Disorders
  • Sunday, Jun 25th
    18:30 – 19:30 ET
    PB0171 - Polymorphisms in MAPk9 and CSF1R Associated with Immune Regulatory Gene and their Impact on Inhibitor Development in Patients with Hemophilia A
    Room: Exhibition
    Presenting Author: saira sultana, M.Phil. – Hemophilia Welfare Society Non-Profit Organization
    Hemophilia and Rare Bleeding Disorders
  • Sunday, Jun 25th
    18:30 – 19:30 ET
    PB0172 - Thrombodynamics: a Novel Assay for Diagnostic Evaluation of Haemophilia A Patients
    Room: Exhibition
    Presenting Author: Ryanne Astrid Arisz, MSc. – Department of Hematology, Erasmus MC, Erasmus University Medical Center Rotterdam, Rotterdam, the Netherlands.
    Co-Author: Lorenzo G.R. Romano, MD – Department of Hematology, Erasmus MC, Erasmus University Medical Center Rotterdam, Rotterdam, the Netherlands
    Co-Author: Janneke de Vries – Department of Hematology, Erasmus MC, Erasmus University Medical Center Rotterdam, Rotterdam, the Netherlands
    Co-Author: Frank W.G. Leebeek, MD, PhD – Erasmus MC, University Medical Center Rotterdam, The Netherlands
    Co-Author: Saskia E.M. Schols – Department of Hematology, Radboud university medical center, Nijmegen, The Netherlands. Hemophilia Treatment Center Nijmegen – Eindhoven – Maastricht, The Netherlands
    Co-Author: Jeroen C.J Eikenboom, MD. PhD – Leiden University Medical Center
    Co-Author: Moniek P.M. de Maat, PhD – Department of Hematology, Erasmus University Medical Center Rotterdam, Rotterdam, The Netherlands
    Hemophilia and Rare Bleeding Disorders
  • Sunday, Jun 25th
    18:30 – 19:30 ET
    PB0173 - Coagulation assay discrepancies for factor IX activity in hemophilia B
    Room: Exhibition
    Presenting Author: Hiroshi Inaba, PhD – Department of Laboratory Medicine, Tokyo Medical University
    Co-Author: Satomi Nishikawa – Sysmex Corporation
    Co-Author: Keiko Shinozawa, PhD – Department of Laboratory Medicine, Tokyo Medical University
    Co-Author: Fumie Nakazawa – Sysmex Corporation
    Co-Author: Kagehiro Amano – Department of Laboratory Medicine, Tokyo Medical University
    Co-Author: Ei Kinai – Department of Laboratory Medicine, Tokyo Medical University
    Hemophilia and Rare Bleeding Disorders
  • Sunday, Jun 25th
    18:30 – 19:30 ET
    PB0174 - Half-life of factor VIII in an adult and pediatric population: Study at 03 centers in western Algeria
    Room: Exhibition
    Presenting Author: Messaoudi Reda, PHD – University Ahmed Benbella N°1 Oran
    Co-Author: Moueden mohamed amine – University Hospital Oran
    Hemophilia and Rare Bleeding Disorders
  • Sunday, Jun 25th
    18:30 – 19:30 ET
    PB0175 - Impact of reagent on the estimation of Eloctate and Adynovate pharmacokinetic (PK) parameters?
    Room: Exhibition
    Presenting Author: Pierre Chelle, PhD – University of Waterloo
    Co-Author: Emma Iserman – Department of Health Research Methods, Evidence, and Impact, McMaster University, Hamilton, ON
    Co-Author: Alfonso Iorio – Department of Health Research Methods, Evidence, and Impact, McMaster University, Hamilton, ON
    Co-Author: Andrea Edginton – School of Pharmacy, Univeristy of Waterloo
    Hemophilia and Rare Bleeding Disorders
  • Sunday, Jun 25th
    18:30 – 19:30 ET
    PB0176 - Laboratory monitoring of severe hemophilia patients during PK at the Hemowab reference center: a retrospective study
    Room: Exhibition
    Co-Author: Mohammed Abdelghafour Sabri, Assistant MD – Laboratory of Hematology, LHUB-ULB, Université Libre de Bruxelles, Belgium
    Presenting Author: Phu Quoc Le, MD, PhD (he/him/his) – Department of Hematology and Oncology, Hôpital Universitaire Des Enfants Reine Fabiola, Université Libre de Bruxelles, Belgium
    Co-Author: Anne Demulder – Laboratory of Hematology, LHUB-ULB, Université Libre de Bruxelles, Belgium
    Co-Author: Andrea Nebbioso – Department of Pediatrics, Hôpitaux Iris Sud, Brussels, Belgium
    Co-Author: Pierre Peters – Laboratory of Hematology, CHU Liège, Belgium
    Co-Author: Laurence Rozen, PhD PharmD – LHUB-ULB, Université Libre de Bruxelles, Belgium
    Hemophilia and Rare Bleeding Disorders
  • Sunday, Jun 25th
    18:30 – 19:30 ET
    PB0177 - An examination of access to preventive therapies for persons with hemophilia (PWH): A pilot survey on behalf of the International Prophylaxis Study Group (IPSG)
    Room: Exhibition
    Co-Author: Karin Berger – Ludwig-Maximilan-University-Hospital
    Presenting Author: Roxy H. O'Rourke, MSc, PhD(c) – Hospital for Sick Children
    Co-Author: Audrey Abad – Hospital for Sick Children
    Co-Author: Louis Aledort – Icahn School of Medicine
    Hemophilia and Rare Bleeding Disorders
  • Sunday, Jun 25th
    18:30 – 19:30 ET
    PB0178 - Factor X enhances the coagulant potentials of Emicizumab.
    Room: Exhibition
    Presenting Author: Kazuki Shimizu, MD (he/him/his) – Department of Pediatrics, Nara Medical University
    Co-Author: Yuto Nakajima, MD PhD – Advanced Medical Science of Thrombosis and Hemostasis, Nara Medical University
    Co-Author: Akihisa Oda – Department of Pediatrics, Nara Medical University
    Co-Author: Eisuke Takami – Medical Affairs Section, KMBiologics Co., Ltd
    Co-Author: Hirotoshi Nakano – Medical Affairs Section, KMBiologics Co., Ltd
    Co-Author: Keiji Nogami – Nara Medical University, Nara, Japan
    Hemophilia and Rare Bleeding Disorders
  • Sunday, Jun 25th
    18:30 – 19:30 ET
    PB0182 - Development of a non-viral gene therapy approach for severe bleeding disorders
    Room: Exhibition
    Co-Author: Khal Hajj – Poseida Therapeutics
    Co-Author: Johannes Schwerk – Poseida Therapeutics
    Co-Author: Joseph Lucas – Poseida Therapeutics
    Presenting Author: Brian Truong, PhD (he/him/his) – Poseida Therapeutics
    Co-Author: Sang Lee – Poseida Therapeutics
    Co-Author: Kevin Briseno – Poseida Therapeutics
    Co-Author: James Yen – Poseida Therapeutics
    Co-Author: Michelle Burrascano – Poseida Therapeutics
    Co-Author: Daniel Smith – Poseida Therapeutics
    Co-Author: Jonnatan Tamayo – Poseida Therapeutics
    Co-Author: Fernando Lopez Espinoza – Poseida Therapeutics
    Co-Author: Pavan Battiprolu – Poseida Therapeutics
    Co-Author: Blair Madison – Poseida Therapeutics
    Co-Author: Brent Warner – Poseida Therapeutics
    Co-Author: Mike Bennett – Poseida Therapeutics
    Co-Author: Joshua Rychak – Poseida Therapeutics, Inc
    Hemophilia and Rare Bleeding Disorders
  • Sunday, Jun 25th
    18:30 – 19:30 ET
    PB0183 - Efficient Gene Transduction in Pigs and Macaques with the Engineered AAV Vector AAV.GT5 for Hemophilia B Gene Therapy
    Room: Exhibition
    Presenting Author: Yuji Kashiwakura, PhD (he/him/his) – Department of Biochemistry, Jichi Medical University School of Medicine
    Co-Author: Kazuhiro Endo – Department of Surgery, Jichi Medical University School of Medicine
    Co-Author: Atsushi Ugajin – Department of Radiology, Jichi Medical University School of Medicine
    Co-Author: Tomohiro Kikuchi – Department of Radiology, Jichi Medical University School of Medicine
    Co-Author: Shuji Hishikawa – Department of Surgery, Jichi Medical University School of Medicine
    Co-Author: Hitoyasu Nakamura – Department of Radiology, Jichi Medical University School of Medicine
    Co-Author: Yuko Katakai – The Corporation for Production and Research of Laboratory Primates
    Co-Author: Nemekhbayar Baatartsogt – Department of Biochemistry, Jichi Medical University School of Medicine
    Co-Author: Takafumi Hiramoto – Department of Biochemistry, Jichi Medical University School of Medicine
    Co-Author: Morisada Hayakawa – Department of Biochemistry, Jichi Medical University School of Medicine
    Co-Author: Nobuhiko Kamoshita – Department of Biochemistry, Jichi Medical University School of Medicine
    Co-Author: Shoji Yamazaki – Clinical Research Center, Jichi Medical University Hospital
    Co-Author: Akihiro Kume – Clinical Research Center, Jichi Medical University Hospital
    Co-Author: Harushi Mori – Department of Radiology, Jichi Medical University School of Medicine
    Co-Author: Naohiro Sata – Department of Surgery, Jichi Medical University School of Medicine
    Co-Author: Yoichi Sakata – Department of Biochemistry, Jichi Medical University School of Medicine
    Co-Author: Shin-ichi Muramatsu – Devision of Neurological Gene Therapy, Center for Open Innovation, Jichi Medical University
    Co-Author: Tsukasa Ohmori, MD, PhD (he/him/his) – Department of Biochemistry, Jichi Medical University School of Medicine
    Hemophilia and Rare Bleeding Disorders
  • Sunday, Jun 25th
    18:30 – 19:30 ET
    PB0184 - Ultrasound Mediated Delivery of CRISPR/Cas9 Plasmid in Hemophilia A Mice Shows Therapeutic levels of FVIII Following NHEJ Gene Editing
    Room: Exhibition
    Presenting Author: Savannah M. Lawton, BS – Seattle Children's Research Institute
    Co-Author: Meng-Ni Fan – Seattle Children's Research Institute
    Co-Author: Ting-Yen Chao – Seattle Children's Research Institute
    Co-Author: Chun-Yu Chen, PhD – Seattle Children's Research Institute
    Co-Author: Ellen Xu – Seattle Children's Research Institute
    Co-Author: Xiaohe Cai – Seattle Children's Research Institute
    Co-Author: Carol Miao – Seattle Children's Research Institute
    Hemophilia and Rare Bleeding Disorders
  • Sunday, Jun 25th
    18:30 – 19:30 ET
    PB0185 - Immunologic Response to AAV Directed Expression of Enhanced Hemostatic Variant FVIII-QQ in Mice
    Room: Exhibition
    Presenting Author: Anna R. Sternberg, PhD – Children's Hospital of Philadelphia
    Co-Author: Robert J. Davidson – Children's Hospital of Philadelphia
    Co-Author: Noelle C. Novak – Children's Hospital of Philadelphia
    Co-Author: Amelia R. Wilhelm – Children's Hospital of Philadelphia
    Co-Author: Lindsey A. George, MD – University of Pennsylvania
    Hemophilia and Rare Bleeding Disorders
  • Sunday, Jun 25th
    18:30 – 19:30 ET
    PB0186 - Results from BeneGene-1 Study: Prospective collection of bleeding rate in hemophilia B patients prior to phase 3 study (BeneGene-2) of fidanacogene elaparvovec
    Room: Exhibition
    Presenting Author: Davide Matino, MD (he/him/his) – Department of Medicine, Division of Hematology, McMaster University, Hamilton, ON
    Co-Author: Hazzaa Alzahrani – Adult Haematology, King Faisal Specialist Hospital and Research Centre Riyadh, Saudi Arabia
    Co-Author: Adam Cuker, MD, MS (he/him/his) – Department of Medicine and Department of Pathology & Laboratory Medicine, Perelman School of Medicine, University of Pennsylvania, Philadelphia, PA, USA
    Co-Author: Jan Astermark – Department of Hematology Oncology and Radiation Physics, Skane University Hospital, and Institution of Translational Medicine, Lund University, Malmö, Sweden
    Co-Author: Laurent Frenzel – Department of Haematology, Institut Necker
    Co-Author: Olga Katsarou – Blood Transfusion Centre, National Reference Centre for Congenital Bleeding Disorders, Laiko General Hospital
    Co-Author: Kaan Kavakli – Department of Hematology, Ege University Children’s Hospital, Izmir, Turkey
    Co-Author: Robert Klamroth, MD, PhD (he/him/his) – Vivantes Klinikum im Friedrichshain, Clinic for Internal Medicine Angiology and Haemostaseology
    Co-Author: Amy Shapiro – Indiana Hemophilia & Thrombosis Center, Indianapolis, IN, USA
    Co-Author: Jiaan-Der Wang – Center for Rare Disease and Hemophilia, Taichung Veterans General Hospital
    Co-Author: Joanne Fuiman – Pfizer Inc.
    Co-Author: John McKay – Pfizer Inc.
    Co-Author: Pengling Sun – Pfizer Inc.
    Co-Author: Jeremy Rupon, MD,PhD – Pfizer Inc.
    Hemophilia and Rare Bleeding Disorders
  • Sunday, Jun 25th
    18:30 – 19:30 ET
    PB0187 - Impact of One-Stage Clotting Assay Reagents on Factor XIa Levels and Clotting Time with High Activity Factor IX (R338L) Variant
    Room: Exhibition
    Co-Author: Swapnil Rakhe – Pfizer Inc.
    Co-Author: Daniel LeBlanc – Pfizer Inc.
    Presenting Author: Jeremy Rupon, MD,PhD – Pfizer Inc.
    Co-Author: Debra D. Pittman, MS – Pfizer Inc.
    Hemophilia and Rare Bleeding Disorders
  • Sunday, Jun 25th
    18:30 – 19:30 ET
    PB0188 - Improved Quality of Life in People with Hemophilia A Following Gene Therapy with Dirloctocogene Samoparvovec (SPK-8011)
    Room: Exhibition
    Presenting Author: Margaret V. Ragni, MD, MPH (she/her/hers) – Department of Medicine, University of Pittsburgh, Pittsburgh, PA, USA
    Co-Author: Matthew Evans – Department of Medicine, Division of Hematology and Oncology, Penn State Health Milton S. Hershey Medical Center
    Co-Author: Stacy E. Croteau – Department of Pediatrics, Harvard Medical School, and the Division of Hematology and Oncology, Boston Children’s Hospital
    Co-Author: Huyen Tran – Australian Centre for Blood Diseases, Monash University
    Co-Author: Benjamin J. Samelson-Jones, PhD, MD – Division of Hematology and the Raymond G. Perelman Center for Cellular and Molecular Therapeutics, Children’s Hospital of Philadelphia
    Co-Author: Jerome Teitel, MD – St Michael's Hospital Haemophilia Treatment Centre, University of Toronto
    Co-Author: John E.J. Rasko – Department of Cell and Molecular Therapies, Royal Prince Alfred Hospital, and the Gene and Stem Cell Therapy Program, Centenary Institute, Faculty of Medicine and Health, University of Sydney
    Co-Author: Spencer Sullivan – Mississippi Center for Advanced Medicine
    Co-Author: Jill Moormeier – Department of Medicine, UMKC School of Medicine
    Co-Author: Kristina M. Haley – Department of Pediatrics, Oregon Health & Science University
    Co-Author: Kristen Jaworski – Spark Therapeutics, Inc.
    Co-Author: Amy MacDougall – Spark Therapeutics, Inc.
    Co-Author: Alex Long – Spark Therapeutics, Inc.
    Co-Author: Savina Jaeger – Spark Therapeutics, Inc.
    Co-Author: Tiffany Chang – Spark Therapeutics, Inc.
    Co-Author: Gallia Levy – Spark Therapeutics, Inc.
    Hemophilia and Rare Bleeding Disorders
  • Sunday, Jun 25th
    18:30 – 19:30 ET
    PB0189 - Knowledge and attitudes of haemophilic patients toward gene therapy
    Room: Exhibition
    Presenting Author: Ilaria Cutica, PhD (she/her/hers) – Department of Oncology and Hematoncology, University of Milan, Italy
    Co-Author: Mimosa Mortarino – Angelo Bianchi Bonomi Hemophilia and Thrombosis Center, Fondazione IRCCS Ca’ Granda Ospedale Maggiore Policlinico and Fondazione Luigi Villa, Milan
    Co-Author: Isabella Garagiola – Angelo Bianchi Bonomi Hemophilia and Thrombosis Center, Fondazione IRCCS Ca’ Granda Ospedale Maggiore Policlinico and Fondazione Luigi Villa, Milan
    Co-Author: Gabriella Pravettoni – Department of Oncology and Hematoncology, University of Milan, Italy
    Co-Author: Flora Peyvandi, MD, PhD (she/her/hers) – IRCCS Ca' Granda Maggiore Hospital Foundation, Angelo Bianchi Bonomi Hemophilia and Thrombosis Center, Milano, Italy; Università degli Studi di Milano, Department of Pathophysiology and Transplantation, Milano, Italy
    Hemophilia and Rare Bleeding Disorders
  • Sunday, Jun 25th
    18:30 – 19:30 ET
    PB0190 - Structural, functional and carcinogenicity as essential liver biomarkers for gene therapy of hemophilia A
    Room: Exhibition
    Co-Author: Steven W. Pipe, MD – University of Michigan, Ann Arbor, MI, USA
    Co-Author: Gil Gonen Yaacovi, PhD – ASC Therapeutics
    Presenting Author: Oscar Segurado – ASC Therapeutics
    Hemophilia and Rare Bleeding Disorders
  • Sunday, Jun 25th
    18:30 – 19:30 ET
    PB0191 - myGTR: a patient engagement tool from the World Federation of Hemophilia Gene Therapy Registry
    Room: Exhibition
    Co-Author: Toong Youttananukorn, PhD – World Federation of Hemophilia
    Co-Author: Barbara A. Konkle, MD (she/her/hers) – University of Washington
    Co-Author: Donna Coffin, MSc Epid (she/her/hers) – World Federation of Hemophilia
    Presenting Author: Mayss Naccache, MSc – World Federation of Hemophilia
    Co-Author: Cary Clark – International Society on Thrombosis and Haemostasis
    Co-Author: Lindsey A. George, MD – University of Pennsylvania
    Co-Author: Alfonso Iorio – Department of Health Research Methods, Evidence, and Impact, McMaster University, Hamilton, ON
    Co-Author: Wolfgang Miesbach, MD – University Hospital Frankfurt, Frankfurt, Germany
    Co-Author: Declan Noone – European Haemophilia Consortium
    Co-Author: Flora Peyvandi, MD, PhD (she/her/hers) – IRCCS Ca' Granda Maggiore Hospital Foundation, Angelo Bianchi Bonomi Hemophilia and Thrombosis Center, Milano, Italy; Università degli Studi di Milano, Department of Pathophysiology and Transplantation, Milano, Italy
    Co-Author: Steven W. Pipe, MD – University of Michigan, Ann Arbor, MI, USA
    Co-Author: Michael Recht, MD, PhD, MBA (he/him/his) – National Hemophilia Foundation
    Co-Author: Mark W. Skinner, JD (he/him/his) – Institute for Policy Advancement Ltd.
    Co-Author: Leonard A. Valentino – Rush Hemophilia and Thrombophilia Center, Rush University Medical Center, Chicago, Illinois, USA
    Co-Author: Johnny Mahlangu, MD (he/him/his) – Haemophilia Comprehensive Care Centre, Charlotte Maxeke Johannesburg Academic Hospital, University of the Witwatersrand and National Health Laboratory Service, Johannesburg, South Africa
    Co-Author: Glenn F. Pierce, MD PhD – World Federation of Hemophilia
    Hemophilia and Rare Bleeding Disorders
  • Sunday, Jun 25th
    18:30 – 19:30 ET
    PB0192 - Novel Patient-directed Learning in the Era of Novel Therapies
    Room: Exhibition
    Presenting Author: Fiona Robinson, PhD (she/her/hers) – European Haemophilia Consortium
    Hemophilia and Rare Bleeding Disorders
  • Sunday, Jun 25th
    18:30 – 19:30 ET
    PB0193 - Financial impact of switching to emicizumab from conventional haemostatic agents in acquired haemophilia A
    Room: Exhibition
    Presenting Author: Praveen Gounder, MBBS FRACP FRCPA – Concord Repatriation General Hospital, Sydney
    Co-Author: Julianne Chong, n/a – Concord Repatriation General Hospital
    Co-Author: Caroline Dix, MBBS MSc FRACP FRCPA – Department of Clinical Haematology, The Alfred Hospital, Melbourne, VIC, Australia
    Co-Author: Marc L. Ellis, MBBS, PhD, FRACP, FRCPA – Concord Repatriation General Hospital
    Co-Author: Camille Durivage – Concord Repatriation General Hospital
    Co-Author: Nicole Wong Doo – Concord Repatriation General Hospital
    Co-Author: Uyen Walker – Concord Repatriation General Hospital
    Co-Author: Huyen Tran – Australian Centre for Blood Diseases, Monash University
    Co-Author: Vivien M. Chen, MBBS PhD FRACP FRCPAA (she/her/hers) – ANZAC Research Institute, University of Sydney
    Hemophilia and Rare Bleeding Disorders
  • Sunday, Jun 25th
    18:30 – 19:30 ET
    PB0194 - Comparison of intraindividual bleeding outcomes pre- and post-emicizumab in Australian adults and children with haemophilia A with and without inhibitors: a nationwide real-world experience
    Room: Exhibition
    Presenting Author: Radha Ramanan, MBBS (Hons) FRACP FRCPA – Department of Haematology, Alfred Health, Melbourne, VIC, Australia
    Co-Author: Sumit PARIKH, PhD – Australian Haemophilia Centre Directors’ Organisation, Melbourne, VIC, Australia
    Co-Author: James D. McFadyen – Department of Haematology, Alfred Health, Melbourne, VIC, Australia
    Co-Author: Huyen Tran – Australian Centre for Blood Diseases, Monash University
    Hemophilia and Rare Bleeding Disorders
  • Sunday, Jun 25th
    18:30 – 19:30 ET
    PB0195 - Efanesoctocog Alfa Versus Emicizumab in the Prophylactic Treatment of Adolescents and Adults with Severe Hemophilia A Without Inhibitors: A Matching-Adjusted Indirect Comparison
    Room: Exhibition
    Co-Author: Maria Teresa Alvarez-Román, MD, PhD – Department of Hematology, University Hospital La Paz, Autonoma University of Madrid, Madrid, Spain
    Co-Author: Nana Kragh, MSc – Sobi, Stockholm, Sweden
    Co-Author: Patricia Guyot – Sanofi, Cambridge, Massachusetts, USA
    Co-Author: Amanda Wilson – Sanofi, Cambridge, Massachusetts, USA
    Co-Author: Piotr Wojciechowski – Putnam PHMR, Krakow, Poland
    Co-Author: Wojciech Margas – Putnam PHMR, Krakow, Poland
    Co-Author: Marlena Wdowiak – Putnam PHMR, Krakow, Poland
    Co-Author: Elena Santagostino – Sobi, Basel, Switzerland
    Presenting Author: Alix Arnaud, MsC (she/her/hers) – Sanofi, Cambridge, Massachusetts, USA
    Hemophilia and Rare Bleeding Disorders
  • Sunday, Jun 25th
    18:30 – 19:30 ET
    PB0196 - Concizumab enhances thrombin generation potential in plasma from patients with FV-Amsterdam.
    Room: Exhibition
    Presenting Author: Rolf T. Urbanus, PhD – Center for Benign Haematology, Thrombosis and Haemostasis, Van Creveldkliniek, University Medical Center Utrecht, Utrecht University, Utrecht, the Netherlands
    Co-Author: Vossa van der Vegte – Center for Benign Haematology, Thrombosis and Haemostasis, Van Creveldkliniek, University Medical Center Utrecht, Utrecht University, Utrecht, the Netherlands
    Co-Author: Roger E.G Schutgens, MD, PhD, MSc (he/him/his) – Center for Benign Hematology, Thrombosis and Hemostasis, Van Creveldkliniek, University Medical Center Utrecht and University Utrecht, Utrecht, The Netherlands
    Hemophilia and Rare Bleeding Disorders
  • Sunday, Jun 25th
    18:30 – 19:30 ET
    PB0197 - Efficacy of adjusted weight-based dosing of DDAVP in type 1 von Willebrand disease
    Room: Exhibition
    Presenting Author: Craig D. Seaman, MD, MS – University of Pittsburgh
    Hemophilia and Rare Bleeding Disorders
  • Sunday, Jun 25th
    18:30 – 19:30 ET
    PB0199 - Type 2B von Willebrand disease – 30 years of experience in a Portuguese Reference Centre
    Room: Exhibition
    Presenting Author: Catarina Câmara, MD (she/her/hers) – Centro Hospitalar Universitário Lisboa Norte
    Co-Author: Joana S G Pestana, MD (she/her/hers) – Hospital do Espírito Santo - Évora
    Co-Author: Carolina Peixoto – Centro Hospitalar Universitário Lisboa Norte
    Co-Author: Filipa Pires – Centro Hospitalar Universitário Lisboa Norte
    Co-Author: Jorge Félix, MD – Centro Hospitalar Universitário Lisboa Norte
    Co-Author: Catarina J. Jacinto – Centro Hospitalar Universitário Lisboa Norte
    Co-Author: Artur Pereira – Centro Hospitalar Universitário Lisboa Norte
    Co-Author: Fátima Rodrigues – Centro Hospitalar Universitário Lisboa Norte
    Co-Author: Cristina Catarino, Dr (she/her/hers) – Centro Hospitalar Universitário Lisboa Norte
    Hemophilia and Rare Bleeding Disorders
  • Sunday, Jun 25th
    18:30 – 19:30 ET
    PB0201 - Efanesoctocog Alfa Versus Extended Half-Life Factor VIII Therapies for Prophylaxis in Adolescents and Adults with Severe Hemophilia A: A Matching-Adjusted Indirect Comparison and Meta-Analysis
    Room: Exhibition
    Co-Author: Robert Klamroth, MD, PhD (he/him/his) – Vivantes Klinikum im Friedrichshain, Clinic for Internal Medicine Angiology and Haemostaseology
    Co-Author: Patricia Guyot – Sanofi, Cambridge, Massachusetts, USA
    Presenting Author: Alix Arnaud, MsC (she/her/hers) – Sanofi, Cambridge, Massachusetts, USA
    Co-Author: Amanda Wilson – Sanofi, Cambridge, Massachusetts, USA
    Co-Author: Piotr Wojciechowski – Putnam PHMR, Krakow, Poland
    Co-Author: Marlena Wdowiak – Putnam PHMR, Krakow, Poland
    Co-Author: Wojciech Margas – Putnam PHMR, Krakow, Poland
    Co-Author: Ekaterina Gresko – Sobi
    Co-Author: Nana Kragh, MSc – Sobi, Stockholm, Sweden
    Hemophilia and Rare Bleeding Disorders
  • Sunday, Jun 25th
    18:30 – 19:30 ET
    PB0202 - The Impact of Iron Deficiency Anemia on Activation of Coagulation in Hereditary Hemorrhagic Telangiectaisa
    Room: Exhibition
    Presenting Author: Shatadal Ghosh – University of North Carolina at Chapel Hill
    Co-Author: Kimberley Youkhana, MD – Department of Medicine, University of North Carolina, Chapel Hill
    Co-Author: Steven P. Grover, PhD – Division of Hematology and Blood Research Center, University of North Carolina, Chapel Hill
    Co-Author: Suk Paul Oh – Barrow Neurological Research Institute
    Co-Author: Karen Smith – University of North Carolina
    Co-Author: Brandi N. Reeves, MD – University of North Carolina at Chapel Hill
    Co-Author: Rafal Pawlinski, PhD – Division of Hematology and Blood Research Center, University of North Carolina at Chapel Hill
    Co-Author: Raj S. Kasthuri – University of North Carolina at Chapel Hill
    Hemophilia and Rare Bleeding Disorders
  • Sunday, Jun 25th
    18:30 – 19:30 ET
    PB0203 - Altered Bleeding Phenotype in Patients with Co-inheritance of Genetic Variants in Thrombosis and Hemostases Genes in Rare Bleeding Disorders
    Room: Exhibition
    Presenting Author: Sterre Willems, Msc – Radboud university medical center, Hemophilia Treatment Center, Nijmegen – Eindhoven – Maastricht
    Co-Author: Annet Simons – Department of Human Genetics, Radboud university medical center
    Co-Author: Joline L. Saes – Department of Hematology, Radboud university medical center, Nijmegen, The Netherlands. Hemophilia Treatment Center Nijmegen – Eindhoven – Maastricht, The Netherlands
    Co-Author: Marjon H. Cnossen – Department of Pediatric Hematology, Erasmus MC – Sophia Children’s Hospital, University Medical Center Rotterdam, Rotterdam, The Netherlands
    Co-Author: Paul L. den Exter – Department of Thrombosis and Hemostasis, Leiden University Medical Center, Leiden, The Netherlands
    Co-Author: Ilmar C. Kruis – Netherlands Hemophilia Society, Nijkerk, The Netherlands
    Co-Author: Karina Meijer, MD, PhD (she/her/hers) – Department of Hematology, University Medical Center Groningen, University of Groningen, Groningen, The Netherlands
    Co-Author: Laurens Nieuwenhuizen – Hemophilia Treatment Center Nijmegen – Eindhoven – Maastricht, The Netherlands. Department of Hematology, Maxima Medical Center, Eindhoven, The Netherlands.
    Co-Author: Marjolein Peters – Department of Pediatric Hematology, Amsterdam University Medical Centers, location Emma Children’s Hospital, Amsterdam, The Netherlands
    Co-Author: Roger E.G Schutgens, MD, PhD, MSc (he/him/his) – Center for Benign Hematology, Thrombosis and Hemostasis, Van Creveldkliniek, University Medical Center Utrecht and University Utrecht, Utrecht, The Netherlands
    Co-Author: Marjan Weiss – Department of Human Genetics, Radboud university medical center
    Co-Author: Nicole M.A. Blijlevens – Department of Hematology, Radboud university medical center, Nijmegen, the Netherlands
    Co-Author: Waander L. van Heerde – Department of Hematology, Radboud university medical center, Nijmegen, The Netherlands. Hemophilia Treatment Center Nijmegen – Eindhoven – Maastricht, The Netherlands. Enzyre BV, Novio Tech Campus, Nijmegen, The Netherlands.
    Co-Author: Saskia E.M. Schols – Department of Hematology, Radboud university medical center, Nijmegen, The Netherlands. Hemophilia Treatment Center Nijmegen – Eindhoven – Maastricht, The Netherlands
    Hemophilia and Rare Bleeding Disorders
  • Sunday, Jun 25th
    18:30 – 19:30 ET
    PB0204 - Correlation Between the Clinical Phenotype and Genotype Profiles in Children with Congenital Factor VII Deficiency
    Room: Exhibition
    Presenting Author: Rachel Kronenfeld, MD – University of Miami Miller School of Medicine/Jackson Memorial Hospital
    Co-Author: Joanna A. Davis – University of Miami Miller School of Medicine/Jackson Memorial Hospital
    Co-Author: Fernando F. Corrales-Medina, MD (he/him/his) – University of Miami-Hemophilia Treatment Center
    Hemophilia and Rare Bleeding Disorders
  • Sunday, Jun 25th
    18:30 – 19:30 ET
    PB0205 - High prevalence of heavy menstrual bleeding in women with rare bleeding disorders in the Netherlands: retrospective data from the RBiN study
    Room: Exhibition
    Presenting Author: Dominique P.M.S.M Maas, MD – Department of Hematology, Radboud university medical center, Nijmegen, The Netherlands. Hemophilia Treatment Center Nijmegen – Eindhoven – Maastricht, The Netherlands
    Co-Author: Joline L. Saes – Department of Hematology, Radboud university medical center, Nijmegen, The Netherlands. Hemophilia Treatment Center Nijmegen – Eindhoven – Maastricht, The Netherlands
    Co-Author: Nicole M.A. Blijlevens – Department of Hematology, Radboud university medical center, Nijmegen, the Netherlands
    Co-Author: Marjon H. Cnossen – Department of Pediatric Hematology, Erasmus MC – Sophia Children’s Hospital, University Medical Center Rotterdam, Rotterdam, The Netherlands
    Co-Author: Paul L. den Exter – Department of Thrombosis and Hemostasis, Leiden University Medical Center, Leiden, The Netherlands
    Co-Author: Olivier W.H. van der Heijden – Department of Obstetrics and Gynecology, Radboud university medical center, Nijmegen, The Netherlands
    Co-Author: Ilmar C. Kruis – Netherlands Hemophilia Society, Nijkerk, The Netherlands
    Co-Author: Karina Meijer, MD, PhD (she/her/hers) – Department of Hematology, University Medical Center Groningen, University of Groningen, Groningen, The Netherlands
    Co-Author: Marjolein Peters – Department of Pediatric Hematology, Amsterdam University Medical Centers, location Emma Children’s Hospital, Amsterdam, The Netherlands
    Co-Author: Roger E.G Schutgens, MD, PhD, MSc (he/him/his) – Center for Benign Hematology, Thrombosis and Hemostasis, Van Creveldkliniek, University Medical Center Utrecht and University Utrecht, Utrecht, The Netherlands
    Co-Author: Waander L. van Heerde – Department of Hematology, Radboud university medical center, Nijmegen, The Netherlands. Hemophilia Treatment Center Nijmegen – Eindhoven – Maastricht, The Netherlands. Enzyre BV, Novio Tech Campus, Nijmegen, The Netherlands.
    Co-Author: Laurens Nieuwenhuizen – Hemophilia Treatment Center Nijmegen – Eindhoven – Maastricht, The Netherlands. Department of Hematology, Maxima Medical Center, Eindhoven, The Netherlands.
    Co-Author: Saskia E.M. Schols – Department of Hematology, Radboud university medical center, Nijmegen, The Netherlands. Hemophilia Treatment Center Nijmegen – Eindhoven – Maastricht, The Netherlands
    Hemophilia and Rare Bleeding Disorders
  • Sunday, Jun 25th
    18:30 – 19:30 ET
    PB0206 - Isolated prolongation of APTT with abnormal bleeding phenotype due to intrinsic tenase defect – A case series.
    Room: Exhibition
    Presenting Author: Tulasi Geevar, MBBS, MD (she/her/hers) – Christian Medical College and Hospital Vellore
    Co-Author: Rutvi Gautam Dave, MBBS, MD, Post-Doctoral Fellow – Christian Medical College and Hospital Vellore
    Co-Author: Surendar singh – Christian Medical College and Hospital Vellore
    Co-Author: Ramya Vijayan – Christian Medical College and Hospital
    Co-Author: Joy Mammen – Christian Medical College and Hospital Vellore
    Co-Author: Sukesh Chandran Nair – Christian Medical College and Hospital Vellore
    Hemophilia and Rare Bleeding Disorders
  • Sunday, Jun 25th
    18:30 – 19:30 ET
    PB0207 - Joint bleeding and joint evaluation in von Willebrand Disease assessed using the Haemophilia Early Arthropathy Detection with Ultrasound (HEAD-US) score
    Room: Exhibition
    Presenting Author: Joana S G Pestana, MD (she/her/hers) – Hospital do Espírito Santo - Évora
    Co-Author: Catarina Câmara, MD (she/her/hers) – Centro Hospitalar Universitário Lisboa Norte
    Co-Author: Catarina J. Jacinto – Centro Hospitalar Universitário Lisboa Norte
    Co-Author: Carolina Peixoto, MD – Centro Hospitalar Universitário Lisboa Norte
    Co-Author: Jorge Félix, MD – Centro Hospitalar Universitário Lisboa Norte
    Co-Author: Filipa Pires – Centro Hospitalar Universitário Lisboa Norte
    Co-Author: Fátima Rodrigues – Centro Hospitalar Universitário Lisboa Norte
    Co-Author: Artur Pereira – Centro Hospitalar Universitário Lisboa Norte
    Co-Author: Cristina Catarino, Dr (she/her/hers) – Centro Hospitalar Universitário Lisboa Norte
    Hemophilia and Rare Bleeding Disorders
  • Sunday, Jun 25th
    18:30 – 19:30 ET
    PB0208 - Tittle: Spleen rupture in Afibrinogenemia: hemorrhagic or thrombotic
    Room: Exhibition
    Presenting Author: Claudia Djambas Khayat, MD, MSc (she/her/hers) – Hotel Dieu de France Hospital, Saint Joseph University Beirut
    Co-Author: Georges Khayat – Hotel Dieu de France Saint Joseph University
    Co-Author: Kamal Hachem – Hotel Dieu de France hospital Saint Joseph University
    Co-Author: Zaki Ghorayeb – Hotel Dieu de France Hospital Saint Joseph University
    Hemophilia and Rare Bleeding Disorders
  • Sunday, Jun 25th
    18:30 – 19:30 ET
    PB0209 - Clinical manifestations of patients with congenital dysfibrinogenemia with the most common hotspot mutation in FGA gene p.Arg35His
    Room: Exhibition
    Presenting Author: Tomas Simurda, MD, PhD. – National Centre of Hemostasis and Thrombosis, Department of Hematology and Transfusiology, Comenius University in Bratislava, Jessenius Faculty of Medicine in Martin and University Hospital in Martin, Slovakia
    Co-Author: Miroslava Drotarova, MD – National Centre of Hemostasis and Thrombosis, Department of Hematology and Transfusiology, Comenius University in Bratislava, Jessenius Faculty of Medicine in Martin and University Hospital in Martin, Slovakia
    Co-Author: Jana Zolkova, DSc, PhD (she/her/hers) – National Centre of Hemostasis and Thrombosis, Department of Hematology and Transfusiology, Comenius University in Bratislava, Jessenius Faculty of Medicine in Martin and University Hospital in Martin, Slovakia
    Co-Author: Zuzana Kolkova – Biomedical Center Martin, Comenius University in Bratislava, Jessenius Faculty of Medicine in Martin
    Co-Author: Dusan Loderer – Biomedical Center Martin, Comenius University in Bratislava, Jessenius Faculty of Medicine in Martin
    Co-Author: Ingrid Skornova, Ing. – National Center of Hemostasis and Thrombosis, Department of Hematology and Transfusion Medicine, Comenius University in Bratislava, Jessenius Faculty of Medicine in Martin and University Hospital in Martin, Martin, Slovakia
    Co-Author: Monika Brunclikova, MD – National Centre of Hemostasis and Thrombosis, Department of Hematology and Transfusiology, Comenius University in Bratislava, Jessenius Faculty of Medicine in Martin and University Hospital in Martin, Slovakia
    Co-Author: Marian Grendar – Biomedical Center Martin, Comenius University in Bratislava, Jessenius Faculty of Medicine in Martin
    Co-Author: Zora Lasabova – Department of Molecular Biology and Genomics, Comenius University in Bratislava, Jessenius Faculty of Medicine in Martin
    Co-Author: Jan Stasko, MD, PhD (he/him/his) – National Center of Hemostasis and Thrombosis, Department of Hematology and Transfusion Medicine, Comenius University in Bratislava, Jessenius Faculty of Medicine in Martin and University Hospital in Martin, Martin, Slovakia
    Co-Author: Peter Kubisz – National Center of Hemostasis and Thrombosis, Department of Hematology and Transfusion Medicine, Comenius University in Bratislava, Jessenius Faculty of Medicine in Martin and University Hospital in Martin, Martin, Slovakia
    Hemophilia and Rare Bleeding Disorders
  • Sunday, Jun 25th
    18:30 – 19:30 ET
    PB0210 - Heterozygous structural variation mimicking homozygous substitution in MCFD2 in a French patient with combined Factor V and Factor VIII deficiency.
    Room: Exhibition
    Co-Author: Yohann Jourdy – Hospices Civils de Lyon, Groupe Hospitalier Est, Service d’hématologie biologique, Bron, France
    Co-Author: Pierre Chamouni – Haemophilia Treatment Centre, University Hospital, Rouen, France
    Co-Author: Mathilde Fretigny – Hospices Civils de Lyon, Groupe Hospitalier Est, Service d’hématologie biologique, Bron, France
    Co-Author: Virginie Barbay – Haemophilia Treatment Centre, University Hospital, Rouen, France
    Co-Author: Véronique Le Cam Duchez, MD PhD (she/her/hers) – Rouen University Hospital
    Co-Author: Victor Bobee – CHU de Rouen, Hôpital Charles Nicolle, Service d’hématologie biologique, Rouen, France
    Co-Author: Simon Lanne – Laboratoire Defrance, Le Petit Quevilly, France
    Co-Author: Pascale Schneider – Hôpital Charles-Nicolle, Service d'hémato-oncologie pédiatrie, Rouen, France
    Presenting Author: Christine Vinciguerra, PharmD, phD – Hospices Civils de Lyon, Groupe Hospitalier Est, Service d’hématologie biologique, Bron, France
    Hemophilia and Rare Bleeding Disorders
  • Sunday, Jun 25th
    18:30 – 19:30 ET
    PB0211 - The utilities of multiple genetic analyses for rare coagulation deficiencies and rare bleeding disorders
    Room: Exhibition
    Presenting Author: Yuri Uchiyama, MD, PhD – Department Rare Disease Genomics, Yokohama City University Hospital
    Co-Author: Yoshiyuki Ogawa, MD, PhD – Department of Hematology, Gunma University Graduate School of Medicine, Maebashi, Japan
    Co-Author: Kunio Yanagisawa – Infection Control and Prevention Center, Gunma University Hospital
    Co-Author: Akira Matsumoto, MD (he/him/his) – Department of Hematology, Gunma University Graduate School of Medicine, Maebashi, Japan
    Co-Author: Takeshi Mizuguchi – Department of Human Genetics, Yokohama City University Graduate School of Medicine
    Co-Author: Hideki Uchiumi – Department of Hematology, Gunma University Graduate School of Medicine, Maebashi, Japan
    Co-Author: Hiroshi Handa – Department of Hematology, Gunma University Graduate School of Medicine
    Co-Author: Naomichi Matsumoto – Department of Human Genetics, Yokohama City University Graduate School of Medicine
    Hemophilia and Rare Bleeding Disorders
  • Sunday, Jun 25th
    18:30 – 19:30 ET
    PB0212 - Patient with spontaneous and severe bleeding episodes diagnosed of Vascular Ehlers-Danlos Syndrome with a de novo pathogenic variant
    Room: Exhibition
    Presenting Author: shally Marcellini-Antonio, Sr., MD (she/her/hers) – Department of Haematology, General Hospital of Segovia, Segovia, Spain.
    Co-Author: Irene Corrales-Insa – Congenital Coagulopathies Laboratory, Banc de Sang i Teixits, Barcelona, Spain.
    Co-Author: Perla Bandini – Congenital Coagulopathies Laboratory, Banc de Sang i Teixits, Barcelona, Spain.
    Co-Author: Nina Borrás – Congenital Coagulopathies Laboratory, Banc de Sang i Teixits, Barcelona, Spain.
    Co-Author: Laura Martin-fernández – Congenital Coagulopathies Laboratory, Banc de Sang i Teixits, Barcelona, Spain.
    Co-Author: Pilar Galán-Álvarez – Department of Haematology, General Hospital of Segovia, Segovia, Spain.
    Co-Author: Ana torres-Tienza – Department of Haematology, General Hospital of Segovia, Segovia, Spain.
    Co-Author: Francisco Vidal- Pérez – Congenital Coagulopathies Laboratory, Banc de Sang i Teixits, Barcelona, Spain.
    Co-Author: Sandra Valencia-Castillo – Department of Haematology, General Hospital of Segovia, Segovia, Spain.
    Co-Author: Aranzazu García-Mateo – Department of Haematology, General Hospital of Segovia, Segovia, Spain.
    Co-Author: Carmen Olivier-Cornacchia – Department of Haematology, General Hospital of Segovia, Segovia, Spain.
    Co-Author: José Antonio Queizán-Hernández – Department of Haematology, General Hospital of Segovia, Segovia, Spain.
    Hemophilia and Rare Bleeding Disorders
  • Sunday, Jun 25th
    18:30 – 19:30 ET
    PB0213 - Efanesoctocog alfa vs. Standard Half-Life (Octocog Alfa) FVIII Therapies for Prophylaxis in Adolescents and Adults with Severe Hemophilia A: A Matching-Adjusted Indirect Comparison and Meta-Analysis
    Room: Exhibition
    Co-Author: Alberto Tosetto, MD – Hematology Department, San Bortolo Hospital, Vicenza, Italy.
    Co-Author: Alix Arnaud, MsC (she/her/hers) – Sanofi, Cambridge, Massachusetts, USA
    Presenting Author: Nana Kragh, MSc – Sobi, Stockholm, Sweden
    Co-Author: Amanda Wilson – Sanofi, Cambridge, Massachusetts, USA
    Co-Author: Piotr Wojciechowski – Putnam PHMR, Krakow, Poland
    Co-Author: Marlena Wdowiak – Putnam PHMR, Krakow, Poland
    Co-Author: Wojciech Margas – Putnam PHMR, Krakow, Poland
    Co-Author: Linda Bystricka – Sobi, Stockholm, Sweden
    Co-Author: Patricia Guyot – Sanofi, Cambridge, Massachusetts, USA
    Hemophilia and Rare Bleeding Disorders
  • Sunday, Jun 25th
    18:30 – 19:30 ET
    PB0214 - Evaluation of innovative laboratory tests to predict a thrombotic phenotype in a family with dysfibrinogenemia and a novel FGG mutation
    Room: Exhibition
    Presenting Author: Amaury LL Monard, MD (she/her/hers) – Department of internel Medicine and Central Diagnostic Laboratory MUMC+, Maastricht, The Netherlands
    Co-Author: Floor C.J.I. Heubel-Moenen – Department Hematology, MUMC+, Maastricht, the Netherlands
    Co-Author: Elisabetta Castoldi, PhD – Department of Biochemistry, CARIM, Maastricht University, Maastricht (The Netherlands)
    Co-Author: Ilaria de simone, MA – Department of Biochemistry, Faculty of Health, Medicine and Life Sciences, Maastricht University, Maastricht, The Netherlands
    Co-Author: Paola van der Meijden, PhD – Department of Biochemistry, Faculty of Health, Medicine and Life Sciences, Maastricht University, Maastricht, The Netherlands
    Co-Author: Kanin Wichapong – Department of Biochemistry, Faculty of Health, Medicine and Life Sciences, Maastricht University, Maastricht, The Netherlands
    Co-Author: William van Doorn – Department of Central Diagnostic Laboratory, MUMC+, Maastricht, The Netherlands
    Co-Author: Stefano Spada, MSc – Center for Thrombosis and Hemostasis (CTH), University Medical Centre Mainz, Germany
    Co-Author: Dave Hellenbrand – Department of Central Diagnostic Laboratory, MUMC +, Maastricht, The Netherlands
    Co-Author: Alexander Stork – Internal Medicine, St Anna Ziekenhuis, Geldrop, The Netherlands
    Co-Author: Hugo ten Cate, MD, PhD, FAHA (he/him/his) – Thrombosis Expertise Center, Heart & Vascular Center, Maastricht University Medical Center, Maastricht, the Netherlands
    Co-Author: Erik A.M. Beckers – Department of Hematology, Maastricht University Medical Center + and Maastricht University, Maastricht, The Netherlands
    Co-Author: Yvonne Henskens, MSc PhD – Central Diagnostic Laboratory at Maastricht University Medical Centre+
    Hemophilia and Rare Bleeding Disorders
  • Sunday, Jun 25th
    18:30 – 19:30 ET
    PB0215 - Assessment of global hemostatic assay by ROTEM in 63 patients with congenital dysfibrinogenemia
    Room: Exhibition
    Presenting Author: Miroslava Drotarova, MD – National Centre of Hemostasis and Thrombosis, Department of Hematology and Transfusiology, Comenius University in Bratislava, Jessenius Faculty of Medicine in Martin and University Hospital in Martin, Slovakia
    Co-Author: Tomas Simurda, MD, PhD. – National Centre of Hemostasis and Thrombosis, Department of Hematology and Transfusiology, Comenius University in Bratislava, Jessenius Faculty of Medicine in Martin and University Hospital in Martin, Slovakia
    Co-Author: Zuzana Kolkova – Biomedical Center Martin, Comenius University in Bratislava, Jessenius Faculty of Medicine in Martin
    Co-Author: Dusan Loderer – Biomedical Center Martin, Comenius University in Bratislava, Jessenius Faculty of Medicine in Martin
    Co-Author: Peter Kubisz – National Center of Hemostasis and Thrombosis, Department of Hematology and Transfusion Medicine, Comenius University in Bratislava, Jessenius Faculty of Medicine in Martin and University Hospital in Martin, Martin, Slovakia
    Co-Author: Jan Stasko, MD, PhD (he/him/his) – National Center of Hemostasis and Thrombosis, Department of Hematology and Transfusion Medicine, Comenius University in Bratislava, Jessenius Faculty of Medicine in Martin and University Hospital in Martin, Martin, Slovakia
    Co-Author: Monika Brunclikova, MD – National Centre of Hemostasis and Thrombosis, Department of Hematology and Transfusiology, Comenius University in Bratislava, Jessenius Faculty of Medicine in Martin and University Hospital in Martin, Slovakia
    Co-Author: Jana Zolkova, DSc, PhD (she/her/hers) – National Centre of Hemostasis and Thrombosis, Department of Hematology and Transfusiology, Comenius University in Bratislava, Jessenius Faculty of Medicine in Martin and University Hospital in Martin, Slovakia
    Co-Author: Ingrid Skornova, Ing. – National Center of Hemostasis and Thrombosis, Department of Hematology and Transfusion Medicine, Comenius University in Bratislava, Jessenius Faculty of Medicine in Martin and University Hospital in Martin, Martin, Slovakia
    Co-Author: Rita Marchi – UNIGE
    Co-Author: Alessandro Casini, MD – Division of Angiology and Hemostasis, Faculty of Medicine, Geneva University Hospitals, Geneva, Switzerland
    Hemophilia and Rare Bleeding Disorders
  • Sunday, Jun 25th
    18:30 – 19:30 ET
    PB0216 - Cancer in patients with bleeding disorders : a French monocentric retrospective study.
    Room: Exhibition
    Presenting Author: Jordan WIMMER – Hematology Laboratory, Hôpitaux Universitaires de Strasbourg, France
    Co-Author: Annick BRUNOT – Hemophilia Treatment Center, Groupe hospitalier de la région de Mulhouse et Sud Alsace, France
    Co-Author: Olivier FEUGEAS (he/him/his) – Hemophilia Treatment Center, Hôpitaux Universitaires de Strasbourg, France
    Co-Author: Agathe HERB – Hematology Laboratory, Hôpitaux Universitaires de Strasbourg, France
    Co-Author: Laurent SATTLER – Hematology Laboratory, Hôpitaux Universitaires de Strasbourg, France
    Co-Author: Dominique DESPREZ – hopital de Strasbourg
    Hemophilia and Rare Bleeding Disorders
  • Sunday, Jun 25th
    18:30 – 19:30 ET
    PB0217 - Genotypic distribution in congenital rare bleeding disorders patients of Asian Indian origin: Results of a collaborative ISTH-RTC study
    Room: Exhibition
    Co-Author: Amit Sharma, PhD – All India Institute of Medical Sciences
    Co-Author: Sneha Singh, PhD (she/her/hers) – Institute of Experimental Hematology and Transfusion Medicine, University Clinic Bonn
    Co-Author: Behnaz Pezeshkpoor, PhD (she/her/hers) – University Clinic Bonn AöR, Institute of Experimental Haematology and Transfusion Medicine, Bonn, Germany
    Co-Author: Anna Pavlova – University Clinic Bonn AöR, Institute of Experimental Haematology and Transfusion Medicine, Bonn, Germany
    Co-Author: Samhitha Urs Ramaraje Urs, MSc – Institute of Experimental Haematology and Transfusion Medicine, University Clinic Bonn
    Presenting Author: Haroon Javed, MSc – Institute of Experimental Haematology and Transfusion Medicine, University Hospital Bonn
    Co-Author: Kamal Kishor, PhD – All India Institute of Medical Sciences
    Co-Author: Ravi Ranjan, PhD – ALL INDIA INSTITUT OF MEDICAL SCIENCES, NEW DELHI
    Co-Author: Manoranjan Mahapatra – AIIMS NEW DELHI
    Co-Author: Johannes Oldenburg, MD (he/him/his) – University Clinic Bonn AöR, Institute of Experimental Haematology and Transfusion Medicine, Bonn, Germany
    Co-Author: Arijit Biswas, PD Dr (Biol) – Institute of Experimental Haematology and Transfusion Medicine, University Clinic Bonn
    Hemophilia and Rare Bleeding Disorders
  • Sunday, Jun 25th
    18:30 – 19:30 ET
    PB0218 - Trisomy X conferring moderate hemophilia A by extremely skewed X-chromosome inactivation
    Room: Exhibition
    Presenting Author: Keiko Shinozawa, PhD – Department of Laboratory Medicine, Tokyo Medical University
    Co-Author: Kenji Niiya – Department of Internal Medicine, Junpukai Health Management Center
    Co-Author: Seiichi Fujimoto – Department of Pediatrics, Chugoku Central Hospital
    Co-Author: Masato Bingo – Department of Laboratory Medicine, Tokyo Medical University
    Co-Author: Takeshi Hagiwara – Department of Laboratory Medicine, Tokyo Medical University
    Co-Author: Hiroshi Inaba, PhD – Department of Laboratory Medicine, Tokyo Medical University
    Co-Author: Kagehiro Amano – Department of Laboratory Medicine, Tokyo Medical University
    Co-Author: Katsuyuki Fukutake – Department of Blood Coagulation, Ogikubo Hospital
    Co-Author: Ei Kinai – Department of Laboratory Medicine, Tokyo Medical University
    Hemophilia and Rare Bleeding Disorders
  • Sunday, Jun 25th
    18:30 – 19:30 ET
    PB0219 - Utility of ACMG classification to support interpretation of molecular genetic test results in patients with FVII deficiency
    Room: Exhibition
    Presenting Author: Sonja Rosa Alesci, MD, PhD (she/her/hers) – IMD blood coagulation Hochtaunus
    Co-Author: Hecking Carola – IMD blood coagulation centre Hochtaunus
    Co-Author: Racké Benjamin – Institute of immunogenetics Kaiserslautern
    Co-Author: Carl Erik Dempfle – IMD blood coagulation centre Mannheim
    Hemophilia and Rare Bleeding Disorders
  • Sunday, Jun 25th
    18:30 – 19:30 ET
    PB0220 - Clinical presentation and bleeding severity in women with autosomal inherited bleeding disorders and hemophilia carriers: real-life data from the Spanish Registry
    Room: Exhibition
    Co-Author: Nuria Fernández-Mosteirín, PhD MD – Hospital Universitario Miguel Servet (Zaragoza)
    Co-Author: Cristina Sierra Aisa, MD – Hospital Universitario Cruces (Barakalo-Bizkaia)
    Co-Author: Jose Mª Bastida, PhD, MD – Complejo Asistencial Universitario de Salamanca-IBSAL-USAL (Salamanca)
    Co-Author: Faustino García Candel – Hospital Clínico Universitario Virgen de la Arrixaca (Murcia)
    Presenting Author: Manuel Rodriguez López, Jr., MD – Hospital Álvaro Cunqueiro (Vigo)
    Co-Author: Francisco José López Jaime, MD – Hemostasis and Thrombosis Unit, Regional University Hospital of Málaga, IBIMA, Málaga, Spain.
    Co-Author: Eugenia Fernández Mellid – Hospital Clínico Universitario de Santiago (Santiago de Compostela)
    Co-Author: Agustín Rodríguez-Alén – Hematology Department, Hospital Universitario de Toledo, Spain
    Hemophilia and Rare Bleeding Disorders
  • Sunday, Jun 25th
    18:30 – 19:30 ET
    PB0221 - Clinical heterogeneity of congenital dysfibrinogenemia within a two-generation family in Brazil
    Room: Exhibition
    Presenting Author: Thaís D R Nóbrega – University of São Paulo Medical School
    Co-Author: Paula Villaça – University of São Paulo Medical School
    Co-Author: Erica Okazaki – Clinics Hospital of the University of São Paulo Medical School
    Co-Author: Cynthia Rothschild, Master (she/her/hers) – ICESP - University of São Paulo Medical School
    Co-Author: Bianca Stefanello – Clinics Hospital of the University of São Paulo Medical School
    Co-Author: Tania R. F. da Rocha – Clinics Hospital of the University of São Paulo Medical School
    Co-Author: Vanderson Rocha – Clinics Hospital of the University of São Paulo Medical School
    Co-Author: Fernanda A. Orsi – University of São Paulo Medical School
    Hemophilia and Rare Bleeding Disorders
  • Sunday, Jun 25th
    18:30 – 19:30 ET
    PB0222 - A novel c.952G>T mutation in the FGG gene exon 8 causing Hypodysfibrinogenemia
    Room: Exhibition
    Co-Author: Aniello Casoria, MD – Federico II University of Naples
    Co-Author: Ciro Miele – UOC Laboratory Medicine of Hematology and Hemostasis; Federico II University, Naples, Italy
    Co-Author: Filomena Capasso – UOC Laboratory Medicine of Hematology and Hemostasis; Federico II University, Naples, Italy
    Co-Author: Rosaria Mormile – Haematology, Department of Translational and precision Medicine, Sapienza University, Rome, Italy
    Co-Author: Luigi Bisceglia – Division of medical Genetics IRCCS Casa Sollievo della Sofferenza, San Giovanni Rotondo, Italy
    Co-Author: Gennaro Vecchione – Division of medical Genetics IRCCS Casa Sollievo della Sofferenza, San Giovanni Rotondo, Italy
    Co-Author: Fedinando Cirillo – Department of Clinical Medicine and Surgery, Federico II University, Naples, Italy
    Co-Author: Ignazio Frangipane – Department of Clinical Medicine and Surgery, Federico II University, Naples, Italy
    Co-Author: Paolo Conca – Department of Clinical Medicine and Surgery, Federico II University, Naples, Italy
    Co-Author: Ernesto Cimino – Department of Clinical Medicine and Surgery, Federico II University, Naples, Italy
    Presenting Author: Antonella Tufano, MD, PhD (she/her/hers) – Department of Clinical Medicine and Surgery, University of Naples, Federico II
    Hemophilia and Rare Bleeding Disorders
  • Sunday, Jun 25th
    18:30 – 19:30 ET
    PB0224 - Effective management of surgical procedures of inherited FVII deficient patients – 15 years experience at University Hospital in Ostrava
    Room: Exhibition
    Presenting Author: Radomira Hrdlickova (she/her/hers) – University Hospital Ostrava
    Co-Author: Sarka Blahutova – University Hospital Ostrava
    Co-Author: Zuzana Cermakova – University Hospital Ostrava
    Hemophilia and Rare Bleeding Disorders
  • Sunday, Jun 25th
    18:30 – 19:30 ET
    PB0225 - Evaluation of Real-world Treatment Patterns and Outcomes in Patients with Von Willebrand Disease Treated Prophylactically with recombinant Von Willebrand Factor in the United States: Interim Analysis
    Room: Exhibition
    Co-Author: Jonathan C. Roberts – Bleeding & Clotting Disorders Institute
    Co-Author: Maissaa Janbain – Louisiana Center for Bleeding and Clotting Disorders, Tulane University Medical Center, LA, USA
    Co-Author: Jessica R. Marden – Analysis Group, Inc
    Co-Author: Sanjana Sundaresan – Analysis Group, Inc
    Co-Author: Sarah A. Hale, MS, PhD – Takeda Pharmaceuticals
    Presenting Author: Jorge Caicedo, MD – Takeda Pharmaceuticals U.S.A., Inc
    Hemophilia and Rare Bleeding Disorders
  • Sunday, Jun 25th
    18:30 – 19:30 ET
    PB0226 - Bleeding and clotting in the same patient: A case of Factor XI deficiency and thrombosis.
    Room: Exhibition
    Presenting Author: Maynolia Naidoo, MBChB (she/her/hers) – Department of Molecular Medicine and Haematology, University of the Witwatersrand, and the National Health Laboratory Service.
    Co-Author: Johnny Mahlangu, MD (he/him/his) – Haemophilia Comprehensive Care Centre, Charlotte Maxeke Johannesburg Academic Hospital, University of the Witwatersrand and National Health Laboratory Service, Johannesburg, South Africa
    Co-Author: Nolukholo Ncete, N/A – Department of Molecular Medicine and Haematology, University of the Witwatersrand, and the National Health Laboratory Service.
    Hemophilia and Rare Bleeding Disorders
  • Sunday, Jun 25th
    18:30 – 19:30 ET
    PB0227 - Symptomatic Factor X Deficiency in a Single Family with a Genetic Mutation Previously Reported as of Uncertain Significance
    Room: Exhibition
    Presenting Author: Faryal Munir, MBBS, MD, FAAP – The University of Texas, MD Anderson Cancer Center
    Co-Author: Jiasen He, MD – The University of Texas, MD Anderson Cancer Center
    Co-Author: Nidra Rodriguez – The University of Texas MD, Anderson Cancer Center; The University of Texas Health Science Center at Houston, McGovern Medical SchAsool, Gulf States Hemophilia and Thrombophilia Center
    Hemophilia and Rare Bleeding Disorders
  • Sunday, Jun 25th
    18:30 – 19:30 ET
    PB0228 - A Prospective, Observational Study of Bleeding and Quality of Life in Patients with Glanzmann Thrombasthenia in the United Kingdom: A First Report
    Room: Exhibition
    Co-Author: Ulrike Lorch – Richmond Pharmacology, London, United Kingdom
    Co-Author: Thomas York – Richmond Pharmacology, London, United Kingdom
    Co-Author: Kate Khair, RN, PhD – Haemnet, London, United Kingdom
    Co-Author: Luke Pembroke – Haemnet, London, United Kingdom
    Presenting Author: Catherine J. Rea, MA, PhD – Hemab Therapeutics
    Hemophilia and Rare Bleeding Disorders
  • Sunday, Jun 25th
    18:30 – 19:30 ET
    PB0229 - DESIGNING THE RYPLAZIM® (PLASMINOGEN, HUMAN-tvmh) ARM OF ATHN TRANSENDS: SAFETY AND EFFECTIVENESS IN PEOPLE WITH PLASMINOGEN DEFICIENCY
    Room: Exhibition
    Presenting Author: Lynn Malec, MD, MSc – Versiti Blood Research Institute, Milwaukee, WI, USA; Division of Hematology & Oncology, Departments of Medicine and Pediatrics, Medical College of Wisconsin, Milwaukee, WI, USA
    Co-Author: Rebecca Bialas – Plasminogen Deficiency Foundation
    Co-Author: Carrie O'Neill – American Thrombosis and Hemostasis Network
    Co-Author: Karen Thibaudeau – Prometic Bioproduction
    Co-Author: Elaine Warner – Kedrion Biopharma
    Co-Author: Erin Weigel – Kedrion Biopharma
    Co-Author: Michael Recht, MD, PhD, MBA (he/him/his) – National Hemophilia Foundation
    Hemophilia and Rare Bleeding Disorders
  • Sunday, Jun 25th
    18:30 – 19:30 ET
    PB0230 - First insight into the presurgical APTT determination practice in Nigeria through a nationwide explorative survey
    Room: Exhibition
    Co-Author: Eyiuche D. Ezigbo, PhD (she/her/hers) – eyiuche.ezigbo@unn.edu.ng
    Co-Author: Uchechukwu ezomike – University of Nigeria Teaching Hospital
    Co-Author: Polit Yelpoji – 3Department of Medical Laboratory Sciences, Faculty of Health Sciences and Technology, College of Health Sciences University of Jos
    Presenting Author: Helen C. Okoye, MD (she/her/hers) – College of Medicine, University of Nigeria
    Co-Author: Theresa U. Nwagha, MD, MPH, FMCPath, MSc (she/her/hers) – University of Nigeria , College of Medicine Ituku Ozalla Campus
    Co-Author: Chidinma Onwuka – Faculty of Medical Science, College of Medicine. University of Nigeria Nsukka/ University of Nigeria Teaching Hospital, Ituku/Ozalla
    Co-Author: Olayanju Olusola – Department of Medical Laboratory Science, College of Medicine and Health Sciences, Afe Babalola University, Ado-Ekiti
    Hemophilia and Rare Bleeding Disorders
  • Sunday, Jun 25th
    18:30 – 19:30 ET
    PB0231 - Liver Transplant Complicated by Reperfusion Injury in a Child with Severe Factor V Deficiency
    Room: Exhibition
    Presenting Author: Mehul Thakkar, MD – Department of Pediatrics, Washington University in St. Louis
    Co-Author: Surbhi Saini – Department of Pediatrics, Washington University in St. Louis
    Co-Author: Janis Stoll – Department of Pediatrics, Washington University in St. Louis
    Co-Author: Sakil Kulkarni – Department of Pediatrics, Washington University in St. Louis
    Co-Author: David Wilson – Department of Pediatrics, Washington University in St. Louis
    Co-Author: Adeel Khan – Department of Surgery, Washington University in St. Louis
    Co-Author: Maria Doyle – Department of Surgery, Washington University in St. Louis
    Co-Author: Melanie Fields – Department of Pediatrics, Washington University in St. Louis
    Hemophilia and Rare Bleeding Disorders
  • Sunday, Jun 25th
    18:30 – 19:30 ET
    PB0233 - Von Willebrand disease in the east Mediterranean region: current situation and gaps
    Room: Exhibition
    Presenting Author: Claudia Djambas Khayat, MD, MSc (she/her/hers) – Hotel Dieu de France Hospital, Saint Joseph University Beirut
    Co-Author: Emna GOUIDER BELHADJALI – Aziza Othmana Hospital, Tunis
    Co-Author: Mohamad El Khorassani – Mohamad V University , Rabat
    Co-Author: Magdy El-Ekiaby – Hematology Unit, Blood Transfusion Centre, Shabrawishi Hospital, Giza Egypt
    Hemophilia and Rare Bleeding Disorders
  • Sunday, Jun 25th
    18:30 – 19:30 ET
    PB0234 - Comprehensive Evaluation of Coagulation and Fibrinolysis Parameters in Patients with Congenital Factor XIII Deficiency in Pakistan: Case Control Study.
    Room: Exhibition
    Presenting Author: Munira Borhany, MBBS, MCPS, FCPS, FRCP (Edin), FRCPath – Haemophilia Welfare Society, Karachi
    Co-Author: Rukhshanda Nadeem – Haemophilia Welfare Society, Karachi
    Co-Author: Bojun Li – Department for BioMedical Research, University of Bern.
    Co-Author: Paulina Stoklosa – Department for BioMedical Research, University of Bern
    Co-Author: Verena Schroeder, PhD – University of Bern
    Hemophilia and Rare Bleeding Disorders
  • Sunday, Jun 25th
    18:30 – 19:30 ET
    PB0235 - Phase 3 Study of the Efficacy, Pharmacokinetics, Immunogenicity and Safety of von Willebrand Factor/Factor VIII Concentrate in Patients with Severe von Willebrand Disease under 6 Years of Age
    Room: Exhibition
    Presenting Author: Akshat Jain – Loma Linda University School of Medicine Center of Excellence for Bleeding Disorders
    Co-Author: Tarja-Elina Weisz – Octapharma Pharmazeutika Produktionsges.m.b.H
    Co-Author: Cristina Solomon, MD MBA – Octapharma AG
    Co-Author: Vladimir Vdovin – Morozovskaya Children's City Clinical Hospital
    Co-Author: Pavel Zharkov – Dmitry Rogachev National Research Center of Pediatric Hematology
    Co-Author: Zorica Trajkova-Antevska – PHI University Clinic for child diseases
    Co-Author: Ester Zapotocka – University Hospital Motol
    Hemophilia and Rare Bleeding Disorders
  • Sunday, Jun 25th
    18:30 – 19:30 ET
    PB0236 - Bleeding episode during a long-term anticoagulation with direct oral anticoagulant: an unusual revelation of a severe factor V deficiency
    Room: Exhibition
    Co-Author: Laurie Goubeau – Service Hematologie Biologique et UF Hemostase Clinique, Hopital Cochin AP-HP. Centre -Universite Paris Cite
    Co-Author: Zoé Guilbert – Service Hematologie Biologique et UF Hemostase Clinique, Hopital Cochin AP-HP.Centre - Universite Paris Cite
    Co-Author: Malika Saadi – Service Cardiologie, Hopital Cochin, AP-HP. Centre – Universite Paris Cite
    Co-Author: Fabien Picard – Service Cardiologie, Hopital Cochin, AP-HP. Centre – Universite Paris Cite
    Co-Author: Lucile Perrin – Service Cardiologie, Hopital Cochin, AP-HP. Centre – Universite Paris Cite
    Co-Author: Ladislas Capdevila – Service Hematologie Biologique et UF Hemostase Clinique, Hopital Cochin AP-HP.Centre - Universite Paris Cite
    Co-Author: Michaela Fontenay – Service Hematologie Biologique et UF Hemostase Clinique, Hopital Cochin AP-HP.Centre - Universite Paris Cite
    Co-Author: Jérôme Duchemin – Service Hematologie Biologique et UF Hemostase Clinique, Hopital Cochin AP-HP.Centre - Universite Paris Cite
    Co-Author: Valérie Proulle – Service Hematologie Biologique et UF Hemostase Clinique, Hopital Cochin AP-HP.Centre - Universite Paris Cite
    Presenting Author: Charlyne Brakta – Service Hématologie Biologique et Hémostase Clinique, Hôpital Cochin AP-HP.Centre - Université Paris Cité
    Hemophilia and Rare Bleeding Disorders
  • Sunday, Jun 25th
    18:30 – 19:30 ET
    PB0237 - Inhibitor in congenital FXI deficiency
    Room: Exhibition
    Co-Author: Tereza Fenclová (she/her/hers) – National Reference Laboratory for Disorders in Hemostasis, Institute of Hematology and Blood Transfusion
    Co-Author: Dana Provaznikova, PhD (she/her/hers) – National Reference Laboratory for Disorders in Hemostasis, Institute of Hematology and Blood Transfusion, Prague, Czech Republic
    Co-Author: Renata Liskova – National Reference Laboratory for Disorders in Hemostasis, Institute of Hematology and Blood Transfusion, Prague, Czech Republic
    Co-Author: Alena Radovska – National Reference Laboratory for Disorders in Hemostasis, Institute of Hematology and Blood Transfusion, Prague, Czech Republic
    Co-Author: Martina Simonikova – National Reference Laboratory for Disorders in Hemostasis, Institute of Hematology and Blood Transfusion, Prague, Czech Republic
    Co-Author: Jan Loužil – Centre for Thrombosis and Hemostasis, Institute of Hematology and Blood Transfusion
    Co-Author: Daniela Češpivová – National Reference Laboratory for Disorders in Hemostasis, Institute of Hematology and Blood Transfusion
    Co-Author: Frantisek Marecek – National Reference Laboratory for Disorders in Hemostasis, Institute of Hematology and Blood Transfusion, Prague, Czech Republic
    Co-Author: Peter Salaj – Centre for Thrombosis and Hemostasis, Institute of Hematology and Blood Transfusion
    Presenting Author: Ingrid Hrachovinova – National Reference Laboratory for Disorders in Hemostasis, Institute of Hematology and Blood Transfusion, Prague, Czech Republic
    Hemophilia and Rare Bleeding Disorders
  • Sunday, Jun 25th
    18:30 – 19:30 ET
    PB0238 - Prospective, Phase III Study of the Efficacy, Safety, and Pharmacokinetics of a Human Antithrombin III Concentrate in Congenital Antithrombin Deficiency During Surgery or Childbirth
    Room: Exhibition
    Presenting Author: Craig Kessler, MD (he/him/his) – Georgetown University Hospital
    Co-Author: Mariko Hashimoto – Octapharma USA Inc.
    Co-Author: Martina Jansen – Octapharma Pharmazeutika Produktionsgesellschaft mbH
    Co-Author: Michael D. Tarantino – Bleeding & Clotting Disorders Institute, Peoria, IL, USA
    Hemophilia and Rare Bleeding Disorders
  • Sunday, Jun 25th
    18:30 – 19:30 ET
    PB0239 - Hereditary coagulation factor FVII deficiency caused by compound heterozygous mutation
    Room: Exhibition
    Presenting Author: Rongfu Zhou, PhD,MD – Nanjing Drum Tower Hospital, The Affiliated Hospital of Nanjing University Medical School, Nanjing, China
    Co-Author: Wenjing Gao – Nanjing Medical University
    Hemophilia and Rare Bleeding Disorders
  • Sunday, Jun 25th
    18:30 – 19:30 ET
    PB0240 - Possible Autoimmune Acquired Factor 13 deficiency : Tailoring management in a resource constrained setting in India, A Case Report.
    Room: Exhibition
    Presenting Author: Mona Vijayaran, MBBS MD DM – Sahara Hospital Lucknow
    Co-Author: Surbhi Gupta – Sahara Hospital Lucknow
    Co-Author: Shamick Biswas – Sahara Hospital Lucknow
    Co-Author: Mishra Sanjay – KGMU, Lucknow
    Hemophilia and Rare Bleeding Disorders
  • Sunday, Jun 25th
    18:30 – 19:30 ET
    PB0242 - Epistaxis in a patient with Glanzmann Thrombasthenia : about a Strasbourg case revealing an endonasal tumor
    Room: Exhibition
    Presenting Author: Olivier FEUGEAS (he/him/his) – Hemophilia Treatment Center, Hôpitaux Universitaires de Strasbourg, France
    Co-Author: Laurent SATTLER – Hematology Laboratory, Hôpitaux Universitaires de Strasbourg, France
    Co-Author: Jordan WIMMER – Hematology Laboratory, Hôpitaux Universitaires de Strasbourg, France
    Co-Author: Agathe HERB – Hematology Laboratory, Hôpitaux Universitaires de Strasbourg, France
    Co-Author: Christian DEBRY – ENT Department, Hôpitaux Universitaires de Strasbourg, France
    Co-Author: Dominique DESPREZ – hopital de Strasbourg
    Hemophilia and Rare Bleeding Disorders
  • Monday, Jun 26th
    07:00 – 07:45 ET
    MC 13.1 - Carriers of Hemophilia: Can We Do Better at Diagnosing Them?
    Room: Wilcom Room at the InterContinental Montreal
    Speaker: Manuel Carcao, MD, FRCPC – Division of Haematology/Oncology, Department of Paediatrics, Hospital for Sick Children, University of Toronto, Toronto, Canada
    Hemophilia and Rare Bleeding Disorders
  • Monday, Jun 26th
    08:00 – 09:15 ET
    SOA 14.4 - What Do We Do When the Cause of the Bleeding Is Unclear?
    Room: 710A
    Moderator: Shannon Jackson, MD (she/her/hers) – Providence Hematology, St. Paul’s Hospital, Vancouver, BC, Canada
    Moderator: Ingrid Pabinger, MD – Clinical Division of Hematology and Hemostaseology, Department of Medicine I, Medical University of Vienna, Vienna, Austria
    Hemophilia and Rare Bleeding Disorders
  • Monday, Jun 26th
    08:00 – 08:25 ET
    SOA 14.1 - What Goes Unseen: Unrecognized Inheritance Contributing to Bleeding in Rare Bleeding Disorders and Hemophilia
    Room: 710A
    Speaker: Diane Nugent, MD (she/her/hers) – CHOC Childrens and Center for Inherited Blood Disorders
    Hemophilia and Rare Bleeding Disorders
  • Monday, Jun 26th
    08:25 – 08:50 ET
    SOA 14.2 - The Role of Non-Replacement Therapies in Bleeding Disorders Other Than Hemophilia
    Room: 710A
    Speaker: Flora Peyvandi, MD, PhD (she/her/hers) – IRCCS Ca' Granda Maggiore Hospital Foundation, Angelo Bianchi Bonomi Hemophilia and Thrombosis Center, Milano, Italy; Università degli Studi di Milano, Department of Pathophysiology and Transplantation, Milano, Italy
    Hemophilia and Rare Bleeding Disorders
  • Monday, Jun 26th
    08:50 – 09:15 ET
    SOA 14.3 - Investigating Patients for Bleeding Disorders When Most of the “Usual” Ones Have Been Ruled Out
    Room: 710A
    Speaker: Johanna Gebhart, MD, PhD (she/her/hers) – Clinical Division of Hematology and Hemostaseology, Department of Medicine I, Medical University of Vienna, Vienna, Austria
    Hemophilia and Rare Bleeding Disorders
  • Monday, Jun 26th
    10:45 – 12:00 ET
    OC 30.6 - Hemophilia Gene Therapy Basic Science
    Room: 517
    Moderator: David Lillicrap, MD – Department of Pathology and Molecular Medicine, Queen's University
    Moderator: Radek Kaczmarek, PhD – Department of Pediatrics, Indiana University School of Medicine
    Hemophilia and Rare Bleeding Disorders
  • Monday, Jun 26th
    10:45 – 12:00 ET
    OC 33.6 - Hemophilia Basic Science - Novel Therapies and Joint Disease
    Room: 710B
    Moderator: Jean St-Louis, MD, FRCPC (he/him/his) – Université de Montréal
    Moderator: Jordan A. Shavit, MD, PhD (he/him/his) – Department of Pediatrics and Department of Human Genetics, University of Michigan Medical School
    Hemophilia and Rare Bleeding Disorders
  • Monday, Jun 26th
    10:45 – 11:00 ET
    OC 30.1 - A Novel Strategy for Platelet-Specific Gene Therapy for the Treatment of Hemophilia A via Intranasal Delivery Lentiviral Vectors Containing Factor VIII
    Room: 517
    Presenting Author: Cameron W. Rementer, PhD – Seattle Children's Research Institute
    Co-Author: Chong Li – Seattle Children's Research Institute - Seattle, Washington
    Co-Author: Chun-Yu Chen, PhD – Seattle Children's Research Institute
    Co-Author: Carol Miao – Seattle Children's Research Institute
    Hemophilia and Rare Bleeding Disorders
  • Monday, Jun 26th
    10:45 – 11:00 ET
    OC 33.1 - Neutrophil extracellular traps promote gasdermin-D-dependent joint damage in hemophilia
    Room: 710B
    Presenting Author: Tomasz W. Kaminski, PharmD – University of Pittsburgh
    Co-Author: Tomasz Brzoska, PhD (he/him/his) – University of Pittsburgh
    Co-Author: Omika Katoch – University of Pittsburgh
    Co-Author: Margaret V. Ragni, MD, MPH (she/her/hers) – Department of Medicine, University of Pittsburgh, Pittsburgh, PA, USA
    Co-Author: Prithu Sundd, PhD (he/him/his) – University of Pittsburgh
    Hemophilia and Rare Bleeding Disorders
  • Monday, Jun 26th
    11:00 – 11:15 ET
    OC 30.2 - Stable Factor VIII Expression and Improvement in Bleeding Phenotype Following Early Childhood Treatment with Adeno-Associated Viral Gene Therapy in the Severe Hemophilia A Dog Model
    Room: 517
    Presenting Author: Paul Batty, MBBS, PhD (he/him/his) – University College London
    Co-Author: Alexandre Menard – Kingston Health Sciences Center
    Co-Author: Christine Brown – Queen's University
    Co-Author: Lorianne Harpell – Queen's University
    Co-Author: Ashrafali M. Ismail – BioMarin Pharmaceutical
    Co-Author: Aomei M. Mo – Queen's University
    Co-Author: Abbey Pender – Queen's University
    Co-Author: Bridget Yates – BioMarin Pharmaceutical
    Co-Author: Andrew Winterborn – Queen's University
    Co-Author: Sylvia Fong, PhD – BioMarin Pharmaceutical
    Co-Author: David Lillicrap, MD – Department of Pathology and Molecular Medicine, Queen's University
    Hemophilia and Rare Bleeding Disorders
  • Monday, Jun 26th
    11:00 – 11:15 ET
    OC 33.2 - Maladaptive Lymphangiogenesis is Associated with Synovial Iron Accumulation and Delayed Clearance in FVIII-/- Mice After Induced Hemarthrosis
    Room: 710B
    Co-Author: Bilgimol Chumappumkal Joseph, PhD – University of California San Diego
    Co-Author: Esther Cooke – University of California San Diego
    Co-Author: Chanond Nasamran – University of California San Diego
    Co-Author: Kathleen Fisch – University of California San Diego
    Presenting Author: Annette von Drygalski, MD – University of California San Diego
    Hemophilia and Rare Bleeding Disorders
  • Monday, Jun 26th
    11:15 – 11:30 ET
    OC 30.3 - In vivo gene editing of hemophilia A mice using CRISPR/Cas9 mRNA LNP shows long-term expression of endogenous FVIII
    Room: 517
    Presenting Author: Chun-Yu Chen, PhD – Seattle Children's Research Institute
    Co-Author: Xiaohe Cai – Seattle Children's Research Institute
    Co-Author: Carol Miao – Seattle Children's Research Institute
    Hemophilia and Rare Bleeding Disorders
  • Monday, Jun 26th
    11:15 – 11:30 ET
    OC 33.3 - Evaluating the impact of anti-PEG antibodies on activation of PEGylated therapeutic FVIII products
    Room: 710B
    Presenting Author: Behnaz Pezeshkpoor, PhD (she/her/hers) – University Clinic Bonn AöR, Institute of Experimental Haematology and Transfusion Medicine, Bonn, Germany
    Co-Author: Ann-Cristin Berkemeier – University Clinic Bonn AöR, Institute of Experimental Haematology and Transfusion Medicine, Bonn, Germany
    Co-Author: Isabell Matuschek – University Clinic Bonn AöR, Institute of Experimental Haematology and Transfusion Medicine, Bonn, Germany
    Co-Author: Katrin Hartlieb – University Clinic Bonn AöR, Institute of Experimental Haematology and Transfusion Medicine, Bonn, Germany
    Co-Author: Johannes Oldenburg, MD (he/him/his) – University Clinic Bonn AöR, Institute of Experimental Haematology and Transfusion Medicine, Bonn, Germany
    Hemophilia and Rare Bleeding Disorders
  • Monday, Jun 26th
    11:30 – 11:45 ET
    OC 30.4 - Efficacy and Safety of AAV Delivery of a Novel Factor VIII Variant with Improved Secretion in a Non-Human Primate Model
    Room: 517
    Co-Author: Maria C. Seleme – The Children's Hospital of Philadelphia
    Presenting Author: Jonathan R. Lindgren, B.S. (he/him/his) – The Children's Hospital of Philadelphia
    Co-Author: Giang N. Nguyen – The Children's Hospital of Philadelphia
    Co-Author: Allysen C. Henriksen – The Children's Hospital of Philadelphia
    Co-Author: Charles-Antoine Assenmacher – School of Veterinary Medicine, University of Pennsylvania
    Co-Author: Amy Muehlmatt – Comparative Medicine Services Core, The Children's Hospital of Philadelphia
    Co-Author: Geary R. Smith – Comparative Medicine Services Core, The Children's Hospital of Philadelphia
    Co-Author: Melanie McFadden – Comparative Medicine Services Core, The Children's Hospital of Philadelphia
    Co-Author: Denise E. Sabatino, PhD (she/her/hers) – The Children's Hospital of Philadelphia
    Hemophilia and Rare Bleeding Disorders
  • Monday, Jun 26th
    11:30 – 11:45 ET
    OC 33.4 - Loss of Factor VIII in Zebrafish Does Not Result in Severe Hemophilia A Due to an Altered Balance with Natural Anticoagulants
    Room: 710B
    Presenting Author: Catherine E. RIchter, MS (she/her/hers) – University of Michigan
    Co-Author: Jordan A. Shavit, MD, PhD (he/him/his) – Department of Pediatrics and Department of Human Genetics, University of Michigan Medical School
    Hemophilia and Rare Bleeding Disorders
  • Monday, Jun 26th
    11:45 – 12:00 ET
    OC 30.5 - Expression and Activity of Human Factor VIII (hFVIII) Following Single and Repeat Administration of an Integrating Non-viral Gene Therapy in Multiple Mouse Models of Severe Hemophilia A
    Room: 517
    Co-Author: Brian Truong, PhD (he/him/his) – Poseida Therapeutics
    Co-Author: Khal Hajj – Poseida Therapeutics
    Co-Author: Giang Nguyen – Children's Hospital of Philadelphia
    Co-Author: Johannes Schwerk – Poseida Therapeutics
    Co-Author: Jonnatan Tamayo – Poseida Therapeutics
    Co-Author: Daniel Smith – Poseida Therapeutics
    Co-Author: Manjunath Goolyam – Takeda Pharmaceutical Company
    Co-Author: Daniel Abernathy – Takeda Pharmaceutical Company
    Co-Author: Fernando Lopez Espinoza – Poseida Therapeutics
    Co-Author: Michelle Burrascano – Poseida Therapeutics
    Co-Author: James Yen – Poseida Therapeutics
    Co-Author: Kevin Briseno – Poseida Therapeutics
    Co-Author: Joseph Lucas – Poseida Therapeutics
    Co-Author: Pavan Battiprolu – Poseida Therapeutics
    Co-Author: Mike Bennett – Poseida Therapeutics
    Co-Author: Blair Madison – Poseida Therapeutics
    Presenting Author: Denise E. Sabatino, PhD (she/her/hers) – The Children's Hospital of Philadelphia
    Co-Author: Brent Warner – Poseida Therapeutics
    Co-Author: Eric Ostertag – Poseida Therapeutics
    Co-Author: Joshua Rychak – Poseida Therapeutics, Inc
    Hemophilia and Rare Bleeding Disorders
  • Monday, Jun 26th
    11:45 – 12:00 ET
    OC 33.5 - Structural characterization of coagulation factor VIII
    Room: 710B
    Presenting Author: Samhitha Urs Ramaraje Urs, MSc – Institute of Experimental Haematology and Transfusion Medicine, University Clinic Bonn
    Co-Author: Sneha Singh, PhD (she/her/hers) – Institute of Experimental Hematology and Transfusion Medicine, University Clinic Bonn
    Co-Author: Haroon Javed, MSc – Institute of Experimental Haematology and Transfusion Medicine, University Hospital Bonn
    Co-Author: MD Mubassherul Islam – Institute of Experimental Haematology and Transfusion Medicine, University Clinic Bonn
    Co-Author: Deniz Ugurlar – Materials and Structural Analysis Division, Thermo Fisher Scientific, Achtseweg Noord, 5651 GG Eindhoven, the Netherlands.
    Co-Author: Boxue Ma – Materials and Structural Analysis Division, Thermo Fisher Scientific, Achtseweg Noord, 5651 GG Eindhoven, the Netherlands
    Co-Author: Jean Luc Pellequer – Institut de Biologie Structurale, Methods and Electron Microscopy group, Grenoble, France
    Co-Author: Jean-Marie Teulon – Institut de Biologie Structurale, Methods and Electron Microscopy group, Grenoble, France
    Co-Author: Daphna Fenel – Institut de Biologie Structurale, Methods and Electron Microscopy group, Grenoble, France
    Co-Author: Anna Pepanian – University of Bonn
    Co-Author: Diana Imhof – University of Bonn
    Co-Author: Johannes Oldenburg, MD (he/him/his) – University Clinic Bonn AöR, Institute of Experimental Haematology and Transfusion Medicine, Bonn, Germany
    Co-Author: Arijit Biswas, PD Dr (Biol) – Institute of Experimental Haematology and Transfusion Medicine, University Clinic Bonn
    Hemophilia and Rare Bleeding Disorders
  • Monday, Jun 26th
    14:45 – 16:00 ET
    OC 43.6 - Hemophilia Clinical - Factor VIII Mimetics
    Room: 710B
    Moderator: Mark Belletrutti, MD MSc FRCPC (he/him/his) – BC Children's Hospital, University of British Columbia
    Moderator: Caterina Casari, PhD (she/her/hers) – Laboratory for Hemostasis, Inflammation and Thrombosis, Unité Mixte de Recherche S1176, Institut National de la Santé et de la Recherche Médicale, Université Paris-Saclay
    Hemophilia and Rare Bleeding Disorders
  • Monday, Jun 26th
    14:45 – 16:00 ET
    OC 44.6 - Hemophilia Basic Science - Inhibitors
    Room: 520
    Moderator: Margaret V. Ragni, MD, MPH (she/her/hers) – Department of Medicine, University of Pittsburgh, Pittsburgh, PA, USA
    Moderator: Davide Matino, MD (he/him/his) – Department of Medicine, Division of Hematology, McMaster University, Hamilton, ON
    Hemophilia and Rare Bleeding Disorders
  • Monday, Jun 26th
    14:45 – 15:00 ET
    OC 43.1 - A survey on clinical praxis in initiating emicizumab prophylaxis in previously untreated patients in the PedNet centers
    Room: 710B
    Co-Author: Susanna Ranta – Dep. of Pediatrics, Clinic of Coag. Disorders Karolinska Hospital
    Co-Author: Jayashree Motwani – Department of Paediatric Haematology, Birmingham Children's Hospital, United Kingdom
    Co-Author: Jan Blatny – Children’s University Hospital Brno
    Co-Author: Martina Bührlen – Klinikum Bremen Mitte
    Co-Author: Manuel Carcao, MD, FRCPC – Division of Haematology/Oncology, Department of Paediatrics, Hospital for Sick Children, University of Toronto, Toronto, Canada
    Co-Author: Hervé Chambost – AP-HM, Department of Pediatric Hematology Oncology, Children Hospital La Timone & Aix Marseille University, INSERM, INRA, C2VN, Marseille, France
    Co-Author: Carmen Escuriola-Ettingshausen, MD – Haemophilia Centre Rhine-Main, Mörfelden-Walldorf, Germany
    Co-Author: Kathelijn Fischer, MD, PhD (she/her/hers) – Center for Benign Haematology, Thrombosis and Haemostasis, Van Creveldkliniek, University Medical Center Utrecht, Utrecht University, The Netherlands
    Co-Author: Mutlu Kartal-Kaess, MD (she/her/hers) – Inselspital Bern, Bern, Schweiz
    Co-Author: Gili Kenet – The PedNet Foundation
    Co-Author: Christoph Male, MD, MSc – Department of Paediatrics, Medical University of Vienna, Vienna, Austria.
    Co-Author: Beatrice Nolan – Department of Haematology, Children's Health Ireland at Crumlin, Dublin, Ireland.
    Co-Author: Roseline d'Oiron, MD – Centre for Haemophilia and Rare Congenital Bleeding Disorders, Bicêtre Hospital AP-HP, University of Paris-Saclay and UMR_S1176 INSERM, Le Kremlin-Bicêtre, France
    Co-Author: Martin Olivieri (he/him/his) – Paediatric Thrombosis and Haemostasis Unit, Paediatric Haemophilia Center, Dr. von Hauner Children's Hospital, LMU Clinic, Munich, Germany
    Co-Author: Nadine Gretenkort Andersson – Lund University
    Presenting Author: Christoph Koenigs, Dr. Dr. – University Hospital Frankfurt, Department of Paediatrics and Adolescent Medicine, Frankfurt, Germany
    Hemophilia and Rare Bleeding Disorders
  • Monday, Jun 26th
    14:45 – 15:00 ET
    OC 44.1 - Structural studies of blood coagulation factor VIII bound to patient-derived inhibitory antibodies
    Room: 520
    Co-Author: Kenneth C. Childers – Western Washington University
    Co-Author: Nathan Avery – Western Washington University
    Co-Author: Pete Lollar – Aflac Cancer and Blood Disorders Center, Children’s Healthcare of Atlanta, Department of Pediatrics, Emory University School of Medicine
    Co-Author: Chris Doering – Aflac Cancer and Blood Disorders Center, Children’s Healthcare of Atlanta, Department of Pediatrics, Emory University School of Medicine
    Co-Author: Carmen Coxon – Department of Biotherapeutics, National Institute for Biological Standards and Control
    Presenting Author: Paul C. Spiegel, Jr., PhD (he/him/his) – Western Washington University
    Hemophilia and Rare Bleeding Disorders
  • Monday, Jun 26th
    15:00 – 15:15 ET
    OC 43.2 - Low-dose Emicizumab prophylaxis in severe hemophilia A patients – a pilot study with a much anticipated promise for a resource limited country
    Room: 710B
    Presenting Author: Rucha Patil, PhD (she/her/hers) – ICMR-National Institute of Immunohaematology, Mumbai, India
    Co-Author: Chandrakala s – Seth GS Medical College and KEM Hospital, Mumbai, India
    Co-Author: Farah Jijina – Seth GS Medical College and KEM Hospital, Mumbai, India
    Hemophilia and Rare Bleeding Disorders
  • Monday, Jun 26th
    15:00 – 15:15 ET
    OC 44.2 - Developing humanized mouse models as a testing platform for immune tolerance induction therapy for antibody-positive hemophilia A patients
    Room: 520
    Presenting Author: Li-Fu Chen – Department of Clinical Laboratory Sciences and Medical Biotechnology, National Taiwan University
    Co-Author: Sheng-Chieh Chou, MD. (he/him/his) – Division of Hematology, Department of Internal Medicine, National Taiwan University Hospital
    Co-Author: Yi-Hsuan Wu – Department of Clinical Laboratory Sciences and Medical Biotechnology, National Taiwan University
    Co-Author: Yen-Ting Chang – Department of Clinical Laboratory Sciences and Medical Biotechnology, National Taiwan University
    Co-Author: Chien-Hong Liu – Department of Clinical Laboratory Sciences and Medical Biotechnology, National Taiwan University
    Co-Author: Chin-Yu Cheng – Department of Laboratory Medicine, National Taiwan University Hospital
    Co-Author: Bin-Bin Lin – Department of Laboratory Medicine, National Taiwan University Hospital
    Co-Author: Cheng-An Hsu – Department of Laboratory Medicine, National Taiwan University Hospital
    Co-Author: I-Shing Yu – Laboratory Animal Center; Collage of Medicine, National Taiwan University
    Co-Author: Shu-Wha Lin – Department of Clinical Laboratory Sciences and Medical Biotechnology, National Taiwan University; Department of Laboratory Medicine, National Taiwan University Hospital
    Hemophilia and Rare Bleeding Disorders
  • Monday, Jun 26th
    15:15 – 15:30 ET
    OC 43.3 - Surgery in people with hemophilia A receiving emicizumab prophylaxis: real-world experience from a single French Reference Center of Hemophilia
    Room: 710B
    Presenting Author: Charlyne Brakta – Service Hématologie Biologique et Hémostase Clinique, Hôpital Cochin AP-HP.Centre - Université Paris Cité
    Co-Author: Natalie Stieltjes – Centre de Ressource et de Competences-Maladies Hemorragiques Constitutionnelles, Hopital Cochin APHP.Centre
    Co-Author: Sophie Combe – Centre de Ressource et de Competences-Maladies Hemorragiques Constitutionnelles, Hopital Cochin APHP.Centre
    Co-Author: Nadra Ounnoughene – Centre de Ressource et de Competences-Maladies Hemorragiques Constitutionnelles, Hopital Cochin APHP.Centre
    Co-Author: Jérôme Duchemin – Service Hematologie Biologique et UF Hemostase Clinique, Hopital Cochin AP-HP.Centre - Universite Paris Cite
    Co-Author: Ladislas Capdevila – Service Hematologie Biologique et UF Hemostase Clinique, Hopital Cochin AP-HP.Centre - Universite Paris Cite
    Co-Author: Laurie Goubeau – Service Hematologie Biologique et UF Hemostase Clinique, Hopital Cochin AP-HP. Centre -Universite Paris Cite
    Co-Author: Michaela Fontenay – Service Hematologie Biologique et UF Hemostase Clinique, Hopital Cochin AP-HP.Centre - Universite Paris Cite
    Co-Author: Valérie Roussel Robert – Centre de Ressource et de Competences-Maladies Hemorragiques Constitutionnelles, Hopital Cochin APHP.Centre
    Co-Author: Valérie Proulle – Service Hematologie Biologique et UF Hemostase Clinique, Hopital Cochin AP-HP.Centre - Universite Paris Cite
    Hemophilia and Rare Bleeding Disorders
  • Monday, Jun 26th
    15:15 – 15:30 ET
    OC 44.3 - Exploring red blood cells as a novel tolerogenic approach for factor VIII inhibitors employing immuno-dominant FVIII derived peptides presented on MHC class II
    Room: 520
    Presenting Author: Mariarosaria Miranda, MA – Department of Molecular Hematology, Sanquin Research and Landsteiner Laboratory, Amsterdam, The Netherlands
    Co-Author: Eelke Brandsma – Department of Hematopoiesise, Sanquin Research, Amsterdam, The Netherlands
    Co-Author: Paul Kaijen – Department of Molecular Hematology, Sanquin Research, Amsterdam, The Netherlands
    Co-Author: Floris Van Alphen – Department of Molecular Hematology, Sanquin Research, 1066 CX Amsterdam, the Netherlands
    Co-Author: Robin Van Bruggen – Department of Molecular Hematology, Sanquin Research, Amsterdam, The Netherlands
    Co-Author: Karin Fijnvandraat – Amsterdam UMC, University of Amsterdam, Emma Children’s Hospital, Pediatric Hematology Amsterdam, Netherlands
    Co-Author: Sebastien Lacroix-Desmazes, PhD – Centre De Recherche Des Cordeliers, Paris, France
    Co-Author: Jan Voorberg – Department of Molecular Hematology, Sanquin Research and Landsteiner Laboratory
    Hemophilia and Rare Bleeding Disorders
  • Monday, Jun 26th
    15:30 – 15:45 ET
    OC 43.4 - Effectiveness of emicizumab under real-world conditions in patients of all ages with hemophilia A with and without FVIII inhibitors: interim analysis of the non-interventional study EMIIL
    Room: 710B
    Presenting Author: Johannes Oldenburg, MD (he/him/his) – University Clinic Bonn AöR, Institute of Experimental Haematology and Transfusion Medicine, Bonn, Germany
    Co-Author: Carmen Escuriola-Ettingshausen, MD – Haemophilia Centre Rhine-Main, Mörfelden-Walldorf, Germany
    Co-Author: Pierre Fontana, MD PhD (he/him/his) – Division of Angiology and Haemostasis, University Hospitals of Geneva, Switzerland
    Co-Author: Swee Wenning – SRH Kurpfalzkrankenhaus, Heidelberg, Germany
    Co-Author: Christian Pfrepper, MD – Division of Hemostaseology, University Hospital Leipzig, Germany
    Co-Author: Bianca Heidersdorf – Roche Pharma AG, Grenzach-Wyhlen, Germany
    Co-Author: Patrick Udvardi – Roche Pharma Schweiz AG, Basel, Switzerland
    Co-Author: Manuela Albisetti – University Children’s Hospital Zurich, Zurich, Switzerland
    Hemophilia and Rare Bleeding Disorders
  • Monday, Jun 26th
    15:30 – 15:45 ET
    OC 44.4 - Association of chemokine CXCL13 and follicular helper T cells in hemophilia A patient and murine model with inhibitors
    Room: 520
    Presenting Author: Yingyu Chen, PhD – Department of Hematology, Fujian Institute of Hematology, Fujian Medical University Union Hospital
    Co-Author: Liping Luo – Department of Hematology, Fujian Institute of Hematology, Fujian Medical University Union Hospital
    Co-Author: Qiaoyun Zheng – Department of Hematology, Fujian Institute of Hematology, Fujian Medical University Union Hospital
    Co-Author: Zhenyu Chen – Department of Hematology, Fujian Institute of Hematology, Fujian Medical University Union Hospital
    Co-Author: Qizhen Shi, MD, PhD – Medical College of Wisconsin, Versiti Blood Research Institute, Children's Research Institute
    Hemophilia and Rare Bleeding Disorders
  • Monday, Jun 26th
    15:45 – 16:00 ET
    OC 43.5 - Should immune tolerance be pursued in the era of Emicizumab? Longitudinal follow up of a FVIII inhibitor cohort - Real World Data
    Room: 710B
    Co-Author: Sarina Levy-Mendelovich, MD – The National Hemophilia Center, and Amalia Biron Research Institute of Thrombosis and Hemostasis, Sheba Medical Center, Ramat Gan, Israel
    Co-Author: Nitzan Atia – Sheba Medical Center
    Co-Author: Ivan Budnik – University of IOWA
    Presenting Author: Assaf Barg, MD – The National Hemophilia Center, and Amalia Biron Research Institute of Thrombosis and Hemostasis, Sheba Medical Center, Ramat Gan, Israel
    Co-Author: Einat Avishai – Tel Aviv University
    Co-Author: Rima Dardik – Tel Aviv University
    Co-Author: Omri Cohen, MD – Sheba medical center, Tel Aviv University
    Co-Author: Tami Brutman-Barazani – Sheba Medical Center
    Co-Author: Tami Livnat, Prof. (she/her/hers) – Tel Aviv University
    Co-Author: Gili Kenet, MD – The National Hemophilia Center, and Amalia Biron Research Institute of Thrombosis and Hemostasis, Sheba Medical Center, Tel Hashomer, Tel Aviv University, Tel Aviv, Israel
    Hemophilia and Rare Bleeding Disorders
  • Monday, Jun 26th
    15:45 – 16:00 ET
    OC 44.5 - A gut metabolite-based dietary therapy influences FVIII inhibitor production with novel relationships between the gut microbiota, blood metabolome, and immune cell frequencies
    Room: 520
    Presenting Author: Matthew Cormier, PhD (he/him/his) – Queen's University
    Co-Author: Erin Burnett – Queen's University, Pathology and Molecular Medicine
    Co-Author: Kate Nesbitt – Queen's University
    Co-Author: Aomei M. Mo – Queen's University
    Co-Author: Eliana Marino – Monash University
    Co-Author: Christine Hough – Queen's University
    Co-Author: David Lillicrap, MD – Department of Pathology and Molecular Medicine, Queen's University
    Hemophilia and Rare Bleeding Disorders
  • Monday, Jun 26th
    18:30 – 19:30 ET
    PB0614 - Use of a Microfluidic Model to Evaluate Platelet Function in Traumatic Brain Injury Patients Pre- and Post- Platelet Transfusion
    Room: Exhibition
    Presenting Author: Devin M. Dishong – Trauma and Transfusion Medicine Research Center, Department of Surgery, University of Pittsburgh
    Co-Author: Emily P. Mihalko, PhD – Trauma and Transfusion Medicine Research Center, Department of Surgery, University of Pittsburgh
    Co-Author: Amudan J. Srinivasan, MD – Trauma and Transfusion Medicine Research Center, Department of Surgery, University of Pittsburgh
    Co-Author: Lara Hoteit, MD – Trauma and Transfusion Medicine Research Center, Department of Surgery, University of Pittsburgh
    Co-Author: Nijmeh Alsaadi – Trauma and Transfusion Medicine Research Center, Department of Surgery, University of Pittsburgh
    Co-Author: Ronit Kar – University of Pittsburgh - School of Medicine
    Co-Author: David O. Okonkwo – Department of Neurosurgery, University of Pittsburgh
    Co-Author: Jason L. Sperry – Department of Surgery, University of Pittsburgh
    Co-Author: Matthew D. Neal, MD FACS (he/him/his) – University of Pittsburgh
    Co-Author: Susan M. Shea, MSME, PhD (she/her/hers) – Trauma and Transfusion Medicine Research Center, Department of Surgery and Department of Bioengineering, University of Pittsburgh
    Hemophilia and Rare Bleeding Disorders
  • Monday, Jun 26th
    18:30 – 19:30 ET
    PB0616 - UK National External Quality Assessment Scheme for Blood coagulation (UK NEQAS BC) evaluation of the point of care fibrinogen device
    Room: Exhibition
    Co-Author: Dianne P. Kitchen, MSc – UK NEQAS BC
    Co-Author: Emily Erskine – Sheffield teaching hospitals NHS trust
    Co-Author: Lilia Brown, MSc – UK NEQAS for Blood Coagulation
    Co-Author: Christopher Mark Peter Reilly-Stitt, MSc – UK NEQAS BC
    Co-Author: Ian Jennings – UK NEQAS BC
    Presenting Author: Steve Kitchen, PhD – Sheffield Haemophilia and Thrombosis Centre
    Co-Author: Isobel Walker – UK NEQAS BC
    Hemophilia and Rare Bleeding Disorders
  • Monday, Jun 26th
    18:30 – 19:30 ET
    PB0617 - Kinetics of Clot Formation and Fibrinolysis in Severely Injured Trauma Patients
    Room: Exhibition
    Presenting Author: Andrew R. Gosselin, BS (he/him/his) – Rutgers University
    Co-Author: Christopher Bargoud – Rutgers-Robert Wood Johnson Medical School
    Co-Author: Shane Mathew – Rutgers-Robert Wood Johnson Medical School
    Co-Author: Ashley Toussaint – Rutgers-Robert Wood Johnson Medical School
    Co-Author: Marie Macor – Rutgers-Robert Wood Johnson Medical Center
    Co-Author: Susette Coyle – Rutgers-Robert Wood Johnson Medical Center
    Co-Author: Valerie Tutwiler, PhD – Rutgers-State University of New Jersey
    Co-Author: Joseph Hanna – Rutgers-Robert Wood Johnson Medical School
    Hemophilia and Rare Bleeding Disorders
  • Monday, Jun 26th
    18:30 – 19:30 ET
    PB0620 - (Mis)labeling hemophilia severity: Exploring the illness cognitions of persons with hemophilia.
    Room: Exhibition
    Presenting Author: Roy Khalife, MD, MHPE, FRCPC (he/him/his) – Department of Medicine (Hematology), University of Ottawa
    Co-Author: Lindsay Cowley – Ottawa Hospital Research Institute, The Ottawa Hospital
    Co-Author: Kori LaDonna – Department of Innovation in Medical Education, University of Ottawa
    Hemophilia and Rare Bleeding Disorders
  • Monday, Jun 26th
    18:30 – 19:30 ET
    PB0621 - : Emicizumab plasma concentrations are not related to bleeding rates using standard dosing, a call for dose adaptation
    Room: Exhibition
    Co-Author: Konrad van der Zwet, MD – Center for Benign Haematology, Thrombosis and Haemostasis, Van Creveldkliniek, University Medical Center Utrecht, Utrecht University
    Co-Author: Lize F.D. van Vulpen – Center for Benign Haematology, Thrombosis and Haemostasis, Van Creveldkliniek, University Medical Center Utrecht, Utrecht University, The Netherlands
    Co-Author: Paul R. van der Valk – Center for Benign Haematology, Thrombosis and Haemostasis, Van Creveldkliniek, University Medical Center Utrecht, Utrecht University, The Netherlands
    Co-Author: Idske C.L Kremer Hovinga, MD PhD – Center for Benign Haematology, Thrombosis and Haemostasis, Van Creveldkliniek, University Medical Center Utrecht, Utrecht University, The Netherlands
    Co-Author: Karin P. M. van Galen, MD PhD MsC – Center for Benign Haematology, Thrombosis and Haemostasis, Van Creveldkliniek, University Medical Center Utrecht, Utrecht University, Utrecht, The Netherlands
    Co-Author: Roger E.G Schutgens, MD, PhD, MSc (he/him/his) – Center for Benign Hematology, Thrombosis and Hemostasis, Van Creveldkliniek, University Medical Center Utrecht and University Utrecht, Utrecht, The Netherlands
    Presenting Author: Kathelijn Fischer, MD, PhD (she/her/hers) – Center for Benign Haematology, Thrombosis and Haemostasis, Van Creveldkliniek, University Medical Center Utrecht, Utrecht University, The Netherlands
    Hemophilia and Rare Bleeding Disorders
  • Monday, Jun 26th
    18:30 – 19:30 ET
    PB0622 - A Report of the Measurement of Steady State Emicizumab Levels in an Irish cohort of Persons with Severe Haemophilia A
    Room: Exhibition
    Presenting Author: Paula E. Grennan, BSc and MSc – St. James's Hospital, Dublin
    Co-Author: Mary Byrne – National Coagulation Centre, St James's Hospital, Dublin
    Co-Author: Mairead Doyle, MSc – National Coagulation Centre, St James's Hospital, Dublin
    Co-Author: Niamh Larkin – St. James's Hospital, Dublin
    Co-Author: Michelle Lavin, MB, PhD (she/her/hers) – National Coagulation Centre, St. James Hospital and Irish Centre for Vascular Biology, School of Pharmacy and Biomolecular Sciences, Royal College of Physicians and Surgeons in Ireland (RCSI)
    Co-Author: James S. O'Donnell, MB, PhD – Irish Centre for Vascular Biology, Royal College of Surgeons in Ireland,Dublin, Ireland
    Co-Author: Niamh O'Connell, MD – National Coagulation Centre, St James's Hospital, Dublin
    Co-Author: Kevin Ryan – National Coagulation Centre, St James's Hospital, Dublin
    Hemophilia and Rare Bleeding Disorders
  • Monday, Jun 26th
    18:30 – 19:30 ET
    PB0623 - An enriched population pharmacokinetic model for recombinant factor IX-Fc fusion including young children with haemophilia B
    Room: Exhibition
    Co-Author: Sjoerd F. Koopman, MSc. – Hospital Pharmacy-Clinical Pharmacology, Amsterdam University Medical Centers, Amsterdam, The Netherlands
    Co-Author: Tine M.H.J. Goedhart – Department of Pediatric Hematology and Oncology, Erasmus MC Sophia Children's Hospital, University Medical Center Rotterdam, Rotterdam, The Netherlands
    Co-Author: Laura H. Bukkems – Hospital Pharmacy-Clinical Pharmacology, Amsterdam University Medical Centers, Amsterdam, The Netherlands
    Co-Author: Frank W.G. Leebeek, MD, PhD – Erasmus MC, University Medical Center Rotterdam, The Netherlands
    Co-Author: Karin Fijnvandraat – Amsterdam UMC, University of Amsterdam, Emma Children’s Hospital, Pediatric Hematology Amsterdam, Netherlands
    Co-Author: Michiel Coppens, MD, PhD (he/him/his) – Amsterdam University Medical Centers, Amsterdam, The Netherlands
    Co-Author: Mary Mathias – Haemophilia Comprehensive Care Centre, Great Ormond Street Hospital for Children NHS Foundation Trust, London, United Kingdom
    Co-Author: Peter W. Collins, MD – Arthur Bloom Haemophilia Centre, School of Medicine, Cardiff University Hospital, Cardiff, United Kingdom
    Co-Author: Robert C. Tait – Department of Haematology, Royal Infirmary, Glasgow, United Kingdom
    Co-Author: Nicola Curry, MD, FRCP, FRCPath – Oxford University Hospitals NHS Foundation Trust
    Co-Author: Jaenette Payne – Department of Paediatric Haematology, Sheffield Children’s NHS Foundation Trust, Sheffield, United Kingdom
    Co-Author: Pratima Chowdary, MD – Katharine Dormandy Haemophilia and Thrombosis Centre, Royal Free London NHS Foundation Trust, London, United Kingdom
    Co-Author: Ron A.A. Mathôt – Hospital Pharmacy-Clinical Pharmacology, Amsterdam University Medical Centers, Amsterdam, The Netherlands
    Co-Author: Marjon H. Cnossen – Department of Pediatric Hematology, Erasmus MC – Sophia Children’s Hospital, University Medical Center Rotterdam, Rotterdam, The Netherlands
    Presenting Author: Caroline Mussert, MD – Erasmus MC Sophia Children's Hospital, University Medical Center Rotterdam
    Hemophilia and Rare Bleeding Disorders
  • Monday, Jun 26th
    18:30 – 19:30 ET
    PB0624 - A-SURE: Intra-patient Comparison of Prophylactic Effectiveness of a Recombinant Factor VIII Fc Fusion Protein Versus Standard Half-life Factor VIII in Hemophilia A
    Room: Exhibition
    Co-Author: Johannes Oldenburg, MD (he/him/his) – University Clinic Bonn AöR, Institute of Experimental Haematology and Transfusion Medicine, Bonn, Germany
    Co-Author: Charles Hay – University Department of Haematology, Manchester Royal Infirmary, Manchester, United Kingdom
    Co-Author: Flora Peyvandi, MD, PhD (she/her/hers) – IRCCS Ca' Granda Maggiore Hospital Foundation, Angelo Bianchi Bonomi Hemophilia and Thrombosis Center, Milano, Italy; Università degli Studi di Milano, Department of Pathophysiology and Transplantation, Milano, Italy
    Co-Author: Anna-Elina Lehtinen – Coagulation Disorders Unit, Department of Hematology, Helsinki University Hospital Comprehensive Cancer Center and University of Helsinki, Helsinki, Finland
    Presenting Author: Ingrid Pabinger, MD – Clinical Division of Hematology and Hemostaseology, Department of Medicine I, Medical University of Vienna, Vienna, Austria
    Co-Author: Eveline Nüesch – Sobi, Basel, Switzerland
    Co-Author: Håkan Malmström – Sobi, Stockholm, Sweden
    Co-Author: Aletta Falk – Sobi, Stockholm, Sweden
    Co-Author: Stefan Lethagen – Sobi, Stockholm, Sweden
    Hemophilia and Rare Bleeding Disorders
  • Monday, Jun 26th
    18:30 – 19:30 ET
    PB0625 - Emicizumab Prophylaxis in People with Hemophilia A Aged ≥50 Years with Comorbidities: Experience From the ATHN 7 Hemophilia Natural History Study
    Room: Exhibition
    Co-Author: Tyler W. Buckner – University of Colorado Anschutz Medical Campus
    Co-Author: Nabil Daoud – American Thrombosis and Hemostasis Network
    Co-Author: Lucy Lee – Genentech, Inc.
    Co-Author: Paul Morton – Genentech, Inc.
    Co-Author: Carrie O'Neill – American Thrombosis and Hemostasis Network
    Co-Author: Michael Wang, MD – University of Colorado Denver Hemophilia and Thrombosis Center
    Presenting Author: Michael Recht, MD, PhD, MBA (he/him/his) – National Hemophilia Foundation
    Hemophilia and Rare Bleeding Disorders
  • Monday, Jun 26th
    18:30 – 19:30 ET
    PB0626 - Quantitative pharmacokinetic model to characterize and extrapolate long-term FVIII activity levels in patients with severe hemophilia A treated with valactocogene roxaparvovec
    Room: Exhibition
    Presenting Author: Suresh Agarwal, PhD – BioMarin Pharmaceuticals Inc.
    Co-Author: Andreas Tiede, MD PhD (he/him/his) – Department of Hematology, Hemostasis, Oncology and Stem Cell Transplantation, Hannover Medical School, Hannover, Germany
    Co-Author: Tara M. Robinson – BioMarin Pharmaceutical Inc., Novato, CA, USA
    Co-Author: Joshua Henshaw – BioMarin Pharmaceuticals Inc.
    Hemophilia and Rare Bleeding Disorders
  • Monday, Jun 26th
    18:30 – 19:30 ET
    PB0627 - Management of invasive procedures in patients with Hemophilia A receiving Emicizumab prophylaxis: Real-world data from a national Hemophilia treatment center.
    Room: Exhibition
    Presenting Author: Omri Cohen, MD – Sheba medical center, Tel Aviv University
    Co-Author: Ivan Budnik – University of IOWA
    Co-Author: Noa Ludan – Sackler School of Medicine, Tel Aviv University, Israel
    Co-Author: Shani Kassia Lyskov – Sackler School of Medicine, Tel Aviv University, Israel
    Co-Author: Orly Efros, MD, MHA (she/her/hers) – National Hemophilia Center and Thrombosis & Hemostasis Institute, Sheba Medical Center, Israel. Sackler Faculty of Medicine, Tel Aviv University, Israel.
    Co-Author: Aharon Lubetsky – National Hemophilia Center and Thrombosis & Hemostasis Institute, Sheba Medical Center, Israel. Sackler Faculty of Medicine, Tel Aviv University, Israel.
    Co-Author: Shadan Lalezari – Sheba medical center, Tel Aviv University
    Co-Author: Mudi Misgav – Sheba medical center, Tel Aviv University
    Co-Author: Gili Kenet, MD – The National Hemophilia Center, and Amalia Biron Research Institute of Thrombosis and Hemostasis, Sheba Medical Center, Tel Hashomer, Tel Aviv University, Tel Aviv, Israel
    Co-Author: Assaf Barg, MD – The National Hemophilia Center, and Amalia Biron Research Institute of Thrombosis and Hemostasis, Sheba Medical Center, Ramat Gan, Israel
    Hemophilia and Rare Bleeding Disorders
  • Monday, Jun 26th
    18:30 – 19:30 ET
    PB0628 - The World Federation of Hemophilia Living Guidelines Model
    Room: Exhibition
    Presenting Author: Mona M. Mayla, MBA MEd (she/her/hers) – World Federation of Hemophilia
    Co-Author: Donna Coffin, MSc Epid (she/her/hers) – World Federation of Hemophilia
    Co-Author: Glenn F. Pierce, MD PhD – World Federation of Hemophilia
    Co-Author: Sandra Zelman-Lewis – EBQ Consulting Inc.
    Hemophilia and Rare Bleeding Disorders
  • Monday, Jun 26th
    18:30 – 19:30 ET
    PB0629 - Designing the Efanesoctocog Alfa Module of ATHN Transcends: Safety, Tolerability, and Effectiveness in Previously Untreated Patients with Hemophilia A
    Room: Exhibition
    Presenting Author: Lynn Malec, MD, MSc – Versiti Blood Research Institute, Milwaukee, WI, USA; Division of Hematology & Oncology, Departments of Medicine and Pediatrics, Medical College of Wisconsin, Milwaukee, WI, USA
    Co-Author: Shannon L. Carpenter – Children's Mercy Kansas City
    Co-Author: Carrie O'Neill – American Thrombosis and Hemostasis Network
    Co-Author: Courtney Thornburg, MD, MS (she/her/hers) – Rady Children's Hospital-San Diego
    Co-Author: Michael Recht, MD, PhD, MBA (he/him/his) – National Hemophilia Foundation
    Hemophilia and Rare Bleeding Disorders
  • Monday, Jun 26th
    18:30 – 19:30 ET
    PB0630 - Final Analysis of Long-term Clinical Outcomes of Prophylaxis With a Recombinant Factor VIII Fc Fusion Protein in Adults Aged ≥50 Years With Severe Hemophilia A
    Room: Exhibition
    Presenting Author: Doris V. Quon, MD, PhD (she/her/hers) – Luskin Orthopaedic Institute for Children
    Co-Author: Shannon Jackson, MD (she/her/hers) – Providence Hematology, St. Paul’s Hospital, Vancouver, BC, Canada
    Co-Author: Maria Teresa Alvarez-Román, MD, PhD – Department of Hematology, University Hospital La Paz, Autonoma University of Madrid, Madrid, Spain
    Co-Author: Umer Khan – Sanofi, San Diego, CA, USA
    Co-Author: Sandra Casiano – Sanofi, Cambridge, MA, USA
    Hemophilia and Rare Bleeding Disorders
  • Monday, Jun 26th
    18:30 – 19:30 ET
    PB0632 - Quality of life outcomes following treatment with octocog alfa in patients with hemophilia A: 9-year interim read-out of the real-world AHEAD international study
    Room: Exhibition
    Presenting Author: Kate Khair, RN, PhD – Haemnet, London, United Kingdom
    Co-Author: Margareth C. Ozelo, MD, PhD (she/her/hers) – Hemocentro UNICAMP, Department of Internal Medicine, School of Medical Sciences, University of Campinas, Campinas, São Paulo, Brazil
    Co-Author: Cedric Hermans, MD, PhD (he/him/his) – St-Luc University Hospital
    Co-Author: Renchi Yang, MD (he/him/his) – Institute of Hematology and Blood Diseases Hospital, Chinese Academy of Medical Sciences and Peking Union Medical College, Tianjin, China
    Co-Author: Randy Guerra, MD – Takeda Development Center Americas, Inc., Cambridge, MA, USA
    Co-Author: Joan Gu – Takeda Development Center Americas, Inc., Cambridge, MA, USA
    Co-Author: Pooja Oberai, MD MS (she/her/hers) – Takeda Development Center Americas, Inc., Cambridge, MA, USA
    Co-Author: Manuel Carcao, MD, FRCPC – Division of Haematology/Oncology, Department of Paediatrics, Hospital for Sick Children, University of Toronto, Toronto, Canada
    Hemophilia and Rare Bleeding Disorders
  • Monday, Jun 26th
    18:30 – 19:30 ET
    PB0633 - Understanding the Requirement for Additional Factor VIII Infusion Associated with Novel Haemophilia A Treatments: An Expert Elicitation Exercise
    Room: Exhibition
    Presenting Author: Sandra Santos – BioMarin Pharmaceutical Inc.
    Co-Author: Enrico Ferri Grazzi – HCD Economics Ltd.
    Co-Author: Tom Burke – HCD Economics Ltd.
    Hemophilia and Rare Bleeding Disorders
  • Monday, Jun 26th
    18:30 – 19:30 ET
    PB0634 - A Phase 3, single-arm, multicenter, open-label, one-way crossover study to evaluate the efficacy and safety of fitusiran prophylaxis in people with severe hemophilia A or B, with or without inhibitors
    Room: Exhibition
    Presenting Author: Christian Sussebach, MD – Sanofi
    Co-Author: Barbara Kittner – Sanofi
    Co-Author: Jiarui Chi – Sanofi
    Co-Author: Marion Afonso – Sanofi
    Co-Author: Shauna Andersson – Sanofi
    Hemophilia and Rare Bleeding Disorders
  • Monday, Jun 26th
    18:30 – 19:30 ET
    PB0635 - A usability study assessing handling and preference of the concizumab pen-injector in patients with haemophilia and caregivers
    Room: Exhibition
    Presenting Author: Niklas K. Rasmussen, MD (he/him/his) – Novo Nordisk A/S, Søborg, Denmark
    Co-Author: Birgitte Berg – Novo Nordisk A/S, Søborg, Denmark
    Co-Author: Anne Sia Louise Christiansen – Novo Nordisk A/S, Søborg, Denmark
    Co-Author: Jesper S. Neergaard – Novo Nordisk A/S, Søborg, Denmark
    Co-Author: Sanket Shah – Novo Nordisk Inc., Plainsboro NJ USA
    Co-Author: Gitte Ter-Borch – Novo Nordisk A/S, Søborg, Denmark
    Co-Author: Thomas Sparre – Novo Nordisk A/S, Søborg, Denmark
    Hemophilia and Rare Bleeding Disorders
  • Monday, Jun 26th
    18:30 – 19:30 ET
    PB0636 - Clinical outcomes following treatment with octocog alfa in patients with severe hemophilia A and pre-existing target joints: 9-year interim read-out of the real-world AHEAD international study
    Room: Exhibition
    Presenting Author: Margareth C. Ozelo, MD, PhD (she/her/hers) – Hemocentro UNICAMP, Department of Internal Medicine, School of Medical Sciences, University of Campinas, Campinas, São Paulo, Brazil
    Co-Author: Cedric Hermans, MD, PhD (he/him/his) – St-Luc University Hospital
    Co-Author: Kate Khair, RN, PhD – Haemnet, London, United Kingdom
    Co-Author: Renchi Yang, MD (he/him/his) – Institute of Hematology and Blood Diseases Hospital, Chinese Academy of Medical Sciences and Peking Union Medical College, Tianjin, China
    Co-Author: Randy Guerra, MD – Takeda Development Center Americas, Inc., Cambridge, MA, USA
    Co-Author: Joan Gu – Takeda Development Center Americas, Inc., Cambridge, MA, USA
    Co-Author: Pooja Oberai, MD MS (she/her/hers) – Takeda Development Center Americas, Inc., Cambridge, MA, USA
    Co-Author: Manuel Carcao, MD, FRCPC – Division of Haematology/Oncology, Department of Paediatrics, Hospital for Sick Children, University of Toronto, Toronto, Canada
    Hemophilia and Rare Bleeding Disorders
  • Monday, Jun 26th
    18:30 – 19:30 ET
    PB0637 - Epidemiological, clinical and radiological profile of articular pathology (joint disease) in the Cameroonian haemophiliac
    Room: Exhibition
    Presenting Author: ANNICK NDOUMBA NKENGUE, MD – Cameroon Hemophilia Treatment Centre, Department of Hematology and Blood Transfusion, Yaoundé University Teaching Hospital
    Co-Author: MICHAEL NKO'O AMVENE – Faculty of Medicine and Biomedical Sciences, University of Yaoundé I, Cameroon
    Co-Author: DANIEL HANDY EONE – Department of surgery, Yaounde Central Hospital, Cameroon
    Co-Author: ERIC MAGNY TIAM – Department of radiology, Yaoundé University Teaching Hospital
    Co-Author: CLAUDE TAYOU – Cameroon Hemophilia Treatment Centre, Department of Hematology and Blood Transfusion, Yaoundé University Teaching Hospital
    Co-Author: PIERRE ONGOLO ZOGO – Department of radiology, Yaounde Central Hospital, Cameroon
    Co-Author: DORA MBANYA – Cameroon Hemophilia Treatment Centre, Department of Hematology and Blood Transfusion, Yaoundé University Teaching Hospital
    Hemophilia and Rare Bleeding Disorders
  • Monday, Jun 26th
    18:30 – 19:30 ET
    PB0638 - Final data from A-MOVE: 12-Month Prospective Multicentre Study to Investigate the Impact of Systematic Joint Examination on Treatment Management Decisions in Patients with Hemophilia A in France
    Room: Exhibition
    Co-Author: Brigitte Pan-Petesch – CRC-MHC Brest – Service Hématologie, Unité Hémostase Clinique
    Co-Author: Nicolas Drillaud – CRC-MHC, CHU Hôtel-Dieu
    Co-Author: Hervé Chambost – AP-HM, Department of Pediatric Hematology Oncology, Children Hospital La Timone & Aix Marseille University, INSERM, INRA, C2VN, Marseille, France
    Presenting Author: Aurélien Lebreton – Service d’hématologie, CHU Clermont-Ferrand, Hôpital Estaing
    Co-Author: Jean-Baptiste Valentin – CRC-MHC Tours
    Co-Author: Romain Jailler – Centre Hospitalier Métropole Savoie
    Co-Author: Oussama Mahdout – Sobi
    Co-Author: Jacob Järås – Sobi
    Co-Author: Kirsten Berger – Sobi
    Co-Author: Ekaterina Gresko – Sobi
    Co-Author: Yohann Repessé, MD-PhD (he/him/his) – CRC-MHC Caen
    Hemophilia and Rare Bleeding Disorders
  • Monday, Jun 26th
    18:30 – 19:30 ET
    PB0639 - Haemophilia; Ageing and Frailty
    Room: Exhibition
    Presenting Author: Susan Shapiro, MD, PhD (she/her/hers) – Oxford University Hospitals National Health Service Foundation Trust, Oxford, UK
    Co-Author: Stephanie Taylor – Oxford University Hospitals NHS Foundation Trust, UK
    Co-Author: William McKeown – Antrim Area Hospital, Northern Ireland; UK Haemophilia Society
    Co-Author: Gina Sangha – Oxford University Hospitals, UK
    Hemophilia and Rare Bleeding Disorders
  • Monday, Jun 26th
    18:30 – 19:30 ET
    PB0640 - Safety and Efficacy of Combined Dual Antiplatelet Therapy and FVIII Prophylaxis in Hemophilia A Patients after the Acute Coronary Syndrome
    Room: Exhibition
    Presenting Author: Pasquale Agosti, MD, PhD – Università degli Studi di Milano, Department of Pathophysiology and Transplantation and Fondazione Luigi Villa, Milan, Italy
    Co-Author: Simona Maria Siboni – Fondazione IRCCS Ca' Granda, Ospedale Maggiore Policlinico, Angelo Bianchi Bonomi Hemophilia and Thrombosis Center
    Co-Author: Alessandro Ciavarella, MD (he/him/his) – Fondazione IRCCS Ca' Granda - Ospedale Maggiore Policlinico, Centro Emofilia e Trombosi Angelo Bianchi Bonomi
    Co-Author: Sara Arcudi, MD – Fondazione IRCCS Ca' Granda - Ospedale Maggiore Policlinico, Centro Emofilia e Trombosi Angelo Bianchi Bonomi
    Co-Author: Federico Boggio – Università degli Studi di Milano
    Co-Author: Roberta Gualtierotti, MD, PhD – Fondazione IRCCS Ca' Granda - Ospedale Maggiore Policlinico, Centro Emofilia e Trombosi Angelo Bianchi Bonomi
    Co-Author: Flora Peyvandi, MD, PhD (she/her/hers) – IRCCS Ca' Granda Maggiore Hospital Foundation, Angelo Bianchi Bonomi Hemophilia and Thrombosis Center, Milano, Italy; Università degli Studi di Milano, Department of Pathophysiology and Transplantation, Milano, Italy
    Hemophilia and Rare Bleeding Disorders
  • Monday, Jun 26th
    18:30 – 19:30 ET
    PB0641 - Association Between Physical Activity and Bleeding Events in People with Hemophilia A Receiving Emicizumab Prophylaxis: Interim Analysis of the TSUBASA Study
    Room: Exhibition
    Presenting Author: Teruhisa Fujii, MD (he/him/his) – Division of Transfusion Medicine/Hemophilia Treatment Center, Hiroshima University Hospital, Hiroshima, Japan
    Co-Author: Kagehiro Amano – Department of Laboratory Medicine, Tokyo Medical University
    Co-Author: Akihiro Sawada – Department of Respiratory Medicine and Hematology, Hyogo Medical University, Hyogo, Japan
    Co-Author: Azusa Nagao, MD, MSc – Department of Blood Coagulation, Ogikubo Hospital, Tokyo, Japan
    Co-Author: Chiai Nagae – Department of Pediatrics, St. Marianna University School of Medicine, Kanagawa, Japan
    Co-Author: Masanori Nojima – Center for Translational Research/Division of Advanced Medicine Promotion, Institute of Medical Science, University of Tokyo, Tokyo, Japan
    Co-Author: Nobuaki Suzuki – Department of Transfusion Medicine, Nagoya University Hospital, Nagoya, Japan
    Co-Author: Daisuke Nosaka – Chugai Pharmaceutical Co., Ltd, Tokyo, Japan
    Co-Author: Tomomi Shimura – Chugai Pharmaceutical Co., Ltd, Tokyo, Japan
    Co-Author: Yoshimasa Sugao – Chugai Pharmaceutical Co., Ltd, Tokyo, Japan
    Co-Author: Keiji Nogami – Nara Medical University, Nara, Japan
    Hemophilia and Rare Bleeding Disorders
  • Monday, Jun 26th
    18:30 – 19:30 ET
    PB0642 - Determinants of the bleeding phenotype in persons with non-severe hemophilia
    Room: Exhibition
    Co-Author: Fabienne R. Kloosterman, MD – Amsterdam UMC, University of Amsterdam, Emma Children’s Hospital, Pediatric Hematology, Meibergdreef 9, Amsterdam, Netherlands
    Co-Author: Anne-Fleur Zwagemaker – Amsterdam UMC, University of Amsterdam, Emma Children’s Hospital, Pediatric Hematology, Meibergdreef 9, Amsterdam, Netherlands
    Co-Author: Catherine N. N. Bagot, Dr MBBS MD – Department of Haematology, Glasgow Royal Infirmary, Glasgow, United Kingdom
    Co-Author: Erik A.M. Beckers – Department of Hematology, Maastricht University Medical Center + and Maastricht University, Maastricht, The Netherlands
    Co-Author: Sara Boyce – Department of Haematology, University Hospital Southampton, Southampton, United Kingdom
    Co-Author: Paul Brons – Department of Pediatric Hemato-Oncology, Radboud University Medical Center, Nijmegen, The Netherlands
    Co-Author: Giancarlo Castaman, MD – Center for Bleeding Disorders and Coagulation, Careggi University Hospital, Florence, Italy
    Co-Author: Peter W. Collins, MD – Arthur Bloom Haemophilia Centre, School of Medicine, Cardiff University Hospital, Cardiff, United Kingdom
    Co-Author: Jeroen C.J Eikenboom, MD. PhD – Leiden University Medical Center
    Co-Author: Charles Hay – University Department of Haematology, Manchester Royal Infirmary, Manchester, United Kingdom
    Co-Author: Shannon Jackson, MD (she/her/hers) – Providence Hematology, St. Paul’s Hospital, Vancouver, BC, Canada
    Co-Author: Frank W.G. Leebeek, MD, PhD – Erasmus MC, University Medical Center Rotterdam, The Netherlands
    Co-Author: Christoph Male, MD, MSc – Department of Paediatrics, Medical University of Vienna, Vienna, Austria.
    Co-Author: Karina Meijer, MD, PhD (she/her/hers) – Department of Hematology, University Medical Center Groningen, University of Groningen, Groningen, The Netherlands
    Co-Author: Laurens Nieuwenhuizen – Hemophilia Treatment Center Nijmegen – Eindhoven – Maastricht, The Netherlands. Department of Hematology, Maxima Medical Center, Eindhoven, The Netherlands.
    Co-Author: Susan Shapiro, MD, PhD (she/her/hers) – Oxford University Hospitals National Health Service Foundation Trust, Oxford, UK
    Co-Author: Michiel Coppens, MD, PhD (he/him/his) – Amsterdam University Medical Centers, Amsterdam, The Netherlands
    Co-Author: Karin Fijnvandraat – Amsterdam UMC, University of Amsterdam, Emma Children’s Hospital, Pediatric Hematology Amsterdam, Netherlands
    Presenting Author: Samantha Gouw, MD, PhD (she/her/hers) – The University of Amsterdam
    Hemophilia and Rare Bleeding Disorders
  • Monday, Jun 26th
    18:30 – 19:30 ET
    PB0643 - Efficacy of emicizumab prophylaxis in patients with severe hemophilia A in Germany: Follow-up evaluation of real-life-data documented by smart medication eDiary
    Room: Exhibition
    Co-Author: Wolfgang Mondorf, MD – HZRM
    Co-Author: Hermann Eichler, MD (he/him/his) – Institute of Clinical Haemostaseology and Transfusion Medicine, University and University Hospital of the Saarland, Homburg, Germany
    Co-Author: Ronald Fischer – SRH Kurpfalzkrankenhaus Heidelberg
    Co-Author: Katharina Holstein, MD (she/her/hers) – University Hospital Hamburg Eppendorf
    Co-Author: Robert Klamroth, MD, PhD (he/him/his) – Vivantes Klinikum im Friedrichshain, Clinic for Internal Medicine Angiology and Haemostaseology
    Co-Author: Wolfgang Miesbach, MD – University Hospital Frankfurt, Frankfurt, Germany
    Co-Author: Heinrich Richter – Hämophiliezentrum Münster
    Co-Author: Karolin Trautmann – Universitätsklinikum Carl Gustav Carus Dresden
    Co-Author: Ulrich Sachs, PhD – Institute for Clinical Immunology, Transfusion Medicine and Hemostasis, Justus-Liebig-University, Langhansstr. 7, 35392 Giessen, Germany.
    Presenting Author: Carmen Escuriola-Ettingshausen, MD – Haemophilia Centre Rhine-Main, Mörfelden-Walldorf, Germany
    Hemophilia and Rare Bleeding Disorders
  • Monday, Jun 26th
    18:30 – 19:30 ET
    PB0644 - Evaluation of the burden of bone fractures in people living with hemophilia: a registry-based case-control study.
    Room: Exhibition
    Presenting Author: Federico Germini, MD, MSc, PhD – Department of Medicine, McMaster University, Hamilton, ON
    Co-Author: Chatree Chai-Adisaksopha, MD – Department of Internal Medicine, Chiang Mai University, Chiang Mai, Thailand
    Co-Author: Quazi Ibrahim – Department of Health Research Methods, Evidence, and Impact, McMaster University, Hamilton, ON
    Co-Author: Emma Iserman – Department of Health Research Methods, Evidence, and Impact, McMaster University, Hamilton, ON
    Co-Author: Melissa Rattle – Niagara Health, Niagara, ON
    Co-Author: Arun Keepanasseril – Department of Health Research Methods, Evidence, and Impact (HEI), McMaster University, Hamilton, Canada
    Co-Author: Alfonso Iorio – Department of Health Research Methods, Evidence, and Impact, McMaster University, Hamilton, ON
    Co-Author: Davide Matino, MD (he/him/his) – Department of Medicine, Division of Hematology, McMaster University, Hamilton, ON
    Hemophilia and Rare Bleeding Disorders
  • Monday, Jun 26th
    18:30 – 19:30 ET
    PB0645 - Evaluation of the Effect of Factor VIII on the Measurement of Emicizumab Levels in Plasma
    Room: Exhibition
    Presenting Author: Paula E. Grennan, BSc and MSc – St. James's Hospital, Dublin
    Co-Author: Mary Byrne – National Coagulation Centre, St James's Hospital, Dublin
    Co-Author: Mairead Doyle, MSc – National Coagulation Centre, St James's Hospital, Dublin
    Co-Author: Michelle Lavin, MB, PhD (she/her/hers) – National Coagulation Centre, St. James Hospital and Irish Centre for Vascular Biology, School of Pharmacy and Biomolecular Sciences, Royal College of Physicians and Surgeons in Ireland (RCSI)
    Co-Author: James S. O'Donnell, MB, PhD – Irish Centre for Vascular Biology, Royal College of Surgeons in Ireland,Dublin, Ireland
    Co-Author: Niamh O'Connell, MD – National Coagulation Centre, St James's Hospital, Dublin
    Co-Author: Kevin Ryan – National Coagulation Centre, St James's Hospital, Dublin
    Hemophilia and Rare Bleeding Disorders
  • Monday, Jun 26th
    18:30 – 19:30 ET
    PB0646 - Feasibility of self-ultrasound scanning of the knee joint in untrained individuals: Can artificial intelligence help?
    Room: Exhibition
    Presenting Author: Pascal N. Tyrrell, PhD (he/him/his) – University of Toronto
    Co-Author: Victor S. Blanchette – Hospital for Sick Children
    Co-Author: Fatma Eltawil – Mohawk College, Institute for Applied Health Sciences, McMaster University
    Co-Author: Susan Kras – Mohawk College, Institute for Applied Health Sciences, McMaster University
    Co-Author: Christian Brink Scholz – Novo Nordisk A/S
    Co-Author: Marek Zak – Novo Nordisk A/S
    Co-Author: Johannes Roth – University of Ottawa, Children’s Hospital of Eastern Ontario
    Hemophilia and Rare Bleeding Disorders
  • Monday, Jun 26th
    18:30 – 19:30 ET
    PB0647 - Life expectancy and mortality of patients with haemophilia A and haemophilia B in Australia
    Room: Exhibition
    Co-Author: Sumit PARIKH, PhD – Australian Haemophilia Centre Directors’ Organisation, Melbourne, VIC, Australia
    Co-Author: Chee Wee TAN – SA Pathology, Adelaide, SA, Australia
    Co-Author: Simon BROWN – Queensland Children Hospital, Brisbane, QLD, Australia
    Co-Author: Chris BARNES – Royal Children Hospital, Melbourne, VIC, Australia
    Co-Author: Stephanie P’NG – Fiona Stanley Hospital, Perth, WA, Australia
    Co-Author: Tina CARTER – Perth Children Hospital, Perth, WA, Australia
    Presenting Author: Huyen Tran – Australian Centre for Blood Diseases, Monash University
    Hemophilia and Rare Bleeding Disorders
  • Monday, Jun 26th
    18:30 – 19:30 ET
    PB0648 - Mitigating the risk of bleeds and the risk for inhibitor formation when treating previously untreated patients (PUPs) with severe haemophilia A – a single-centre approach
    Room: Exhibition
    Presenting Author: Susan Halimeh – Gerinnungszentrum Rhein-Ruhr
    Co-Author: Hannelore Rott – Gerinnungszentrum Rhein-Ruhr
    Hemophilia and Rare Bleeding Disorders
  • Monday, Jun 26th
    18:30 – 19:30 ET
    PB0649 - Results From the RESIST Study for Tolerance Induction in Patients With Poor Prognosis for ITI Success
    Room: Exhibition
    Presenting Author: Christoph Koenigs, Dr. Dr. – University Hospital Frankfurt, Department of Paediatrics and Adolescent Medicine, Frankfurt, Germany
    Co-Author: Anja Schmidt – Goethe University Frankfurt, University Hospital, Department of Paediatrics and Adolescent Medicine, Clinical and Molecular Haemostasis, Frankfurt am Main, Germany
    Co-Author: Emilia Salzmann-Manrique – Goethe University Frankfurt, University Hospital, Department of Pediatrics, Frankfurt am Main, Germany
    Co-Author: Aleksander Orlowski – Goethe University Frankfurt, University Hospital, Department of Paediatrics and Adolescent Medicine, Clinical and Molecular Haemostasis, Frankfurt am Main, Germany
    Co-Author: Diana Stichel – Goethe University Frankfurt, University Hospital, Department of Paediatrics and Adolescent Medicine, Clinical and Molecular Haemostasis, Frankfurt am Main, Germany
    Co-Author: Manuel Carcao, MD, FRCPC – Division of Haematology/Oncology, Department of Paediatrics, Hospital for Sick Children, University of Toronto, Toronto, Canada
    Co-Author: Anthony KC. Chan, MBBS – McMaster University, McMaster Children’s Hospital, Hamilton, Canada
    Co-Author: Michael Guerrera – Department of Pediatrics, Children’s National Hospital, Washington, USA
    Co-Author: Michael R Jeng – Department of Pediatrics, Stanford University School of Medicine, USA
    Co-Author: Robert J. Klaassen, MD, FRCP(C) – Children’s Hospital of Eastern Ontario
    Co-Author: Roshni Kulkarni – Department of Pediatrics and Human Development, Michigan State University, East Lansing, Michigan, USA
    Co-Author: Madhvi Rajpurkar, MD – Department of Pediatrics, Central Michigan University, Mount Pleasant, Michigan, USA
    Co-Author: Ulrike Reiss – Hemophilia Treatment Center, Department of Hematology, St. Jude Children’s Research Hospital, Memphis, Tennessee, USA
    Co-Author: Joann Sanders – Cook Children's Hematology and Oncology, Fort Worth, Texas, USA
    Co-Author: Elena Santagostino – Bianchi Bonomi Hemophilia and Thrombosis Center, Maggiore Hospital Policlinico, Milan, Italy
    Co-Author: Leonard A. Valentino – Rush Hemophilia and Thrombophilia Center, Rush University Medical Center, Chicago, Illinois, USA
    Co-Author: Nadia Ewing – Department of Pediatrics, City of Hope National Medical Center, Duarte, California, USA
    Hemophilia and Rare Bleeding Disorders
  • Monday, Jun 26th
    18:30 – 19:30 ET
    PB0650 - Safety and Efficacy of Recombinant Fusion Protein Linking Coagulation Factor IX with Albumin (rIX-FP) in Pediatric Patients with Hemophilia B: A review of results from Phase 3 trial studies
    Room: Exhibition
    Co-Author: Hervé Chambost – AP-HM, Department of Pediatric Hematology Oncology, Children Hospital La Timone & Aix Marseille University, INSERM, INRA, C2VN, Marseille, France
    Presenting Author: Douglass Drelich, MD – CSL Behring, King of Prussia, Pennsylvania, USA
    Co-Author: Wilfried Seifert – CSL Behring, Marburg, Germany
    Co-Author: Giancarlo Castaman, MD – Center for Bleeding Disorders and Coagulation, Careggi University Hospital, Florence, Italy
    Hemophilia and Rare Bleeding Disorders
  • Monday, Jun 26th
    18:30 – 19:30 ET
    PB0651 - The axis NETosis-activated protein C may modulate the hemostatic status of patients with hemophilia A
    Room: Exhibition
    Co-Author: Julia Oto – Hemostasis, Thrombosis, Arteriosclerosis and Vascular Biology Research Group, Medical Research Institute Hospital La Fe, Valencia, Spain
    Presenting Author: Raquel Herranz, MSc (she/her/hers) – Hemostasis, Thrombosis, Arteriosclerosis and Vascular Biology Research Group, Medical Research Institute Hospital La Fe, Valencia, Spain
    Co-Author: Maria Castaño – Hemostasis, Thrombosis, Arteriosclerosis and Vascular Biology Research Group, Medical Research Institute Hospital La Fe, Valencia, Spain
    Co-Author: Fernando Cana – Hemostasis, Thrombosis, Arteriosclerosis and Vascular Biology Research Group, Medical Research Institute Hospital La Fe, Valencia, Spain
    Co-Author: Isabel Aleman-Cabrera – Haemostasis, Thrombosis, Arteriosclerosis and Vascular Biology Research Group, Medical Research Institute Hospital La Fe, Valencia, Spain
    Co-Author: Emma Plana – Haemostasis, Thrombosis, Arteriosclerosis and Vascular Biology Research Group, Medical Research Institute Hospital La Fe, Valencia, Spain; Angiology and Vascular Surgery Service, La Fe University and Polytechnic Hospital, Valencia, Spain
    Co-Author: Antonio Moscardo – Haemostasis, Thrombosis, Arteriosclerosis and Vascular Biology Research Group, Medical Research Institute Hospital La Fe, Valencia, Spain; Thrombosis and Haemostasis Unit, Haematology Service, La Fe University and Polytechnic Hospital, Valencia, Spain.
    Co-Author: Ana Cid – Haemostasis, Thrombosis, Arteriosclerosis and Vascular Biology Research Group, Medical Research Institute Hospital La Fe, Valencia, Spain; Thrombosis and Haemostasis Unit, Haematology Service, La Fe University and Polytechnic Hospital, Valencia, Spain
    Co-Author: Saturnino Haya – Haemostasis, Thrombosis, Arteriosclerosis and Vascular Biology Research Group, Medical Research Institute Hospital La Fe, Valencia, Spain; Thrombosis and Haemostasis Unit, Haematology Service, La Fe University and Polytechnic Hospital, Valencia, Spain
    Co-Author: Santiago Bonanad – Haemostasis, Thrombosis, Arteriosclerosis and Vascular Biology Research Group, Medical Research Institute Hospital La Fe, Valencia, Spain; Thrombosis and Haemostasis Unit, Haematology Service, La Fe University and Polytechnic Hospital, Valencia, Spain
    Co-Author: Pilar Medina – Hemostasis, Thrombosis, Arteriosclerosis and Vascular Biology Research Group, Medical Research Institute Hospital La Fe, Valencia, Spain
    Hemophilia and Rare Bleeding Disorders
  • Monday, Jun 26th
    18:30 – 19:30 ET
    PB0653 - Can thrombin generation assays be used to guide the use of anticoagulants in people with haemophilia? – an exploratory study
    Room: Exhibition
    Presenting Author: Caroline Dix, MBBS MSc FRACP FRCPA – Department of Clinical Haematology, The Alfred Hospital, Melbourne, VIC, Australia
    Co-Author: James D. McFadyen – Department of Haematology, Alfred Health, Melbourne, VIC, Australia
    Co-Author: Huyen Tran – Australian Centre for Blood Diseases, Monash University
    Hemophilia and Rare Bleeding Disorders
  • Monday, Jun 26th
    18:30 – 19:30 ET
    PB0654 - Combined Point of Care Tools Improve Treatment Adherence and Health-Related Quality of Life in Patients with Hemophilia under regular prophylaxis: an Observational Mulicenter Prospective Study
    Room: Exhibition
    Presenting Author: Mariasanta Napolitano, 310885 – Department of Health Promotion, Mother and Child Care, Internal Medicine and Medical Specialties (ProMISE), University of Palermo, Palermo, Italy
    Co-Author: Matteo Nicola Dario Di Minno – Department of Clinical Medicine and Surgery, Federico II University
    Co-Author: Ilenia Lorenza Calcaterra – Department of Clinical Medicine and Surgery, Federico II University
    Co-Author: renato marino – University Hospital of Bari
    Co-Author: giuseppe malcangi – university hospital of Bari
    Co-Author: Marta Mattana – University of Palermo
    Co-Author: Simona Raso, MD,PhD (she/her/hers) – Department of Hematology and Rare Diseases, Azienda Ospedaliera Ospedali Riuniti Villa Sofia-Cervello, Palermo, Italy.
    Co-Author: Gaetano Giffrida – university hospital of Catania
    Co-Author: maria Francesca Mansueto – University Hospital "P. Giaccone", Palermo
    Co-Author: Dalila Scaturro – Department of Surgical, Oncological and Stomatologica Science,University of Palermo
    Co-Author: Giulia Letizia Mauro – Department of Surgical, Oncological and Stomatologica Science, University of Palermo
    Co-Author: Sergio Siragusa – Haematology Unit, Thrombosis and Haemostasis Reference Regional Center, University of Palermo, Palermo, Italy
    Hemophilia and Rare Bleeding Disorders
  • Monday, Jun 26th
    18:30 – 19:30 ET
    PB0656 - Impact of moderate to vigorous-intensity physical activities on pharmacokinetic-guided extended half-life FVIII concentrates prophylaxis severe hemophilia A patients
    Room: Exhibition
    Co-Author: Chonlatis Srichumpuang, MD – King Chulalongkorn Memorial Hospital
    Presenting Author: Darintr Sosothikul, MD (she/her/hers) – Department of Pediatrics, Faculty of Medicine, Chulalongkorn University, Bangkok, Thailand
    Hemophilia and Rare Bleeding Disorders
  • Monday, Jun 26th
    18:30 – 19:30 ET
    PB0657 - Is implementation of pharmacokinetic-guided dosing of factor replacement therapy in bleeding disorders on TARGET? A scoping review to map barriers and facilitators
    Room: Exhibition
    Co-Author: Tine Goedhart, MD – Erasmus MC Sophia Children's Hospital, University Medical Center Rotterdam
    Co-Author: Alexander Janssen – Amsterdam University Medical Centers, University of Amsterdam
    Presenting Author: Caroline Mussert, MD – Erasmus MC Sophia Children's Hospital, University Medical Center Rotterdam
    Co-Author: Ron A.A. Mathôt – Department of Hospital Pharmacy & Clinical Pharmacology, Amsterdam UMC – location AMC, The Netherlands.
    Co-Author: Marjon H. Cnossen – Department of Pediatric Hematology, Erasmus MC – Sophia Children’s Hospital, University Medical Center Rotterdam, Rotterdam, The Netherlands
    Hemophilia and Rare Bleeding Disorders
  • Monday, Jun 26th
    18:30 – 19:30 ET
    PB0658 - Low-dose immune tolerance induction in patients with hemophilia A and inhibitor receiving emicizumab prophylaxis: preliminary results of the Brazilian experience
    Room: Exhibition
    Presenting Author: Carolina Costa-Lima, Master's degree and PHD student (she/her/hers) – Hemocentro UNICAMP, University of Campinas, Campinas, SP, Brazil
    Co-Author: Vanessa B. Faiotto – Hemocentro UNICAMP, University of Campinas, Campinas, SP, Brazil
    Co-Author: Ana P. P. Francisco – Hemocentro UNICAMP, University of Campinas, Campinas, SP, Brazil
    Co-Author: Nivia M. Foschi – Hemocentro UNICAMP, University of Campinas, Campinas, SP, Brazil
    Co-Author: Andrea L. A. Sambo – Hemocentro UNICAMP, University of Campinas, Campinas, SP, Brazil
    Co-Author: Mariana M T M. T. Hosokawa – 1. Hemocentro UNICAMP, University of Campinas, Campinas, SP, Brazil
    Co-Author: Valdirene C. F. Stahl – Hemocentro UNICAMP, University of Campinas, Campinas, SP, Brazil
    Co-Author: Samuel S. Medina – Hemocentro UNICAMP, University of Campinas, Campinas, SP, Brazil
    Co-Author: Jessica O. Frade-Guanaes, MsC – Hemocentro UNICAMP, University of Campinas, Campinas, SP, Brazil
    Co-Author: Silmara L. Montalvao, PhD (she/her/hers) – Hemocentro UNICAMP, University of Campinas, Campinas, SP, Brazil
    Co-Author: Marina P. P. Colella – Hemocentro UNICAMP, University of Campinas, Campinas, SP, Brazil
    Co-Author: Gabriela G. Yamaguti-Hayakawa, MD, PhD (she/her/hers) – Hemocentro UNICAMP, University of Campinas, Campinas, SP, Brazil
    Co-Author: Margareth C. Ozelo, MD, PhD (she/her/hers) – Hemocentro UNICAMP, Department of Internal Medicine, School of Medical Sciences, University of Campinas, Campinas, São Paulo, Brazil
    Hemophilia and Rare Bleeding Disorders
  • Monday, Jun 26th
    18:30 – 19:30 ET
    PB0659 - Patients with hemophilia A have increased levels of circulating activated protein C: potential contribution to their hemostatic status
    Room: Exhibition
    Co-Author: Julia Oto – Hemostasis, Thrombosis, Arteriosclerosis and Vascular Biology Research Group, Medical Research Institute Hospital La Fe, Valencia, Spain
    Presenting Author: Raquel Herranz, MSc (she/her/hers) – Hemostasis, Thrombosis, Arteriosclerosis and Vascular Biology Research Group, Medical Research Institute Hospital La Fe, Valencia, Spain
    Co-Author: Fernando Cana – Hemostasis, Thrombosis, Arteriosclerosis and Vascular Biology Research Group, Medical Research Institute Hospital La Fe, Valencia, Spain
    Co-Author: Antonio Moscardo – Haemostasis, Thrombosis, Arteriosclerosis and Vascular Biology Research Group, Medical Research Institute Hospital La Fe, Valencia, Spain; Thrombosis and Haemostasis Unit, Haematology Service, La Fe University and Polytechnic Hospital, Valencia, Spain.
    Co-Author: Maria Castaño – Hemostasis, Thrombosis, Arteriosclerosis and Vascular Biology Research Group, Medical Research Institute Hospital La Fe, Valencia, Spain
    Co-Author: Isabel Aleman-Cabrera – Haemostasis, Thrombosis, Arteriosclerosis and Vascular Biology Research Group, Medical Research Institute Hospital La Fe, Valencia, Spain
    Co-Author: Emma Plana – Haemostasis, Thrombosis, Arteriosclerosis and Vascular Biology Research Group, Medical Research Institute Hospital La Fe, Valencia, Spain; Angiology and Vascular Surgery Service, La Fe University and Polytechnic Hospital, Valencia, Spain
    Co-Author: Luis Gomez-Cambronero – Haemostasis, Thrombosis, Arteriosclerosis and Vascular Biology Research Group, Medical Research Institute Hospital La Fe, Valencia, Spain; Thrombosis and Haemostasis Unit, Haematology Service, La Fe University and Polytechnic Hospital, Valencia, Spain.
    Co-Author: Ana Cid – Haemostasis, Thrombosis, Arteriosclerosis and Vascular Biology Research Group, Medical Research Institute Hospital La Fe, Valencia, Spain; Thrombosis and Haemostasis Unit, Haematology Service, La Fe University and Polytechnic Hospital, Valencia, Spain
    Co-Author: Saturnino Haya – Haemostasis, Thrombosis, Arteriosclerosis and Vascular Biology Research Group, Medical Research Institute Hospital La Fe, Valencia, Spain; Thrombosis and Haemostasis Unit, Haematology Service, La Fe University and Polytechnic Hospital, Valencia, Spain
    Co-Author: Santiago Bonanad – Haemostasis, Thrombosis, Arteriosclerosis and Vascular Biology Research Group, Medical Research Institute Hospital La Fe, Valencia, Spain; Thrombosis and Haemostasis Unit, Haematology Service, La Fe University and Polytechnic Hospital, Valencia, Spain
    Co-Author: Pilar Medina – Hemostasis, Thrombosis, Arteriosclerosis and Vascular Biology Research Group, Medical Research Institute Hospital La Fe, Valencia, Spain
    Hemophilia and Rare Bleeding Disorders
  • Monday, Jun 26th
    18:30 – 19:30 ET
    PB0661 - Real-world Effectiveness and Safety of Damoctocog Alfa Pegol in Canadian Patients with Hemophilia A: Interim Results from the HEM-POWR Study
    Room: Exhibition
    Presenting Author: Davide Matino, MD (he/him/his) – Department of Medicine, Division of Hematology, McMaster University, Hamilton, ON
    Co-Author: Alfonso Iorio – Department of Health Research Methods, Evidence, and Impact, McMaster University, Hamilton, ON
    Co-Author: Anthony KC. Chan, MBBS – McMaster University, McMaster Children’s Hospital, Hamilton, Canada
    Co-Author: Nasrin Samji – McMaster Children’s Hospital, Hamilton, Canada
    Hemophilia and Rare Bleeding Disorders
  • Monday, Jun 26th
    18:30 – 19:30 ET
    PB0663 - Risk Factors for Atherosclerosis in Patients with Hemophilia
    Room: Exhibition
    Presenting Author: Alessandro Ciavarella, MD (he/him/his) – Fondazione IRCCS Ca' Granda - Ospedale Maggiore Policlinico, Centro Emofilia e Trombosi Angelo Bianchi Bonomi
    Co-Author: Francesco Tafuri – Fondazione IRCCS Ca' Granda - Ospedale Maggiore Policlinico, Centro Emofilia e Trombosi Angelo Bianchi Bonomi
    Co-Author: Federico Boggio – Università degli Studi di Milano
    Co-Author: Maria Abbattista, PhD – Fondazione IRCCS Ca' Granda - Ospedale Maggiore Policlinico, Centro Emofilia e Trombosi Angelo Bianchi Bonomi
    Co-Author: Sara Arcudi, MD – Fondazione IRCCS Ca' Granda - Ospedale Maggiore Policlinico, Centro Emofilia e Trombosi Angelo Bianchi Bonomi
    Co-Author: Roberta Gualtierotti, MD, PhD – Fondazione IRCCS Ca' Granda - Ospedale Maggiore Policlinico, Centro Emofilia e Trombosi Angelo Bianchi Bonomi
    Co-Author: Claudia Mistretta – Fondazione IRCCS Ca' Granda - Ospedale Maggiore Policlinico, Centro Emofilia e Trombosi Angelo Bianchi Bonomi
    Co-Author: Gabriella Nicolò – Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico di Milano, Department of Healthcare Professions, Milan, Italy
    Co-Author: Simona Siboni – Fondazione IRCCS Ca' Granda - Ospedale Maggiore Policlinico, Centro Emofilia e Trombosi Angelo Bianchi Bonomi
    Co-Author: Flora Peyvandi, MD, PhD (she/her/hers) – IRCCS Ca' Granda Maggiore Hospital Foundation, Angelo Bianchi Bonomi Hemophilia and Thrombosis Center, Milano, Italy; Università degli Studi di Milano, Department of Pathophysiology and Transplantation, Milano, Italy
    Hemophilia and Rare Bleeding Disorders
  • Monday, Jun 26th
    18:30 – 19:30 ET
    PB0664 - Treatment adherence in young people with hemophilia: perceptions of UK healthcare professionals
    Room: Exhibition
    Presenting Author: Julie Jordan, RGN BSN (she/her/hers) – CSL Behring, UK
    Hemophilia and Rare Bleeding Disorders
  • Monday, Jun 26th
    18:30 – 19:30 ET
    PB0665 - 5 Years of Prophylaxis with emicizumab in children and adults with hemophilia A with and without inhibitors in a Portuguese Hemophilia Center – outcomes in bleeding and surgery
    Room: Exhibition
    Presenting Author: Cristina Catarino, Dr (she/her/hers) – Centro Hospitalar Universitário Lisboa Norte
    Co-Author: Filipa Pires – Centro Hospitalar Universitário Lisboa Norte
    Co-Author: Carolina Peixoto, MD – Centro Hospitalar Universitário Lisboa Norte
    Co-Author: Catarina Câmara, MD (she/her/hers) – Centro Hospitalar Universitário Lisboa Norte
    Co-Author: Catarina J. Jacinto – Centro Hospitalar Universitário Lisboa Norte
    Co-Author: Joana S G Pestana, MD (she/her/hers) – Hospital do Espírito Santo - Évora
    Co-Author: Jorge Félix, MD – Centro Hospitalar Universitário Lisboa Norte
    Co-Author: Patrícia Afonso – Centro Hospitalar Universitário Lisboa Norte
    Co-Author: Elsa Rocha – Hospital Faro
    Co-Author: Artur Pereira – Centro Hospitalar Universitário Lisboa Norte
    Co-Author: Fátima Rodrigues – Centro Hospitalar Universitário Lisboa Norte
    Hemophilia and Rare Bleeding Disorders
  • Monday, Jun 26th
    18:30 – 19:30 ET
    PB0666 - Clinical outcomes following treatment with octocog alfa in patients with hemophilia A: 9-year interim read-out of the real-world AHEAD international study
    Room: Exhibition
    Presenting Author: Manuel Carcao, MD, FRCPC – Division of Haematology/Oncology, Department of Paediatrics, Hospital for Sick Children, University of Toronto, Toronto, Canada
    Co-Author: Margareth C. Ozelo, MD, PhD (she/her/hers) – Hemocentro UNICAMP, Department of Internal Medicine, School of Medical Sciences, University of Campinas, Campinas, São Paulo, Brazil
    Co-Author: Cedric Hermans, MD, PhD (he/him/his) – St-Luc University Hospital
    Co-Author: Kate Khair, RN, PhD – Haemnet, London, United Kingdom
    Co-Author: Randy Guerra, MD – Takeda Development Center Americas, Inc., Cambridge, MA, USA
    Co-Author: Joan Gu – Takeda Development Center Americas, Inc., Cambridge, MA, USA
    Co-Author: Pooja Oberai, MD MS (she/her/hers) – Takeda Development Center Americas, Inc., Cambridge, MA, USA
    Co-Author: Renchi Yang, MD (he/him/his) – Institute of Hematology and Blood Diseases Hospital, Chinese Academy of Medical Sciences and Peking Union Medical College, Tianjin, China
    Hemophilia and Rare Bleeding Disorders
  • Monday, Jun 26th
    18:30 – 19:30 ET
    PB0667 - Development and clinical utility of anti-emicizumab antibody detection assays
    Room: Exhibition
    Co-Author: Carla Valsecchi – Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico, Angelo Bianchi Bonomi Hemophilia and Thrombosis Center, Milan, Italy
    Co-Author: Lucia Schiavone – Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico, Angelo Bianchi Bonomi Hemophilia and Thrombosis Center, Milan, Italy
    Co-Author: Sara Arcudi, MD – Fondazione IRCCS Ca' Granda - Ospedale Maggiore Policlinico, Centro Emofilia e Trombosi Angelo Bianchi Bonomi
    Co-Author: Roberta Gualtierotti, MD, PhD – Fondazione IRCCS Ca' Granda - Ospedale Maggiore Policlinico, Centro Emofilia e Trombosi Angelo Bianchi Bonomi
    Co-Author: Cristina Novembrino, PhD – Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico, Angelo Bianchi Bonomi Hemophilia and Thrombosis Center, Milan, Italy
    Co-Author: Marten Beeg – Istituto di Ricerche Farmacologiche Mario Negri IRCCS, Department of Biochemistry and Molecular Pharmacology, Milan, Italy
    Co-Author: Marco Gobbi – Istituto di Ricerche Farmacologiche Mario Negri IRCCS, Department of Biochemistry and Molecular Pharmacology, Milan, Italy
    Presenting Author: Flora Peyvandi, MD, PhD (she/her/hers) – IRCCS Ca' Granda Maggiore Hospital Foundation, Angelo Bianchi Bonomi Hemophilia and Thrombosis Center, Milano, Italy; Università degli Studi di Milano, Department of Pathophysiology and Transplantation, Milano, Italy
    Hemophilia and Rare Bleeding Disorders
  • Monday, Jun 26th
    18:30 – 19:30 ET
    PB0668 - Emicizumab treatment regimen based on vial size along with quantification of emicizumab plasma concentration. Real-world experience from a single pediatric center in Argentina.
    Room: Exhibition
    Presenting Author: Gabriela B. Sciuccati, MD (she/her/hers) – Hospital de Pediatría "Prof. Dr. J.P.Garrahan"
    Co-Author: Rodolfo E. Sueldo, PhD – Laboratorio de Hematología y Hemostasia. Hospital César Milstein Laboratorio de Hemostasia. Servicio de Hematología y Oncología Hospital de Pediatría Prof. Dr. Juan P. Garrahan
    Co-Author: Carolina Cervio, MD (she/her/hers) – Hospital de Pediatría "Prof. Dr. Juan P. Garrahan"
    Co-Author: Maria B. Bianco – Hospital de Pediatria Porf Dr Juan P Garrahan
    Co-Author: Juan P. Frontroth, Biochemist (he/him/his) – Hospital de Pediatría "Prof. Dr. J.P.Garrahan"
    Co-Author: Silvina E. Annetta – Hospital de Pediatria Porf Dr Juan P Garrahan
    Co-Author: Mirta D. Hepner – Hospital de Pediatría "Prof. Dr. J.P.Garrahan"
    Hemophilia and Rare Bleeding Disorders
  • Monday, Jun 26th
    18:30 – 19:30 ET
    PB0669 - Final Analysis of Long-term Clinical Outcomes of Recombinant Factor IX Fc Fusion Protein Prophylaxis in Adults ≥50 Years With Severe Hemophilia B
    Room: Exhibition
    Presenting Author: Margaret V. Ragni, MD, MPH (she/her/hers) – Department of Medicine, University of Pittsburgh, Pittsburgh, PA, USA
    Co-Author: Savita Rangarajan, MD, FRCP, FRCPath – Faculty of Medicine, University of Southampton, Southampton, UK
    Co-Author: Sandra Casiano – Sanofi, Cambridge, MA, USA
    Co-Author: Umer Khan – Sanofi, San Diego, CA, USA
    Hemophilia and Rare Bleeding Disorders
  • Monday, Jun 26th
    18:30 – 19:30 ET
    PB0670 - Nationwide survey on the care reality of people with mild hemophilia A and B in Germany - The Burden of mild Hemophilia
    Room: Exhibition
    Presenting Author: Sonja Rosa Alesci, MD, PhD (she/her/hers) – IMD blood coagulation Hochtaunus
    Co-Author: Susan Halimeh – Gerinnungszentrum Rhein-Ruhr
    Co-Author: Martin Olivieri (he/him/his) – Paediatric Thrombosis and Haemostasis Unit, Paediatric Haemophilia Center, Dr. von Hauner Children's Hospital, LMU Clinic, Munich, Germany
    Co-Author: Wolfgang Miesbach, MD – University Hospital Frankfurt, Frankfurt, Germany
    Co-Author: Katharina Holstein, MD (she/her/hers) – University Hospital Hamburg Eppendorf
    Co-Author: Christoph Koenigs, Dr. Dr. – University Hospital Frankfurt, Department of Paediatrics and Adolescent Medicine, Frankfurt, Germany
    Hemophilia and Rare Bleeding Disorders
  • Monday, Jun 26th
    18:30 – 19:30 ET
    PB0671 - Poor correlation between biomarkers and MRI-detected joint damage in a cross-sectional study of persons with non-severe hemophilia A
    Room: Exhibition
    Co-Author: Fabienne R. Kloosterman, MD – Amsterdam UMC, University of Amsterdam, Emma Children’s Hospital, Pediatric Hematology, Meibergdreef 9, Amsterdam, Netherlands
    Co-Author: Anne-Fleur Zwagemaker – Amsterdam UMC, University of Amsterdam, Emma Children’s Hospital, Pediatric Hematology, Meibergdreef 9, Amsterdam, Netherlands
    Co-Author: Anne C. Bay-Jensen – Immunoscience, Nordic Bioscience , Biomarkers and Research, Herlev, Denmark
    Co-Author: Marjon H. Cnossen – Department of Pediatric Hematology, Erasmus MC – Sophia Children’s Hospital, University Medical Center Rotterdam, Rotterdam, The Netherlands
    Co-Author: Marieke J.H.A. Kruip – Department of Hematology, Erasmus MC, Erasmus University Medical Center Rotterdam, Rotterdam, The Netherlands
    Co-Author: Frank W.G. Leebeek, MD, PhD – Erasmus MC, University Medical Center Rotterdam, The Netherlands
    Co-Author: Robert Hemke – Department of Radiology and Nuclear Medicine, Amsterdam University Medical Centers, University of Amsterdam, Amsterdam Movement Sciences, Amsterdam, the Netherlands
    Co-Author: Mario Maas – Department of Radiology and Nuclear Medicine, Amsterdam University Medical Centers, University of Amsterdam, Amsterdam Movement Sciences, Amsterdam, the Netherlands
    Co-Author: Karin Fijnvandraat – Amsterdam UMC, University of Amsterdam, Emma Children’s Hospital, Pediatric Hematology Amsterdam, Netherlands
    Co-Author: Samantha Gouw, MD, PhD (she/her/hers) – The University of Amsterdam
    Presenting Author: Michiel Coppens, MD, PhD (he/him/his) – Amsterdam University Medical Centers, Amsterdam, The Netherlands
    Hemophilia and Rare Bleeding Disorders
  • Monday, Jun 26th
    18:30 – 19:30 ET
    PB0672 - Real-World data on Hemophilia A patients switching to either BAY 94-9027 or BAY 81-8973 from Emicizumab using the ATHNdataset
    Room: Exhibition
    Presenting Author: Michael Recht, MD, PhD, MBA (he/him/his) – National Hemophilia Foundation
    Co-Author: Jessica Charlet, MSc, PhD (she/her/hers) – Bayer Pharmaceuticals
    Co-Author: Thomas Moulton, MD (he/him/his) – Bayer Pharmaceuticals
    Co-Author: Martin Chandler – American Thrombosis Hemostasis Network
    Hemophilia and Rare Bleeding Disorders
  • Monday, Jun 26th
    18:30 – 19:30 ET
    PB0674 - The Impact of Suboptimal Adherence to Factor Replacement Therapy on Time Spent Below Target Factor Trough Levels: Simulations Using Population Pharmacokinetic Modeling
    Room: Exhibition
    Co-Author: Jessica Wojciechowski – Pfizer Inc, Groton, CT, USA
    Co-Author: Satyaprakash Nayak – Pfizer Inc, Cambridge, MA, USA
    Co-Author: Ginger Anderson – Pfizer Inc, Groton, CT, USA
    Co-Author: Patrick F. Fogarty, MD – Pfizer Inc, New York, NY, USA
    Presenting Author: Lisa Wilcox, PhD (she/her/hers) – Pfizer Inc
    Hemophilia and Rare Bleeding Disorders
  • Monday, Jun 26th
    18:30 – 19:30 ET
    PB0675 - The reverse two-sample in one-clinic visit factor VIII pharmacokinetic protocol using myPKFiT: the Brazilian experience
    Room: Exhibition
    Presenting Author: Mariella C. Della-Piazza, MD, MSc (she/her/hers) – Hemocentro UNICAMP, University of Campinas
    Co-Author: Vanessa B. Faiotto – Hemocentro UNICAMP, University of Campinas, Campinas, SP, Brazil
    Co-Author: Alessandra N. L Prezotti, MD, MsC, pHD (she/her/hers) – Centro de Hematologia e Hemoterapia do Espirito Santo (HEMOES)
    Co-Author: Debora Rocha – Centro de Hematologia e Hemoterapia do Espirito Santo (HEMOES)
    Co-Author: Ana P. P. Francisco – Hemocentro UNICAMP, University of Campinas, Campinas, SP, Brazil
    Co-Author: Andrea L. A. Sambo – Hemocentro UNICAMP, University of Campinas, Campinas, SP, Brazil
    Co-Author: Mariana M. T. Hosokawa – Hemocentro UNICAMP, University of Campinas, Campinas, SP, Brazil
    Co-Author: Valdirene C. F. Stahl – Hemocentro UNICAMP, University of Campinas, Campinas, SP, Brazil
    Co-Author: Samuel S. Medina – Hemocentro UNICAMP, University of Campinas, Campinas, SP, Brazil
    Co-Author: Nivia M. Foschi – Hemocentro UNICAMP, University of Campinas, Campinas, SP, Brazil
    Co-Author: Marina P. Colella – Hemocentro UNICAMP, University of Campinas, Campinas, SP, Brazil
    Co-Author: Carolina Costa-Lima, Master's degree and PHD student (she/her/hers) – Hemocentro UNICAMP, University of Campinas, Campinas, SP, Brazil
    Co-Author: Silmara L. Montalvao, PhD (she/her/hers) – Hemocentro UNICAMP, University of Campinas, Campinas, SP, Brazil
    Co-Author: Gabriela G. Yamaguti-Hayakawa, MD, PhD (she/her/hers) – Hemocentro UNICAMP, University of Campinas, Campinas, SP, Brazil
    Co-Author: Margareth C. Ozelo, MD, PhD (she/her/hers) – Hemocentro UNICAMP, Department of Internal Medicine, School of Medical Sciences, University of Campinas, Campinas, São Paulo, Brazil
    Hemophilia and Rare Bleeding Disorders
  • Monday, Jun 26th
    18:30 – 19:30 ET
    PB0679 - Clinical Characteristics and Disease Outcomes in Previously Treated Patients with Haemophilia: Results from a Real-World Study in Europe and United States
    Room: Exhibition
    Presenting Author: Jennifer Mellor, MSc (she/her/hers) – Adelphi Real World
    Co-Author: Keisha Golden – Adelphi Real World
    Co-Author: Stevie Olsen – Adelphi Real World
    Co-Author: Nathan M. Ball, N/A – Adelphi Real World
    Co-Author: Jade Garratt-Wheeldon – Adelphi Real World
    Hemophilia and Rare Bleeding Disorders
  • Monday, Jun 26th
    18:30 – 19:30 ET
    PB0680 - Clinical characteristics, therapy and outcome of children with Hemophilia B and inhibitors: a PedNet study
    Room: Exhibition
    Presenting Author: Assaf Barg, MD – The National Hemophilia Center, and Amalia Biron Research Institute of Thrombosis and Hemostasis, Sheba Medical Center, Ramat Gan, Israel
    Co-Author: Marloes De Kovel, MSc – PedNet Haemophilia Research Foundation, Baarn, the Netherlands.
    Co-Author: Helen Pergantou – Haemophilia Centre/Haemostasis and Thrombosis Unit, “Aghia Sophia” Children’s Hospital, Athens, Greece
    Co-Author: Roseline d'Oiron, MD – Centre for Haemophilia and Rare Congenital Bleeding Disorders, Bicêtre Hospital AP-HP, University of Paris-Saclay and UMR_S1176 INSERM, Le Kremlin-Bicêtre, France
    Co-Author: Beatrice Nolan – Department of Haematology, Children's Health Ireland at Crumlin, Dublin, Ireland.
    Co-Author: Carmen Escuriola-Ettingshausen, MD – Haemophilia Centre Rhine-Main, Mörfelden-Walldorf, Germany
    Co-Author: Kathelijn Fischer, MD, PhD (she/her/hers) – Center for Benign Haematology, Thrombosis and Haemostasis, Van Creveldkliniek, University Medical Center Utrecht, Utrecht University, The Netherlands
    Co-Author: Nadine Gretenkort Andersson – Department of Paediatrics and Malmö Centre for Thrombosis and Haemostasis, Skåne University Hospital, Malmö, Sweden.
    Co-Author: Heidi Glosli – Division of Paediatric and Adolescent Medicine Centre for Rare Disorders Oslo University Hospital Oslo Norway.
    Co-Author: Maria Teresa Alvarez-Román, MD, PhD – Department of Hematology, University Hospital La Paz, Autonoma University of Madrid, Madrid, Spain
    Co-Author: Jayashree Motwani – Department of Paediatric Haematology, Birmingham Children's Hospital, United Kingdom
    Co-Author: Gili Kenet, MD – The National Hemophilia Center, and Amalia Biron Research Institute of Thrombosis and Hemostasis, Sheba Medical Center, Tel Hashomer, Tel Aviv University, Tel Aviv, Israel
    Co-Author: Christoph Male, MD, MSc – Department of Paediatrics, Medical University of Vienna, Vienna, Austria.
    Hemophilia and Rare Bleeding Disorders
  • Monday, Jun 26th
    18:30 – 19:30 ET
    PB0681 - German experience with simoctocog alfa during surgery in female haemophilia A carriers
    Room: Exhibition
    Presenting Author: Natascha Marquardt, MD – Institute for Experimental Hematology and Transfusion Medicine, University Clinic Bonn
    Co-Author: Johannes Oldenburg, MD (he/him/his) – University Clinic Bonn AöR, Institute of Experimental Haematology and Transfusion Medicine, Bonn, Germany
    Hemophilia and Rare Bleeding Disorders
  • Monday, Jun 26th
    18:30 – 19:30 ET
    PB0682 - In vitro Response to Bypassing Agents and Long Term Follow-up of Patients with Severe Hemophilia A on Prophylaxis with Emicizumab.
    Room: Exhibition
    Co-Author: Abel Dos Santos Ortas – La Paz University Hospital
    Co-Author: Elena García Arias-Salgado, PhD – La Paz University Hospital
    Co-Author: Elena Monzón Manzano (she/her/hers) – La Paz University Hospital
    Co-Author: Paula Acuña Butta – La Paz University Hospital
    Co-Author: Sara García Barcenilla – La Paz University Hospital
    Co-Author: Maria Teresa Alvarez-Román, MD, PhD – Department of Hematology, University Hospital La Paz, Autonoma University of Madrid, Madrid, Spain
    Co-Author: Maria Isabel Rivas Pollmar – La Paz University Hospital
    Co-Author: Mónica Martín Salces – La Paz University Hospital
    Co-Author: Laura González Rodríguez – La Paz University Hospital
    Presenting Author: Nora V V. Butta Coll, PhD – La Paz University Hospital-IdiPAZ
    Co-Author: Víctor Jiménez Yuste, MD PhD – La Paz University Hospital
    Hemophilia and Rare Bleeding Disorders
  • Monday, Jun 26th
    18:30 – 19:30 ET
    PB0683 - Patients at higher risk of spontaneous joint bleeding during emicizumab prophylaxis: a study on global coagulation assays and arthropathy scores
    Room: Exhibition
    Presenting Author: Sara Arcudi, MD – Fondazione IRCCS Ca' Granda - Ospedale Maggiore Policlinico, Centro Emofilia e Trombosi Angelo Bianchi Bonomi
    Co-Author: Roberta Gualtierotti, MD, PhD – Fondazione IRCCS Ca' Granda - Ospedale Maggiore Policlinico, Centro Emofilia e Trombosi Angelo Bianchi Bonomi
    Co-Author: Erica Scalambrino, MA – Fondazione IRCCS Cà Grand Ospedale Maggiore Policlinico, Angelo Bianchi Bonomi Hemophilia and Thrombosis Center
    Co-Author: Marigrazia Clerici – Fondazione IRCCS Ca' Granda, Ospedale Maggiore Policlinico, Angelo Bianchi Bonomi Hemophilia and Thrombosis Center, Milan, Italy
    Co-Author: Shermarke Hassan – Department of Clinical Epidemiology, Leiden University Medical Center, Leiden, the Netherlands
    Co-Author: Gabriella Nicolò – Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico di Milano, Department of Healthcare Professions, Milan, Italy
    Co-Author: Alessandro Ciavarella, MD (he/him/his) – Fondazione IRCCS Ca' Granda - Ospedale Maggiore Policlinico, Centro Emofilia e Trombosi Angelo Bianchi Bonomi
    Co-Author: Valentina Begnozzi – Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico, Angelo Bianchi Bonomi Hemophilia and Thrombosis Center, Milan, Italy
    Co-Author: Elena Boccalandro – Fondazione IRCCS Ca' Granda, Ospedale Maggiore Policlinico, Angelo Bianchi Bonomi Hemophilia and Thrombosis Center, Milan, Italy
    Co-Author: Simona Maria Siboni – Fondazione IRCCS Ca' Granda, Ospedale Maggiore Policlinico, Angelo Bianchi Bonomi Hemophilia and Thrombosis Center
    Co-Author: Cristina Novembrino, PhD – Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico, Angelo Bianchi Bonomi Hemophilia and Thrombosis Center, Milan, Italy
    Co-Author: Carla Valsecchi – Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico, Angelo Bianchi Bonomi Hemophilia and Thrombosis Center, Milan, Italy
    Co-Author: Flora Peyvandi, MD, PhD (she/her/hers) – IRCCS Ca' Granda Maggiore Hospital Foundation, Angelo Bianchi Bonomi Hemophilia and Thrombosis Center, Milano, Italy; Università degli Studi di Milano, Department of Pathophysiology and Transplantation, Milano, Italy
    Hemophilia and Rare Bleeding Disorders
  • Monday, Jun 26th
    18:30 – 19:30 ET
    PB0684 - Quality of life in patients & caregivers living with hemophilia A without inhibitors in spain, interim analysis of the HEMOLIFE study
    Room: Exhibition
    Presenting Author: Maria Teresa Alvarez-Román, MD, PhD – Department of Hematology, University Hospital La Paz, Autonoma University of Madrid, Madrid, Spain
    Co-Author: Inmaculada Soto – Hospital Universitario Central de Asturias
    Co-Author: María Garcia – General Health Psychologist
    Co-Author: Ramiro José Núñez Vázquez – Hospital Universitario Virgen del Rocío. Instituto de Biomedicina de Sevilla (IBIS), Sevilla, Spain.
    Co-Author: Laura Quintana – Hospital Universitario Doctor Negrín
    Co-Author: Olga Benítez, MD – Vall d'Hebrón Barcelona Hospital Campus
    Co-Author: Francisco José López Jaime, MD – Hemostasis and Thrombosis Unit, Regional University Hospital of Málaga, IBIMA, Málaga, Spain.
    Co-Author: Laura Entrena – Hospital Universitario Virgen de las Nieves
    Co-Author: Itziar Guerra – Roche Farma
    Co-Author: Hortensia De la Corte-Rodríguez – La Paz University Hospital
    Hemophilia and Rare Bleeding Disorders
  • Monday, Jun 26th
    18:30 – 19:30 ET
    PB0685 - A retrospective review of Heavy Menstrual Bleeding in women with inherent bleeding disorders – a need for Joint Gynaecology-Haematology clinic
    Room: Exhibition
    Co-Author: Sandhya Munireddy – Department of Haematology, University Hospitals of Leicestershire NHS Trust
    Co-Author: Styliani Salta – Leicester Royal Infirmary
    Presenting Author: Bethan Myers, MA (Cantab) MB BCh FRCP FRCPath – Leicester Royal Infirmary
    Hemophilia and Rare Bleeding Disorders
  • Monday, Jun 26th
    18:30 – 19:30 ET
    PB0686 - Clinical decisions and factors influencing the management of persons with hemophilia requiring antithrombotic therapy: A qualitative study.
    Room: Exhibition
    Presenting Author: Kelsey Uminski, MD, FRCPC (she/her/hers) – Division of Hematology and Hematological Malignancies, Department of Medicine, University of Calgary, Calgary, AB, Canada
    Co-Author: Tzu-Fei Wang, MD, MPH (she/her/hers) – Department of Medicine, University of Ottawa at The Ottawa Hospital and Ottawa Hospital Research Institute, Ottawa, ON, Canada
    Co-Author: Alan Tinmouth – Division of Hematology, Department of Medicine, University of Ottawa at the Ottawa Hospital, Ottawa, ON, Canada
    Co-Author: Roy Khalife, MD, MHPE, FRCPC (he/him/his) – Department of Medicine (Hematology), University of Ottawa
    Hemophilia and Rare Bleeding Disorders
  • Monday, Jun 26th
    18:30 – 19:30 ET
    PB0687 - Comorbidities in an Aging Bleeding Disorder Population: A Retrospective Comparison Study.
    Room: Exhibition
    Co-Author: Richard M. Daly, N/A – University of Limerick.
    Co-Author: Mairead Goggin – Cork University Hospital
    Co-Author: Brid Booth-Fleming – Cork University Hospital
    Co-Author: Norma Collins – Cork University Hospital
    Co-Author: Brid Firtear – Cork University Hospital
    Co-Author: Annmarie Ryan-Hall – Cork University Hospital
    Co-Author: Cleona Duggan – Cork University Hospital
    Presenting Author: Maeve P. Crowley – Department of Haematology, Cork University Hospital, Wilton, T12 DC4A Cork, Ireland
    Hemophilia and Rare Bleeding Disorders
  • Monday, Jun 26th
    18:30 – 19:30 ET
    PB0689 - Efficacy/effectiveness of extended half-life factor VIII concentrates on the prophylaxis of people with hemophilia A: A systematic review and meta-analysis
    Room: Exhibition
    Co-Author: Maiara Silva Araújo – Faculty of Pharmacy, Universidade Federal de Minas Gerais
    Co-Author: Roberto Lúcio Muniz Júnior, Jr. – Faculty of Pharmacy, Universidade Federal de Minas Gerais
    Presenting Author: Mariana Michel Barbosa, PhD (she/her/hers) – Faculty of Pharmacy, Universidade Federal de Minas Gerais
    Co-Author: Ricardo M. Camelo, MD, MSc, MBA – Faculty of Pharmacy, Universidade Federal de Minas Gerais
    Co-Author: Juliana Alvares-Teodoro – Faculty of Pharmacy, Universidade Federal de Minas Gerais
    Hemophilia and Rare Bleeding Disorders
  • Monday, Jun 26th
    18:30 – 19:30 ET
    PB0690 - Factor X consumption could cause attenuation of emicizumab effect; A case report of severe hemophilia A with inhibitor treated by emicizumab and factor VIII-bypassing agents
    Room: Exhibition
    Presenting Author: Kuniyoshi Mizumachi, MD (he/him/his) – Department of Pediatrics
    Co-Author: Yuto Nakajima, MD PhD – Advanced Medical Science of Thrombosis and Hemostasis, Nara Medical University
    Co-Author: Naruto Shimonishi, PhD – The Course of Thrombosis and Hemostasis Molecular Pathology, Nara Medical University
    Co-Author: Shoko Furukawa – Department of Pediatrics, Nara Medical University
    Co-Author: Kenichi Ogiwara, MD, PhD (he/him/his) – Nara Medical University
    Co-Author: Masahiro Takeyama, MD, PhD – Department of Pediatrics, Nara Medical University
    Co-Author: Keiji Nogami – Nara Medical University, Nara, Japan
    Hemophilia and Rare Bleeding Disorders
  • Monday, Jun 26th
    18:30 – 19:30 ET
    PB0691 - Inhibitor Eradication Strategies in Patients with Non-Severe Hemophilia A
    Room: Exhibition
    Co-Author: Sanober Nusrat, MD (she/her/hers) – University of Oklahoma Health Sciences Center
    Presenting Author: Osman Khan, MD, MS – University of Oklahoma Health Sciences Center
    Hemophilia and Rare Bleeding Disorders
  • Monday, Jun 26th
    18:30 – 19:30 ET
    PB0692 - Matching-adjusted indirect comparison of rIX-FP versus rFIXFc for prophylactic treatment of hemophilia B
    Room: Exhibition
    Co-Author: Songkai Yan – CSL Behring, King of Prussia, PA, USA
    Co-Author: Becky Hooper – EVERSANA, Burlington, Canada
    Co-Author: Soraya Benchikh El Fegoun – CSL Behring, Bern, Switzerland
    Co-Author: Wilfried Seifert – CSL Behring, Marburg, Germany
    Co-Author: Jason Steenkamp – EVERSANA, Burlington, Canada
    Presenting Author: Maria Elisa Mancuso, MD, PhD – Center for Thrombosis and Hemorrhagic Diseases, IRCCS Humanitas Research Hospital, Rozzano, Milan, Italy
    Hemophilia and Rare Bleeding Disorders
  • Monday, Jun 26th
    18:30 – 19:30 ET
    PB0693 - Efficacy and Safety of Eptacog Beta (Recombinant Activated FVII) in Patients with Hemophilia A or B with Inhibitors According to Time to Initial Infusion: a Post-Hoc Analysis from PERSEPT-1
    Room: Exhibition
    Presenting Author: Cedric Hermans, MD, PhD (he/him/his) – St-Luc University Hospital
    Co-Author: Miguel Escobar, MD – University of Texas Health Science Center of Houston, McGovern Medical School, Gulf States Hemophilia and Thrombophilia Center, Houston, Texas
    Co-Author: Yasmina Abajas – University of North Carolina at Chapel Hill
    Co-Author: Suchitra Acharya, MD – Cohen Children’s Medical Center, Northwell Health
    Co-Author: Maria Teresa Alvarez-Román, MD, PhD – Department of Hematology, University Hospital La Paz, Autonoma University of Madrid, Madrid, Spain
    Co-Author: Glaivy Batsuli – Emory University, Department of Pediatrics
    Co-Author: Yesim Dargaud – Hôpital Cardiologique Louis Pradel, Université Lyon 1
    Co-Author: Maissaa Janbain – Louisiana Center for Bleeding and Clotting Disorders, Tulane University Medical Center, LA, USA
    Co-Author: Philip Kuriakose – Wayne State University Medical School, Henry Ford Health System
    Co-Author: Johnny Mahlangu, MD (he/him/his) – Haemophilia Comprehensive Care Centre, Charlotte Maxeke Johannesburg Academic Hospital, University of the Witwatersrand and National Health Laboratory Service, Johannesburg, South Africa
    Co-Author: Maria Elisa Mancuso, MD, PhD (she/her/hers) – IRCCS Humanitas Research Hospital
    Co-Author: Wolfgang Miesbach, MD – University Hospital Frankfurt, Frankfurt, Germany
    Co-Author: Shenghua Yuan – LFB-USA
    Co-Author: Ian Mitchell – HEMA Biologics
    Co-Author: Manuel Carcao, MD, FRCPC – Division of Haematology/Oncology, Department of Paediatrics, Hospital for Sick Children, University of Toronto, Toronto, Canada
    Hemophilia and Rare Bleeding Disorders
  • Monday, Jun 26th
    18:30 – 19:30 ET
    PB0694 - A chemiluminescent-based multiparameter platform for simultaneous measurement of factor VIII activity and thrombin generation
    Room: Exhibition
    Presenting Author: Lisa van Engelshoven, MSc. – Employee
    Co-Author: Danique Steeghs, MSc – Employee
    Co-Author: Nerissa M. M. Coolen – Employee
    Co-Author: Steven P. L. Kuijpers – Employee
    Co-Author: Mark van Geffen – Employee
    Co-Author: Rachel M. Vestering-Stenger – Employee
    Co-Author: Cornelis van 't veer – Employee
    Co-Author: Waander L. van Heerde – Enzyre BV
    Hemophilia and Rare Bleeding Disorders
  • Monday, Jun 26th
    18:30 – 19:30 ET
    PB0695 - Comparison of Platelet Quality and Hemostatic Function Across Apheresis Collection Platforms
    Room: Exhibition
    Presenting Author: Katelin C. Rahn – Trauma and Transfusion Medicine Research Center, Department of Surgery, University of Pittsburgh
    Co-Author: Amudan J. Srinivasan, MD – Trauma and Transfusion Medicine Research Center, Department of Surgery, University of Pittsburgh
    Co-Author: Colby McIntosh – United States Army Institute of Surgical Research
    Co-Author: James Bynum – Department of Surgery, University of Texas Health Science Center at San Antonio
    Co-Author: Andrew Cap – United States Army Institute of Surgical Research
    Co-Author: Kimberly A. Thomas – Vitalant Research Institute
    Co-Author: Philip C. Spinella, MD – University of Pittsburgh School of Medicine
    Co-Author: Kristin Cardenas – United States Army Institute of Surgical Research
    Co-Author: Susan M. Shea, MSME, PhD (she/her/hers) – Trauma and Transfusion Medicine Research Center, Department of Surgery and Department of Bioengineering, University of Pittsburgh
    Hemophilia and Rare Bleeding Disorders
  • Monday, Jun 26th
    18:30 – 19:30 ET
    PB0696 - Management of bleeding in people with hemophilia A on prophylaxis with emicizumab in emergency situations: Recommendations from a Spanish expert panel
    Room: Exhibition
    Presenting Author: Víctor Jiménez Yuste, MD PhD – La Paz University Hospital
    Co-Author: Maria Teresa Alvarez-Román, MD, PhD – Department of Hematology, University Hospital La Paz, Autonoma University of Madrid, Madrid, Spain
    Co-Author: Ruben Berrueco Moreno – Hospital Sant Joan de Deu
    Co-Author: Santiago Bonanad – Hospital Universitari i Politècnic La Fe
    Co-Author: Jose Manuel Calvo Villas, MD (he/him/his) – HOSPITAL UNIVERSITARIO MIGUEL SERVET ZARAGOZA
    Co-Author: Rebeca Gonzalez Gonzalez – Hospital Universitario Severo Ochoa,
    Co-Author: Jose Ramon Gonzalez Porras – Hospital Clínico Universitario Salamanca
    Co-Author: Ramiro José Núñez Vázquez – Hospital Universitario Virgen del Rocío. Instituto de Biomedicina de Sevilla (IBIS), Sevilla, Spain.
    Co-Author: Manuel Rodriguez López, Jr., MD – Hospital Álvaro Cunqueiro (Vigo)
    Hemophilia and Rare Bleeding Disorders
  • Monday, Jun 26th
    18:30 – 19:30 ET
    PB0697 - To Test or Not to Test: Do all individuals with non-severe hemophilia A need DDAVP response testing?
    Room: Exhibition
    Presenting Author: Julia C. Hews-Girard, PhD (she/her/hers) – University of Calgary, School of Nursing
    Co-Author: Man-Chiu Poon – Division of Hematology and Hematological Malignancies, Department of Medicine, University of Calgary, Calgary, AB, Canada
    Hemophilia and Rare Bleeding Disorders
  • Monday, Jun 26th
    18:30 – 19:30 ET
    PB0698 - Determinants of desmopressin response in bleeding disorders: a systematic review and meta-analysis
    Room: Exhibition
    Presenting Author: Sebastiaan N.J Laan, MSc – Department of Internal Medicine, Division of Thrombosis and Hemostasis, Einthoven Laboratory for Vascular and Regenerative Medicine, Leiden University Medical Center, Leiden, The Netherlands
    Co-Author: Jessica Del Castillo Alferez, Msc (she/her/hers) – Department of Molecular Hematology, Sanquin Research, Amsterdam, The Netherlands.
    Co-Author: Suzanne C. Cannegieter, MD PhD – Department of Clinical Epidemiology, Leiden University Medical Center
    Co-Author: Karin Fijnvandraat – Amsterdam UMC, University of Amsterdam, Emma Children’s Hospital, Pediatric Hematology Amsterdam, Netherlands
    Co-Author: Marieke J.H.A. Kruip – Department of Hematology, Erasmus MC, Erasmus University Medical Center Rotterdam, Rotterdam, The Netherlands
    Co-Author: Saskia le Cessie – Department of Clinical Epidemiology – LUMC – Netherlands and Department of biomedical data sciences – LUMC - Netherlands
    Co-Author: Ruben Bierings, PhD – Department of Hematology, Erasmus MC, University Medical Center Rotterdam, the Netherlands
    Co-Author: Jeroen C.J Eikenboom, MD. PhD – Leiden University Medical Center
    Co-Author: Iris van Moort, PhD – Department of Hematology – Erasmus MC, Erasmus University Medical Center - Netherlands
    Hemophilia and Rare Bleeding Disorders
  • Monday, Jun 26th
    18:30 – 19:30 ET
    PB0699 - Idarucizumab for Dabigatran Reversal: a Systematic Review and Meta-analysis of Indications and Outcomes
    Room: Exhibition
    Presenting Author: Sabine F.B van der Horst, MD (she/her/hers) – Department of Medicine - Thrombosis & Hemostasis, Leiden University Medical Center
    Co-Author: Emily S.L Martens, MD/PhD-student – Leiden University Medical Center
    Co-Author: Paul L. den Exter – Department of Thrombosis and Hemostasis, Leiden University Medical Center, Leiden, The Netherlands
    Co-Author: Mettine Bos, PhD – Leiden University Medical Center
    Co-Author: Menno V. Huisman – Department of Medicine - Thrombosis and Hemostasis, Leiden University Medical Center, Leiden, the Netherlands
    Co-Author: Erik Klok, MD, PhD, FESC – Leiden University Medical Center
    Hemophilia and Rare Bleeding Disorders
  • Monday, Jun 26th
    18:30 – 19:30 ET
    PB0700 - FXI inhibitor safety in hemophilia patients: computational prediction of thrombin generation.
    Room: Exhibition
    Presenting Author: Ethan C. Oseas, MS (he/him/his) – Oregon Health & Science University
    Co-Author: Hari Lakshmanan, MS, PhD – Oregon Health & Science University
    Co-Author: Cristina Puy, PhD – Oregon Health & Science University
    Co-Author: Si Han Wang, PhD (she/her/hers) – Oregon Health & Science University
    Co-Author: Meghan E. Fallon – Oregon Health & Science University
    Co-Author: Erik I. Tucker – Aronora, Inc.
    Co-Author: Joseph J. Shatzel – Oregon Health & Science University
    Co-Author: Christina U. Lorentz – Aronora, Inc
    Co-Author: Owen J.T McCarty, PhD, FAHA – Oregon Health & Science University
    Co-Author: David Gailani, MD – Vanderbilt University Medical Center
    Hemophilia and Rare Bleeding Disorders
  • Monday, Jun 26th
    18:30 – 19:30 ET
    PB0702 - Every Minute Counts: "Door to Factor" Issue Times
    Room: Exhibition
    Co-Author: Michelle h. Bech, MN ACNP (A) (she/her/hers) – Adult Bleeding Disorder Program
    Presenting Author: Shannon Jackson, MD (she/her/hers) – Providence Hematology, St. Paul’s Hospital, Vancouver, BC, Canada
    Hemophilia and Rare Bleeding Disorders
  • Monday, Jun 26th
    18:30 – 19:30 ET
    PB0703 - Successful management of hemarthrosis in a patient with severe hemophilia A with an inhibitor, on emicizumab.
    Room: Exhibition
    Presenting Author: Amanda Bettle, PNP – IWK Division Hematology/Oncology
    Co-Author: Victoria Price – Division Pediatric Hematology/Oncology, IWK Health; Department of Pediatrics, Dalhousie University
    Co-Author: Allison Reid – IWK Division of Hematology/Oncology
    Co-Author: Meghan Pike – IWK Division of Hematology/Oncology
    Co-Author: Lindsay Fitzpatrick – IWK Division of Hematology/Oncology
    Hemophilia and Rare Bleeding Disorders
  • Monday, Jun 26th
    18:30 – 19:30 ET
    PB0704 - Clinical approach and monitoring treatment of menorrhagia with PBAC (Pictorial Blood Loss Assessment Chart) in 20 VWD patients
    Room: Exhibition
    Presenting Author: Li-Ting Wang, Nursing – Hemophilia and Rare disease treatment center, Tungs’Taichung MetroHabor Hospital
    Co-Author: Shin-Nan Cheng, Medical Doctor – Hemophilia center, Department of Pediatrics, Tungs’ Taichung MetroHarbor Hospital, Taichung
    Hemophilia and Rare Bleeding Disorders
  • Tuesday, Jun 27th
    10:45 – 12:00 ET
    OC 50.6 - Hemophilia Clinical - Inhibitors
    Room: 516
    Moderator: Samantha Gouw, MD, PhD (she/her/hers) – The University of Amsterdam
    Moderator: Lynn Malec, MD, MSc – Versiti Blood Research Institute, Milwaukee, WI, USA; Division of Hematology & Oncology, Departments of Medicine and Pediatrics, Medical College of Wisconsin, Milwaukee, WI, USA
    Hemophilia and Rare Bleeding Disorders
  • Tuesday, Jun 27th
    10:45 – 12:00 ET
    OC 52.6 - Hemophilia Gene Therapy for Hemophilia B
    Room: 710B
    Moderator: Lindsey A. George, MD – University of Pennsylvania
    Moderator: Johnny Mahlangu, MBBCH, MMed – University of the Witwatersradn
    Hemophilia and Rare Bleeding Disorders
  • Tuesday, Jun 27th
    10:45 – 11:00 ET
    OC 50.1 - Levels of IgG4 distinguish immune tolerance induction outcome in patients with inherited hemophilia A: results from the BrazIT Study
    Room: 516
    Presenting Author: Daniel G. Chaves, Msc, PhD (he/him/his) – Fundação Centro de Hematologia e Hemoterapia de Minas Gerais (Hemominas), Minas Gerais, Brazil
    Co-Author: Brendon Ayala – Faculdade de Medicina, Universidade Federal de Minas Gerais, Minas Gerais, Brazil
    Co-Author: Ricardo M. Camelo, MD, MSc, MBA – Faculty of Pharmacy, Universidade Federal de Minas Gerais
    Co-Author: Maíse M. Dias – Hospital das Clínicas da Faculdade de Medicina de Ribeirão Preto, Universidade de São Paulo, São Paulo, Brazil
    Co-Author: Tânia H. Anegawa – Centro Regional de Hematologia e Hemoterapia de Londrina, Paraná, Brazil
    Co-Author: Andrea G. de Oliveira – Fundação Centro de Hematologia e Hemoterapia de Minas Gerais (Hemominas), Minas Gerais, Brazil
    Co-Author: Rosângela A. Ribeiro – Centro de Hematologia e Hemoterapia do Ceará (Hemoce), Ceará, Brazil
    Co-Author: Mônica H. Cerqueira – Instituto de Hematologia do Estado do Rio de Janeiro (Hemorio), Rio de Janeiro, Brazil
    Co-Author: Leina Y. Etto – Centro de Hematologia e Hemoterapia da Paraíba (Hemoíba), Paraíba, Brazil
    Co-Author: Fábia M R A Callado – Fundação de Hematologia e Hemoterapia de Pernambuco (Hemope), Pernambuco, Brazil
    Co-Author: Vivian K B Franco – Centro de Hematologia e Hemoterapia de Santa Catarina (Hemosc), Santa Catarina, Brazil
    Co-Author: Maria do Rosário F. Roberti – Centro de Hematologia e Hemoterapia de Goiás (Hemogo), Goiás, Brazil
    Co-Author: Maria Aline F. Cerqueira – Centro de Hematologia e Hemoterapia do Piauí (Hemopi), Piauí, Brazil
    Co-Author: Ieda S. Pinto – Fundação Centro de Hematologia e Hemoterapia do Pará (Hemopa), Pará, Brazil
    Co-Author: Suely Rezende, MD, PhD (she/her/hers) – Universidade Federal de Minas Gerais
    Hemophilia and Rare Bleeding Disorders
  • Tuesday, Jun 27th
    10:45 – 11:00 ET
    OC 52.1 - Assessing the safety profile of AMT-060 and etranacogene dezaparvovec gene therapies across clinical trials in people with severe/moderately severe hemophilia B
    Room: 710B
    Presenting Author: Wolfgang Miesbach, MD – University Hospital Frankfurt, Frankfurt, Germany
    Co-Author: Michael Recht, MD, PhD, MBA (he/him/his) – National Hemophilia Foundation
    Co-Author: Nigel S. Key – Division of Hematology, University of North Carolina, Chapel Hill, NC, USA
    Co-Author: Roberto Guillen-Gonzalez – CSL Behring, King of Prussia, PA, USA;
    Co-Author: Krupa Sivamurthy – CSL Behring, King of Prussia, PA, USA
    Co-Author: Paul E. Monahan – CSL Behring, King of Prussia, PA, USA
    Co-Author: Steven W. Pipe, MD – University of Michigan, Ann Arbor, MI, USA
    Hemophilia and Rare Bleeding Disorders
  • Tuesday, Jun 27th
    11:00 – 11:15 ET
    OC 50.2 - Low dose FVIII injections as a potential treatment to prevent Inhibitor development in Hemophilia A - an in vivo study
    Room: 516
    Presenting Author: Wajeeha Zaheer (she/her/hers) – McMaster University
    Co-Author: Davide Matino, MD (he/him/his) – Department of Medicine, Division of Hematology, McMaster University, Hamilton, ON
    Co-Author: Anthony KC. Chan, MBBS – McMaster University, McMaster Children’s Hospital, Hamilton, Canada
    Hemophilia and Rare Bleeding Disorders
  • Tuesday, Jun 27th
    11:00 – 11:15 ET
    OC 52.2 - Residual burden of liver disease after HCV-clearance in hemophilia: a word of caution in the era of gene therapy.
    Room: 710B
    Presenting Author: Vincenzo La Mura, MD PhD – Department of Pathophysiology and Transplantation, University of Milan, Milan, Italy
    Co-Author: Niccolò Bitto – Foundation I.R.C.C.S. Ca’ Granda, Ospedale Maggiore Policlinico, Angelo Bianchi Bonomi and Thrombosis center, Milan, Italy
    Co-Author: Cecilia Capelli – Foundation I.R.C.C.S. Ca’ Granda, Ospedale Maggiore Policlinico, Angelo Bianchi Bonomi and Thrombosis center, Milan, Italy
    Co-Author: Camilla Caputo – Foundation I.R.C.C.S. Ca’ Granda, Ospedale Maggiore Policlinico, Angelo Bianchi Bonomi and Thrombosis center, Milan, Italy
    Co-Author: Simona Siboni – Fondazione IRCCS Ca' Granda - Ospedale Maggiore Policlinico, Centro Emofilia e Trombosi Angelo Bianchi Bonomi
    Co-Author: Sara Arcudi, MD – Fondazione IRCCS Ca' Granda - Ospedale Maggiore Policlinico, Centro Emofilia e Trombosi Angelo Bianchi Bonomi
    Co-Author: Alessandro Ciavarella, MD (he/him/his) – Fondazione IRCCS Ca' Granda - Ospedale Maggiore Policlinico, Centro Emofilia e Trombosi Angelo Bianchi Bonomi
    Co-Author: Roberta Gualtierotti, MD, PhD – Fondazione IRCCS Ca' Granda - Ospedale Maggiore Policlinico, Centro Emofilia e Trombosi Angelo Bianchi Bonomi
    Co-Author: Anna Ludovica Fracanzani – Department of Pathophysiology and Traplantation, University of Milan, Milan, Italy.
    Co-Author: Angelo Sangiovanni – Foundation I.R.C.C.S. Ca’ Granda, Ospedale Maggiore Policlinico, Gastroenterology and Hepatology, Milan, Italy.
    Co-Author: Flora Peyvandi, MD, PhD (she/her/hers) – IRCCS Ca' Granda Maggiore Hospital Foundation, Angelo Bianchi Bonomi Hemophilia and Thrombosis Center, Milano, Italy; Università degli Studi di Milano, Department of Pathophysiology and Transplantation, Milano, Italy
    Hemophilia and Rare Bleeding Disorders
  • Tuesday, Jun 27th
    11:15 – 11:30 ET
    OC 50.3 - Inhibitor development upon switch after 50 EDs from plasma-derived to recombinant FVIII in PUPs with severe haemophilia A: the PUP-SWITCH study results
    Room: 516
    Presenting Author: Syna Miri, MSc – Università degli Studi di Milano, Department of Biomedical Sciences for Health, Milan, Italy
    Co-Author: Frits R. R. Rosendaal – Department of Clinical Epidemiology, Leiden University Medical Center, Leiden, The Netherlands
    Co-Author: Kaan Kavakli – Ege Hemophilia Center, Izmir, Turkey
    Co-Author: Peyman Eshghi, MD – Pediatric Congenital Hematologic Disorders Research Center, Shahid Beheshti University of Medical Sciences, Tehran, Iran.
    Co-Author: Soha Mohammadi Moghaddam – Pediatric Congenital Hematologic Disorders Center, Shahid Beheshti University of Medical Sciences, Tehran, Iran
    Co-Author: Mohsen Elalfy – Ain Shams University, Cairo, Egypt
    Co-Author: Susan Halimeh – Gerinnungszentrum Rhein-Ruhr
    Co-Author: Dilek Gürlek Gökçebay – Ministry of Health Ankara City Hospital, Ankara, Turkey
    Co-Author: Namık Özbek – Ministry of Health Ankara City Hospital, Ankara, Turkey
    Co-Author: Tiraje Celkan – Cerrahpaşa Faculty of Medicine, İstanbul University, Istanbul, Turkey
    Co-Author: Ahmad Mohammadi – Seyed Shohada Hospital, Esfahan Hemophilia Treatment Centre, Esfahan, Iran
    Co-Author: Mehran Karimi, MD – Shiraz University of Medical Sciences, Shiraz, Iran
    Co-Author: Bariş Yılmaz – Marmara University, Istanbul, Turkey
    Co-Author: Canan Albayrak, MD (she/her/hers) – Ondokuz Mayis University, Faculty of Medicine, Samsun, Turkey
    Co-Author: Burçak Tatli Güneş – Tepecik Education and Research Hospital, Izmir, Turkey
    Co-Author: Zühre Kaya, MD – Gazi University Faculty of Medicine, Department of Pediatric Hematology
    Co-Author: Yilmaz Ay – Pamukkale University Faculty of Medicine, Denizli, Turkey
    Co-Author: Sinan Akbayram – Gaziantep University Faculty of Medicine, Gaziantep, Turkey
    Co-Author: Hale Ören, MD (she/her/hers) – Dokuz Eylül University Faculty of Medicine
    Co-Author: Flora Peyvandi, MD, PhD (she/her/hers) – IRCCS Ca' Granda Maggiore Hospital Foundation, Angelo Bianchi Bonomi Hemophilia and Thrombosis Center, Milano, Italy; Università degli Studi di Milano, Department of Pathophysiology and Transplantation, Milano, Italy
    Hemophilia and Rare Bleeding Disorders
  • Tuesday, Jun 27th
    11:15 – 11:30 ET
    OC 52.3 - Efficacy and Safety of Fidanacogene Elaparvovec in Adults with Moderately Severe or Severe Hemophilia B: Results from the Phase 3 BENEGENE-2 Gene Therapy Trial
    Room: 710B
    Presenting Author: Adam Cuker, MD, MS (he/him/his) – Department of Medicine and Department of Pathology & Laboratory Medicine, Perelman School of Medicine, University of Pennsylvania, Philadelphia, PA, USA
    Co-Author: Hazzaa Alzahrani – Adult Haematology, King Faisal Specialist Hospital and Research Centre Riyadh, Saudi Arabia
    Co-Author: Jan Astermark – Department of Hematology Oncology and Radiation Physics, Skane University Hospital, and Institution of Translational Medicine, Lund University, Malmö, Sweden
    Co-Author: Laurent Frenzel – Department of Haematology, Institut Necker
    Co-Author: Olga Katsarou – Blood Transfusion Centre, National Reference Centre for Congenital Bleeding Disorders, Laiko General Hospital
    Co-Author: Kaan Kavakli – Department of Hematology, Ege University Children’s Hospital, Izmir, Turkey
    Co-Author: Robert Klamroth, MD, PhD (he/him/his) – Vivantes Klinikum im Friedrichshain, Clinic for Internal Medicine Angiology and Haemostaseology
    Co-Author: Davide Matino, MD (he/him/his) – Department of Medicine, Division of Hematology, McMaster University, Hamilton, ON
    Co-Author: Amy Shapiro – Indiana Hemophilia & Thrombosis Center, Indianapolis, IN, USA
    Co-Author: Jiaan-Der Wang – Center for Rare Disease and Hemophilia, Taichung Veterans General Hospital
    Co-Author: Joanne Fuiman – Pfizer Inc.
    Co-Author: John McKay – Pfizer Inc.
    Co-Author: Pengling Sun – Pfizer Inc.
    Co-Author: Jeremy Rupon, MD,PhD – Pfizer Inc.
    Hemophilia and Rare Bleeding Disorders
  • Tuesday, Jun 27th
    11:30 – 11:45 ET
    OC 50.4 - Maternal microchimerism promote FVIII tolerance in haemophilia A children with inhibitor under ITI
    Room: 516
    Co-Author: Zekun Li, PhD – Hemophilia Comprehensive Care Center, Hematology Center, Beijing Children’s Hospital, Capital Medical University, National Center for Children’s Health
    Co-Author: Yeling lu – Faculty of Laboratory Medicine, Ruijin Hospital, Shanghai Jiaotong University School of Medicine, Shanghai, China
    Presenting Author: Zhenping CHEN, MD – Beijing Children’s Hospital, Capital Medical University
    Co-Author: Jing Dai – Shanghai Jiaotong University School of Medicine affiliated Ruijin Hospital
    Co-Author: Wenman Wu – Department of Clinical Laboratory Medicine
    Co-Author: Xuefeng Wang – Faculty of Laboratory Medicine, Ruijin Hospital, Shanghai Jiaotong University School of Medicine
    Co-Author: Runhui Wu – Beijing Children’s Hospital, Capital Medical University, Beijing, China
    Hemophilia and Rare Bleeding Disorders
  • Tuesday, Jun 27th
    11:30 – 11:45 ET
    OC 52.4 - The impact of steroids following gene therapy for haemophilia: results from the Exigency study
    Room: 710B
    Co-Author: Kathryn Jenner – Haemnet
    Co-Author: Michael Holland – Haemnet
    Co-Author: Luke Pembroke – Haemnet, London, United Kingdom
    Co-Author: Kate Khair, RN, PhD – Haemnet, London, United Kingdom
    Hemophilia and Rare Bleeding Disorders
  • Tuesday, Jun 27th
    11:45 – 12:00 ET
    OC 50.5 - Prediction of inhibitor development in previously untreated children with hemophilia A using a machine-learning network and information theory quantifiers: Results from the HEMFIL Cohort Study
    Room: 516
    Presenting Author: Letícia Lemos Jardim, PhD (she/her/hers) – Instituto René Rachou (Fiocruz Minas), Belo Horizonte, Minas Gerais, Brazil
    Co-Author: Tiago A. Schieber – Faculdade de Ciências Econômicas
    Co-Author: Marcio Portugal Santana – Fundação Hemominas
    Co-Author: Vivian K B Franco – Centro de Hematologia e Hemoterapia de Santa Catarina (Hemosc), Santa Catarina, Brazil
    Co-Author: Mônica H. Cerqueira – Instituto de Hematologia do Estado do Rio de Janeiro (Hemorio), Rio de Janeiro, Brazil
    Co-Author: Claudia Santos Lorenzato – Centro de Hematologia e Hemoterapia do Paraná (HEMEPAR),
    Co-Author: Luciana Werneck Zuccherato, PhD – Faculty of Medicine, Universidade Federal de Minas Gerais
    Co-Author: Daniel Gonçalves Chaves – Fundação Hemominas
    Co-Author: Suely Rezende, MD, PhD (she/her/hers) – Universidade Federal de Minas Gerais
    Hemophilia and Rare Bleeding Disorders
  • Tuesday, Jun 27th
    11:45 – 12:00 ET
    OC 52.5 - Phase 3 HOPE-B trial of etranacogene dezaparvovec in severe/moderately severe hemophilia B: A post hoc responder analysis of participants who received full dose and responded to treatment
    Room: 710B
    Presenting Author: Steven W. Pipe, MD – University of Michigan, Ann Arbor, MI, USA
    Co-Author: Frank W.G. Leebeek, MD, PhD – Erasmus MC, University Medical Center Rotterdam, The Netherlands
    Co-Author: Michael Recht, MD, PhD, MBA (he/him/his) – National Hemophilia Foundation
    Co-Author: Nigel S. Key – Division of Hematology, University of North Carolina, Chapel Hill, NC, USA
    Co-Author: Susan Lattimore – Hemophilia Center, Oregon Health & Science University, Portland, OR, USA
    Co-Author: Giancarlo Castaman, MD – Center for Bleeding Disorders and Coagulation, Careggi University Hospital, Florence, Italy
    Co-Author: Michiel Coppens, MD, PhD (he/him/his) – Amsterdam University Medical Centers, Amsterdam, The Netherlands
    Co-Author: Yanyan Li – CSL Behring, King of Prussia, PA, USA
    Co-Author: Paul E. Monahan – CSL Behring, King of Prussia, PA, USA
    Co-Author: Wolfgang Miesbach, MD – University Hospital Frankfurt, Frankfurt, Germany
    Hemophilia and Rare Bleeding Disorders
  • Tuesday, Jun 27th
    14:45 – 16:00 ET
    OC 59.6 - Hemophilia - Novel Therapies I (anti-TFPI)
    Room: 517
    Moderator: Maria Elisa Mancuso, MD, PhD (she/her/hers) – IRCCS Humanitas Research Hospital
    Moderator: Soumitra  Tole, MD MSc FRCPC (he/him/his) – Children's Hospital, London Health Science Centre; Western University
    Hemophilia and Rare Bleeding Disorders
  • Tuesday, Jun 27th
    14:45 – 15:00 ET
    OC 59.1 - Concizumab prophylaxis in patients with haemophilia A or B without inhibitors: Efficacy and safety results from the primary analysis of the phase 3 explorer8 study
    Room: 517
    Presenting Author: Pratima Chowdary, MD – Katharine Dormandy Haemophilia and Thrombosis Centre, Royal Free London NHS Foundation Trust, London, United Kingdom
    Co-Author: Pantep Angchaisuksiri, MD – Division of Hematology, Department of Medicine, Ramathibodi Hospital, Mahidol University, Bangkok, Thailand
    Co-Author: Shashikant Apte – Sahyadri Speciality Hospital, Pune, Maharashtra, India
    Co-Author: Anthony KC. Chan, MBBS – McMaster University, McMaster Children’s Hospital, Hamilton, Canada
    Co-Author: Sanja H. Jacobsen – Novo Nordisk A/S, Søborg, Denmark
    Co-Author: Victor Jiménez Yuste – Haematology Department, La Paz University Hospital, IdiPAZ, Universidad Autónoma Madrid, Madrid, Spain
    Co-Author: Jay Jay Thaung Zaw – Novo Nordisk A/S, Søborg, Denmark
    Co-Author: Allison P. Wheeler – Department of Pathology, Microbiology and Immunology, Vanderbilt University Medical Center, Nashville, TN, USA
    Co-Author: Jerzy Windyga, Prof. dr med. (he/him/his) – Institute of Hematology and Transfusion Medicine
    Co-Author: Hermann Eichler, MD (he/him/his) – Institute of Clinical Haemostaseology and Transfusion Medicine, University and University Hospital of the Saarland, Homburg, Germany
    Hemophilia and Rare Bleeding Disorders
  • Tuesday, Jun 27th
    15:00 – 15:15 ET
    OC 59.2 - Analyzing Concizumab mechanism of action by a Mathematical Modeling Approach
    Room: 517
    Co-Author: Kenji Miyazawa – Colorado School of Mines
    Co-Author: Alan E. Mast, MD, PhD (he/him/his) – Versiti
    Co-Author: Michael Dockal – Novo Nordisk
    Co-Author: Marianne Kjalke, PhD (she/her/hers) – Department of Rare Blood Disorders, Novo Nordisk A/S, Måløv, Denmark
    Presenting Author: Karin Leiderman, PhD (she/her/hers) – University of North Carolina at Chapel Hill
    Hemophilia and Rare Bleeding Disorders
  • Tuesday, Jun 27th
    15:15 – 15:30 ET
    OC 59.3 - Pooled Safety Results from the Multidose explorer Studies of Concizumab in Patients with Haemophilia
    Room: 517
    Presenting Author: Hermann Eichler, MD (he/him/his) – Institute of Clinical Haemostaseology and Transfusion Medicine, University and University Hospital of the Saarland, Homburg, Germany
    Co-Author: Tadashi Matsushita – Department of Transfusion Medicine, Nagoya University Hospital, Nagoya, Japan.
    Co-Author: Pantep Angchaisuksiri, MD – Division of Hematology, Department of Medicine, Ramathibodi Hospital, Mahidol University, Bangkok, Thailand
    Co-Author: Giancarlo Castaman, MD – Center for Bleeding Disorders and Coagulation, Careggi University Hospital, Florence, Italy
    Co-Author: Galal Eliraqi – Novo Nordisk, Søborg, Denmark
    Co-Author: Kaan Kavakli – Department of Hematology, Ege University Children’s Hospital, Izmir, Turkey
    Co-Author: Michelle C. Ogden – Novo Nordisk, Søborg, Denmark
    Co-Author: Josephine S. Rasmussen – Novo Nordisk, Søborg, Denmark
    Co-Author: Allison P. Wheeler – Department of Pathology, Microbiology and Immunology, Vanderbilt University Medical Center, Nashville, TN, USA
    Co-Author: Amy Shapiro – Indiana Hemophilia & Thrombosis Center, Indianapolis, IN, USA
    Co-Author: Jan Astermark – Department of Hematology Oncology and Radiation Physics, Skane University Hospital, and Institution of Translational Medicine, Lund University, Malmö, Sweden
    Hemophilia and Rare Bleeding Disorders
  • Tuesday, Jun 27th
    15:30 – 15:45 ET
    OC 59.4 - Health-related quality of life, treatment burden and patient preference in patients with haemophilia A/B without inhibitors on concizumab prophylaxis: results from the phase 3 explorer8 study
    Room: 517
    Presenting Author: Guy Young, MD – Children's Hospital Los Angeles
    Co-Author: Gary M. Benson, BCh BAO FRCP FRCPath – Belfast Health and Social Care Trust
    Co-Author: Hermann Eichler, MD (he/him/his) – Institute of Clinical Haemostaseology and Transfusion Medicine, University and University Hospital of the Saarland, Homburg, Germany
    Co-Author: Johnny Mahlangu, MD (he/him/his) – Haemophilia Comprehensive Care Centre, Charlotte Maxeke Johannesburg Academic Hospital, University of the Witwatersrand and National Health Laboratory Service, Johannesburg, South Africa
    Co-Author: Jan Odgaard-Jensen – Novo Nordisk A/S, Søborg, Denmark
    Co-Author: Jesper S. Neergaard – Novo Nordisk A/S, Søborg, Denmark
    Co-Author: Jay Jay Thaung Zaw – Novo Nordisk A/S, Søborg, Denmark
    Co-Author: Jameela Sathar – Department of Hematology, Hospital Ampang, Ampang, Selangor, Malaysia
    Co-Author: Huyen Tran – Australian Centre for Blood Diseases, Monash University
    Co-Author: Tadashi Matsushita – Department of Transfusion Medicine, Nagoya University Hospital, Nagoya, Japan.
    Hemophilia and Rare Bleeding Disorders
  • Tuesday, Jun 27th
    15:45 – 16:00 ET
    OC 59.5 - Evaluation of Concizumab in Hemophilia Using Microfluidic Flow Assays
    Room: 517
    Presenting Author: Megan P. Jewell, PhD (she/her/hers) – University of Colorado Anschutz Medical Campus
    Co-Author: Adam Wufsus – Novo Nordisk
    Co-Author: Chiara Pallini – Novo Nordisk
    Co-Author: Michael Dockal – Novo Nordisk
    Co-Author: Marianne Kjalke, PhD (she/her/hers) – Department of Rare Blood Disorders, Novo Nordisk A/S, Måløv, Denmark
    Co-Author: Keith B. Neeves, PhD – University of Colorado Anschutz Medical Campus
    Hemophilia and Rare Bleeding Disorders
  • Tuesday, Jun 27th
    18:30 – 19:30 ET
    PB1225 - Acquired haemophilia in the COVID-19 pandemic era – does vaccination or infection increase its risk and influence outcomes?
    Room: Exhibition
    Presenting Author: April Chia, MBBS, MRCP – Singapore General Hospital
    Co-Author: Wan Hui Wong – Singapore General Hospital
    Co-Author: Chuen Wen Tan – Department of Haematology, Singapore General Hospital Singapore
    Co-Author: Hartirathpal Kaur – Singapore General Hospital
    Co-Author: Sim Leng Tien – Singapore General Hospital
    Co-Author: Lai Heng Lee, MBBS FRCP (she/her/hers) – Singapore General Hospital
    Co-Author: Heng Joo Ng – Singapore General Hospital
    Co-Author: Yan Chin Tan – Sengkang General Hospital
    Hemophilia and Rare Bleeding Disorders
  • Tuesday, Jun 27th
    18:30 – 19:30 ET
    PB1226 - Acquired haemophilia A in Finland: a nationwide study of incidence, treatment and outcomes
    Room: Exhibition
    Presenting Author: Vuokko Nummi, MD, PhD – Coagulation Disorder Unit, Helsinki University Hospital
    Co-Author: Leena Hiltunen – Department of Haemostasis, Finnish Red Cross Blood Service, Helsinki, Finland
    Co-Author: Timea Szanto – Coagulation Disorders Unit, Department of Hematology, Helsinki University Hospital Comprehensive Cancer Center and University of Helsinki, Helsinki, Finland
    Co-Author: Eira Poikonen – Coagulation Disorders Unit, Department of Hematology, Helsinki University Hospital Comprehensive Cancer Center and University of Helsinki, Helsinki, Finland
    Co-Author: Anna-Elina Lehtinen – Coagulation Disorders Unit, Department of Hematology, Helsinki University Hospital Comprehensive Cancer Center and University of Helsinki, Helsinki, Finland
    Hemophilia and Rare Bleeding Disorders
  • Tuesday, Jun 27th
    18:30 – 19:30 ET
    PB1227 - Lupus anticoagulant in acquired hemophilia A subjects in Quebec: data from the Quebec Reference Center for Inhibitors
    Room: Exhibition
    Presenting Author: Clémence Merlen, PhD (she/her/hers) – Division of Hematology-Oncology, CHU Sainte-Justine, Université de Montréal
    Co-Author: Ronald Yan – Department of Hematology, Dalhousie University
    Co-Author: Katherine Robinson – Division of Hematology , Department of Medicine , Department of Pathology
    Co-Author: Jean St-Louis – Division of Hematology-Oncology, Department of Pediatrics, Université de Montréal, CHU Sainte-Justine, Montréal, Quebec, Canada.
    Co-Author: Georges-Etienne Rivard – Division of Hematology-Oncology, Department of Pediatrics, Université de Montréal, CHU Sainte-Justine, Montréal, Quebec, Canada
    Co-Author: Arnaud Bonnefoy – Division of Hematology-Oncology, CHU Sainte-Justine, Université de Montréal
    Hemophilia and Rare Bleeding Disorders
  • Tuesday, Jun 27th
    18:30 – 19:30 ET
    PB1228 - Inhibitor detection in acquired hemophilia A: a comparison between the Nijmegen modified Bethesda assay and an anti-FVIII ELISA
    Room: Exhibition
    Presenting Author: Marie-Astrid van Dievoet, MD – Department of laboratory medicine, Cliniques universitaires St. Luc, Brussels Belgium
    Co-Author: Cedric Hermans, MD, PhD (he/him/his) – St-Luc University Hospital
    Co-Author: Catherine Lambert – Cliniques Universitaires Saint-Luc
    Hemophilia and Rare Bleeding Disorders
  • Tuesday, Jun 27th
    18:30 – 19:30 ET
    PB1229 - Haemostatic control with recombinant porcine factor VIII in acquired haemophilia A
    Room: Exhibition
    Presenting Author: Anna Maria Buczma, PhD (she/her/hers) – Department of Hemostasis Disorders and Internal Medicine, Institute of Hematology and Transfusion Medicine, Warsaw, Poland
    Co-Author: Beata Baran – Laboratory of Hemostasis and Metabolic Diseases, Institute of Hematology and Transfusion Medicine, Warsaw, Poland
    Co-Author: Piotr Paluszkiewicz – Department of General and Oncologic Surgery, Institute of Hematology and Transfusion Medicine, Warsaw, Poland
    Co-Author: Magdalena Korwin – Public Clinical Eye Hospital, Warsaw, Poland
    Co-Author: Adela Gwozdowska – Department of Hemostasis Disorders and Internal Medicine, Institute of Hematology and Transfusion Medicine, Warsaw, Poland
    Co-Author: Slawomir Jurek – Department of Hemostasis Disorders and Internal Medicine, Institute of Hematology and Transfusion Medicine, Warsaw, Poland
    Co-Author: Jerzy Windyga, Prof. dr med. (he/him/his) – Institute of Hematology and Transfusion Medicine
    Hemophilia and Rare Bleeding Disorders
  • Tuesday, Jun 27th
    18:30 – 19:30 ET
    PB1230 - Single centre review of practice for treatment of Acquired Haemophilia A patients
    Room: Exhibition
    Presenting Author: Georgina Santiapillai, MBBS – Katharine Dormandy Haemophilia and Thrombosis Centre, Royal Free Hospital, London, UK
    Co-Author: Rosemary Haldon – Katharine Dormandy Haemophilia and Thrombosis Centre, Royal Free Hospital, London, UK
    Co-Author: Anne Riddell – Katharine Dormandy Haemophilia and Thrombosis Centre, Royal Free Hospital, London, UK
    Co-Author: Pratima Chowdary, MD – Katharine Dormandy Haemophilia and Thrombosis Centre, Royal Free London NHS Foundation Trust, London, United Kingdom
    Co-Author: Anja Drebes – Katharine Dormandy Haemophilia and Thrombosis Centre, Royal Free Hospital, London, UK
    Co-Author: Keith Gomez – Katharine Dormandy Haemophilia and Thrombosis Centre, Royal Free Hospital, London, UK
    Co-Author: Janette Kemp – Katharine Dormandy Haemophilia and Thrombosis Centre, Royal Free Hospital, London, UK
    Co-Author: Thynn Thynn Yee – Katharine Dormandy Haemophilia and Thrombosis Centre, Royal Free London NHS Foundation Trust, London, UK
    Co-Author: Paul Batty, MBBS, PhD (he/him/his) – University College London
    Hemophilia and Rare Bleeding Disorders
  • Tuesday, Jun 27th
    18:30 – 19:30 ET
    PB1233 - A single-center study of reduced-dose corticosteroids therapy for patients with acquired hemophilia A.
    Room: Exhibition
    Presenting Author: Yoshiyuki Ogawa, MD, PhD – Department of Hematology, Gunma University Graduate School of Medicine, Maebashi, Japan
    Co-Author: Kunio Yanagisawa – Infection Control and Prevention Center, Gunma University Hospital
    Co-Author: Akira Matsumoto, MD (he/him/his) – Department of Hematology, Gunma University Graduate School of Medicine, Maebashi, Japan
    Co-Author: Mikiya Kajita – Department of Hematology, Gunma University Graduate School of Medicine
    Co-Author: Yuri Miyazawa – Department of Hematology, Gunma University Graduate School of Medicine
    Co-Author: Nobuhiko Kobayashi – Department of Hematology, Gunma University Graduate School of Medicine
    Co-Author: Tsukasa Osaki – Yamagata University School of Medicine
    Co-Author: Masayoshi Souri – Yamagata University School of Medicine
    Co-Author: Akitada Ichinose – Yamagata University School of Medicine
    Co-Author: Hiroshi Handa – Department of Hematology, Gunma University Graduate School of Medicine
    Hemophilia and Rare Bleeding Disorders
  • Tuesday, Jun 27th
    18:30 – 19:30 ET
    PB1234 - Prevalence of studies with Acquired von Willebrand Syndrome laboratory profile at the Hospital Italiano de Buenos Aires (HIBA)
    Room: Exhibition
    Co-Author: Cibrán Yunes Rodrigo – Instituto Univeristario del Hospital Italiano
    Co-Author: Marina S. López – Hospital Italiano de Buenos Aires
    Co-Author: Claudio S. Berger – Hospital Italiano de Buenos Aires
    Co-Author: Privitera Verónica – Hematology. Clinical Departement, Hospital Italiano de Buenos Aires
    Co-Author: Chuliber Fernando, MD – Grupo CAHT
    Presenting Author: Marta E. Martinuzzo, PhD (she/her/hers) – Hospital Italiano de Buenos Aires
    Hemophilia and Rare Bleeding Disorders
  • Tuesday, Jun 27th
    18:30 – 19:30 ET
    PB1235 - Acquired hemophilia A in very old patients: issues on therapy choice. A case report
    Room: Exhibition
    Co-Author: Mariana Gradim – Immunohemotherapy Department, Instituto Português de Oncologia do Porto Francisco Gentil, Porto, Portugal
    Presenting Author: Rui Alves – Immunohemotherapy Department, Instituto Português de Oncologia de Lisboa Francisco Gentil, Lisboa, Portugal
    Co-Author: Rita Queirós – Immunohemotherapy Department, Centro Hospitalar Universitário de São João, Porto, Portugal
    Co-Author: Diana Leão – Immunohemotherapy Department, Centro Hospitalar Universitário de São João, Porto, Portugal
    Co-Author: Lídia Costa – Immunohemotherapy Department, Centro Hospitalar Universitário de São João, Porto, Portugal
    Co-Author: Susana Fernandes – Immunohemotherapy Department, Centro Hospitalar Universitário de São João, Porto, Portugal
    Co-Author: Manuela Lopes – Immunohemotherapy Department, Centro Hospitalar Universitário de São João, Porto, Portugal
    Co-Author: Manuela Carvalho – Immunohemotherapy Department, Centro Hospitalar Universitário de São João, Porto, Portugal
    Co-Author: Carmo Koch – Immunohemotherapy Department, Centro Hospitalar Universitário de São João, Porto, Portugal
    Hemophilia and Rare Bleeding Disorders
  • Tuesday, Jun 27th
    18:30 – 19:30 ET
    PB1236 - Real world experience of perioperative management in people with hemophilia receiving extended half life FVIII and FIX concentrates: A multicentric and cross-sectional study in Northern Spain
    Room: Exhibition
    Co-Author: Nuria Fernández-Mosteirín, PhD MD – Hospital Universitario Miguel Servet (Zaragoza)
    Co-Author: Julia Coll Vallier – Hospital Universitario de Navarra
    Co-Author: Olga Castro González – Hospital Universitario Central de Asturias
    Co-Author: Maialen Lasa Eguialde – Hospital Universitario Donostia
    Co-Author: Cristina Sierra Aisa, MD – Hospital Universitario Cruces (Barakalo-Bizkaia)
    Co-Author: Manuel Rodriguez López, Jr., MD – Hospital Álvaro Cunqueiro (Vigo)
    Co-Author: Belen Gonzalez Mesones – Marqués de Valdecilla Universitary Hospital
    Co-Author: Maria Victoria Aznar Moreno – Hospital Universitario de Navarra
    Co-Author: M Aranzazu Aguirre Arrizabalaga – Hospital Universitario Donostia
    Co-Author: Maria Araiz Ramirez – Hospital Universitario Donostia
    Co-Author: María José Paloma Mora – Hospital Universitario de Navarra, Pamplona, Spain
    Co-Author: Inmaculada Soto – Hospital Universitario Central de Asturias
    Presenting Author: Jose Manuel Calvo Villas, MD (he/him/his) – HOSPITAL UNIVERSITARIO MIGUEL SERVET ZARAGOZA
    Hemophilia and Rare Bleeding Disorders
  • Tuesday, Jun 27th
    18:30 – 19:30 ET
    PB1237 - Validation of a semi-automated Von Willebrand Multimer assay for use in VWD classification
    Room: Exhibition
    Co-Author: Mairead Doyle, MSc – National Coagulation Centre, St James's Hospital, Dublin
    Presenting Author: Mary Byrne – National Coagulation Centre, St James's Hospital, Dublin
    Co-Author: Brendan Mullaney – St James Hospital
    Co-Author: Cathriona Keenan – St James Hospital
    Co-Author: Michelle Lavin, MB, PhD (she/her/hers) – National Coagulation Centre, St. James Hospital and Irish Centre for Vascular Biology, School of Pharmacy and Biomolecular Sciences, Royal College of Physicians and Surgeons in Ireland (RCSI)
    Co-Author: James S. O'Donnell, MB, PhD – Irish Centre for Vascular Biology, Royal College of Surgeons in Ireland,Dublin, Ireland
    Co-Author: Niamh O'Connell, MD – National Coagulation Centre, St James's Hospital, Dublin
    Hemophilia and Rare Bleeding Disorders
  • Tuesday, Jun 27th
    18:30 – 19:30 ET
    PB1238 - Improvement of haemorrhagic outcomes after changing paradigm treatment of haemophilia in the real world: six years of experience in a Portuguese comprehensive care centre
    Room: Exhibition
    Co-Author: Eugénia Cruz, MD, PhD – Thrombosis and Hemostasis Unit, Clinical Haematology Service, Centro Hospitalar Universitário do Porto, Porto, Portugal
    Co-Author: Maria Coutinho – Thrombosis and Hemostasis Unit, Clinical Haematology Service, Centro Hospitalar Universitário do Porto, Porto, Portugal
    Co-Author: Fernanda Leite – Thrombosis and Hemostasis Unit, Clinical Haematology Service, Centro Hospitalar Universitário do Porto, Porto, Portugal
    Co-Author: Filipa Fonseca Dias – Thrombosis and Hemostasis Unit, Clinical Haematology Service, Centro Hospitalar Universitário do Porto, Porto, Portugal
    Co-Author: Mónica Pereira – Thrombosis and Hemostasis Unit, Clinical Haematology Service, Centro Hospitalar Universitário do Porto, Porto, Portugal
    Presenting Author: Sara Morais, MD – Thrombosis and Hemostasis Unit, Clinical Haematology Service, Centro Hospitalar Universitário do Porto, Porto, Portugal
    Hemophilia and Rare Bleeding Disorders
  • Tuesday, Jun 27th
    18:30 – 19:30 ET
    PB1239 - Prophylaxis with Extended Half-life Products in Patients with Hemophilia A: Real-life Data of the Milan Cohort
    Room: Exhibition
    Presenting Author: Alessandro Ciavarella, MD (he/him/his) – Fondazione IRCCS Ca' Granda - Ospedale Maggiore Policlinico, Centro Emofilia e Trombosi Angelo Bianchi Bonomi
    Co-Author: Addolorata Truma, MD – Università degli Studi di Milano, Department of Pathophysiology and Transplantation
    Co-Author: Francesco Ballardini – Fondazione IRCCS Ca' Granda - Ospedale Maggiore Policlinico, Centro Emofilia e Trombosi Angelo Bianchi Bonomi.
    Co-Author: Maria Abbattista, PhD – Fondazione IRCCS Ca' Granda - Ospedale Maggiore Policlinico, Centro Emofilia e Trombosi Angelo Bianchi Bonomi
    Co-Author: Sara Arcudi, MD – Fondazione IRCCS Ca' Granda - Ospedale Maggiore Policlinico, Centro Emofilia e Trombosi Angelo Bianchi Bonomi
    Co-Author: Roberta Gualtierotti, MD, PhD – Fondazione IRCCS Ca' Granda - Ospedale Maggiore Policlinico, Centro Emofilia e Trombosi Angelo Bianchi Bonomi
    Co-Author: Claudia Mistretta – Fondazione IRCCS Ca' Granda - Ospedale Maggiore Policlinico, Centro Emofilia e Trombosi Angelo Bianchi Bonomi
    Co-Author: Gabriella Nicolò – Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico di Milano, Department of Healthcare Professions, Milan, Italy
    Co-Author: Cristina Novembrino, PhD – Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico, Angelo Bianchi Bonomi Hemophilia and Thrombosis Center, Milan, Italy
    Co-Author: Simona Maria Siboni – Fondazione IRCCS Ca' Granda, Ospedale Maggiore Policlinico, Angelo Bianchi Bonomi Hemophilia and Thrombosis Center
    Co-Author: Flora Peyvandi, MD, PhD (she/her/hers) – IRCCS Ca' Granda Maggiore Hospital Foundation, Angelo Bianchi Bonomi Hemophilia and Thrombosis Center, Milano, Italy; Università degli Studi di Milano, Department of Pathophysiology and Transplantation, Milano, Italy
    Hemophilia and Rare Bleeding Disorders
  • Tuesday, Jun 27th
    18:30 – 19:30 ET
    PB1241 - ATHN 11: Observational Study of Long-Term Outcomes of Liver Transplantation
    Room: Exhibition
    Presenting Author: Margaret V. Ragni, MD, MPH (she/her/hers) – Department of Medicine, University of Pittsburgh, Pittsburgh, PA, USA
    Co-Author: Brian Hu – ATHN
    Co-Author: Jessica Callis – American Thrombosis Hemostasis Network
    Co-Author: Matthew Manuel – ATHN
    Co-Author: Jarren Santos – ATHN
    Co-Author: Kenneth Friedman – Versiti Blood Research Institute
    Co-Author: Peter Kouides, MD – Mary M. Gooley Hemophilia Centre, Rochester, NY, USA
    Co-Author: Philip Kuriakose – Wayne State University Medical School, Henry Ford Health System
    Co-Author: Andrew D. Leavitt – Adult Hemophilia Treatment Center, University of California San Francisco, San Francisco, CA, USA
    Co-Author: Ming Lim – University Utah
    Co-Author: Nicoletta Machin – University Pittsburgh
    Co-Author: Michael Recht, MD, PhD, MBA (he/him/his) – National Hemophilia Foundation
    Hemophilia and Rare Bleeding Disorders
  • Tuesday, Jun 27th
    18:30 – 19:30 ET
    PB1243 - Comparison of Quality of Life and Bleeding Phenotypes in People with Congenital Hemophilia A: Longitudinal Study from the PicnicHealth Database of PROMIS®-29 v2.0 scores
    Room: Exhibition
    Co-Author: Jessica Scrimshire – F. Hoffmann-La Roche Ltd
    Co-Author: Spyros Roumpanis – F. Hoffmann-La Roche Ltd
    Presenting Author: Martynas Aizenas – F. Hoffmann-La Roche Ltd
    Co-Author: Gillian Hanson – PicnicHealth
    Co-Author: Emily Cibelli – PicnicHealth
    Co-Author: Krisha Patel – PicnicHealth
    Co-Author: Francis Nissen – F. Hoffmann-La Roche Ltd
    Hemophilia and Rare Bleeding Disorders
  • Tuesday, Jun 27th
    18:30 – 19:30 ET
    PB1244 - Early joint damage detection in pediatric patients with moderate and severe hemophilia: usefulness for treatment individualization
    Room: Exhibition
    Presenting Author: Rubén Berrueco, PhD – Hospital Sant Joan de Déu
    Co-Author: Natalia Rodriguez – Sant Joan de Déu Pediatric Hospital
    Co-Author: Nuria Caballero – Sant Joan de Déu Pediatric Hospital
    Hemophilia and Rare Bleeding Disorders
  • Tuesday, Jun 27th
    18:30 – 19:30 ET
    PB1245 - Efficacy, safety and dosing of pasteurized plasma-derived von Willebrand factor/Factor VIII concentrate for the treatment of von Willebrand Disease: a systematic review
    Room: Exhibition
    Presenting Author: Carmen Escuriola-Ettingshausen, MD – Haemophilia Centre Rhine-Main, Mörfelden-Walldorf, Germany
    Co-Author: Riitta Lassila, MD, PhD (she/her/hers) – Helsinki University Hospital, Coagulation Disorders Unit, Department of Haematology, Comprehensive Cancer Centre, and Research Program Unit in System Oncology, University of Helsinki, Helsinki, Finland
    Co-Author: Gines Escolar – Hemostasis and Erythropathology Laboratory, Hematopathology, Department of Pathology, Centre de Diagnòstic Biomèdic (CDB), Hospital Clínic de Barcelona, Institut d'Investigacions Biomèdiques August Pi i Sunyer (IDIBAPS), Universitat de Barcelona, Barcelona, Spain.
    Co-Author: Christoph Male, MD, MSc – Department of Paediatrics, Medical University of Vienna, Vienna, Austria.
    Co-Author: Kathrin Schirner – CSL Behring Innovation GmbH, Marburg, Germany
    Co-Author: Lisa Heyder – CSL Behring Innovation GmbH, Marburg, Germany
    Co-Author: Erik Berntorp – Clinical Coagulation Research, Department of Translational Medicine, Lund University, Malmö, Sweden
    Hemophilia and Rare Bleeding Disorders
  • Tuesday, Jun 27th
    18:30 – 19:30 ET
    PB1247 - Iron deficiency in inherited bleeding disorders in a hemophilia center
    Room: Exhibition
    Presenting Author: Jorge Félix, MD – Centro Hospitalar Universitário Lisboa Norte
    Co-Author: Catarina J. Jacinto – Centro Hospitalar Universitário Lisboa Norte
    Co-Author: Cristina Catarino, Dr (she/her/hers) – Centro Hospitalar Universitário Lisboa Norte
    Co-Author: Filipa Pires – Centro Hospitalar Universitário Lisboa Norte
    Co-Author: Carolina Peixoto, MD – Centro Hospitalar Universitário Lisboa Norte
    Co-Author: Catarina Câmara, MD (she/her/hers) – Centro Hospitalar Universitário Lisboa Norte
    Co-Author: Joana S G Pestana, MD (she/her/hers) – Hospital do Espírito Santo - Évora
    Co-Author: Fátima Rodrigues – Centro Hospitalar Universitário Lisboa Norte
    Co-Author: Artur Pereira – Centro Hospitalar Universitário Lisboa Norte
    Hemophilia and Rare Bleeding Disorders
  • Tuesday, Jun 27th
    18:30 – 19:30 ET
    PB1248 - Patient-reported outcomes using the Patient-Reported Outcomes, Burdens and Experiences survey following Emicizumab initiation in patients with severe Hemophilia A without inhibitors at a single centre
    Room: Exhibition
    Presenting Author: Ingrid A. Blydt-Hansen, MD – Department of Internal Medicine, University of British Columbia
    Co-Author: Shannon Jackson, MD (she/her/hers) – Providence Hematology, St. Paul’s Hospital, Vancouver, BC, Canada
    Co-Author: Michelle h. Bech, MN ACNP (A) (she/her/hers) – Adult Bleeding Disorder Program
    Hemophilia and Rare Bleeding Disorders
  • Tuesday, Jun 27th
    18:30 – 19:30 ET
    PB1249 - Prospective, Observational Study of the Clinical Characteristics of Adults and Adolescents With Severe Hemophilia A
    Room: Exhibition
    Presenting Author: Pratima Chowdary, MD – Katharine Dormandy Haemophilia and Thrombosis Centre, Royal Free London NHS Foundation Trust, London, United Kingdom
    Co-Author: Liane Khoo – Haemophilia Treatment Centre, Royal Prince Alfred Hospital, NSW Health Pathology, Sydney, Australia
    Co-Author: Michael Wang – Hemophilia and Thrombosis Center, University of Colorado Anschutz Medical Campus, Colorado USA
    Co-Author: Hervé Chambost – AP-HM, Department of Pediatric Hematology Oncology, Children Hospital La Timone & Aix Marseille University, INSERM, INRA, C2VN, Marseille, France
    Co-Author: Anthony KC. Chan, MBBS – McMaster University, McMaster Children’s Hospital, Hamilton, Canada
    Co-Author: Angel Moryusef – Sanofi, Cambridge, MA, USA
    Co-Author: Annemieke Willemze – Sanofi, Amsterdam, Netherlands
    Co-Author: Johannes Oldenburg, MD (he/him/his) – University Clinic Bonn AöR, Institute of Experimental Haematology and Transfusion Medicine, Bonn, Germany
    Hemophilia and Rare Bleeding Disorders
  • Tuesday, Jun 27th
    18:30 – 19:30 ET
    PB1250 - Quality of Life in Females and Males with Mild Congenital Hemophilia A: A Longitudinal Study from the PicnicHealth Database of PROMIS®-29 v2.0 Scores
    Room: Exhibition
    Co-Author: Angela C. Weyand, MD (she/her/hers) – University of Michigan Medical School
    Co-Author: Francis Nissen – F. Hoffmann-La Roche Ltd
    Co-Author: Spyros Roumpanis – F. Hoffmann-La Roche Ltd
    Co-Author: Katya Moreno – F. Hoffmann-La Roche Ltd
    Presenting Author: Dakota Rosenfelt, PharmD, RPh, MBAc (he/him/his) – Genentech, Inc.
    Co-Author: Gillian Hanson – PicnicHealth
    Co-Author: Emily Cibelli – PicnicHealth
    Co-Author: Krisha Patel – PicnicHealth
    Co-Author: Jessica Scrimshire – F. Hoffmann-La Roche Ltd
    Hemophilia and Rare Bleeding Disorders
  • Tuesday, Jun 27th
    18:30 – 19:30 ET
    PB1251 - The use of extended half-life factor IX products in the surgical setting – a UK hemophilia center experience
    Room: Exhibition
    Presenting Author: Molly Musarara, RN, BSC(Hons) – Katharine Dormandy Haemophilia and Thrombosis Centre, Royal Free London NHS Foundation Trust, London, UK
    Co-Author: Elsa Aradom – Katharine Dormandy Haemophilia and Thrombosis Centre, Royal Free London NHS Foundation Trust, London, UK
    Co-Author: Emma Charnick – Katharine Dormandy Haemophilia and Thrombosis Centre, Royal Free London NHS Foundation Trust, London, UK
    Co-Author: Nawal Asir – Katharine Dormandy Haemophilia and Thrombosis Centre, Royal Free London NHS Foundation Trust, London, UK
    Co-Author: Thynn Thynn Yee – Katharine Dormandy Haemophilia and Thrombosis Centre, Royal Free London NHS Foundation Trust, London, UK
    Hemophilia and Rare Bleeding Disorders
  • Tuesday, Jun 27th
    18:30 – 19:30 ET
    PB1252 - Value of Hemophilia Drug Treatment Using Analysis of the Area Under the Curve
    Room: Exhibition
    Co-Author: Erik Berntorp – Clinical Coagulation Research, Department of Translational Medicine, Lund University, Malmö, Sweden
    Co-Author: Adam Fridhammer – The Swedish Institute for Health Economics, Lund, Sweden
    Co-Author: Sofie Persson – The Swedish Institute for Health Economics, Lund, Sweden
    Co-Author: Katarina Steen Carlsson – The Swedish Institute for Health Economics, Lund, Sweden
    Presenting Author: Emilio Musi, MD, MBA – Bayer Pharma
    Hemophilia and Rare Bleeding Disorders
  • Tuesday, Jun 27th
    18:30 – 19:30 ET
    PB1254 - A New Tool to Assist in Treatment Selection – The World Federation of Hemophilia (WFH) Shared Decision-Making (SDM) Tool
    Room: Exhibition
    Presenting Author: Donna Coffin, MSc Epid (she/her/hers) – World Federation of Hemophilia
    Co-Author: Declan Noone – European Haemophilia Consortium
    Co-Author: Julia Chadwick – WFH
    Co-Author: Mayss Naccache, MSc – World Federation of Hemophilia
    Co-Author: Brendan Hayes – NHF
    Co-Author: Mark W. Skinner, JD (he/him/his) – Institute for Policy Advancement Ltd.
    Co-Author: Courtney Thornburg, MD, MS (she/her/hers) – Rady Children's Hospital-San Diego
    Co-Author: Thomas Sannie – Association française des hémophiles
    Hemophilia and Rare Bleeding Disorders
  • Tuesday, Jun 27th
    18:30 – 19:30 ET
    PB1255 - An update on real-world use of rVIII-SingleChain in patients with haemophilia A in Germany: Interim results from a prospective, non-interventional study
    Room: Exhibition
    Presenting Author: Martin Olivieri (he/him/his) – Paediatric Thrombosis and Haemostasis Unit, Paediatric Haemophilia Center, Dr. von Hauner Children's Hospital, LMU Clinic, Munich, Germany
    Co-Author: Sabrina Juranek – Paediatric Thrombosis and Haemostasis Unit, Dr. von Hauner Children´s Hospital LMU Munich, Germany
    Co-Author: Florian Langer – Universitätsklinikum Eppendorf, II. Medizinische Klinik und Poliklinik, Hubertus Wald Tumorzentrum, Universitäres Cancer Center Hamburg (UCCH), Hamburg, Germany
    Co-Author: Carmen Escuriola-Ettingshausen, MD – Haemophilia Centre Rhine-Main, Mörfelden-Walldorf, Germany
    Co-Author: Thomas Linhoff – CSL Behring, Hattersheim, Germany.
    Co-Author: Johannes Oldenburg, MD (he/him/his) – University Clinic Bonn AöR, Institute of Experimental Haematology and Transfusion Medicine, Bonn, Germany
    Hemophilia and Rare Bleeding Disorders
  • Tuesday, Jun 27th
    18:30 – 19:30 ET
    PB1256 - Complication Analysis in Korean Patients with Hemophilia A from 2007 to 2019: A Nationwide Study by the Health Insurance Review and Assessment Service Database
    Room: Exhibition
    Presenting Author: Ye Jee Shim, PhD – Keimyung University School of Medicine, Keimyung University Dongsan Hospital
    Co-Author: Young Bae Choi – Ajou University School of Medicine, Ajou University Hospital
    Hemophilia and Rare Bleeding Disorders
  • Tuesday, Jun 27th
    18:30 – 19:30 ET
    PB1257 - Diagnostic Tool for Patients with Hemophilia: from Bedside to Comprehensive Investigation
    Room: Exhibition
    Presenting Author: Ampaiwan Chuansumrit – Department of Pediatrics, Faculty of Medicine Ramathibodi Hospital, Mahidol University, Bangkok, Thailand
    Co-Author: Rungrote Natesirinilkul, MD – Department of Pediatrics, Faculty of Medicine, Chiang Mai University, Chiang Mai, Thailand
    Co-Author: Nongnuch Sirachainan, MD – Faculty of Medicine Ramathibodi hospital, Mahidol University, Bangkok, Thailand
    Co-Author: Pacharapan Surapolchai – Department of Pediatrics, Faculty of Medicine, Thammasat University, Pathumthani, Thailand
    Co-Author: Theera Ruchutrakool – Department of Medicine, Faculty of Medicine Siriraj Hospital, Mahidol University, Bangkok, Thailand
    Co-Author: Praguywan Kadegasem – Department of Pediatrics, Faculty of Medicine, Ramathibodi Hospital, Mahidol University, Bangkok, Thailand
    Co-Author: Noppawan Tangbubpha – Department of Pediatrics, Faculty of Medicine, Ramathibodi Hospital, Mahidol University, Bangkok, Thailand
    Co-Author: Tanyanee Khlangtan – Department of Pediatrics, Faculty of Medicine, Ramathibodi Hospital, Mahidol University, Bangkok, Thailand
    Hemophilia and Rare Bleeding Disorders
  • Tuesday, Jun 27th
    18:30 – 19:30 ET
    PB1258 - Discrepancies Between Laboratory Assays In Hemophilia A Pediatric Patients Receiving Prophylaxis
    Room: Exhibition
    Co-Author: Alkistis Adramerina, MD Msc – 1st Pediatric Department Aristotle University of Thessaloniki, Greece
    Presenting Author: Aikaterini Teli, MD, PhD – 1st Pediatric Department Aristotle University of Thessaloniki, Greece
    Co-Author: Maria Vousvouki, Master of Science (she/her/hers) – 1st Pediatric Department Aristotle University of Thessaloniki, Greece
    Co-Author: Athina Efstathiou – 1st Pediatric Department, School of Medicine, Faculty of Health Sciences, Aristotle University of Thessaloniki, Greece
    Co-Author: Symeon Symeonidis – 1st Pediatric Department, School of Medicine, Faculty of Health Sciences, Aristotle University of Thessaloniki, Greece
    Co-Author: Antigoni Theodoridou – 1st Pediatric Department, School of Medicine, Faculty of Health Sciences, Aristotle University of Thessaloniki, Greece
    Co-Author: Spyros Gerou – "Analysis" Lab
    Co-Author: Marina Economou – 1st Pediatric Department Aristotle University of Thessaloniki, Greece
    Hemophilia and Rare Bleeding Disorders
  • Tuesday, Jun 27th
    18:30 – 19:30 ET
    PB1259 - Emicizumab prophylaxis: a novel alternative therapy for severe Hemophilia A patients with and without inhibitors.
    Room: Exhibition
    Presenting Author: Munira Borhany, MBBS, MCPS, FCPS, FRCP (Edin), FRCPath – Haemophilia Welfare Society, Karachi
    Co-Author: Rukhshanda Nadeem – Haemophilia Welfare Society, Karachi
    Co-Author: Raheel Ahmed – Haemophilia Welfare Society, Karachi
    Hemophilia and Rare Bleeding Disorders
  • Tuesday, Jun 27th
    18:30 – 19:30 ET
    PB1260 - Importance of molecular diagnostics to classify the severity of hemophilia A: a brief experience of Fundação Hemominas in Brazil
    Room: Exhibition
    Co-Author: Carolina Guimarães Ramos Matosinho, PhD – FundaçãoCentro de Hematologia e Hemoterapia do Estado de Minas Gerais (Hemominas), Belo Horizonte, Minas Gerais, Brazil
    Co-Author: Sophia Soares Perpétuo, N/A – Fundação Centro de Hematologia e Hemoterapia do Estado de Minas Gerais (Hemominas)Belo Horizonte, MG, Brasil
    Presenting Author: Daniel G. Chaves, Msc, PhD (he/him/his) – Fundação Centro de Hematologia e Hemoterapia de Minas Gerais (Hemominas), Minas Gerais, Brazil
    Hemophilia and Rare Bleeding Disorders
  • Tuesday, Jun 27th
    18:30 – 19:30 ET
    PB1261 - Matching Adjusted Indirect Comparisons Between Personalized Prophylaxis with Simoctocog Alfa versus Standard Prophylaxis with Turoctocog Alfa in Adults with Severe Hemophilia A
    Room: Exhibition
    Presenting Author: Fernando F. Corrales-Medina, MD (he/him/his) – University of Miami-Hemophilia Treatment Center
    Co-Author: Aida Mashenka Moreno Gonzalez – Hospital Infantil de México Federico Gómez
    Co-Author: Berenice Sánchez Jara – Department of Pediatric Hematology. Centro Médico Nacional (CMN) La Raza
    Hemophilia and Rare Bleeding Disorders
  • Tuesday, Jun 27th
    18:30 – 19:30 ET
    PB1263 - Third Interim Subgroup Analysis of the Effectiveness and Safety of Damoctocog Alfa Pegol in Patients with Hemophilia A Treated Every 5 or Every 7 Days: Results from the Real-World HEM-POWR Study
    Room: Exhibition
    Co-Author: Mark T. Reding – Center for Bleeding and Clotting Disorders, University of Minnesota, Minneapolis, MN, USA
    Co-Author: Maria Teresa Alvarez-Román, MD, PhD – Department of Hematology, University Hospital La Paz, Autonoma University of Madrid, Madrid, Spain
    Co-Author: Martin Sanabria – Bayer, Basel, Switzerland
    Co-Author: Giancarlo Castaman, MD – Center for Bleeding Disorders and Coagulation, Careggi University Hospital, Florence, Italy
    Co-Author: Maissaa Janbain – Louisiana Center for Bleeding and Clotting Disorders, Tulane University Medical Center, LA, USA
    Co-Author: Tadashi Matsushita – Department of Transfusion Medicine, Nagoya University Hospital, Nagoya, Japan.
    Presenting Author: Karina Meijer, MD, PhD (she/her/hers) – Department of Hematology, University Medical Center Groningen, University of Groningen, Groningen, The Netherlands
    Co-Author: Kathrin Schmidt – Bayer, Berlin, Germany
    Co-Author: Johannes Oldenburg, MD (he/him/his) – University Clinic Bonn AöR, Institute of Experimental Haematology and Transfusion Medicine, Bonn, Germany
    Hemophilia and Rare Bleeding Disorders
  • Tuesday, Jun 27th
    18:30 – 19:30 ET
    PB1264 - Thrombin generation assay as a treatment tracking tool in hemophilia patients: a retrospective cohort study
    Room: Exhibition
    Co-Author: Mohammed Abdelghafour Sabri, Assistant MD – Laboratory of Hematology, LHUB-ULB, Université Libre de Bruxelles, Belgium
    Presenting Author: Laurence Rozen, PhD PharmD – LHUB-ULB, Université Libre de Bruxelles, Belgium
    Co-Author: Anne Demulder – Laboratory of Hematology, LHUB-ULB, Université Libre de Bruxelles, Belgium
    Co-Author: Andrea Nebbioso – Department of Pediatrics, Hôpitaux Iris Sud, Brussels, Belgium
    Co-Author: Pierre Peters – Laboratory of Hematology, CHU Liège, Belgium
    Co-Author: Phu Quoc Le, MD, PhD (he/him/his) – Department of Hematology and Oncology, Hôpital Universitaire Des Enfants Reine Fabiola, Université Libre de Bruxelles, Belgium
    Hemophilia and Rare Bleeding Disorders
  • Tuesday, Jun 27th
    18:30 – 19:30 ET
    PB1265 - “HERMES” - HEmophilia Related MEntal illnesS: A cross-sectional, multicenter study in Switzerland
    Room: Exhibition
    Presenting Author: Mutlu Kartal-Kaess, MD (she/her/hers) – Inselspital Bern, Bern, Schweiz
    Co-Author: Laura Aliena Maier – Inselspital Bern
    Co-Author: Michael Kaess – UPD Bern, University of Bern
    Co-Author: Albisetti Pedroni Manuela – Kinderspital Zurich
    Co-Author: Alice Trincero – University Hospital Zurich USZ
    Co-Author: Lukas Graf – Center for Laboratory Medicine, Hemophilia- and Hemostasis Center St. Gallen
    Co-Author: Heinz Hengartner – Ostschweizer Kinderspital
    Co-Author: Pierre Fontana, MD PhD (he/him/his) – Division of Angiology and Haemostasis, University Hospitals of Geneva, Switzerland
    Co-Author: Nicolas von der Weid – UKBB Basel
    Co-Author: Katrin Scheinemann – Ostschweizer Kinderspital
    Co-Author: Silvia von Mackensen – University of Hamburg
    Co-Author: Stefan Lerch – UPD, University of Bern
    Co-Author: Corinna Reichl – UPD, University of Bern
    Co-Author: Johanna A. Kremer-Hovinga – Centre of Laboratory Medicine Section Hemostasis Inselspital Bern
    Hemophilia and Rare Bleeding Disorders
  • Tuesday, Jun 27th
    18:30 – 19:30 ET
    PB1268 - Clinical Outcomes with Octocog Alfa in Patients with Hemophilia A in China: 1-year of Follow-up of the AHEAD International Study
    Room: Exhibition
    Co-Author: Runhui Wu – Beijing Children’s Hospital, Capital Medical University, Beijing, China
    Co-Author: Zhenyu Li – The Affiliated Hospital of Xuzhou Medical University, Xuzhou, China
    Co-Author: Jing Sun – Nanfang Hospital, Nanfang Medical University, Guangzhou, China
    Co-Author: Xin Du – Shenzhen Second People's Hospital, The First Affiliated Hospital of Shenzhen University, Shenzhen, China
    Co-Author: Xinsheng Zhang – Shandong Blood Center, Jinan, China
    Co-Author: Ying Wang – Shenzhen Children's Hospital, Shenzhen, China
    Co-Author: Qun Hu – Tongji Hospital, Tongji Medical College of Huazhong University of Science and Technology, Wuhan, China
    Co-Author: Rongfu Zhou, PhD,MD – Nanjing Drum Tower Hospital, The Affiliated Hospital of Nanjing University Medical School, Nanjing, China
    Presenting Author: Joan Gu – Takeda Development Center Americas, Inc., Cambridge, MA, USA
    Co-Author: Randy Guerra, MD – Takeda Development Center Americas, Inc., Cambridge, MA, USA
    Co-Author: Pooja Oberai, MD MS (she/her/hers) – Takeda Development Center Americas, Inc., Cambridge, MA, USA
    Co-Author: Renchi Yang, MD (he/him/his) – Institute of Hematology and Blood Diseases Hospital, Chinese Academy of Medical Sciences and Peking Union Medical College, Tianjin, China
    Hemophilia and Rare Bleeding Disorders
  • Tuesday, Jun 27th
    18:30 – 19:30 ET
    PB1269 - Comorbidities - an additional burden in the real life of patients with haemophilia
    Room: Exhibition
    Presenting Author: Cristina E. Ursu (she/her/hers) – Onco-Hematology Research Unit, Romanian Academy of Medical Sciences, Children Emergency Hospital “Louis Turcanu” Timisoara, European Hemophilia Treatment Centre, 300011 Timisoara, Romania
    Co-Author: Margit Serban – Onco-Hematology Research Unit, Romanian Academy of Medical Sciences, Children Emergency Hospital “Louis Turcanu” Timisoara, European Hemophilia Treatment Centre, 300011 Timisoara, Romania
    Co-Author: Petre Serban – Medical Centre for Education and Rehabilitation of Children and Young Adults, European Hemophilia Treatment Centre, 305100 Buzias, Romania
    Co-Author: Adina Traila – Medical Centre for Education and Rehabilitation of Children and Young Adults, European Hemophilia Treatment Centre, 305100 Buzias, Romania
    Co-Author: Daniel Andrei – Romanian Hemophilia Association
    Co-Author: Ines Vaide – Department of Hemato-Oncology, Institute of Clinical Medicine, University of Tartu, Estonia
    Co-Author: Cristian Jinca – Department of Pediatrics, Division of Onco-Hematology, “ Victor Babes ” University of Medicine and Pharmacy Timisoara, 300041 Timisoara, Romania
    Co-Author: Estera Boeriu – Department of Pediatrics, Division of Onco-Hematology, “ Victor Babes ” University of Medicine and Pharmacy Timisoara, 300041 Timisoara, Romania
    Co-Author: Teodora Smaranda Arghirescu, MD, PhD – Department of Pediatrics, Division of Onco-Hematology, “ Victor Babes ” University of Medicine and Pharmacy Timisoara, 300041 Timisoara, Romania
    Hemophilia and Rare Bleeding Disorders
  • Tuesday, Jun 27th
    18:30 – 19:30 ET
    PB1270 - Hematopoietic stem cell transplantation in a newborn suffering from severe combined immunodeficiency and severe hemophilia A
    Room: Exhibition
    Presenting Author: Sarah Schober, MD – University Children’s Hospital Tuebingen, Department I – General Pediatrics, Hematology/Oncology, Tuebingen, Germany
    Co-Author: Ursula Holzer – University Children’s Hospital Tuebingen, Department I – General Pediatrics, Hematology/Oncology, Tuebingen, Germany
    Co-Author: Peter Lang – University Children’s Hospital Tuebingen, Department I – General Pediatrics, Hematology/Oncology, Tuebingen, Germany
    Co-Author: Michaela Döring – University Children’s Hospital Tuebingen, Department I – General Pediatrics, Hematology/Oncology, Tuebingen, Germany
    Co-Author: Martin Olivieri (he/him/his) – Paediatric Thrombosis and Haemostasis Unit, Paediatric Haemophilia Center, Dr. von Hauner Children's Hospital, LMU Clinic, Munich, Germany
    Co-Author: Vanya Icheva – University Children’s Hospital Tuebingen, Department II – Pediatric Cardiology, Intensive Care Medicine and Pulmonology, Tuebingen, Germany
    Hemophilia and Rare Bleeding Disorders
  • Tuesday, Jun 27th
    18:30 – 19:30 ET
    PB1272 - Impact of the difference in the cutoff point of the values of clotting factors VIII and IX in the definition of women with hemophilia and hemophilia carrier
    Room: Exhibition
    Presenting Author: Thaís D R Nóbrega – University of São Paulo Medical School
    Co-Author: Guilherme A. Maia – Instituto do Cancer do Estado de São Paulo - ICESP
    Co-Author: Paula R. Villaça – Clinics Hospital of the University of São Paulo Medical School
    Co-Author: Bianca Stefanello – Clinics Hospital of the University of São Paulo Medical School
    Co-Author: Erica Okazaki – Clinics Hospital of the University of São Paulo Medical School
    Co-Author: Tania R. F. da Rocha – Clinics Hospital of the University of São Paulo Medical School
    Co-Author: Cynthia Rothschild, Master (she/her/hers) – ICESP - University of São Paulo Medical School
    Co-Author: Frederica R. M. Y. Cassis – University of São Paulo Medical School
    Co-Author: Eliane P. N. Sandoval – University of São Paulo Medical School
    Co-Author: Fernanda A. Orsi – University of São Paulo Medical School
    Hemophilia and Rare Bleeding Disorders
  • Tuesday, Jun 27th
    18:30 – 19:30 ET
    PB1273 - Inhibitor Recurrence on Emicizumab Prophylaxis in Tolerized Patients with Severe Hemophilia A
    Room: Exhibition
    Co-Author: Gaudas B. Trakymas – Vilnius University
    Co-Author: Agne Morkunaite – Vilnius University
    Presenting Author: Sonata Saulyte Trakymiene, MD PhD – Vilnius University Hospital Santaros Clinics
    Hemophilia and Rare Bleeding Disorders
  • Tuesday, Jun 27th
    18:30 – 19:30 ET
    PB1274 - Joint health in patients with hemophilia: data from real life practice in Colombia
    Room: Exhibition
    Co-Author: Francisco Yepes – Medicarte
    Co-Author: Sandro Parra – Medicarte
    Co-Author: Carolina Becerra – Medicarte
    Co-Author: Claudia Sossa – Medicarte
    Presenting Author: Saskia Prasca-Tapia, MD – Medicarte
    Co-Author: Jorge Donado – Medicarte
    Co-Author: Natalia a. Duque, N/A – Medicarte
    Hemophilia and Rare Bleeding Disorders
  • Tuesday, Jun 27th
    18:30 – 19:30 ET
    PB1275 - Multicenter and cross-sectional study of joint damage of patients with non-severe hemophilia: A "Mediterranean Group" study
    Room: Exhibition
    Presenting Author: Ihosvany Fernández-Bello, PhD (he/him/his) – Hemostasis and Thrombosis Unit, Regional University Hospital of Málaga, IBIMA, Málaga, Spain.
    Co-Author: Francisco José López Jaime, MD – Hemostasis and Thrombosis Unit, Regional University Hospital of Málaga, IBIMA, Málaga, Spain.
    Co-Author: Jose Manuel Calvo Villas, MD (he/him/his) – HOSPITAL UNIVERSITARIO MIGUEL SERVET ZARAGOZA
    Co-Author: Ana Marco – University General Hospital Dr. Balmis, Alicante, Spain
    Co-Author: Sonia Herrero Martín – University Hospital of Guadalajara
    Co-Author: Laura Entrena – Hospital Universitario Virgen de las Nieves
    Co-Author: Adrián Montaño, PhD (he/him/his) – Hemostasis and Thrombosis Unit, Regional University Hospital of Málaga / University of Salamanca
    Co-Author: Bolívar L- Díaz Jordán – General Hospital of Valdepeñas
    Co-Author: Covadonga García Díaz – Hospital Universitario de Burgos
    Co-Author: Sergio Jurado Herrera – Torrecárdenas University Hospital
    Co-Author: Noelia Pérez González – Torrecárdenas University Hospital
    Co-Author: Mariana Canaro – Son Espases University Hospital
    Co-Author: Faustino García Candel – Hospital Clínico Universitario Virgen de la Arrixaca (Murcia)
    Co-Author: Pascual Marco – Department of Clinical Medicine, Universidad Miguel Hernández, Alicante, Spain
    Hemophilia and Rare Bleeding Disorders
  • Tuesday, Jun 27th
    18:30 – 19:30 ET
    PB1277 - Thrombin generation and clot formation and lysis properties in hemophilia A with and without emicizumab
    Room: Exhibition
    Presenting Author: Daniel Kraemmer, MD (he/him/his) – Department of Medicine I, Clinical Division of Haematology and Haemostaseology; Medical University of Vienna, Vienna, Austria
    Co-Author: Judit Rejtő – Medical University of Vienna, Vienna, Austria
    Co-Author: Peter Quehenberger – Department of Laboratory Medicine, Medical University of Vienna, Vienna, Austria
    Co-Author: Cihan Ay, MD (he/him/his) – Clinical Division of Haematology and Haemostaseology, Department of Medicine I, Medical University of Vienna, Vienna, Austria
    Co-Author: Ingrid Pabinger, MD – Clinical Division of Hematology and Hemostaseology, Department of Medicine I, Medical University of Vienna, Vienna, Austria
    Co-Author: Oliver Königsbrügge – Medical University of Vienna
    Hemophilia and Rare Bleeding Disorders
  • Tuesday, Jun 27th
    18:30 – 19:30 ET
    PB1278 - Title: Real-World data on Hemophilia A patients with inhibitors switching to either BAY 94-9027 or BAY 81-8973 in the ATHNdataset
    Room: Exhibition
    Co-Author: Michael Recht, MD, PhD, MBA (he/him/his) – National Hemophilia Foundation
    Presenting Author: Jessica Charlet, MSc, PhD (she/her/hers) – Bayer Pharmaceuticals
    Co-Author: Thomas Moulton, MD (he/him/his) – Bayer Pharmaceuticals
    Co-Author: Martin Chandler – American Thrombosis Hemostasis Network
    Hemophilia and Rare Bleeding Disorders
  • Tuesday, Jun 27th
    18:30 – 19:30 ET
    PB1279 - E- Health applications on Hemophilia patients: review and experience in a reference hospital in Spain
    Room: Exhibition
    Presenting Author: Olga Benítez, MD – Vall d'Hebrón Barcelona Hospital Campus
    Co-Author: Juan Carlos Juarez Gimenez – Hospital Vall d'Hebron
    Hemophilia and Rare Bleeding Disorders
  • Tuesday, Jun 27th
    18:30 – 19:30 ET
    PB1280 - Excellent real world experience using Damoctocog alfa pegol
    Room: Exhibition
    Presenting Author: Olga Benítez, MD – Vall d'Hebrón Barcelona Hospital Campus
    Co-Author: Juan Carlos Juarez Gimenez – Hospital Vall d'Hebron
    Hemophilia and Rare Bleeding Disorders
  • Tuesday, Jun 27th
    18:30 – 19:30 ET
    PB1281 - Natural History of Hepatitis C Virus (HCV) Infection in Korean Hemophilic Cohort
    Room: Exhibition
    Co-Author: Soyon Kim, PhD., MD. – Kim & Lee's Internal Medicine Clinic
    Co-Author: Sanghoon Lee – Kim’s & Lee Internal Medicine Clinic
    Presenting Author: Sugi Jeon (she/her/hers) – Kim’s & Lee Internal Medicine Clinic
    Co-Author: Hugh Kim – KIM'S & Lee internal medicine clinic
    Hemophilia and Rare Bleeding Disorders
  • Tuesday, Jun 27th
    18:30 – 19:30 ET
    PB1282 - Real-World Unmet Needs Of Adult Patients With Severe Hemophilia A Without Inhibitors In Poland: How To Select The Optimal Therapy?
    Room: Exhibition
    Presenting Author: Jerzy Windyga, Prof. dr med. (he/him/his) – Institute of Hematology and Transfusion Medicine
    Co-Author: Joanna Zdziarska – Jagiellonian University Medical College
    Co-Author: Ewa Stefanska-Windyga – Institute of Hematology and Transfusion Medicine
    Co-Author: Weronika Nowak – Medical University of Lodz
    Co-Author: Justyna Kozinska – Medical University of Lublin
    Co-Author: Joanna Rupa-Matysek – Poznan University of Medical Sciences
    Co-Author: Andrzej Mital – Medical University of Gdansk
    Co-Author: Anna Sikorska – Institute of Hematology and Transfusion Medicine
    Co-Author: Jacek Trelinski – Medical University of Lodz
    Hemophilia and Rare Bleeding Disorders
  • Tuesday, Jun 27th
    18:30 – 19:30 ET
    PB1285 - A novel mutation of haemophilia C in a kindred: a F11 splice site variant
    Room: Exhibition
    Presenting Author: Kwok Hei Chan, MBBS (he/him/his) – United Christian Hospital
    Hemophilia and Rare Bleeding Disorders
  • Tuesday, Jun 27th
    18:30 – 19:30 ET
    PB1286 - Cardiac surgery in a patient with severe haemophilia A receiving emicizumab prophylaxis - A case report
    Room: Exhibition
    Presenting Author: Bharath Ram Sreedhar, DNB (he/him/his) – Katharine Dormandy Haemophilia and Thrombosis Centre, Royal Free London NHS Foundation Trust. London, United Kingdom
    Co-Author: Carolyn Maharaj – Katharine Dormandy Haemophilia and Thrombosis Centre, Royal Free London NHS Foundation Trust. London, United Kingdom
    Co-Author: Laura JB Mawer, BA MBBS BChir MRCP PGCert MedEd – Katharine Dormandy Haemophilia and Thrombosis Centre, Royal Free London NHS Foundation Trust. London, United Kingdom
    Co-Author: Paul Batty, MBBS, PhD (he/him/his) – University College London
    Co-Author: Anne Riddell – Katharine Dormandy Haemophilia and Thrombosis Centre, Royal Free Hospital, London, UK
    Co-Author: Molly Musarara, RN, BSC(Hons) – Katharine Dormandy Haemophilia and Thrombosis Centre, Royal Free London NHS Foundation Trust, London, UK
    Co-Author: Elsa Aradom – Katharine Dormandy Haemophilia and Thrombosis Centre, Royal Free London NHS Foundation Trust, London, UK
    Co-Author: Fabio De Robertis – Royal Brompton and Harefield Hospitals, London, United Kingdom
    Co-Author: Silvia Lovato – Royal Brompton and Harefield Hospitals, London, United Kingdom
    Co-Author: Alessandra Verzelloni Sef – Royal Brompton and Harefield Hospitals, London, United Kingdom
    Co-Author: Giuditta Coppola – Royal Brompton and Harefield Hospitals, London, United Kingdom
    Co-Author: Pratima Chowdary, MD – Katharine Dormandy Haemophilia and Thrombosis Centre, Royal Free London NHS Foundation Trust, London, United Kingdom
    Hemophilia and Rare Bleeding Disorders
  • Tuesday, Jun 27th
    18:30 – 19:30 ET
    PB1287 - Efficacy of Florio Haemo in improving health-related quality of life and treatment adherence in patients with Hemophilia
    Room: Exhibition
    Co-Author: Ghaleb Elyamany – Prince Sultam Medical Military City
    Presenting Author: Fahad M. Alabbas, MD – Prince Sultan Medical Military City (PSMMC)
    Co-Author: Luluh Albehlal – Prince Sultam Medical Military City
    Co-Author: Abdullah Tammas – Prince Sultam Medical Military City
    Hemophilia and Rare Bleeding Disorders
  • Tuesday, Jun 27th
    18:30 – 19:30 ET
    PB1288 - Immune tolerance induction (ITI) strategies in haemophilia A patients with inhibitors – data from the MOTIVATE study
    Room: Exhibition
    Presenting Author: Carmen Escuriola-Ettingshausen, MD – Haemophilia Centre Rhine-Main, Mörfelden-Walldorf, Germany
    Co-Author: Robert F. Sidonio, Jr., MD, MSc – Aflac Cancer and Blood Disorders Center, Children’s Healthcare of Atlanta, Department of Pediatrics, Emory University School of Medicine
    Hemophilia and Rare Bleeding Disorders
  • Tuesday, Jun 27th
    18:30 – 19:30 ET
    PB1289 - Real-world data of hemophilia A with inhibitor patients using emicizumab – 1st report in Korea
    Room: Exhibition
    Presenting Author: Seung-min Hahn, MA, MD – Severance Hospital, Yonsei University College of Medicine
    Co-Author: Ye-Jee Shim – Department of Pediatrics, Keimyung University School of Medicine, Keimyung University Dongsan Hospital,
    Co-Author: Soyon Kim, PhD., MD. – Kim & Lee's Internal Medicine Clinic
    Co-Author: Chuhl-Joo Lyu – Department of Pediatrics, Yonsei University College of Medicine
    Co-Author: Young-Shil Park – Department of Pediatrics, Kyung Hee University College of Medicine, Kyung Hee University Hospital at Gangdong
    Hemophilia and Rare Bleeding Disorders
  • Tuesday, Jun 27th
    18:30 – 19:30 ET
    PB1290 - Successful very low dose immune tolerance induction with albutrepenonacog alfa in a severe hemophilia B child with anaphylactic reaction to factor IX
    Room: Exhibition
    Co-Author: Ihosvany Fernández-Bello, PhD (he/him/his) – Hemostasis and Thrombosis Unit, Regional University Hospital of Málaga, IBIMA, Málaga, Spain.
    Presenting Author: Francisco José López Jaime, MD – Hemostasis and Thrombosis Unit, Regional University Hospital of Málaga, IBIMA, Málaga, Spain.
    Co-Author: Adrián Montaño, PhD (he/him/his) – Hemostasis and Thrombosis Unit, Regional University Hospital of Málaga / University of Salamanca
    Co-Author: Rosario Prieto Bonilla – Hematology Service, Hospital Materno-Infantil de Málaga, Málaga, Spain.
    Co-Author: Daniel Bardán Rebollar – Hematology Service, Hospital Materno-Infantil de Málaga, Málaga, Spain.
    Co-Author: Ángeles Palomo Bravo – Hematology Service, Hospital Materno-Infantil de Málaga, Málaga, Spain.
    Hemophilia and Rare Bleeding Disorders
  • Tuesday, Jun 27th
    18:30 – 19:30 ET
    PB1291 - Joint range of motion findings among female patients with hemophilia A from the ATHNdataset
    Room: Exhibition
    Co-Author: Michael Recht, MD, PhD, MBA (he/him/his) – National Hemophilia Foundation
    Co-Author: Lena Charafi – Bayer US Pharmaceuticals
    Presenting Author: Thomas Moulton, MD (he/him/his) – Bayer Pharmaceuticals
    Co-Author: Martin Chandler – American Thrombosis Hemostasis Network
    Hemophilia and Rare Bleeding Disorders
  • Tuesday, Jun 27th
    18:30 – 19:30 ET
    PB1292 - Rationale and Design of pathfinderReal: A Prospective, Non-Interventional Study Assessing Joint Health in Adults With Haemophilia A After Switching to Prophylaxis With Turoctocog Alpha Pegol (N8-GP)
    Room: Exhibition
    Presenting Author: Cihan Ay, MD (he/him/his) – Clinical Division of Haematology and Haemostaseology, Department of Medicine I, Medical University of Vienna, Vienna, Austria
    Co-Author: Azusa Nagao, MD, MSc – Department of Blood Coagulation, Ogikubo Hospital, Tokyo, Japan
    Co-Author: Darla Liles – East Carolina University
    Co-Author: Davide Matino, MD (he/him/his) – Department of Medicine, Division of Hematology, McMaster University, Hamilton, ON
    Co-Author: Gillian Gidley – Leeds Teaching Hospitals Trust
    Co-Author: John Waller – Novo Nordisk
    Co-Author: Laszlo Nemes – Medical Center of Hungarian Defence Forces
    Co-Author: Maria Elisa Mancuso, MD, PhD (she/her/hers) – IRCCS Humanitas Research Hospital
    Co-Author: Olga Benítez, MD – Vall d'Hebrón Barcelona Hospital Campus
    Co-Author: Johannes Oldenburg, MD (he/him/his) – University Clinic Bonn AöR, Institute of Experimental Haematology and Transfusion Medicine, Bonn, Germany
    Hemophilia and Rare Bleeding Disorders
  • Tuesday, Jun 27th
    18:30 – 19:30 ET
    PB1294 - FIRST REPORTED CASE OF CARDIAC SURGERY IN A PATIENT WITH HEMOPHILIA B ON TREATMENT WITH ALBUTREPENONACOG ALFA (rIX-FP).
    Room: Exhibition
    Co-Author: Francisco José López Jaime, MD – Hemostasis and Thrombosis Unit, Regional University Hospital of Málaga, IBIMA, Málaga, Spain.
    Co-Author: Eva María Calavia Aranda – Hemostasis and Thrombosis Unit, Regional University Hospital of Málaga, IBIMA, Málaga, Spain.
    Co-Author: Ana María Mena Santano, PhD – Hemostasis and Thrombosis Unit, Regional University Hospital of Málaga, IBIMA, Málaga, Spain.
    Presenting Author: Ihosvany Fernández-Bello, PhD (he/him/his) – Hemostasis and Thrombosis Unit, Regional University Hospital of Málaga, IBIMA, Málaga, Spain.
    Co-Author: Adrián Montaño, PhD (he/him/his) – Hemostasis and Thrombosis Unit, Regional University Hospital of Málaga / University of Salamanca
    Hemophilia and Rare Bleeding Disorders
  • Tuesday, Jun 27th
    18:30 – 19:30 ET
    PB1296 - A prospective, non-interventional study to investigate the effectiveness of rVIII-SingleChain in patients with hemophilia A
    Room: Exhibition
    Presenting Author: Johannes Oldenburg, MD (he/him/his) – University Clinic Bonn AöR, Institute of Experimental Haematology and Transfusion Medicine, Bonn, Germany
    Co-Author: Sabrina Juranek – Paediatric Thrombosis and Haemostasis Unit, Dr. von Hauner Children´s Hospital LMU Munich, Germany
    Co-Author: Olga Katsarou – Blood Transfusion Centre, National Reference Centre for Congenital Bleeding Disorders, Laiko General Hospital
    Co-Author: Soraya Benchikh El Fegoun – CSL Behring, Bern, Switzerland
    Co-Author: Ingrid Pabinger, MD – Clinical Division of Hematology and Hemostaseology, Department of Medicine I, Medical University of Vienna, Vienna, Austria
    Hemophilia and Rare Bleeding Disorders
  • Tuesday, Jun 27th
    18:30 – 19:30 ET
    PB1297 - A UK Single Centre Experience of Switching Adolescents with Severe Haemophilia A to Turoctocog Alfa Pegol
    Room: Exhibition
    Co-Author: Sarah Pool, PG Cert – Oxford University Hospitals NHS Foundation Trust
    Co-Author: Alice Wilkinson – Oxford University Hospitals NHS Foundation Trust
    Co-Author: Marie Eales – Oxford University Hospitals NHS Foundation Trust
    Co-Author: Ashley Yburan – Oxford University Hospitals NHS Foundation Trust
    Co-Author: Neha Bhatnagar – Oxford University Hospitals NHS Foundation Trust
    Co-Author: Georgina Hall – Oxford University Hospitals NHS Foundation Trust
    Presenting Author: Saket Badle, MBBS MRCPCH FRCPath MD (Res) – Oxford University Hospitals NHS Foundation Trust
    Hemophilia and Rare Bleeding Disorders
  • Tuesday, Jun 27th
    18:30 – 19:30 ET
    PB1299 - Obstetrical decision-making in moderate or severe hemophilia A and B: a qualitative study exploring parents’ experiences, preferences and needs
    Room: Exhibition
    Co-Author: Shannon J. Lane, MPH – McMaster Centre for Transfusion Research, McMaster University
    Co-Author: Nancy Carter, RN, PhD – McMaster University, Hamilton, ON, Canada
    Co-Author: Erika Aberg, MSc, CCGC, CGC – Maritime Medical Genetics Service, IWK Health
    Co-Author: Joan Crane, MD, MSc, FRCSC – Women's Health, Eastern Health; Memorial University of Newfoundland
    Co-Author: Julie Emberley – University of Manitoba
    Co-Author: Nancy M. Heddle, MSc, FSCML (D) – McMaster University
    Co-Author: Robert J. Klaassen, MD, FRCP(C) – Children’s Hospital of Eastern Ontario
    Co-Author: Michelle Sholzberg, MDCM, FRCPC, MSc., MDCM, FRCPC, MSc – Departments of Medicine, and Laboratory Medicine and Pathobiology, Li Ka Shing Knowledge Institute, University of Toronto, Toronto, ON, Canada
    Presenting Author: Anthony KC. Chan, MBBS – McMaster University, McMaster Children’s Hospital, Hamilton, Canada
    Hemophilia and Rare Bleeding Disorders
  • Tuesday, Jun 27th
    18:30 – 19:30 ET
    PB1300 - Intramural Hematoma of Gastrointestinal Tract in People With Hemophilia: A Pooled Study
    Room: Exhibition
    Presenting Author: Chia-Yau Chang, assistant professor – 1. Department of Pediatrics, School of Medicine, College of Medicine, Taipei Medical University; 2. Division of Pediatric Hematology and Oncology, Department of Pediatrics, Taipei Medical University Hospital, Taipei, Taiwan.
    Co-Author: Wei-Jung Teng – School of Medicine, College of Medicine, Taipei Medical University, Taipei, Taiwan
    Co-Author: Ching-Huei Kung – Department of Medical Imaging, Taipei Medical University Hospital, Taipei, Taiwan
    Co-Author: Mei-Mei Cheng – Department of Pediatric Gastroenterology, Department of Pediatrics, Cheng-Hsin General Hospital, Taipei, Taiwan
    Co-Author: Jia-Ruey Tsai – Division of Hematology/Oncology, Department of Internal Medicine, Taipei Medical University Hospital, Taipei, Taiwan
    Hemophilia and Rare Bleeding Disorders
  • Tuesday, Jun 27th
    18:30 – 19:30 ET
    PB1301 - Low-titer inhibitor and decreased FVIII activity to 1.1% with increased bleeding in a 4 year old patient with congenital mild hemophilia A
    Room: Exhibition
    Presenting Author: Ivonne Wieland, MD – Pediatric hematology and Oncology, Hannover medical university
    Co-Author: Katharina Becker (she/her/hers) – Children's Hospital, Hannover Medical School
    Co-Author: Diana Stichel – Goethe University Frankfurt, University Hospital, Department of Paediatrics and Adolescent Medicine, Clinical and Molecular Haemostasis, Frankfurt am Main, Germany
    Co-Author: Christoph Koenigs, Dr. Dr. – University Hospital Frankfurt, Department of Paediatrics and Adolescent Medicine, Frankfurt, Germany
    Hemophilia and Rare Bleeding Disorders
  • Tuesday, Jun 27th
    18:30 – 19:30 ET
    PB1303 - A study of support for hemophilia patients using the "Questionnaire for daily movement and sensory of PwH”
    Room: Exhibition
    Presenting Author: Aya Nakao, PhD – Ehime University Hospital
    Co-Author: jun yamanouchi – Ehime University Hospital
    Co-Author: kentaro kawabe – Ehime University Hospital
    Co-Author: katsuto takenaka – Ehime University Hospital
    Hemophilia and Rare Bleeding Disorders
  • Tuesday, Jun 27th
    18:30 – 19:30 ET
    PB1304 - Development of a Multidisciplinary Bleeding Disorder Committee in a reference hospital
    Room: Exhibition
    Presenting Author: Olga Benítez, MD – Vall d'Hebrón Barcelona Hospital Campus
    Co-Author: Juan Carlos Juarez Gimenez – Hospital Vall d'Hebron
    Co-Author: Eva Alvarez – Hospital Vall d'Hebron
    Co-Author: Olga Benitez – Thrombosis and Hemostasis Unit, Department of Hematology, Vall d'Hebron University Hospital
    Co-Author: Marti Plommer – Hospital Vall d'Hebron
    Co-Author: Jose Bernabeu – Hospital Vall d'Hebron
    Hemophilia and Rare Bleeding Disorders
  • Tuesday, Jun 27th
    18:30 – 19:30 ET
    PB1306 - Inhibitor recurrence following immune tolerance induction in a hemophilia A patient with inhibitor post COVID-19 infection
    Room: Exhibition
    Presenting Author: Shin-Nan Cheng, Medical Doctor – Hemophilia center, Department of Pediatrics, Tungs’ Taichung MetroHarbor Hospital, Taichung
    Co-Author: Li-Ting Wang, Nursing – Hemophilia and Rare disease treatment center, Tungs’Taichung MetroHabor Hospital
    Co-Author: Jui-Ting Yu – Department Hematology and Oncology, Tungs’Taichung MetroHabor Hospital
    Hemophilia and Rare Bleeding Disorders
  • Tuesday, Jun 27th
    18:30 – 19:30 ET
    PB1307 - Management of severe Hemophilia A patients: Low-dose prophylaxis Vs on- demand treatment.
    Room: Exhibition
    Presenting Author: Munira Borhany, MBBS, MCPS, FCPS, FRCP (Edin), FRCPath – Haemophilia Welfare Society, Karachi
    Co-Author: Rabeea Ali – National Institute of Blood Diseases
    Co-Author: Madiha Abid, MSPH – National Institute of Blood diseases and Bone Marrow Transplantation, Street 2/A, Block 17, Gulshan-e-Iqbal, KDA Scheme 24, Karachi, Sindh, Pakistan.
    Co-Author: Sidra Zafar – National Institute of Blood Diseases and Bone Marrow Transplantation
    Co-Author: Rukhshanda Nadeem – Haemophilia Welfare Society, Karachi
    Co-Author: Raheel Ahmed – Haemophilia Welfare Society, Karachi
    Hemophilia and Rare Bleeding Disorders
  • Tuesday, Jun 27th
    18:30 – 19:30 ET
    PB1308 - Successful hip arthroplasty in a patient with combined factor V and factor FVIII deficiency
    Room: Exhibition
    Presenting Author: Wen Yang, MA – Department of Hematology, The Second Affiliated Hospital of Kunming Medical University, Yunnan, China
    Co-Author: Hongli Mu – Department of Hematology, The Second Affiliated Hospital of Kunming Medical University, Yunnan, China
    Co-Author: Zeping Zhou – Department of Hematology, The Second Affiliated Hospital of Kunming Medical University, Yunnan, China
    Hemophilia and Rare Bleeding Disorders
  • Tuesday, Jun 27th
    18:30 – 19:30 ET
    PB1309 - Switching from Factor VIIa to Emicizumab in Patients with Hemophilia A and Inhibitor (HAI) in Korea
    Room: Exhibition
    Co-Author: Soyon Kim, PhD., MD. – Kim & Lee's Internal Medicine Clinic
    Co-Author: Sanghoon Lee – Kim’s & Lee Internal Medicine Clinic
    Presenting Author: Sugi Jeon (she/her/hers) – Kim’s & Lee Internal Medicine Clinic
    Co-Author: Hugh Kim – KIM'S & Lee internal medicine clinic
    Hemophilia and Rare Bleeding Disorders
  • Tuesday, Jun 27th
    18:30 – 19:30 ET
    PB1310 - Urgent reversal of DOAC anticoagulant effect with Prothrombin Complex Concentrate: Experience in Mexico
    Room: Exhibition
    Co-Author: Juan Pablo Macías-Flores, MD – Unidad de Investigación Médica en Trombosis, Hemostasia y Aterogénesis, Instituto Mexicano del Seguro Social
    Co-Author: Atenas Villela-Peña, N/A – Unidad de Investigación Médica en Trombosis, Hemostasia y Aterogénesis, Instituto Mexicano del Seguro Social
    Co-Author: Adriana Tripp-Aguilar, N/A – Unidad de Investigación Médica en Trombosis, Hemostasia y Aterogénesis, Instituto Mexicano del Seguro Social
    Co-Author: Carolina Moreira-Ponce, N/A – Unidad de Investigación Médica en Trombosis, Hemostasia y Aterogénesis, Instituto Mexicano del Seguro Social
    Co-Author: Emmanuel Martínez-Moreno, N/A – Unidad de Investigación Médica en Trombosis, Hemostasia y Aterogénesis, Instituto Mexicano del Seguro Social
    Co-Author: Claudia Telleria-Arispe, N/A – Unidad de Investigación Médica en Trombosis, Hemostasia y Aterogénesis, Instituto Mexicano del Seguro Social
    Presenting Author: Abraham Majluf-Cruz, MD, PhD (he/him/his) – Unidad médica de investigación de trombosis, hemostasia y aterogénesis, Instituto Mexicano del Seguro Social
    Hemophilia and Rare Bleeding Disorders
  • Tuesday, Jun 27th
    18:30 – 19:30 ET
    PB1311 - Prophylactic Efficacy Of VGA039, An Anti-Protein S Monoclonal Antibody, In A Novel Non-Human Primate Model Of Acquired Von Willebrand Disease
    Room: Exhibition
    Co-Author: Ian Huck – Vega Therapeutics
    Co-Author: Lilley Leong – Vega Therapeutics
    Co-Author: Tony Byun – Vega Therapeutics
    Presenting Author: Benjamin Kim, MD, MPhil – Vega Therapeutics
    Co-Author: Alina He – Vega Therapeutics
    Co-Author: Joanne Chan – Vega Therapeutics
    Co-Author: Young Choe – Vega Therapeutics
    Co-Author: Christopher J. Horvath – Vega Therapeutics
    Co-Author: Stephen J. Moore – Vega Therapeutics
    Co-Author: Sandip Panicker, PhD (he/him/his) – Vega Therapeutics
    Co-Author: Graham Parry
    Hemophilia and Rare Bleeding Disorders
  • Tuesday, Jun 27th
    18:30 – 19:30 ET
    PB1312 - “The doctor says so” – Patient Values and Preferences Regarding Resumption of Oral Anticoagulation After Gastrointestinal Bleeding
    Room: Exhibition
    Presenting Author: Nahya Awada, PhD in Public Policy – The Ottawa Hospital and Ottawa Hospital Research Institute
    Co-Author: Kevin Chien, MD – University of Ottawa
    Co-Author: Derek Little – McMaster University
    Co-Author: Marc Carrier, MD – Ottawa Hospital Research Institute, Ottawa, ON, Canada
    Co-Author: Ken Deal – McMaster University
    Co-Author: Joanna C. Dionne – McMaster University
    Co-Author: James Douketis, MD (he/him/his) – McMaster University/St. Joseph's Healthcare
    Co-Author: Nauzer Forbes – University of Calgary
    Co-Author: Anne Holbrook – McMaster University
    Co-Author: Margaret Ostrowski – CanVECTOR
    Co-Author: Tara Robertson – McMaster University
    Co-Author: Dawn Stacey – University of Ottawa
    Co-Author: Carol West (she/her/hers) – CanVECTOR
    Co-Author: Ted Xenodemetropoulos – McMaster University
    Co-Author: Feng Xie – McMaster University
    Co-Author: Deborah M. Siegal, MD MSc FRCPC – The Ottawa Hospital
    Hemophilia and Rare Bleeding Disorders
  • Tuesday, Jun 27th
    18:30 – 19:30 ET
    PB1313 - Factor V as adjunct to fibrinogen and prothrombin complex concentrate in an in vitro model of combined severe trauma-induced coagulopathy and rivaroxaban anticoagulation
    Room: Exhibition
    Presenting Author: Herm-Jan M. Brinkman, PhD (he/him/his) – Department of Molecular Hematology, Sanquin Research, Amsterdam, The Netherlands
    Co-Author: Marleen Zuurveld – Department of Molecular Hematology, Sanquin Research, Amsterdam, The Netherlands
    Co-Author: Joost CM Meijers – Department of Molecular Hematology, Sanquin Research, Amsterdam, The Netherlands
    Hemophilia and Rare Bleeding Disorders
  • Tuesday, Jun 27th
    18:30 – 19:30 ET
    PB1314 - Risk Assessing Medical Inpatients for Bleeding Events: The Medical Inpatients Thrombosis and Hemostasis (MITH) Study
    Room: Exhibition
    Presenting Author: Hanny Al-Samkari, MD (he/him/his) – Harvard Medical School
    Co-Author: Katherine S. Wilkinson, MS – The Larner College of Medicine at the University of Vermont
    Co-Author: Nicholas S. Roetker – Hennepin Healthcare Research Institute
    Co-Author: Andrew D. Sparks, MS – The Larner College of Medicine at the University of Vermont
    Co-Author: Allen B. Repp, MD, MSc (he/him/his) – Department of Medicine, The Larner College of Medicine at the University of Vermont
    Co-Author: Ryan Thomas, MD – Hematology/Oncology Division, Department of Medicine, The Larner College of Medicine at the University of Vermont
    Co-Author: Nicholas L. Smith – Department of Epidemiology, School of Public Health, University of Washington
    Co-Author: Chris Holmes, MD PhD – University of Vermont
    Co-Author: Ryan Packer – University of Vermont
    Co-Author: Mary Cushman, MD, MSc (she/her/hers) – Department of Medicine, Larner College of Medicine at the University of Vermont, USA
    Co-Author: Neil A. Zakai, MD, MSc (he/him/his) – Hematology/Oncology Division, Department of Medicine, The Larner College of Medicine at the University of Vermont
    Hemophilia and Rare Bleeding Disorders
  • Tuesday, Jun 27th
    18:30 – 19:30 ET
    PB1315 - Weight-band dosing with Mim8: using modelling to support a streamlined approach to haemophilia A treatment
    Room: Exhibition
    Co-Author: Mads Kreilgaard – Novo Nordisk A/S
    Presenting Author: Irina Matytsina, MD, MSc Pharm Med – Novo Nordisk A/S
    Co-Author: Paula Persson – Novo Nordisk A/S
    Hemophilia and Rare Bleeding Disorders
  • Tuesday, Jun 27th
    18:30 – 19:30 ET
    PB1316 - Impact of Synonymous Gene Recoding on ADAMTS13
    Room: Exhibition
    Presenting Author: Brian Lin, PhD – US Food and Drug Administration
    Co-Author: Randilu Amarasinghe – US Food and Drug Administration
    Co-Author: Upendra K. Katneni, PhD – US Food and Drug Administration
    Co-Author: Katarzyna I. Jankowska – US Food and Drug Administration
    Co-Author: Nobuko Hamasaki-Katagiri – US Food and Drug Administration
    Co-Author: David D. Holcomb – US Food and Drug Administration
    Co-Author: Nigam Padhiar – US Food and Drug Administration
    Co-Author: Sarah E. Fumagalli – US Food and Drug Administration
    Co-Author: Je-Nie Phue – US Food and Drug Administration
    Co-Author: Wells W. Wu – US Food and Drug Administration
    Co-Author: Arnab Ghosh – Cleveland State University
    Co-Author: Darón I. Freedberg – US Food and Drug Administration
    Co-Author: Ofer Kimchi – Princeton University
    Co-Author: Rong-Fong Shen – US Food and Drug Administration
    Co-Author: Anton A. Komar – Cleveland State University
    Co-Author: Zuben E. Sauna – U.S. Food and Drug Administration
    Co-Author: Chava Kimchi-Sarfaty – US Food and Drug Administration
    Hemophilia and Rare Bleeding Disorders
  • Tuesday, Jun 27th
    18:30 – 19:30 ET
    PB1317 - Assessment of the Combined Effects of Emicizumab and Fitusiran with in vitro Spiking of Emicizumab and Simulated Fitusiran into Factor VIII Deficient Plasma using Thrombin Generation Assay
    Room: Exhibition
    Presenting Author: Sibgha Zaheer, MD MPH – Children's Hospital Los Angeles
    Co-Author: Elizabeth Marquez-Casas – Children's Hospital Los Angeles
    Co-Author: Hande Kizilocak, MD – Children's Hospital Los Angeles
    Co-Author: Guy Young, MD – Children's Hospital Los Angeles
    Hemophilia and Rare Bleeding Disorders
  • Tuesday, Jun 27th
    18:30 – 19:30 ET
    PB1319 - Efficacy, safety and satisfaction of using Emicizumab in Hemophilia A patients without Factor VIII Inhibitors: an integrative review
    Room: Exhibition
    Co-Author: Isabela de Oliveira Araujo (she/her/hers) – Universidade Federal de Juiz de Fora
    Co-Author: Lucas N. Fonseca – Centro Universitário Presidente Antonio Carlos
    Presenting Author: Daniela Oliveira Werneck Rodrigues, PhD (she/her/hers) – Fundação Hemominas
    Hemophilia and Rare Bleeding Disorders
  • Tuesday, Jun 27th
    18:30 – 19:30 ET
    PB1320 - A Phase 1 Study of the Safety, Tolerability, Pharmacokinetics and Pharmacodynamics of MG1113 in Healthy Subjects and Hemophilia Patients
    Room: Exhibition
    Presenting Author: Jung Woo Han, MD – Department of Pediatric Hematology-Oncology, Yonsei Cancer Center, Yonsei University Health System
    Co-Author: Yoonjung Choi – GC Biopharma Corp.
    Co-Author: Seon Hui Kim – GC Biopharma Corp.
    Co-Author: Sangbin Lee – GC Biopharma Corp.
    Co-Author: Ji-Young Park – Department of Clinical Pharmacology and Toxicology, Anam Hospital, Korea University College of Medicine
    Hemophilia and Rare Bleeding Disorders
  • Tuesday, Jun 27th
    18:30 – 19:30 ET
    PB1321 - Efficacy/Effectiveness and Safety of Emicizumab Prophylaxis in the Treatment of Hemophilia A: A Systematic Review with Meta-Analysis
    Room: Exhibition
    Co-Author: Roberto Lúcio Muniz Júnior, Jr. – Faculty of Pharmacy, Universidade Federal de Minas Gerais
    Co-Author: Maiara Silva Araújo – Faculty of Pharmacy, Universidade Federal de Minas Gerais
    Presenting Author: Mariana Michel Barbosa, PhD (she/her/hers) – Faculty of Pharmacy, Universidade Federal de Minas Gerais
    Co-Author: Ricardo M. Camelo, MD, MSc, MBA – Faculty of Pharmacy, Universidade Federal de Minas Gerais
    Co-Author: Juliana Alvares-Teodoro – Faculty of Pharmacy, Universidade Federal de Minas Gerais
    Hemophilia and Rare Bleeding Disorders
  • Tuesday, Jun 27th
    18:30 – 19:30 ET
    PB1322 - Emicizumab wastage estimation for treating people with hemophilia A and inhibitors who failed immune tolerance induction according to the current Brazilian public health protocol
    Room: Exhibition
    Presenting Author: Mariana Michel Barbosa, PhD (she/her/hers) – Faculty of Pharmacy, Universidade Federal de Minas Gerais
    Co-Author: Ricardo M. Camelo, MD, MSc, MBA – Faculty of Pharmacy, Universidade Federal de Minas Gerais
    Co-Author: Augusto Afonso Guerra Júnior – Faculty of Pharmacy, Universidade Federal de Minas Gerais
    Co-Author: Francisco de Assis Acurcio – Faculty of Pharmacy, Universidade Federal de Minas Gerais
    Co-Author: Juliana Alvares-Teodoro – Faculty of Pharmacy, Universidade Federal de Minas Gerais
    Hemophilia and Rare Bleeding Disorders
  • Tuesday, Jun 27th
    18:30 – 19:30 ET
    PB1323 - Impact on thrombin generation of direct oral anticoagulants in a FVIII deficient plasma spiked with emicizumab and human FVIII.
    Room: Exhibition
    Presenting Author: Sylvain Lamoine, PhD – University hospital of Clermont-Ferrand, Hopital Estaing, Clermont-Ferrand, France
    Co-Author: Vincent Jury – University hospital of Clermont-Ferrand, Hopital Estaing, Clermont-Ferrand, France
    Co-Author: Aurélien Lebreton – Service d’hématologie, CHU Clermont-Ferrand, Hôpital Estaing
    Hemophilia and Rare Bleeding Disorders
  • Tuesday, Jun 27th
    18:30 – 19:30 ET
    PB1324 - Evaluation of the analytical performance of a modified one-stage FVIII assay for the plasmatic quantification of Emicizumab
    Room: Exhibition
    Co-Author: Rodolfo E. Sueldo, PhD – Laboratorio de Hematología y Hemostasia. Hospital César Milstein Laboratorio de Hemostasia. Servicio de Hematología y Oncología Hospital de Pediatría Prof. Dr. Juan P. Garrahan
    Presenting Author: Mirta del valle Arias, BSc – Laboratorio de Hematología y Hemostasia. Hospital César Milstein
    Co-Author: Alejandra Baques – Servicio de Hemofilia. Hospital César Milstein
    Hemophilia and Rare Bleeding Disorders
  • Tuesday, Jun 27th
    18:30 – 19:30 ET
    PB1325 - A novel recombinant factor VII D60A may potentially reduce the risk of thrombotic complications
    Room: Exhibition
    Presenting Author: Karnsasin Seanoon, PhD – Department of Pharmacology, Faculty of Science, Mahidol University, Bangkok, Thailand
    Co-Author: Panwajee Payongsri – Department of Biotechnology, Faculty of Science, Mahidol University, Bangkok, Thailand
    Co-Author: Nongnuch Sirachainan, MD – Faculty of Medicine Ramathibodi hospital, Mahidol University, Bangkok, Thailand
    Co-Author: Ampaiwan Chuansumrit – Department of Pediatrics, Faculty of Medicine Ramathibodi Hospital, Mahidol University, Bangkok, Thailand
    Co-Author: Suradej Hongeng – Department of Pediatrics, Faculty of Medicine Ramathibodi Hospital, Mahidol University, Bangkok, Thailand
    Co-Author: Pansakorn Tanratana, MD, PhD – Department of Pharmacology, Faculty of Science, Mahidol University
    Hemophilia and Rare Bleeding Disorders
  • Tuesday, Jun 27th
    18:30 – 19:30 ET
    PB1326 - Real-world data on correlation between emicizumab plasma levels, ex-vivo procoagulant profile and spontaneous joint annualized bleeding rate of patients on emicizumab prophylaxis
    Room: Exhibition
    Co-Author: Francisco José López Jaime, MD – Hemostasis and Thrombosis Unit, Regional University Hospital of Málaga, IBIMA, Málaga, Spain.
    Co-Author: Ana Marco – University General Hospital Dr. Balmis, Alicante, Spain
    Co-Author: Adrián Montaño, PhD (he/him/his) – Hemostasis and Thrombosis Unit, Regional University Hospital of Málaga / University of Salamanca
    Co-Author: Ángeles Palomo Bravo – Hematology Service, Hospital Materno-Infantil de Málaga, Málaga, Spain.
    Co-Author: Francisco D. Muñoz López – Hematology Service, Hospital Materno-Infantil de Málaga, Málaga, Spain.
    Co-Author: Pascual Marco – Department of Clinical Medicine, Universidad Miguel Hernández, Alicante, Spain
    Presenting Author: Ihosvany Fernández-Bello, PhD (he/him/his) – Hemostasis and Thrombosis Unit, Regional University Hospital of Málaga, IBIMA, Málaga, Spain.
    Hemophilia and Rare Bleeding Disorders
  • Tuesday, Jun 27th
    18:30 – 19:30 ET
    PB1327 - Bioequivalence of a Generic Version of rFVIIa (Aryoseven) as Compared to the Branded Version of rFVIIa (Novoseven).
    Room: Exhibition
    Co-Author: Bulent Kantarcioglu, MD – Loyola University Chicago
    Co-Author: Nasir Sadeghi – Loyola University Chicago
    Co-Author: Fakiha Siddiqui, PhD Candidate – Department of Pathology and Laboratory Medicine, Cardiovascular Research Institute, Loyola University Chicago, Health Sciences Division, Maywood, IL, USA.
    Presenting Author: Emily Krupa, BS – Loyola University Chicago
    Co-Author: Debra Hoppensteadt – Loyola University Chicago
    Co-Author: Massimo Iocobelli – Loyola University Chicago
    Co-Author: Jawed Fareed, n/a – Loyola University Medical Center
    Hemophilia and Rare Bleeding Disorders
  • Tuesday, Jun 27th
    18:30 – 19:30 ET
    PB1329 - Retrospective Study of the Effectiveness and Safety of the Use of rIX-FP in Patients with Haemophilia B. Experience of four centres in the Region of Castilla y León.
    Room: Exhibition
    Co-Author: Natalia Carpizo Jiménez – Hospital Universitario Río Hortega de Valladolid
    Co-Author: José Manuel Martín Antorán – Complejo Asistencial de Palencia
    Co-Author: María Paz Martínez Badas – Complejo Asistencial de Ávila
    Co-Author: Covadonga García Díaz – Hospital Universitario de Burgos
    Co-Author: Ana Campano García – Hospital Universitario Río Hortega de Valladolid
    Presenting Author: Elena María Fernández Fontecha – Hospital Universitario Río Hortega de Valladolid
    Co-Author: Miguel Ángel Pozas Mañas – Hospital Universitario Río Hortega de Valladolid
    Co-Author: Luis Javier García Frade – Hospital Universitario Río Hortega de Valladolid
    Hemophilia and Rare Bleeding Disorders
  • Tuesday, Jun 27th
    18:30 – 19:30 ET
    PB1331 - NEW PARADIGM IN THE TREATMENT OF HEMOPHILIA B: SPANISH REAL-LIFE EXPERIENCE WITH rIX-FP
    Room: Exhibition
    Presenting Author: Cristina Sierra Aisa, MD – Hospital Universitario Cruces (Barakalo-Bizkaia)
    Co-Author: Carlos Pisón – Hospital Universitario Araba
    Co-Author: Juan Carlos García-Ruiz – Hospital Cruces
    Co-Author: Ana Moretó Quintana – Hospital Cruces
    Co-Author: Miren Gabilondo – Hospital Universitario Araba
    Co-Author: Angel Pereda – Hospital Universitario Araba
    Co-Author: Jose Maria Guinea – Hospital Universitario Araba
    Hemophilia and Rare Bleeding Disorders
  • Wednesday, Jun 28th
    08:30 – 09:45 ET
    SOA 25.4 - Inhibitors and How Do We Deal With Them in 2023
    Room: 516
    Moderator: Manuel Carcao, MD, FRCPC – Division of Haematology/Oncology, Department of Paediatrics, Hospital for Sick Children, University of Toronto, Toronto, Canada
    Moderator: Kathelijn Fischer, MD PhD MSc (she/her/hers) – University Medical Center Utrecht
    Hemophilia and Rare Bleeding Disorders
  • Wednesday, Jun 28th
    08:30 – 08:55 ET
    SOA 25.1 - Hemophilia A: Inhibitor Prevention and Eradication in 2023 and Beyond
    Room: 516
    Speaker: David Lillicrap, MD – Department of Pathology and Molecular Medicine, Queen's University
    Hemophilia and Rare Bleeding Disorders
  • Wednesday, Jun 28th
    08:55 – 09:20 ET
    SOA 25.2 - Approach to PUPs in 2023
    Room: 516
    Speaker: Samantha Gouw, MD, PhD (she/her/hers) – The University of Amsterdam
    Hemophilia and Rare Bleeding Disorders
  • Wednesday, Jun 28th
    09:20 – 09:45 ET
    SOA 25.3 - Hemophilia B: Where Are We at With Inhibitor Development and Eradication?
    Room: 516
    Speaker: Katharina Holstein, MD (she/her/hers) – University Hospital Hamburg Eppendorf
    Hemophilia and Rare Bleeding Disorders
  • Wednesday, Jun 28th
    10:15 – 11:30 ET
    OC 69.6 - Hemophilia - Novel Therapies II
    Room: 517
    Moderator: Alok Srivastava, MD, FRACP, FRCPA, FRCP – Christian Medical College, Vellore, India
    Moderator: Marie-Claude Pelland-Marcotte, MD PhD (she/her/hers) – Centre Hospitalier Universitaire de Quebec, Universite Laval
    Hemophilia and Rare Bleeding Disorders
  • Wednesday, Jun 28th
    10:15 – 11:30 ET
    OC 75.6 - Rare Bleeding Disorders II
    Room: 510
    Moderator: Diane Nugent, MD (she/her/hers) – CHOC Childrens and Center for Inherited Blood Disorders
    Moderator: Veerle Labarque, MD, PhD – University Hospitals Leuven, Belgium
    Hemophilia and Rare Bleeding Disorders
  • Wednesday, Jun 28th
    10:15 – 10:30 ET
    OC 69.1 - Thrombin-mediated autoregulation restores sensitivity to the coagulation feedback loop et reduces the risk of prothrombotic events associated with FVIII mimetic antibodies
    Room: 517
    Presenting Author: Vincent Muczynski, PhD (he/him/his) – University College London (UCL)
    Co-Author: Angel smith – NovalGen Ltd
    Co-Author: Thibaud Sefiane – INSERM U1176, Hôpital Bicêtre
    Co-Author: Olivier D. Christophe – Laboratory for Hemostasis, Inflammation and Thrombosis, Unité Mixte de Recherche S1176, Institut National de la Santé et de la Recherche Médicale, Université Paris-Saclay, Le Kremlin-Bicêtre, France
    Co-Author: Peter J. Lenting, PhD – Laboratory for Hemostasis, Inflammation and Thrombosis, Unité Mixte de Recherche S1176, Institut National de la Santé et de la Recherche Médicale, Université Paris-Saclay, Le Kremlin-Bicêtre, France
    Co-Author: David Granger – NovalGen Ltd
    Co-Author: Kerry Chester – University College London (UCL)
    Co-Author: Amit C. Nathwani – University College London (UCL)
    Hemophilia and Rare Bleeding Disorders
  • Wednesday, Jun 28th
    10:15 – 10:30 ET
    OC 75.1 - First US Rare Bleeding Disorder Genotype-Phenotype Registry (ATHN 10) Discovers Many Individuals with Both Novel and Multiple Variants Using a Customized 30-Gene Next-Generation Sequencing Panel
    Room: 510
    Presenting Author: Diane Nugent, MD (she/her/hers) – CHOC Childrens and Center for Inherited Blood Disorders
    Co-Author: Shirley Williams – CHOC Childrens Hospital and UC Irvine
    Co-Author: Christina Ashburner – Center for Inherited Blood Disorder
    Co-Author: Nicole Crook – Center for Inherited Blood Disorders
    Co-Author: Haduwa Momoh – American Thrombosis and Hemostasis Network
    Co-Author: Michael Recht, MD, PhD, MBA (he/him/his) – National Hemophilia Foundation
    Co-Author: Martin Chandler – American Thrombosis Hemostasis Network
    Co-Author: Amy Shapiro – Indiana Hemophilia & Thrombosis Center, Indianapolis, IN, USA
    Hemophilia and Rare Bleeding Disorders
  • Wednesday, Jun 28th
    10:30 – 10:45 ET
    OC 69.2 - Costimulatory domains of second- and third-generation CAR-Tregs affect the type of FVIII-specific Treg responses and might be able to stabilize the Treg phenotype
    Room: 517
    Presenting Author: SARAH SCATIGNA, M.S. – University Hospital Frankfurt Am Main
    Co-Author: Julie Warken – University Hospital Frankfurt am Main
    Co-Author: Aleksander Orlowski – Goethe University Frankfurt, University Hospital, Department of Paediatrics and Adolescent Medicine, Clinical and Molecular Haemostasis, Frankfurt am Main, Germany
    Co-Author: Stephan Schultze-Strasser – University Hospital Frankfurt Am Main
    Co-Author: Christoph Koenigs, Dr. Dr. – University Hospital Frankfurt, Department of Paediatrics and Adolescent Medicine, Frankfurt, Germany
    Co-Author: Anja Schmidt – Goethe University Frankfurt, University Hospital, Department of Paediatrics and Adolescent Medicine, Clinical and Molecular Haemostasis, Frankfurt am Main, Germany
    Hemophilia and Rare Bleeding Disorders
  • Wednesday, Jun 28th
    10:30 – 10:45 ET
    OC 75.2 - Obstetrical complications in hereditary fibrinogen disorders: the Fibrinogest Study
    Room: 510
    Co-Author: Justine Hugon-Rodin, MD PhD (she/her/hers) – Gynecology department, Gynaecological Endocrinology Unit, Hospital Saint Joseph, Paris Division of Gynecology, University Hospitals of Geneve, Geneva, Switzerland
    Co-Author: Camille Carrière – Gynecology Department, Bigorre Hospital Center, Tarbes, France
    Co-Author: Nathalie Trillot – Lille University, CHU, Department of Haematology and Clinical Haemostasis Unit, Lille, France
    Co-Author: Nicolas Drillaud – CRC-MHC, CHU Hôtel-Dieu
    Co-Author: Christine Biron – Haemophilia Treatment Centre, University Hospital, Montpellier, France
    Co-Author: Virginie Barbay – Haemophilia Treatment Centre, University Hospital, Rouen, France
    Co-Author: Pierre Chamouni – Haemophilia Treatment Centre, University Hospital, Rouen, France
    Co-Author: Cécile Lavenu Bombled – Service d’hématologie biologique, Centre de Ressources et Compétences Maladies Constitutionnelles rares, CHU Bicêtre, AP-HP, Université Paris-Saclay et UMR S1176 INSERM, Le Kremlin-Bicêtre, France
    Co-Author: Aurélien Lebreton – Service d’hématologie, CHU Clermont-Ferrand, Hôpital Estaing
    Co-Author: Anna Wieland – Department of Hematology and Central Hematology Laboratory, Bern University Hospital, University of Bern, Switzerland
    Co-Author: Mouhamed D Moussa – Pôle d’Anesthésie-Réanimation, CHU Lille, F59000, Lille, France.
    Co-Author: Thomas Brungs – Haemostasis and Thrombosis Unit, CHR Orleans, Orleans, France
    Co-Author: Brigitte Tardy, MD PhD – Université Jean Monnet Saint-Étienne, CHU Saint-Étienne, Centre de traitement de l'hémophilie, Mines Saint-Etienne, INSERM, SAINBIOSE U1059, F-42023 SAINT-ÉTIENNE, FRANCE
    Co-Author: Céline Desconclois – Biological Hematology, Antoine Béclère Hospital, AP-HP, Paris-Saclay University, Clamart, France
    Co-Author: Philippe Beurrier – Hemophilia Treatment Center, Vascular and Coagulation Clinic, University Hospital Angers, France
    Co-Author: Valérie Gay – Hemophilia Treatment Center, Hospital, Chambéry, France
    Co-Author: Ségolène Clasyssens – Haemophilia Treatment Centre, University Hospital, Toulouse, France
    Co-Author: Emmanuel De Maistre – Hématologie Biologique, CHU, Dijon
    Co-Author: Tomas Simurda, MD, PhD. – National Centre of Hemostasis and Thrombosis, Department of Hematology and Transfusiology, Comenius University in Bratislava, Jessenius Faculty of Medicine in Martin and University Hospital in Martin, Slovakia
    Presenting Author: Alessandro Casini, MD – Division of Angiology and Hemostasis, Faculty of Medicine, Geneva University Hospitals, Geneva, Switzerland
    Hemophilia and Rare Bleeding Disorders
  • Wednesday, Jun 28th
    10:45 – 11:00 ET
    OC 69.3 - Mim8 interference on the measurement of FVIII Standard and Extended half-life products using selected FVIII Chromogenic Assays
    Room: 517
    Presenting Author: Mary M. Robinson, PhD (she/her/hers) – Labcorp Coagulation
    Co-Author: William Pickering, PhD (he/him/his) – Colorado Coagulation, Laboratory Corporation of America Holdings
    Co-Author: Caroline Cogswell – Esoterix Colorado Coagulation
    Co-Author: Wan Hui Ong Clausen – NovoNordisk A/S
    Co-Author: Mirella Ezban – NovoNordisk A/S
    Hemophilia and Rare Bleeding Disorders
  • Wednesday, Jun 28th
    10:45 – 11:00 ET
    OC 75.3 - Phenotype and genotype characterization of patients with congenital fibrinogen deficiencies: a retrospective analysis of the PRO-RBDD database
    Room: 510
    Presenting Author: Samin Mohsenian – Università degli Studi di Milano, Department of Pathophysiology and Transplantation, Milan, Italy
    Co-Author: Roberta Palla – Università degli Studi di Milano, Department of Pathophysiology and Transplantation, Milan, Italy
    Co-Author: Marzia menegatti, PhD – Fondazione IRCCS Ca’ Granda Ospedale Maggiore Policlinico and luigi villa foundation, Angelo Bianchi Bonomi Hemophilia and Thrombosis Center, Milan, Italy
    Co-Author: Andrea Cairo – Fondazione IRCCS Ca’Granda Ospedale Maggiore Policlinico, Angelo Bianchi Bonomi Hemophilia and Thrombosis Center
    Co-Author: Anna Lecchi – Fondazione IRCCS Ca’ Granda Ospedale Maggiore Policlinico and luigi villa foundation, Angelo Bianchi Bonomi Hemophilia and Thrombosis Center, Milan, Italy
    Co-Author: Alessandro Casini, MD – Division of Angiology and Hemostasis, Faculty of Medicine, Geneva University Hospitals, Geneva, Switzerland
    Co-Author: Marguerite Neerman-Arbez – Department of Medicine, Faculty of Medicine, University of Geneva, Geneva, Switzerland
    Co-Author: Rosanna Asselta – IRCCS Humanitas Research Hospital, Milan, Italy
    Co-Author: Philippe De Moerloose – Department of Medicine, Faculty of Medicine, University of Geneva, Geneva, Switzerland
    Co-Author: Flora Peyvandi, MD, PhD (she/her/hers) – IRCCS Ca' Granda Maggiore Hospital Foundation, Angelo Bianchi Bonomi Hemophilia and Thrombosis Center, Milano, Italy; Università degli Studi di Milano, Department of Pathophysiology and Transplantation, Milano, Italy
    Hemophilia and Rare Bleeding Disorders
  • Wednesday, Jun 28th
    11:00 – 11:15 ET
    OC 69.4 - Safety, Pharmacokinetics, and Pharmacodynamics of Single Subcutaneous Injection of NXT007, an Emicizumab-Based Next-Generation Bispecific Antibody, in Healthy Volunteers (NXTAGE Study)
    Room: 517
    Presenting Author: Midori Shima, MD, PhD – Thrombosis and Hemostasis Research Center, Nara Medical University, Kashihara, Japan
    Co-Author: Takehiko Sambe – Showa University
    Co-Author: Takuya Miwa – Chugai Pharmaceutical Co., Ltd., Tokyo, Japan
    Co-Author: Koichiro Yoneyama, MSc – Chugai Pharmaceutical Co., Ltd., Tokyo, Japan
    Co-Author: Takaaki Ishida – Chugai Pharmaceutical Co., Ltd., Tokyo, Japan
    Co-Author: Ryoto Ozaki – Chugai Pharmaceutical Co., Ltd., Tokyo, Japan
    Co-Author: Taigi Yamazaki – Showa University
    Co-Author: Shinichi Kobayashi – Showa University
    Hemophilia and Rare Bleeding Disorders
  • Wednesday, Jun 28th
    11:00 – 11:15 ET
    OC 75.4 - Unraveling the molecular base of FXI deficiency in 96 unrelated Caucasian patients by short- and long-read based sequencing methods: biochemical, functional and clinical consequences
    Room: 510
    Co-Author: Juan Jose Rojo-Carrillo – Servicio de Hematología y Oncología Médica, Hospital Universitario Morales Meseguer, Centro Regional de Hemodonación, Universidad de Murcia, IMIB-Pascual Parrilla, CIBERER, Murcia, Spain
    Co-Author: Belen de la morena-Barrio, PhD – Servicio de Hematología y Oncología Médica, Hospital Universitario Morales Meseguer, Centro Regional de Hemodonación, Universidad de Murcia, IMIB-Pascual Parrilla, CIBERER, Murcia, Spain
    Co-Author: Carlos Bravo-Perez – Servicio de Hematología y Oncología Médica, Hospital Universitario Morales Meseguer, Centro Regional de Hemodonación, Universidad de Murcia, IMIB-Pascual Parrilla, CIBERER, Murcia, Spain
    Co-Author: Antonia Miñano – Servicio de Hematología y Oncología Médica, Hospital Universitario Morales Meseguer, Centro Regional de Hemodonación, Universidad de Murcia, IMIB-Pascual Parrilla, CIBERER, Murcia, Spain
    Co-Author: Jose Padilla – Servicio de Hematología y Oncología Médica, Hospital Universitario Morales Meseguer, Centro Regional de Hemodonación, Universidad de Murcia, IMIB-Pascual Parrilla, CIBERER, Murcia, Spain
    Co-Author: Rosa Cifuentes – Servicio de Hematología y Oncología Médica, Hospital Universitario Morales Meseguer, Centro Regional de Hemodonación, Universidad de Murcia, IMIB-Pascual Parrilla, CIBERER, Murcia, Spain
    Co-Author: Ángeles Palomo Bravo – Hematology Service, Hospital Materno-Infantil de Málaga, Málaga, Spain.
    Co-Author: Vicente Vicente – Servicio de Hematología y Oncología Médica, Hospital Universitario Morales Meseguer, Centro Regional de Hemodonación, Universidad de Murcia, IMIB-Pascual Parrilla, CIBERER, Murcia, Spain
    Co-Author: María Luisa Lozano – Servicio de Hematología y Oncología Médica, Hospital Universitario Morales Meseguer, Centro Regional de Hemodonación, Universidad de Murcia, IMIB-Pascual Parrilla, CIBERER, Murcia, Spain
    Co-Author: Javier Corral, PhD – Servicio de Hematología y Oncología Médica, Hospital Universitario Morales Meseguer, Centro Regional de Hemodonación, Universidad de Murcia, IMIB-Pascual Parrilla, CIBERER, Murcia, Spain
    Presenting Author: Maria Eugenia de la Morena-Barrio, PhD – Servicio de Hematología y Oncología Médica, Hospital Universitario Morales Meseguer, Centro Regional de Hemodonación, Universidad de Murcia, IMIB-Arrixaca, CIBERER, Murcia, Spain
    Hemophilia and Rare Bleeding Disorders
  • Wednesday, Jun 28th
    11:15 – 11:30 ET
    OC 69.5 - Outcomes in Adult and Adolescent Patients With Severe Hemophilia A in the Phase 3 XTEND-1 Study Who Switched to Efanesoctocog Alfa Prophylaxis From an Observational Study With Factor VIII Prophylaxis
    Room: 517
    Presenting Author: Sophie Susen, MD, PhD (she/her/hers) – Univ. Lille, Inserm, CHU Lille, Institut Pasteur de Lille, U1011- EGID, F-59000 Lille, France
    Co-Author: Roshni Kulkarni – Department of Pediatrics and Human Development, Michigan State University, East Lansing, MI, USA
    Co-Author: Keiji Nogami – Nara Medical University, Nara, Japan
    Co-Author: Flora Peyvandi, MD, PhD (she/her/hers) – IRCCS Ca' Granda Maggiore Hospital Foundation, Angelo Bianchi Bonomi Hemophilia and Thrombosis Center, Milano, Italy; Università degli Studi di Milano, Department of Pathophysiology and Transplantation, Milano, Italy
    Co-Author: Barbara A. Konkle, MD (she/her/hers) – University of Washington
    Co-Author: Elena Santagostino – Sobi, Basel, Switzerland
    Co-Author: Umer Khan – Sanofi, San Diego, CA, USA
    Co-Author: Annemieke Willemze – Sanofi, Amsterdam, Netherlands
    Co-Author: Linda Bystricka – Sobi, Stockholm, Sweden
    Co-Author: Jennifer Dumont – Sanofi, Cambridge, MA, USA
    Co-Author: Pratima Chowdary, MD – Katharine Dormandy Haemophilia and Thrombosis Centre, Royal Free London NHS Foundation Trust, London, United Kingdom
    Hemophilia and Rare Bleeding Disorders
  • Wednesday, Jun 28th
    11:15 – 11:30 ET
    OC 75.5 - Prothrombin-Wauwatosa, a natural prothrombin variant with increased anticoagulant function and increased bleeding
    Room: 510
    Presenting Author: Jeremy P. Wood, PhD – University of Kentucky
    Co-Author: Xian Li – University of Kentucky
    Co-Author: Dlovan D Mahmood – University of Kentucky
    Co-Author: Martha Sim – University of Kentucky
    Co-Author: Shawn Jobe – Michigan State University
    Hemophilia and Rare Bleeding Disorders
  • Wednesday, Jun 28th
    13:00 – 14:00 ET
    PO08 - Factor XIII Deficiency As Underlying Cause Of Unexplained Intracranial Hemorrhage
    Room: 10
    Presenting Author: JESSICA SANTOYO CUEVA – HOSPITAL CIVIL DE GUADALAJARA DR. JUAN I MENCHACA
    Co-Author: CAROLINA PEREZ ORNELAS – HOSPITAL CIVIL DE GUADALAJARA DR JUAN I MENCHACA
    Co-Author: ILCE ESTEFANIA CONTRERAS ACEVES – HOSPITAL CIVIL DE GUADALAJARA DR JUAN I MENCHACA
    Co-Author: WANGKY CAROLINA CARRASCO RIVERA – HOSPITAL CIVIL DE GUADALAJARA DR JUAN I MENCHACA
    Co-Author: ROSA MARGARITA CRUZ OSORIO – HOSPITAL CIVIL DE GUADALAJARA DR JUAN I MENCHACA
    Co-Author: MISSAEL DE JESUS SALCEDO HERNANDEZ – HOSPITAL CIVIL DE GUADALAJARA DR JUAN I MENCHACA
    Hemophilia and Rare Bleeding Disorders
  • Wednesday, Jun 28th
    13:00 – 14:00 ET
    PO09 - Hemorrhagic phenotype associated with non-severe deficit of factor VII. Experience of a single center.
    Room: 10
    Presenting Author: Bolivar Luis Diaz Jordan, Dr. – Hospital General de Valdepenas
    Hemophilia and Rare Bleeding Disorders
  • Wednesday, Jun 28th
    13:00 – 14:00 ET
    PO10 - Nuwiq Dosing and outcomes In the ManagEment of women/girls with haemophilia A Needing FVIII treatment for Surgery – an International, Open-label, Non-controlled study (NuDIMENSION)
    Room: 10
    Presenting Author: Natascha Marquardt, MD – Institute for Experimental Hematology and Transfusion Medicine, University Clinic Bonn
    Co-Author: Johannes Oldenburg, MD (he/him/his) – University Clinic Bonn AöR, Institute of Experimental Haematology and Transfusion Medicine, Bonn, Germany
    Co-Author: Martina Jansen – Octapharma Pharmazeutika Produktionsgesellschaft mbH
    Co-Author: Sigurd Franz Knaub, PhD – Octapharma AG
    Hemophilia and Rare Bleeding Disorders
  • Wednesday, Jun 28th
    13:00 – 14:00 ET
    PO11 - Impact of simoctocog alfa prophylaxis on bleeding and joint health in Spanish patients with severe haemophilia A
    Room: 10
    Presenting Author: Maria Teresa Alvarez-Román, MD, PhD – Department of Hematology, University Hospital La Paz, Autonoma University of Madrid, Madrid, Spain
    Co-Author: Patricia Gonzalez Marugan – La Paz University Hospital
    Co-Author: Hortensia De la Corte-Rodríguez – La Paz University Hospital
    Co-Author: Maria Isabel Rivas Pollmar – La Paz University Hospital
    Co-Author: Mónica Martín Salces – La Paz University Hospital
    Co-Author: Eduardo García, MD – La Paz University Hospital
    Co-Author: Mar Gutierrez Alvariño – La Paz University Hospital
    Co-Author: Damaris Zagrean – La Paz University Hospital
    Co-Author: Víctor Jiménez Yuste, MD PhD – La Paz University Hospital
    Hemophilia and Rare Bleeding Disorders
  • Wednesday, Jun 28th
    13:00 – 14:00 ET
    PO12 - Acquired Hemophilia A: Case series
    Room: 10
    Presenting Author: Erik A. Vardumyan, Jr. – Armenian Hemophilia and Thrombosis Treatment center
    Co-Author: Nelli S. Sargsyan – Armenian Hemophilia and Thrombosis Treatment center
    Co-Author: Liana Hambardzumyan, Phd – Armenian Hemophilia and Thrombosis Treatment center
    Co-Author: Sona V. Petrosyan – Armenian Hemophilia and Thrombosis Treatment center
    Co-Author: Karine Arustamyan – Armenian Hemophilia and Thrombosis Treatment center
    Co-Author: Gevorg N. Tamamyan – Armenian Hemophilia and Thrombosis Treatment center
    Co-Author: Armine Harutyunyan – Armenian Hemophilia and Thrombosis Treatment center
    Co-Author: Inga Karapetyan, N/A – Armenian Hemophilia and Thrombosis Treatment center
    Co-Author: Samvel Danelyan – Armenian Hemophilia and Thrombosis Treatment center
    Co-Author: Heghine S. Khachatryan, MD, PhD – Armenian Hemophilia and Thrombosis Treatment center
    Hemophilia and Rare Bleeding Disorders
  • Wednesday, Jun 28th
    13:00 – 14:00 ET
    PO13 - Complex management in a PWH and Guillain Barre Syndrome - Diagnostic and treatment challenges
    Room: 10
    Presenting Author: CORINA MARIN, MD (she/her/hers) – FUNDENI CLINICAL INSTITUTE
    Co-Author: ALEXANDRA - NICOLETA TOTOIANU – FUNDENI CLINICAL INSTITUTE
    Co-Author: HORATIU - FLORIN VULTUR – GIURGIU COUNTY EMERGENCY HOSPITAL PEDIATRIC DEPARTMENT
    Co-Author: ADRIANA DIACONU – FUNDENI CLINICAL INSTITUTE
    Hemophilia and Rare Bleeding Disorders
  • Wednesday, Jun 28th
    13:00 – 14:00 ET
    PO14 - Normalised Bleeds Under Surgical Intervention and Less Hospital Frequencies, an Emicizumab Patient Case Experience in Western Kenya.
    Room: 10
    Presenting Author: Moses Elvis Oburah, N/A (he/him/his) – Moi Teaching And Referral Hospital-AMPATH
    Co-Author: Festus Njuguna – Moi Teaching And Referral Hospital-AMPATH
    Co-Author: Cyrus Njuguna – None
    Co-Author: Ramani Ramalingam – Mount Kenya University-Thika
    Co-Author: Carole Jesang Kilach – None
    Hemophilia and Rare Bleeding Disorders
  • Wednesday, Jun 28th
    13:00 – 14:00 ET
    PO15 - Real-World Experience with Emicizumab Prophylaxis in 2 Portuguese Centers: are these 4 boys the first of many?
    Room: 10
    Presenting Author: Cristina Catarino, Dr (she/her/hers) – Centro Hospitalar Universitário Lisboa Norte
    Co-Author: Fátima Rodrigues – Centro Hospitalar Universitário Lisboa Norte
    Co-Author: Raquel Maia – Centro Hospitalar Universitário Lisboa Central
    Co-Author: Artur Pereira – Centro Hospitalar Universitário Lisboa Norte
    Co-Author: Paula Kjollerstrom – Centro Hospitalar Universitário Lisboa Central
    Co-Author: Filipa Pires – Centro Hospitalar Universitário Lisboa Norte
    Co-Author: Joana S G Pestana, MD (she/her/hers) – Hospital do Espírito Santo - Évora
    Co-Author: Sara Batalha – Centro Hospitalar Universitário Lisboa Central
    Hemophilia and Rare Bleeding Disorders
  • Wednesday, Jun 28th
    13:00 – 14:00 ET
    PO16 - Hemorrhagic Complications in Patients with Hemophilia A
    Room: 10
    Presenting Author: Olga Shatalova, PhD – VolSMU
    Co-Author: Olga Leshina – hematology
    Hemophilia and Rare Bleeding Disorders
  • Wednesday, Jun 28th
    13:00 – 14:00 ET
    PO17 - Impact of Bleeding complications and Joint Disease On quality Of life of patients with severe haemophilia A: A case study of Kenyatta National Hospital haemophilia Clinic.
    Room: 10
    Presenting Author: ROSEANNE M. ANGUCHE, MASTERS DEGREE – kenyatta National Hospital
    Hemophilia and Rare Bleeding Disorders
  • Wednesday, Jun 28th
    13:00 – 14:00 ET
    PO18 - Successful long-term tolerance in patients with hemophilia A and inhibitors receiving emicizumab prophylaxis: A single Saudi center experience
    Room: 10
    Presenting Author: Fahad M. Alabbas, MD – Prince Sultan Medical Military City (PSMMC)
    Co-Author: Hanin Khan – Prince Sultam Medical Military City
    Hemophilia and Rare Bleeding Disorders
  • Wednesday, Jun 28th
    13:00 – 14:00 ET
    PO19 - Clinical experiences in managing the transition to rIX-FP: switching, surgical management and on-demand
    Room: 10
    Presenting Author: Miguel Escobar, MD – University of Texas Health Science Center of Houston, McGovern Medical School, Gulf States Hemophilia and Thrombophilia Center, Houston, Texas
    Co-Author: Mark T. Reding – Center for Bleeding and Clotting Disorders, University of Minnesota, Minneapolis, MN, USA
    Co-Author: Johannes Oldenburg, MD (he/him/his) – University Clinic Bonn AöR, Institute of Experimental Haematology and Transfusion Medicine, Bonn, Germany
    Hemophilia and Rare Bleeding Disorders